Diastolic heart failure

disease
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Summary

Diastolic heart failure (MONDO:0006727) is a disease with 2 GWAS associations across 4 studies and 61 clinical trials. Top therapeutic interventions include perhexiline, eplerenone, and ranolazine. A subtype of congestive heart failure — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • GWAS associations: 2
  • Clinical trials: 61

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namediastolic heart failure
Mondo IDMONDO:0006727
EFOEFO:1000899
MeSHD054144
DOIDDOID:9775
SNOMED CT418304008
UMLSC1135196
MedGen210051
MedDRA10069211
Is cancer (heuristic)no

Data availability: 2 GWAS associations (4 studies).

Disease family

This is a subtype of congestive heart failure. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by body system or component › cardiovascular disorderheart disorderheart failurecongestive heart failurediastolic heart failure

Related subtypes (4): rheumatic congestive heart failure, cor pulmonale, systolic heart failure, left ventricular failure

Genetics & variants

GWAS landscape

2 GWAS associations across 4 studies. Top hits map to 1 distinct genes (as reported by GWAS).

Top associations by p-value

rsIDp-valueGeneRisk alleleOdds ratio
rs558727254e-15FTOC0.08
rs14210853e-14FTOT0.08

Top studies (by case count)

StudyLead authorYearCasesControlsTitle
GCST90475984Verma A202419,682419,065Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90477963Verma A20245,379113,041Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90480183Verma A20245,379113,041Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90477962Verma A20241,57357,263Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.

Variant details and genetic-evidence tiers

Tier distribution (top 50 variants)

TierVariants
Tier 1: coding0
Tier 2: splice/UTR0
Tier 3: regulatory0
Tier 4: intronic/intergenic2

MAF distribution

BucketVariants
common (>=0.05)2
low_freq (0.01-0.05)0
rare (<0.01)0
unknown0

Functional consequences

ConsequenceCount
intron_variant2

Top variants

rsIDChrPosAllelesMAFConsequenceGenep-valueTier
rs558727251653775211C>G,T0.404intron_variantFTO4e-15Tier 4: intronic/intergenic
rs14210851653767042T>C0.334intron_variantFTO3e-14Tier 4: intronic/intergenic

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

Drugs indicated for this disease

0 approved, 2 in late-stage (phase 3) trials. Disease-direct ChEMBL indications, not inferred from the associated-gene cohort below.

DrugDevelopment status
SpironolactonePhase 3 (in late-stage trials)
UdenafilPhase 3 (in late-stage trials)

Earlier-phase candidates (phase 2, investigational — efficacy not yet established): Dapagliflozin, Ivabradine, Perhexiline, Potassium Chloride, Ranolazine, Ubidecarenone.

Clinical trials & evidence

Clinical trials

Clinical trials: 61.

Phase distribution (across all retrieved trials)

PhaseTrials
Not specified40
PHASE28
PHASE46
PHASE32
PHASE2/PHASE32
PHASE1/PHASE22
PHASE11

Top trials by phase / activity

NCTPhaseStatusTitle
NCT04160000PHASE4RECRUITINGTreatment Of Atrial Fibrillation In Preserved Cardiac Function Heart Failure
NCT00083772PHASE4TERMINATEDUse of Nesiritide in the Management of Acute Diastolic Heart Failure
NCT00293150PHASE4TERMINATEDReversing Endothelial and Diastolic Dysfunction and Improving Collagen Turnover in Diastolic Heart Failure
NCT01944384PHASE4COMPLETEDImpacts of Aldosterone Blockade on Myocardial Remodeling in Hypertensive Patients With Diastolic Failing Heart
NCT02053246PHASE4TERMINATEDImproving Treatment Personalization of Pulmonary Hypertension Associated With Diastolic Heart Failure
NCT02589977PHASE4COMPLETEDMyocardial Perfusion, Oxidative Metabolism, and Fibrosis in HFpEF
NCT00123955PHASE3COMPLETEDPIE II: Pharmacological Intervention in the Elderly II
NCT01156636PHASE2/PHASE3COMPLETEDPhosphodiesterase-5 (PDE5) Inhibition and Pulmonary Hypertension in Diastolic Heart Failure
NCT01583881PHASE2/PHASE3TERMINATEDDenervation of the renAl sympathetIc nerveS in hearT Failure With nOrmal Lv Ejection Fraction
NCT01599117PHASE3UNKNOWNA Randomized Trial of Udenafil Therapy in Patients With Heart Failure With Preserved Ejection Fraction [ULTIMATE-HFpEF]
NCT05408559PHASE1/PHASE2RECRUITINGPrevention of Age-associated Cardiac and Vascular Dysfunction Using Avmacol ES
NCT00303498PHASE2COMPLETEDA Study of the Effectiveness of Sitaxsentan Sodium in Patients With Diastolic Heart Failure
NCT00309868PHASE1/PHASE2COMPLETEDStudy of Nesiritide in Diastolic Heart Failure.
NCT00662116PHASE2TERMINATEDBeginning a Randomized Evaluation of the AGE Breaker Alagebrium in Diastolic Heart Failure (BREAK-DHF-I)
NCT00757055PHASE2WITHDRAWNIf Channel Blockade With Ivabradine in Patients With Diastolic Heart Failure
NCT00839228PHASE2COMPLETEDPerhexiline Therapy in Heart Failure With Preserved Ejection Fraction Syndrome
NCT01163734PHASE2COMPLETEDRanolazine in Diastolic Heart Failure
NCT01913301PHASE2TERMINATEDA Randomized Double-Blind, Placebo-Controlled, Multiple-Dose Study to Evaluate the Effects of Alagebrium on Exercise in Subjects With Diastolic Heart Failure
NCT02256345PHASE2COMPLETEDPharmacokinetics, Pharmacodynamics, and Impact of Inorganic Nitrate on Exercise in HFpEF
NCT03882710PHASE2COMPLETEDMetoprolol XR in Heart Failure With Normal Ejection Fraction
NCT01185067PHASE1COMPLETEDPhysiological Effects of Grape Seed Extract in Diastolic Heart Failure
NCT05064709Not specifiedRECRUITINGAssessment of CCM in HF With Higher Ejection Fraction
NCT06015776Not specifiedRECRUITINGPurinergic Signaling and the Postmenopausal Heart
NCT06805253Not specifiedRECRUITINGLeft Ventricular Reverse Remodeling Evaluation After Surgical Correction of Aortic Regurgitation
NCT00505336Not specifiedCOMPLETEDThe Effect of Eplerenone and Atorvastatin on Markers of Collagen Turnover in Diastolic Heart Failure
NCT00574756Not specifiedTERMINATEDEffect of Ranolazine on Echocardiographic Indices of Diastolic Dysfunction
NCT00585611Not specifiedTERMINATEDEffects of Statin Therapy on Vascular Properties and Outcomes in Diastolic Heart Failure Patients
NCT00709241Not specifiedCOMPLETEDPsychosocial Patterns and Prognosis in Patients With Heart Failure
NCT00718939Not specifiedCOMPLETEDRheos® Diastolic Heart Failure Trial
NCT00720525Not specifiedCOMPLETEDPulsatile and Steady State Hemodynamics in Diastolic Heart Failure
NCT00773084Not specifiedWITHDRAWNAliskiren and Renin Inhibition in Diastolic Heart Failure
NCT00846404Not specifiedUNKNOWNMarkers of Oxidative Stress Diastolic Dysfunction
NCT00939640Not specifiedCOMPLETEDEffects of the Dietary Approaches to Stop Hypertension(DASH) Sodium-restricted Diet in Diastolic Heart Failure
NCT01030991Not specifiedCOMPLETEDClassification of Heart Failure With Preserved Ejection Fraction
NCT01047631Not specifiedCOMPLETEDRole of Exercise in Diastolic Heart Failure
NCT01157481Not specifiedUNKNOWNDiastolic Heart Failure Management by Nifedipine
NCT01431027Not specifiedCOMPLETEDLeft Ventricular Torsional Hysteresis: A Global Parameter for Diastolic Function
NCT01778894Not specifiedTERMINATEDMathematical Modeling to Determine Basic Muscle Properties in the Failing Heart
NCT01942395Not specifiedTERMINATEDDietary Approaches to Stop Hypertension in ‘Diastolic’ Heart Failure 2 (DASH-DHF 2)
NCT02018497Not specifiedUNKNOWNEssential Hypotension and Allostasis Registry

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
PERHEXILINE43
EPLERENONE42
RANOLAZINE42
REGADENOSON ANHYDROUS42
SPIRONOLACTONE42
IVABRADINE41
NEBIVOLOL41
NESIRITIDE41
POTASSIUM CHLORIDE41
SULFORAPHANE31
UDENAFIL31
ALAGEBRIUM22
CHEMBL407132701
CHEMBL236565801
CHEMBL352643601
CHEMBL430353701
CHEMBL156222301
CHEMBL3045801