Brugada syndrome 2

disease
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Also known as BRGDA2Brugada syndrome caused by mutation in GPD1LBrugada syndrome type 2GPD1L Brugada syndrome

Summary

Brugada syndrome 2 (MONDO:0012728) is a disease with 1 cohort gene.

At a glance

  • Cohort genes: 1
  • ClinVar variants: 36

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical nameBrugada syndrome 2
Mondo IDMONDO:0012728
MeSHC567087
OMIM611777
DOIDDOID:0110219
UMLSC2673193
MedGen382031
GARD0015526
Is cancer (heuristic)no

Also known as: BRGDA2 · Brugada syndrome 2 · Brugada syndrome caused by mutation in GPD1L · Brugada syndrome type 2 · GPD1L Brugada syndrome

Data availability: 36 ClinVar variants · 2 GenCC gene-disease records.

Disease family

Classification path: disease › human disease › disease by body system or component › cardiovascular disorderheart disorderheart conduction diseaseBrugada syndromeBrugada syndrome 2

Related subtypes (8): Brugada syndrome 1, Brugada syndrome 3, Brugada syndrome 4, Brugada syndrome 5, Brugada syndrome 6, Brugada syndrome 7, Brugada syndrome 8, Brugada syndrome 9

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

36 retrieved; paginated sample, class counts are floors:

17 uncertain significance, 9 conflicting classifications of pathogenicity, 7 benign/likely benign, 3 likely benign

ClinVarVariant (HGVS)GeneClassificationReview
1041106NM_015141.4(GPD1L):c.619-9C>AGPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1056227NM_015141.4(GPD1L):c.376del (p.Glu126fs)GPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
180369NM_015141.4(GPD1L):c.520G>A (p.Glu174Lys)GPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
463286NM_015141.4(GPD1L):c.467A>G (p.Asn156Ser)GPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
644362NM_015141.4(GPD1L):c.838G>A (p.Ala280Thr)GPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
786NM_015141.4(GPD1L):c.839C>T (p.Ala280Val)GPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
787NM_015141.4(GPD1L):c.247G>A (p.Glu83Lys)GPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
788NM_015141.4(GPD1L):c.370A>G (p.Ile124Val)GPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
789NM_015141.4(GPD1L):c.817C>T (p.Arg273Cys)GPD1LConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1047243NM_015141.4(GPD1L):c.416G>A (p.Arg139His)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
1326864NM_015141.4(GPD1L):c.914CTG[1] (p.Ala306del)GPD1LUncertain significancecriteria provided, single submitter
1423143NM_015141.4(GPD1L):c.878T>C (p.Met293Thr)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
1496581NM_015141.4(GPD1L):c.158C>G (p.Thr53Arg)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
1515725NM_015141.4(GPD1L):c.853-2A>GGPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
191446NM_015141.4(GPD1L):c.415C>T (p.Arg139Cys)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
218714NM_015141.4(GPD1L):c.977C>A (p.Ala326Glu)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
410225NM_015141.4(GPD1L):c.997G>A (p.Glu333Lys)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
452285NM_015141.4(GPD1L):c.505G>A (p.Gly169Ser)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
487599NM_015141.4(GPD1L):c.775G>A (p.Gly259Arg)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
519421NM_015141.4(GPD1L):c.905C>T (p.Pro302Leu)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
560688NM_015141.4(GPD1L):c.257A>G (p.Gln86Arg)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
571418NM_015141.4(GPD1L):c.560A>G (p.Asn187Ser)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
656217NM_015141.4(GPD1L):c.658C>T (p.Arg220Cys)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
809441NM_015141.4(GPD1L):c.505+2T>GGPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
843122NM_015141.4(GPD1L):c.818G>A (p.Arg273His)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
849031NM_015141.4(GPD1L):c.482A>G (p.Glu161Gly)GPD1LUncertain significancecriteria provided, multiple submitters, no conflicts
1245688NM_015141.4(GPD1L):c.367-10A>TGPD1LBenign/Likely benigncriteria provided, multiple submitters, no conflicts
1250797NM_015141.4(GPD1L):c.367-11C>AGPD1LBenign/Likely benigncriteria provided, multiple submitters, no conflicts
137491NM_015141.4(GPD1L):c.981G>A (p.Val327=)GPD1LBenign/Likely benigncriteria provided, multiple submitters, no conflicts
190760NM_015141.4(GPD1L):c.81T>C (p.Asn27=)GPD1LBenign/Likely benigncriteria provided, multiple submitters, no conflicts

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 3 · Orphanet: 1 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

GenCC gene–disease validity (cohort genes)

the Disease column is the GenCC-asserted condition — a cohort gene’s strongest validity may be for a related predisposition syndrome.

GeneClassificationInheritanceDiseaseRecords
GPD1LLimitedUnknownBrugada syndrome 23

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
GPD1LOrphanet:130Brugada syndrome

Cohort genes → proteins

1 cohort genes, 1 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence1

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
GPD1LHGNC:28956ENSG00000152642Q8N335Glycerol-3-phosphate dehydrogenase 1-like proteingencc,clinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
GPD1LGlycerol-3-phosphate dehydrogenase 1-like proteinPlays a role in regulating cardiac sodium current; decreased enzymatic activity with resulting increased levels of glycerol 3-phosphate activating the DPD1L-dependent SCN5A phosphorylation pathway, may ultimately lead to decreased sodium c…

Protein-family classification

Druggable: 0 · Difficult: 0 · Unknown: 1 · Druggable fraction: 0.0

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Other/Unknown11.8×0.558

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
GPD1LOther/UnknownnoG3P_DH_NAD-dep_C, G3P_DH_NAD-dep, 6-PGluconate_DH-like_C_sf

Expression context

Cohort genes with no expression data: 0.

1 cohort gene are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)1
unknown0

Top tissues across cohort

TissueCohort genes
biceps brachii1
heart right ventricle1
skeletal muscle tissue of biceps brachii1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
GPD1L297ubiquitousmarkerbiceps brachii, heart right ventricle, skeletal muscle tissue of biceps brachii

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
GPD1L2,618

Structural data

PDB: 1 · AlphaFold-only: 0 · No structure: 0

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
GPD1LQ8N3351

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 1. Enrichment computed across 1 evidence-associated genes (1 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Synthesis of PA1292.8×0.003GPD1L

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
glycerol-3-phosphate catabolic process18426.0×9e-04GPD1L
regulation of ventricular cardiac muscle cell membrane depolarization12808.7×0.001GPD1L
NAD+ metabolic process11872.4×0.001GPD1L
ventricular cardiac muscle cell action potential1991.3×0.002GPD1L
positive regulation of sodium ion transport1842.6×0.002GPD1L
positive regulation of protein localization to cell surface1766.0×0.002GPD1L
regulation of heart rate1468.1×0.002GPD1L
carbohydrate metabolic process1135.9×0.007GPD1L

Therapeutics

Drug target analysis

Approved (phase 4): 0 · Phase ≥3: 0 · Phased (≥1): 0 · Undrugged: 1

Druggability breadth: 0 of 1 evidence-associated genes (0%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Top cohort targets by molecule count

SymbolMoleculesMax phase
GPD1L00

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Pharmacogenomics

Cohort genes with a PharmGKB record: 1; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

0 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)0
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug1GPD1L

Undrugged target profiles

1 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
GPD1L0

Clinical trials & evidence

Clinical trials

Clinical trials: 0.