Distal trisomy 11q

disease
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Also known as Chromosome 11, Partial Trisomy 11qdistal duplication 11qdistal trisomy type 11qtelomeric duplication 11qtrisomy 11qter

Summary

Distal trisomy 11q (MONDO:0019885) is a disease with 1 cohort gene.

At a glance

  • Cohort genes: 1
  • ClinVar variants: 1

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namedistal trisomy 11q
Mondo IDMONDO:0019885
MeSHC538294
Orphanet96103
SNOMED CT764447009
UMLSC2931797
MedGen419166
GARD0019318
NORD937
Is cancer (heuristic)no

Also known as: Chromosome 11, Partial Trisomy 11q · distal duplication 11q · distal trisomy type 11q · telomeric duplication 11q · trisomy 11qter

Data availability: 1 ClinVar variant.

Disease family

Classification path: disease › human disease › disease by etiologic mechanism › disease of genetic or genomic mechanism › chromosomal disordersyndrome caused by partial chromosomal duplication › partial duplication of chromosome 11 › chromosome 11q trisomy › distal trisomy 11q

Related subtypes (1): microtriplication 11q24.1

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

1 retrieved; paginated sample, class counts are floors:

1 pathogenic

ClinVarVariant (HGVS)GeneClassificationReview
973579NC_000011.9:g.104288964_134937416dupHTR3APathogeniccriteria provided, single submitter

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 0 · Orphanet: 0 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

Cohort genes → proteins

1 cohort genes, 1 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence1

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
HTR3AHGNC:5297ENSG00000166736P460985-hydroxytryptamine receptor 3Aclinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
HTR3A5-hydroxytryptamine receptor 3AForms serotonin (5-hydroxytryptamine/5-HT3)-activated cation-selective channel complexes, which when activated cause fast, depolarizing responses in neurons.

Protein-family classification

Druggable: 0 · Difficult: 0 · Unknown: 1 · Druggable fraction: 0.0

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Other/Unknown11.8×0.558

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
HTR3AOther/UnknownnoNeurotrans-gated_channel_TM, Neur_channel, Neur_chan_lig-bd

Expression context

Cohort genes with no expression data: 0.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)1
unknown0

Top tissues across cohort

TissueCohort genes
dorsal root ganglion1
male germ line stem cell (sensu Vertebrata) in testis1
pancreatic ductal cell1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
HTR3A120tissue_specificyesdorsal root ganglion, male germ line stem cell (sensu Vertebrata) in testis, pancreatic ductal cell

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
HTR3A1,425

Structural data

PDB: 1 · AlphaFold-only: 0 · No structure: 0

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
HTR3AP460984

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 3. Enrichment computed across 1 evidence-associated genes (1 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Neurotransmitter receptors and postsynaptic signal transmission1100.2×0.020HTR3A
Transmission across Chemical Synapses176.1×0.020HTR3A
Neuronal System144.3×0.023HTR3A

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
serotonin-gated cation-selective signaling pathway13370.4×0.002HTR3A
serotonin receptor signaling pathway11872.4×0.002HTR3A
obsolete inorganic cation transmembrane transport1936.2×0.002HTR3A
regulation of membrane potential1230.8×0.006HTR3A
monoatomic ion transmembrane transport1208.1×0.006HTR3A
chemical synaptic transmission177.3×0.013HTR3A

Therapeutics

Drug target analysis

Approved (phase 4): 1 · Phase ≥3: 1 · Phased (≥1): 1 · Undrugged: 0

Druggability breadth: 1 of 1 evidence-associated genes (100%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Genes with an approved drug

The molecule shown is one approved compound that hits the gene — not necessarily a drug of choice or one indicated for this disease.

SymbolExample approved molecule
HTR3AVARENICLINE

Top cohort targets by molecule count

SymbolMoleculesMax phase
HTR3A984

Drugs targeting cohort genes (top 30)

MoleculeMax phaseTargets in cohort
VARENICLINE4HTR3A
ALOSETRON4HTR3A
ARIPIPRAZOLE4HTR3A
AMOXAPINE4HTR3A
IDARUBICIN4HTR3A
PRUCALOPRIDE4HTR3A
DULOXETINE4HTR3A
CHLOROPROCAINE4HTR3A
ANISOTROPINE4HTR3A
PALONOSETRON4HTR3A
THIOTHIXENE4HTR3A
PYRVINIUM4HTR3A
INDOCYANINE GREEN ACID FORM4HTR3A
DIPHEMANIL4HTR3A
BALSALAZIDE4HTR3A
RABEPRAZOLE4HTR3A
PHENAZOPYRIDINE4HTR3A
SUMATRIPTAN4HTR3A
NITAZOXANIDE4HTR3A
NITROXOLINE4HTR3A
AMLODIPINE4HTR3A
TEGASEROD MALEATE4HTR3A
KETOTIFEN FUMARATE4HTR3A
RAMOSETRON4HTR3A
OMADACYCLINE4HTR3A
CISAPRIDE4HTR3A
DAUNORUBICIN4HTR3A
HYDROXOCOBALAMIN4HTR3A
VORTIOXETINE4HTR3A
TELOTRISTAT ETHYL4HTR3A

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Cohort genes with ChEMBL bioactivity (full, sorted by assay count)

SymbolAssaysType breakdown
HTR3A707Binding:599, Functional:98, ADMET:9, Toxicity:1

Cohort genes with high screening signal

≥100 ChEMBL assays — a studied-ness signal; see Therapeutics for approved-drug status.

SymbolChEMBL assays
HTR3A707

Pharmacogenomics

Cohort genes with a PharmGKB record: 1; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

30 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

CompoundMax phaseCohort target (bioactivity)
VARENICLINE4HTR3A
ALOSETRON4HTR3A
ARIPIPRAZOLE4HTR3A
AMOXAPINE4HTR3A
IDARUBICIN4HTR3A
PRUCALOPRIDE4HTR3A
DULOXETINE4HTR3A
CHLOROPROCAINE4HTR3A
ANISOTROPINE4HTR3A
PALONOSETRON4HTR3A
THIOTHIXENE4HTR3A
PYRVINIUM4HTR3A
INDOCYANINE GREEN ACID FORM4HTR3A
DIPHEMANIL4HTR3A
BALSALAZIDE4HTR3A
RABEPRAZOLE4HTR3A
PHENAZOPYRIDINE4HTR3A
SUMATRIPTAN4HTR3A
NITAZOXANIDE4HTR3A
NITROXOLINE4HTR3A
AMLODIPINE4HTR3A
TEGASEROD MALEATE4HTR3A
KETOTIFEN FUMARATE4HTR3A
RAMOSETRON4HTR3A
OMADACYCLINE4HTR3A
CISAPRIDE4HTR3A
DAUNORUBICIN4HTR3A
HYDROXOCOBALAMIN4HTR3A
VORTIOXETINE4HTR3A
TELOTRISTAT ETHYL4HTR3A

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)1HTR3A
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug0

Undrugged target profiles

0 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

Clinical trials & evidence

Clinical trials

Clinical trials: 0.