Epilepsy, idiopathic generalized 20

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Summary

Epilepsy, idiopathic generalized 20 (MONDO:0980988) is a disease with 1 cohort gene.

At a glance

  • Cohort genes: 1
  • ClinVar variants: 5

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical nameepilepsy, idiopathic generalized 20
Mondo IDMONDO:0980988
OMIM621500
Is cancer (heuristic)no

Data availability: 5 ClinVar variants.

Disease family

Classification path: disease › human disease › disease by etiologic mechanism › disease of genetic or genomic mechanism › hereditary diseasehereditary neurological disease › hereditary generalized epilepsy › idiopathic generalized epilepsy › variable-age onset idiopathic generalized epilepsy syndrome › epilepsy, idiopathic generalized 20

Related subtypes (3): epilepsy with generalized tonic-clonic seizures, juvenile myoclonic epilepsy, juvenile absence epilepsy

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

5 retrieved; paginated sample, class counts are floors:

3 pathogenic, 2 uncertain significance

ClinVarVariant (HGVS)GeneClassificationReview
4759510NM_006885.4(ZFHX3):c.10853C>A (p.Pro3618Gln)ZFHX3Pathogenicno assertion criteria provided
4759512NM_006885.4(ZFHX3):c.4122TGC[1] (p.Ala1376del)ZFHX3Pathogenicno assertion criteria provided
4759513NM_006885.4(ZFHX3):c.10455G>T (p.Lys3485Asn)ZFHX3Pathogenicno assertion criteria provided
2376030NM_006885.4(ZFHX3):c.6161C>T (p.Ala2054Val)ZFHX3Uncertain significancecriteria provided, single submitter
3984467NM_006885.4(ZFHX3):c.2419G>A (p.Glu807Lys)ZFHX3Uncertain significancecriteria provided, single submitter

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 0 · Orphanet: 0 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

Cohort genes → proteins

1 cohort genes, 1 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence1

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
ZFHX3HGNC:777ENSG00000140836Q15911Zinc finger homeobox protein 3clinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
ZFHX3Zinc finger homeobox protein 3Transcriptional regulator which can act as an activator or a repressor.

Protein-family classification

Druggable: 0 · Difficult: 1 · Unknown: 0 · Druggable fraction: 0.0

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Transcription factor18.3×0.121

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
ZFHX3Transcription factornoHD, Matrin/U1-like-C_Znf_C2H2, Homeodomain-like_sf

Expression context

Cohort genes with no expression data: 0.

1 cohort gene are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)1
unknown0

Top tissues across cohort

TissueCohort genes
buccal mucosa cell1
saphenous vein1
synovial joint1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
ZFHX3274ubiquitousmarkersaphenous vein, buccal mucosa cell, synovial joint

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
ZFHX31,649

Structural data

PDB: 1 · AlphaFold-only: 0 · No structure: 0

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
ZFHX3Q159113

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 1. Enrichment computed across 1 evidence-associated genes (1 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
RUNX3 regulates CDKN1A transcription11631.4×6e-04ZFHX3

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
regulation of locomotor rhythm18426.0×0.002ZFHX3
response to transforming growth factor beta11872.4×0.003ZFHX3
regulation of neuron differentiation1732.7×0.005ZFHX3
negative regulation of myoblast differentiation1624.1×0.005ZFHX3
positive regulation of myoblast differentiation1366.4×0.007ZFHX3
positive regulation of cell adhesion1271.8×0.008ZFHX3
circadian regulation of gene expression1234.1×0.008ZFHX3
muscle organ development1166.8×0.010ZFHX3
regulation of DNA-templated transcription131.6×0.046ZFHX3
positive regulation of DNA-templated transcription127.9×0.047ZFHX3
negative regulation of transcription by RNA polymerase II117.7×0.067ZFHX3
positive regulation of transcription by RNA polymerase II114.9×0.073ZFHX3
regulation of transcription by RNA polymerase II111.7×0.086ZFHX3

Therapeutics

Drug target analysis

Approved (phase 4): 0 · Phase ≥3: 0 · Phased (≥1): 0 · Undrugged: 1

Druggability breadth: 0 of 1 evidence-associated genes (0%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Top cohort targets by molecule count

SymbolMoleculesMax phase
ZFHX300

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Pharmacogenomics

Cohort genes with a PharmGKB record: 1; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

0 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)0
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug1ZFHX3

Undrugged target profiles

1 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
ZFHX30

Clinical trials & evidence

Clinical trials

Clinical trials: 0.