Familial temporal lobe epilepsy 5

disease
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Also known as epilepsy, familial temporal lobe, 5epilepsy, familial temporal lobe, type 5ETL5familial temporal lobe epilepsy type 5

Summary

Familial temporal lobe epilepsy 5 (MONDO:0013741) is a disease with 2 cohort genes.

At a glance

  • Cohort genes: 2
  • ClinVar variants: 72

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namefamilial temporal lobe epilepsy 5
Mondo IDMONDO:0013741
OMIM614417
DOIDDOID:0060752
UMLSC3280730
MedGen482360
GARD0018280
Is cancer (heuristic)no

Also known as: epilepsy, familial temporal lobe, 5 · epilepsy, familial temporal lobe, type 5 · ETL5 · familial temporal lobe epilepsy type 5

Data availability: 72 ClinVar variants · 2 GenCC gene-disease records.

Disease family

Classification path: human disease › disease by body system or component › nervous system disordercentral nervous system disorderbrain disorderepilepsyfocal epilepsyfamilial partial epilepsytemporal lobe epilepsy › familial mesial temporal lobe epilepsy › familial temporal lobe epilepsy 5

Related subtypes (2): familial temporal lobe epilepsy 3, familial temporal lobe epilepsy 6

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

72 retrieved; paginated sample, class counts are floors:

55 uncertain significance, 9 conflicting classifications of pathogenicity, 3 benign, 2 benign/likely benign, 2 likely benign, 1 no classifications from unflagged records

ClinVarVariant (HGVS)GeneClassificationReview
281269NM_020361.5(CPA6):c.799G>A (p.Gly267Arg)ARFGEF1-DTConflicting classifications of pathogenicitycriteria provided, conflicting classifications
30791NM_020361.5(CPA6):c.809C>T (p.Ala270Val)ARFGEF1-DTConflicting classifications of pathogenicitycriteria provided, conflicting classifications
363605NM_020361.5(CPA6):c.932G>A (p.Arg311Gln)ARFGEF1-DTConflicting classifications of pathogenicitycriteria provided, conflicting classifications
472765NM_020361.5(CPA6):c.916G>A (p.Val306Ile)ARFGEF1-DTConflicting classifications of pathogenicitycriteria provided, conflicting classifications
539979NM_020361.5(CPA6):c.759G>A (p.Trp253Ter)ARFGEF1-DTConflicting classifications of pathogenicitycriteria provided, conflicting classifications
774243NM_020361.5(CPA6):c.920C>T (p.Ala307Val)ARFGEF1-DTConflicting classifications of pathogenicitycriteria provided, conflicting classifications
363610NM_020361.5(CPA6):c.505T>C (p.Tyr169His)CPA6Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
363614NM_020361.5(CPA6):c.98A>G (p.Tyr33Cys)CPA6Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
393467NM_020361.5(CPA6):c.619C>G (p.Gln207Glu)CPA6Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
1030703NM_020361.5(CPA6):c.1096T>C (p.Tyr366His)ARFGEF1-DTUncertain significancecriteria provided, single submitter
1334016NM_020361.5(CPA6):c.1294C>A (p.Leu432Met)ARFGEF1-DTUncertain significancecriteria provided, single submitter
2664165NM_020361.5(CPA6):c.1007A>G (p.Tyr336Cys)ARFGEF1-DTUncertain significancecriteria provided, single submitter
3065225NM_020361.5(CPA6):c.1207G>T (p.Gly403Ter)ARFGEF1-DTUncertain significancecriteria provided, single submitter
3065258NM_020361.5(CPA6):c.871A>G (p.Thr291Ala)ARFGEF1-DTUncertain significancecriteria provided, single submitter
3234978NM_020361.5(CPA6):c.1205C>A (p.Thr402Asn)ARFGEF1-DTUncertain significancecriteria provided, single submitter
3377700NM_020361.5(CPA6):c.1223T>C (p.Leu408Ser)ARFGEF1-DTUncertain significancecriteria provided, single submitter
363597NM_020361.5(CPA6):c.*260A>CARFGEF1-DTUncertain significancecriteria provided, single submitter
363599NM_020361.5(CPA6):c.1288A>G (p.Met430Val)ARFGEF1-DTUncertain significancecriteria provided, multiple submitters, no conflicts
363602NM_020361.5(CPA6):c.1126+13C>TARFGEF1-DTUncertain significancecriteria provided, single submitter
363604NM_020361.5(CPA6):c.1021A>G (p.Ile341Val)ARFGEF1-DTUncertain significancecriteria provided, multiple submitters, no conflicts
363606NM_020361.5(CPA6):c.797G>T (p.Arg266Leu)ARFGEF1-DTUncertain significancecriteria provided, multiple submitters, no conflicts
363607NM_020361.5(CPA6):c.791G>A (p.Arg264His)ARFGEF1-DTUncertain significancecriteria provided, multiple submitters, no conflicts
363608NM_020361.5(CPA6):c.715A>G (p.Asn239Asp)ARFGEF1-DTUncertain significancecriteria provided, single submitter
3897986NM_020361.5(CPA6):c.1009A>G (p.Lys337Glu)ARFGEF1-DTUncertain significancecriteria provided, single submitter
4277841NM_020361.5(CPA6):c.1153T>C (p.Trp385Arg)ARFGEF1-DTUncertain significancecriteria provided, single submitter
437415NM_020361.5(CPA6):c.994T>C (p.Tyr332His)ARFGEF1-DTUncertain significancecriteria provided, single submitter
444757NM_020361.5(CPA6):c.902C>T (p.Pro301Leu)ARFGEF1-DTUncertain significancecriteria provided, multiple submitters, no conflicts
472761NM_020361.5(CPA6):c.1271C>T (p.Ala424Val)ARFGEF1-DTUncertain significancecriteria provided, multiple submitters, no conflicts
472763NM_020361.5(CPA6):c.757T>G (p.Trp253Gly)ARFGEF1-DTUncertain significancecriteria provided, multiple submitters, no conflicts
657933NM_020361.5(CPA6):c.725G>T (p.Gly242Val)ARFGEF1-DTUncertain significancecriteria provided, multiple submitters, no conflicts

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 5 · Orphanet: 2 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

GenCC gene–disease validity (cohort genes)

the Disease column is the GenCC-asserted condition — a cohort gene’s strongest validity may be for a related predisposition syndrome.

GeneClassificationInheritanceDiseaseRecords
CPA6SupportiveAutosomal dominantbenign familial mesial temporal lobe epilepsy5

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
CPA6Orphanet:163717Familial mesial temporal lobe epilepsy
CPA6Orphanet:36387Genetic epilepsy with febrile seizure plus

Cohort genes → proteins

2 cohort genes, 1 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence2

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
CPA6HGNC:17245ENSG00000165078Q8N4T0Carboxypeptidase A6gencc,clinvar
ARFGEF1-DTHGNC:55237ENSG00000271966ARFGEF1 divergent transcriptclinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
CPA6Carboxypeptidase A6May be involved in the proteolytic inactivation of enkephalins and neurotensin in some brain areas.

Protein-family classification

Druggable: 1 · Difficult: 0 · Unknown: 1 · Druggable fraction: 0.5

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Protease118.3×0.108
Other/Unknown10.9×0.805

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
CPA6ProteaseyesPeptidase_M14, M14A_act_pep, CPAH
ARFGEF1-DTOther/Unknownno

Expression context

Cohort genes with no expression data: 0.

1 cohort gene are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)2
unknown0

Top tissues across cohort

TissueCohort genes
buccal mucosa cell1
mucosa of transverse colon1
urethra1
bone marrow1
bone marrow cell1
ganglionic eminence1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
CPA6103broadmarkerbuccal mucosa cell, mucosa of transverse colon, urethra
ARFGEF1-DT127yesbone marrow cell, bone marrow, ganglionic eminence

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
CPA6605
ARFGEF1-DT0

Structural data

PDB: 0 · AlphaFold-only: 1 · No structure: 1

AlphaFold-only cohort genes (top 30 by pLDDT)

SymbolUniProtpLDDT
CPA6Q8N4T090.93

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 0. Enrichment computed across 2 evidence-associated genes (0 with Reactome annotation).

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
proteolysis134.2×0.029CPA6

Therapeutics

Drug target analysis

Approved (phase 4): 0 · Phase ≥3: 0 · Phased (≥1): 0 · Undrugged: 2

Druggability breadth: 0 of 2 evidence-associated genes (0%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Top cohort targets by molecule count

SymbolMoleculesMax phase
CPA600
ARFGEF1-DT00

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Pharmacogenomics

Cohort genes with a PharmGKB record: 1; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

0 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)0
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug1CPA6
EDifficult family or no structure, no drug1ARFGEF1-DT

Undrugged target profiles

2 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
CPA60
ARFGEF1-DT0

Clinical trials & evidence

Clinical trials

Clinical trials: 0.