anti-NMDA receptor encephalitis

disease
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Also known as limbic encephalitis with N-methyl-D-aspartate receptor antibodieslimbic encephalitis with NMDA receptor antibodies

Summary

anti-NMDA receptor encephalitis (MONDO:0021081) is a disease with 9 GWAS associations across 2 studies and 8 clinical trials. Top therapeutic interventions include rituximab. A subtype of encephalitis — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • Prevalence: Unknown (Worldwide)
  • GWAS associations: 9
  • Phenotypes (HPO): 53
  • Clinical trials: 8

Clinical features

Signs & symptoms

Clinical features (HPO)

53 HPO clinical features (Orphanet curated; top 50 by frequency):

HPO IDTermFrequency
HP:0000708Atypical behaviorVery frequent (80-99%)
HP:0000736Short attention spanVery frequent (80-99%)
HP:0001250SeizureVery frequent (80-99%)
HP:0001289ConfusionVery frequent (80-99%)
HP:0002354Memory impairmentVery frequent (80-99%)
HP:0012229CSF pleocytosisVery frequent (80-99%)
HP:0032264Anti-NMDA receptor antibody positivityVery frequent (80-99%)
HP:0032266CSF anti-NMDA receptor antibody positivityVery frequent (80-99%)
HP:0000738HallucinationsFrequent (30-79%)
HP:0000739AnxietyFrequent (30-79%)
HP:0000746DelusionFrequent (30-79%)
HP:0001945FeverFrequent (30-79%)
HP:0002013VomitingFrequent (30-79%)
HP:0002014DiarrheaFrequent (30-79%)
HP:0002315HeadacheFrequent (30-79%)
HP:0004305Involuntary movementsFrequent (30-79%)
HP:0011289EEG with temporal sharp slow wavesFrequent (30-79%)
HP:0012226Ovarian teratomaFrequent (30-79%)
HP:0012332Abnormal autonomic nervous system physiologyFrequent (30-79%)
HP:0100660DyskinesiaFrequent (30-79%)
HP:0100754ManiaFrequent (30-79%)
HP:0100785InsomniaFrequent (30-79%)
HP:0000709PsychosisOccasional (5-29%)
HP:0000713AgitationOccasional (5-29%)
HP:0000716DepressionOccasional (5-29%)
HP:0000733Abnormal repetitive mannerismsOccasional (5-29%)
HP:0001266ChoreoathetosisOccasional (5-29%)
HP:0001278Orthostatic hypotensionOccasional (5-29%)
HP:0001332DystoniaOccasional (5-29%)
HP:0001336MyoclonusOccasional (5-29%)
HP:0002063RigidityOccasional (5-29%)
HP:0002072ChoreaOccasional (5-29%)
HP:0002133Status epilepticusOccasional (5-29%)
HP:0002179OpisthotonusOccasional (5-29%)
HP:0002197Generalized-onset seizureOccasional (5-29%)
HP:0002300MutismOccasional (5-29%)
HP:0002310Orofacial dyskinesiaOccasional (5-29%)
HP:0002371Loss of speechOccasional (5-29%)
HP:0002463Language impairmentOccasional (5-29%)
HP:0003781Excessive salivationOccasional (5-29%)
HP:0007359Focal-onset seizureOccasional (5-29%)
HP:0008763No social interactionOccasional (5-29%)
HP:0010553Oculogyric crisisOccasional (5-29%)
HP:0012173Orthostatic tachycardiaOccasional (5-29%)
HP:0012333Abnormal sudomotor regulationOccasional (5-29%)
HP:0031258DeliriumOccasional (5-29%)
HP:5200321Amplification of sexual behaviorOccasional (5-29%)
HP:0003006NeuroblastomaVery rare (<1-4%)
HP:0012189Hodgkin lymphomaVery rare (<1-4%)
HP:0100013Neoplasm of the breastVery rare (<1-4%)

Identifiers

Disease identifiers

FieldValue
Canonical nameanti-NMDA receptor encephalitis
Mondo IDMONDO:0021081
MeSHD060426
Orphanet217253
ICD-111568915618
NCITC94853
SNOMED CT716684004
UMLSC2986717
MedGen458943
GARD0020513
Is cancer (heuristic)no

Also known as: anti-NMDA receptor encephalitis · limbic encephalitis with N-methyl-D-aspartate receptor antibodies · limbic encephalitis with NMDA receptor antibodies

Data availability: 9 GWAS associations (2 studies).

Disease family

This is a subtype of encephalitis. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by body system or component › nervous system disordercentral nervous system disorderencephalomyelitisencephalitisanti-NMDA receptor encephalitis

Related subtypes (6): post-vaccinal encephalitis, meningoencephalitis, limbic encephalitis, infectious encephalitis, autoimmune encephalitis, paraneoplastic isolated brainstem encephalitis

Genetics & variants

GWAS landscape

9 GWAS associations across 2 studies. Top hits map to 5 distinct genes (as reported by GWAS).

Top associations by p-value

rsIDp-valueGeneRisk alleleOdds ratio
HLA-DQB1*05:021e-12?2.1
rs109025881e-08LRRK1?2.24
rs37475171e-08IFIH1C1.55
rs753933204e-08ACP2?2.2
HLA-A*11:017e-08?1.56
rs25080081e-07LINC02571 - HLA-BC1.73
HLA-A*02:071e-07?1.73
rs94687312e-07MICC - TMPOP1T0.36
rs1399992284e-06HLA-DRB6, HLA-DRB6A0.7

Top studies (by case count)

StudyLead authorYearCasesControlsTitle
GCST90429007Liu X20243786,576Genome-Wide Association Study Identifies IFIH1 and HLA-DQB1*05:02 Loci Associated With Anti-NMDAR Encephalitis.
GCST90058029Tietz AK20211780Genome-wide Association Study Identifies 2 New Loci Associated With Anti-NMDAR Encephalitis.

Variant details and genetic-evidence tiers

Tier distribution (top 50 variants)

TierVariants
Tier 1: coding1
Tier 2: splice/UTR0
Tier 3: regulatory0
Tier 4: intronic/intergenic8

MAF distribution

BucketVariants
common (>=0.05)9
low_freq (0.01-0.05)0
rare (<0.01)0
unknown0

Functional consequences

ConsequenceCount
intron_variant4
unknown3
missense_variant1
intergenic_variant1

Top variants

rsIDChrPosAllelesMAFConsequenceGenep-valueTier
HLA-DQB1*05:020.081e-12Tier 4: intronic/intergenic
rs1090258815100978492T>C,G0.05intron_variantLRRK11e-08Tier 4: intronic/intergenic
rs37475172162272314T>A,C,G0.32missense_variantIFIH11e-08Tier 1: coding
rs753933201147244920G>C0.05intron_variantACP24e-08Tier 4: intronic/intergenic
HLA-A*11:010.27e-08Tier 4: intronic/intergenic
rs2508008631305720A>G,T0.11intron_variantLINC02571 - HLA-B1e-07Tier 4: intronic/intergenic
HLA-A*02:070.091e-07Tier 4: intronic/intergenic
rs9468731630429437A>G0.14intergenic_variantMICC - TMPOP12e-07Tier 4: intronic/intergenic
rs139999228632556934T>C0.4intron_variantHLA-DRB6, HLA-DRB64e-06Tier 4: intronic/intergenic

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

No druggable-target or therapeutic data for this disease’s cohort.

Clinical trials & evidence

Clinical trials

Clinical trials: 8.

Phase distribution (across all retrieved trials)

PhaseTrials
Not specified7
PHASE21

Top trials by phase / activity

NCTPhaseStatusTitle
NCT03274375PHASE2RECRUITINGImmunoadsorption Therapy in Managing NMDAR Antibodies Encephalitis
NCT05017142Not specifiedRECRUITINGSwiss Pediatric Inflammatory Brain Disease Registry (Swiss-Ped-IBrainD)
NCT06183788Not specifiedRECRUITINGAntibody-mediated NMDA Receptor Encephalitis: Symptoms, Biomarkers, and Mechanisms of the Prolonged Recovery Stage
NCT01865578Not specifiedCOMPLETEDTranscranial Direct Current Stimulation on Cortical Plasticity in Patients With Anti-NMDA Receptor Encephalitis
NCT04339127Not specifiedUNKNOWNAutoimmune Encephalitis With Anti-NMDA Receptor Antibodies Following Herpetic Encephalitis
NCT05738668Not specifiedUNKNOWNClinical-immunological Features of Anti-NMDAR Encephalitis
NCT06023160Not specifiedCOMPLETEDPredicting Functional Outcome and Response to Therapy of Anti-NMDAR Encephalitis at Diagnosis
NCT06915103Not specifiedCOMPLETEDA Case Report of NMDAR Encephalopathy

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
RITUXIMAB41