autosomal dominant Robinow syndrome 3

disease
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Also known as autosomal dominant Robinow syndrome type 3DRS3DVL3 Robinow syndromeRobinow syndrome caused by mutation in DVL3Robinow syndrome, autosomal dominant 3Robinow syndrome, autosomal dominant type 3

Summary

autosomal dominant Robinow syndrome 3 (MONDO:0014819) is a disease caused by DVL3 (GenCC Definitive), with 2 cohort genes.

At a glance

  • Causal gene: DVL3 (GenCC Definitive)
  • Cohort genes: 2
  • ClinVar variants: 29

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical nameautosomal dominant Robinow syndrome 3
Mondo IDMONDO:0014819
OMIM616894
DOIDDOID:0060767
UMLSC4225164
MedGen907878
GARD0018549
Is cancer (heuristic)no

Also known as: autosomal dominant Robinow syndrome type 3 · DRS3 · DVL3 Robinow syndrome · Robinow syndrome caused by mutation in DVL3 · Robinow syndrome, autosomal dominant 3 · Robinow syndrome, autosomal dominant type 3

Data availability: 29 ClinVar variants · 3 GenCC gene-disease records.

Disease family

Classification path: disease › human disease › disease by etiologic mechanism › disease of genetic or genomic mechanism › hereditary disease › autosomal genetic disease › autosomal dominant disease › autosomal dominant Robinow syndromeautosomal dominant Robinow syndrome 3

Related subtypes (2): autosomal dominant Robinow syndrome 2, autosomal dominant Robinow syndrome 1

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

29 retrieved; paginated sample, class counts are floors:

13 uncertain significance, 7 pathogenic, 5 likely pathogenic, 2 conflicting classifications of pathogenicity, 2 pathogenic/likely pathogenic

ClinVarVariant (HGVS)GeneClassificationReview
219218NM_004423.4(DVL3):c.1585del (p.Ala529fs)DVL3Pathogeniccriteria provided, single submitter
219219NM_004423.4(DVL3):c.1715-2A>GDVL3Pathogeniccriteria provided, single submitter
219220NM_004423.4(DVL3):c.1715-1G>ADVL3Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
219221NM_004423.4(DVL3):c.1716del (p.Ser573fs)DVL3Pathogeniccriteria provided, single submitter
219222NM_004423.4(DVL3):c.1749del (p.Ser583fs)DVL3Pathogeniccriteria provided, single submitter
3764613NM_004423.4(DVL3):c.1672_1705del (p.Tyr558fs)DVL3Pathogeniccriteria provided, single submitter
689755NM_004423.4(DVL3):c.1592del (p.Pro531fs)DVL3Pathogeniccriteria provided, single submitter
817264NM_004423.4(DVL3):c.1751_1754del (p.Asp584fs)DVL3Pathogeniccriteria provided, single submitter
488050NM_001466.4(FZD2):c.1301G>T (p.Gly434Val)FZD2Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
1333918NM_004423.4(DVL3):c.1473C>G (p.Tyr491Ter)DVL3Likely pathogeniccriteria provided, single submitter
2664033NM_004423.4(DVL3):c.292del (p.Glu98fs)DVL3Likely pathogenicno assertion criteria provided
3775469NM_004423.4(DVL3):c.1688dup (p.Ser564fs)DVL3Likely pathogeniccriteria provided, single submitter
800837NM_004423.4(DVL3):c.1715-1G>CDVL3Likely pathogenicno assertion criteria provided
981469NM_004423.4(DVL3):c.1715-2delDVL3Likely pathogenicno assertion criteria provided
1445049NM_004423.4(DVL3):c.683G>A (p.Arg228Gln)DVL3Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
2482080NM_004423.4(DVL3):c.466A>T (p.Thr156Ser)DVL3Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
2095173NM_004423.4(DVL3):c.950G>A (p.Arg317Gln)DVL3Uncertain significancecriteria provided, multiple submitters, no conflicts
2441051NM_004423.4(DVL3):c.1949_1950del (p.His650fs)DVL3Uncertain significancecriteria provided, single submitter
2441052NM_004423.4(DVL3):c.1738C>T (p.Arg580Cys)DVL3Uncertain significancecriteria provided, single submitter
2985708NM_004423.4(DVL3):c.808G>A (p.Glu270Lys)DVL3Uncertain significancecriteria provided, multiple submitters, no conflicts
3233373NM_004423.4(DVL3):c.903G>C (p.Gln301His)DVL3Uncertain significancecriteria provided, single submitter
3338369NM_004423.4(DVL3):c.1947_1950del (p.His650fs)DVL3Uncertain significancecriteria provided, single submitter
3376190NM_004423.4(DVL3):c.899T>C (p.Leu300Ser)DVL3Uncertain significancecriteria provided, single submitter
3377076NM_004423.4(DVL3):c.883C>G (p.Pro295Ala)DVL3Uncertain significancecriteria provided, single submitter
3588983NM_004423.4(DVL3):c.190A>T (p.Asn64Tyr)DVL3Uncertain significancecriteria provided, single submitter
3764584NM_004423.4(DVL3):c.1552C>T (p.Gln518Ter)DVL3Uncertain significancecriteria provided, single submitter
4078535NM_004423.4(DVL3):c.1510C>G (p.Leu504Val)DVL3Uncertain significancecriteria provided, single submitter
930245NM_004423.4(DVL3):c.1120G>A (p.Ala374Thr)DVL3Uncertain significancecriteria provided, single submitter
931200NM_004423.4(DVL3):c.706A>G (p.Ser236Gly)DVL3Uncertain significancecriteria provided, single submitter

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 4 · Orphanet: 3 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

GenCC gene–disease validity (cohort genes)

the Disease column is the GenCC-asserted condition — a cohort gene’s strongest validity may be for a related predisposition syndrome.

GeneClassificationInheritanceDiseaseRecords
DVL3DefinitiveAutosomal dominantautosomal dominant Robinow syndrome 34

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
DVL3Orphanet:3107Autosomal dominant Robinow syndrome
FZD2Orphanet:3107Autosomal dominant Robinow syndrome
FZD2Orphanet:93328Autosomal dominant omodysplasia

Cohort genes → proteins

2 cohort genes, 2 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence2

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
DVL3HGNC:3087ENSG00000161202Q92997Segment polarity protein dishevelled homolog DVL-3gencc,clinvar
FZD2HGNC:4040ENSG00000180340Q14332Frizzled-2clinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
DVL3Segment polarity protein dishevelled homolog DVL-3Involved in the signal transduction pathway mediated by multiple Wnt genes.
FZD2Frizzled-2Receptor for Wnt proteins.

Protein-family classification

Druggable: 1 · Difficult: 1 · Unknown: 0 · Druggable fraction: 0.5

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
GPCR112.0×0.112
Scaffold/PPI18.6×0.112

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
DVL3Scaffold/PPInoDEP_dom, DIX, PDZ
FZD2GPCRyesFrizzled/Smoothened_7TM, Frizzled/SFRP, GPCR_2-like_7TM

Expression context

Cohort genes with no expression data: 0.

2 cohort genes are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)2
unknown0

Top tissues across cohort

TissueCohort genes
ganglionic eminence1
mucosa of stomach1
stromal cell of endometrium1
dorsal root ganglion1
embryo1
ventricular zone1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
DVL3287ubiquitousmarkerstromal cell of endometrium, ganglionic eminence, mucosa of stomach
FZD2197ubiquitousmarkerventricular zone, embryo, dorsal root ganglion

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
DVL33,185
FZD21,764

Structural data

PDB: 2 · AlphaFold-only: 0 · No structure: 0

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
DVL3Q929979
FZD2Q143325

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 12. Enrichment computed across 2 evidence-associated genes (2 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 2 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Disassembly of the destruction complex and recruitment of AXIN to the membrane2356.9×9e-05DVL3, FZD2
TCF dependent signaling in response to WNT2117.7×4e-04DVL3, FZD2
Negative regulation of TCF-dependent signaling by DVL-interacting proteins11142.0×0.004DVL3
WNT mediated activation of DVL1713.8×0.004DVL3
WNT5:FZD7-mediated leishmania damping1475.8×0.005DVL3
WNT5A-dependent internalization of FZD2, FZD5 and ROR21439.2×0.005FZD2
PCP/CE pathway1150.3×0.011DVL3
Degradation of DVL1119.0×0.012DVL3
Asymmetric localization of PCP proteins1102.0×0.012FZD2
Class B/2 (Secretin family receptors)195.2×0.012FZD2
Ca2+ pathway189.2×0.012FZD2
RHO GTPases Activate Formins138.8×0.026DVL3

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 2 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
non-canonical Wnt signaling pathway2581.1×5e-05DVL3, FZD2
Wnt signaling pathway, planar cell polarity pathway2455.5×5e-05DVL3, FZD2
canonical Wnt signaling pathway2153.2×3e-04DVL3, FZD2
muscular septum morphogenesis11685.2×0.003FZD2
inner ear receptor cell development11203.7×0.003FZD2
positive regulation of neuron projection arborization11053.2×0.003DVL3
membranous septum morphogenesis1842.6×0.003FZD2
hard palate development1842.6×0.003FZD2
positive regulation of DNA-templated transcription227.9×0.003DVL3, FZD2
endothelial cell differentiation1561.7×0.004FZD2
cochlea morphogenesis1290.6×0.007FZD2
outflow tract morphogenesis1153.2×0.012FZD2
regulation of protein localization1102.8×0.017DVL3
small GTPase-mediated signal transduction191.6×0.017DVL3
positive regulation of JNK cascade181.8×0.017DVL3
regulation of actin cytoskeleton organization178.8×0.017DVL3
sensory perception of smell178.0×0.017FZD2
neuron differentiation150.1×0.024FZD2
Wnt signaling pathway149.9×0.024FZD2
cell-cell signaling134.8×0.031FZD2
response to xenobiotic stimulus134.5×0.031DVL3
protein stabilization133.4×0.031DVL3
positive regulation of transcription by RNA polymerase II17.4×0.130DVL3

Therapeutics

Drug target analysis

Approved (phase 4): 0 · Phase ≥3: 0 · Phased (≥1): 0 · Undrugged: 2

Druggability breadth: 2 of 2 evidence-associated genes (100%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Top cohort targets by molecule count

SymbolMoleculesMax phase
DVL300
FZD200

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Cohort genes with ChEMBL bioactivity (full, sorted by assay count)

SymbolAssaysType breakdown
FZD218Functional:18
DVL33Binding:2, Functional:1

Pharmacogenomics

Cohort genes with a PharmGKB record: 2; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

0 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)0
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug1FZD2
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug1DVL3

Undrugged target profiles

2 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
DVL33
FZD218

Clinical trials & evidence

Clinical trials

Clinical trials: 0.