hepatitis C virus, susceptibility to

disease
On this page

Also known as hepatitis C virus, response to therapy of

Summary

hepatitis C virus, susceptibility to (MONDO:0012292) is a disease with 6 cohort genes.

At a glance

  • Cohort genes: 6
  • ClinVar variants: 19

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namehepatitis C virus, susceptibility to
Mondo IDMONDO:0012292
OMIM609532
UMLSC1835407
MedGen322657
Is cancer (heuristic)no

Also known as: hepatitis C virus, response to therapy of · hepatitis C virus, susceptibility to

Data availability: 19 ClinVar variants.

Disease family

Classification path: disease susceptibility › inherited disease susceptibilityhepatitis C virus, susceptibility to

Related subtypes (283): microvascular complications of diabetes, susceptibility, Mycobacterium tuberculosis, susceptibility, bacteremia, susceptibility, pregnancy loss, recurrent, susceptibility, autoimmune thyroid disease, susceptibility to, susceptibility to HIV infection, appendicitis, proneness to, atherosclerosis susceptibility, multiple sclerosis, susceptibility to, dyslexia, susceptibility to, 1, endometriosis, susceptibility to, 1, osteoarthritis susceptibility 2, essential hypertension, genetic, osteoarthritis susceptibility 1, otitis media, susceptibility to, pelvic organ prolapse, susceptibility to, pulmonary edema of mountaineers, susceptibility to, sarcoidosis, susceptibility to, 1, strabismus, susceptibility to, thyrotoxic periodic paralysis, susceptibility to, 1, predisposition to invasive fungal disease due to CARD9 deficiency, celiac disease, susceptibility to, 1, hemolytic uremic syndrome, atypical, susceptibility to, 1, hypervitaminosis a, susceptibility to, kuru, susceptibility to, leprosy, susceptibility to, 3, nonarteritic anterior ischemic optic neuropathy, susceptibility to, diabetes mellitus, insulin-dependent, X-linked, susceptibility to, coronary heart disease, susceptibility to, 3, dyslexia, susceptibility to, 9, systemic lupus erythematosus, susceptibility to, 15, Leber optic atrophy, susceptibility to, dyslexia, susceptibility to, 2, Helicobacter pylori infection, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 1, inherited susceptibility to asthma, renal dysplasia, cystic, susceptibility to, systemic lupus erythematosus, susceptibility to, 1, leishmaniasis, tegumentary, susceptibility to, xanthomatosis, susceptibility to, hyperlipidemia, combined, 1, urinary tract infections, recurrent, susceptibility to, hypertension, essential, susceptibility to, 1, hepatic fibrosis, severe, susceptibility to, due to Schistosoma mansoni infection, dyslexia, susceptibility to, 3, Ascaris lumbricoides infection, susceptibility to, hypertension, essential, susceptibility to, 2, epilepsy, idiopathic generalized, susceptibility to, 7, systemic lupus erythematosus, susceptibility to, 2, systemic lupus erythematosus, susceptibility to, 3, nephrolithiasis, uric acid, susceptibility to, atrioventricular septal defect, susceptibility to, 2, vitiligo-associated multiple autoimmune disease susceptibility 1, polysubstance abuse, susceptibility to, dyslexia, susceptibility to, 6, glaucoma, normal tension, susceptibility to, anorexia nervosa, susceptibility to, 1, stroke, susceptibility to, 1, dyslexia, susceptibility to, 5, epilepsy, idiopathic generalized, susceptibility to, 2, familial meningioma, celiac disease, susceptibility to, 5, systemic lupus erythematosus with hemolytic anemia, susceptibility to, 1, hypertension, essential, susceptibility to, 3, coronary heart disease, susceptibility to, 1, bulimia nervosa, susceptibility to, 1, leprosy, susceptibility to, 2, epilepsy, idiopathic generalized, susceptibility to, 9, Parkinson disease 11, autosomal dominant, susceptibility to, focal segmental glomerulosclerosis 3, susceptibility to, autoimmune disease, susceptibility to, 1, osteoarthritis susceptibility 3, systemic lupus erythematosus with nephritis, susceptibility to, 1, systemic lupus erythematosus with nephritis, susceptibility to, 2, systemic lupus erythematosus with nephritis, susceptibility to, 3, coronary heart disease, susceptibility to, 2, coronary heart disease, susceptibility to, 4, autoimmune disease, susceptibility to, 2, autoimmune disease, susceptibility to, 3, systemic lupus erythematosus, susceptibility to, 4, myocardial infarction, susceptibility to, major depressive disorder 1, legionnaire disease, susceptibility to, myocardial infarction, susceptibility to, 2, major depressive disorder 2, hypertension, essential, susceptibility to, 4, epilepsy, idiopathic generalized, susceptibility to, 3, myoclonic epilepsy, juvenile, susceptibility to, 3, orofacial cleft 6, susceptibility to, coronary heart disease, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 1, attention deficit-hyperactivity disorder, susceptibility to, 2, attention deficit-hyperactivity disorder, susceptibility to, 3, attention deficit-hyperactivity disorder, susceptibility to, 4, Alzheimer disease 9, susceptibility to respiratory infections associated with CD8alpha chain mutation, dyslexia, susceptibility to, 8, autoimmune disease, susceptibility to, 4, epilepsy, idiopathic generalized, susceptibility to, 4, celiac disease, susceptibility to, 4, celiac disease, susceptibility to, 2, celiac disease, susceptibility to, 3, leprosy, susceptibility to, 1, systemic lupus erythematosus, susceptibility to, 5, systemic lupus erythematosus, susceptibility to, 6, opioid dependence, susceptibility to, 1, systemic lupus erythematosus, susceptibility to, 7, systemic lupus erythematosus, susceptibility to, 8, hypertension, essential, susceptibility to, 5, hypertension, essential, susceptibility to, 6, Parkinson disease 13, autosomal dominant, susceptibility to, West Nile virus, susceptibility to, hepatitis B virus, susceptibility to, Buruli ulcer, susceptibility to, osteoarthritis susceptibility 4, systemic lupus erythematosus, susceptibility to, 9, coronary heart disease, susceptibility to, 7, hypertension, essential, susceptibility to, 7, leprosy, susceptibility to, 4, hypertension, essential, susceptibility to, 8, epilepsy, idiopathic generalized, susceptibility to, 13, coronary heart disease, susceptibility to, 8, myoclonic epilepsy, juvenile, susceptibility to, 4, susceptibility to visceral leishmaniasis, 2, susceptibility to visceral leishmaniasis, 3, celiac disease, susceptibility to, 6, epilepsy, idiopathic generalized, susceptibility to, 5, epilepsy, childhood absence, susceptibility to, 6, celiac disease, susceptibility to, 7, celiac disease, susceptibility to, 8, celiac disease, susceptibility to, 9, celiac disease, susceptibility to, 10, celiac disease, susceptibility to, 11, celiac disease, susceptibility to, 12, celiac disease, susceptibility to, 13, coronary heart disease, susceptibility to, 9, systemic lupus erythematosus, susceptibility to, 10, systemic lupus erythematosus, susceptibility to, 11, systemic lupus erythematosus, susceptibility to, 12, epilepsy, childhood absence, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 6, systemic lupus erythematosus, susceptibility to, 13, sarcoidosis, susceptibility to, 2, sarcoidosis, susceptibility to, 3, osteoarthritis susceptibility 5, osteoarthritis susceptibility 6, focal segmental glomerulosclerosis 4, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 8, herpes simplex encephalitis, susceptibility to, 2, attention deficit-hyperactivity disorder, susceptibility to, 7, epilepsy, idiopathic generalized, susceptibility to, 10, pelvic organ prolapse, susceptibility to, 2, systemic lupus erythematosus, susceptibility to, 14, leprosy, susceptibility to, 5, thyrotoxic periodic paralysis, susceptibility to, 2, hearing loss, cisplatin-induced, susceptibility to, susceptibility to mononeuropathy of the median nerve, mild, fatty liver disease, nonalcoholic, susceptibility to, 2, leprosy, susceptibility to, 6, autoimmune disease, susceptibility to, 6, Parkinson disease 5, autosomal dominant, susceptibility to, aspergillosis, susceptibility to, sick sinus syndrome 3, susceptibility to, Parkinson disease 18, autosomal dominant, susceptibility to, epilepsy, juvenile myoclonic, susceptibility to, 9, dengue virus, susceptibility to, coronary heart disease, susceptibility to, 6, podoconiosis, susceptibility to, peripartum cardiomyopathy, susceptibility to, influenza, severe, susceptibility to, thyrotoxic periodic paralysis, susceptibility to, 3, human herpesvirus 8, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 12, herpes simplex encephalitis, susceptibility to, 3, herpes simplex encephalitis, susceptibility to, 4, pulmonary hypertension, neonatal, susceptibility to, craniosynostosis 5, susceptibility to, melioidosis, susceptibility to, chronic mountain sickness, susceptibility to, herpes simplex encephalitis, susceptibility to, 7, epilepsy, idiopathic generalized, susceptibility to, 14, hereditary neoplastic syndrome, autosomal recessive Mendelian susceptibility to mycobacterial diseases due to partial IFNgammaR1 deficiency, autosomal recessive Mendelian susceptibility to mycobacterial diseases due to partial IFNgammaR2 deficiency, susceptibility to localized juvenile periodontitis, inherited susceptibility to mycobacterial diseases, neural tube defects, susceptibility to, multiple system atrophy 1, susceptibility to, nephrolithiasis susceptibility caused by SLC26A1, myoclonic epilepsy, juvenile, susceptibility to, 1, epilepsy, childhood absence, susceptibility to, 1, autism, susceptiblity to, susceptibility to visceral leishmaniasis, 1, malaria, susceptibility to, spondyloarthropathy, susceptibility to, herpes simplex encephalitis, susceptibility to, 1, epilepsy, idiopathic generalized, susceptibility to, 18, epilepsy, idiopathic generalized, susceptibility to, 15, hepatitis, fulminant viral, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 16, autosomal recessive mendelian susceptibility to mycobacterial diseases due to partial jak1 deficiency, aortic aneurysm, familial thoracic 11, susceptibility to, craniosynostosis 7, amyotrophic lateral sclerosis, susceptibility to, 24, amyotrophic lateral sclerosis, susceptibility to, 25, epilepsy, juvenile myoclonic, susceptibility to, 10, susceptibility to angioedema induced by ACE inhibitors, epidermodysplasia verruciformis, susceptibility to, exfoliation syndrome, susceptibility to, basal cell carcinoma, susceptibility to, graft-versus-host disease, susceptibility to, narcolepsy, susceptibility to, pulmonary disease, chronic obstructive, susceptibility to, restless legs syndrome, susceptibility to, psoriasis, susceptibility to, age related macular degeneration, susceptibility to, allergic rhinitis, susceptibility to, dermatitis, atopic, susceptibility to, Hirschsprung disease, susceptibility to, diabetes mellitus, ketosis-prone, schizophrenia, susceptibility to, radioulnar synostosis, nonsyndromic, susceptibility to, lumbar disk herniation, susceptibility to, lumbar disk degeneration, susceptibility to, psoriatic arthritis, susceptibility to, migraine with or without aura, susceptibility to, Alzheimer disease, susceptibility to, mitochondrial, Asperger syndrome, susceptibility to, tobacco addiction, susceptibility to, lipodystrophy, partial, acquired, susceptibility to, Graves disease, susceptibility to, 1, epilepsy, idiopathic generalized, susceptibility to, 17, breast-ovarian cancer, familial, susceptibility to, blepharospasm, benign essential, susceptibility to, hemorrhage, intracerebral, susceptibility to, IgA nephropathy, susceptibility to, hemolytic uremic syndrome, atypical, susceptibility to, 7, vitiligo-associated multiple autoimmune disease susceptibility 6, delayed sleep phase syndrome, susceptibility to, encephalitis, acute, infection-induced, susceptibility to, malignant hyperthermia, susceptibility to, multicentric Castleman disease, susceptibility to, pelvic organ prolapse, susceptibility to, 1, amyotrophic lateral sclerosis, susceptibility to, 13, Graves disease, susceptibility to, X-linked 2, autoimmune thyroid disease, susceptibility to, 5, atrioventricular septal defect, susceptibility to, 1, epilepsy, juvenile myoclonic, susceptibility to, 6, autoimmune disease, susceptibility to, 5, epilepsy, idiopathic generalized, susceptibility to, 6, seasonal affective disorder, susceptibility to, ventricular fibrillation during myocardial infarction, susceptibility to, UV-induced skin damage, susceptibility to, antisocial behavior, susceptibility to, aplastic anemia, susceptibility to, cardiomyopathy, familial hypertrophic, 4, susceptibility to, cirrhosis, noncryptogenic, susceptibility to, coronary artery disease, severe, susceptibility to, dengue fever, susceptibility to, dengue hemorrhagic fever, susceptibility to, dengue shock syndrome, susceptibility to, dyslexia, susceptibility to, 4, dyslexia, susceptibility to, 7, efavirenz central nervous system toxicity, susceptibility to, obesity, susceptibility to, bleeding disorder, platelet-type, 13, susceptibility to, Schistosoma mansoni infection, susceptibility/resistance to, Parkinson disease 24, autosomal dominant, susceptibility to, iron overload, susceptibility to, hydrocephalus, congenital, 5, susceptibility to, hearing loss, noise-induced, susceptibility to, hyperemesis gravidarum, susceptibility to, Parkinson disease 26, autosomal dominant, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 19, polycystic kidney disease 9, susceptibility to, rhabdomyolysis, susceptibility to, scoliosis, isolated, susceptibility to, dystonia 38, susceptibility to, gallbladder disease 4, epilepsy, juvenile absence, susceptibility to, GBA1-related Parkinson disease, susceptibility, SH2B3-related immune system disorder

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

19 retrieved; paginated sample, class counts are floors:

6 uncertain significance, 4 not provided, 3 benign, 2 likely benign, 2 benign/likely benign, 1 pathogenic, 1 conflicting classifications of pathogenicity

ClinVarVariant (HGVS)GeneClassificationReview
1710531NC_000001.11:g.206773552T>CIL10Pathogeniccriteria provided, single submitter
190992NM_002838.5(PTPRC):c.3545T>C (p.Leu1182Ser)PTPRCConflicting classifications of pathogenicitycriteria provided, conflicting classifications
992556NM_001394783.1(CCR5):c.187A>T (p.Ser63Cys)CCR5Uncertain significancecriteria provided, multiple submitters, no conflicts
56170NM_002273.4(KRT8):c.1412G>A (p.Gly471Glu)KRT8Uncertain significancecriteria provided, single submitter
1384148NM_002838.5(PTPRC):c.248C>T (p.Thr83Ile)PTPRCUncertain significancecriteria provided, multiple submitters, no conflicts
1675115NM_002838.5(PTPRC):c.592C>A (p.Leu198Ile)PTPRCUncertain significancecriteria provided, single submitter
440228NM_002838.5(PTPRC):c.982A>G (p.Ile328Val)PTPRCUncertain significancecriteria provided, multiple submitters, no conflicts
4277341NM_003265.3(TLR3):c.633+136G>TTLR3Uncertain significancecriteria provided, single submitter
14631NM_002273.4(KRT8):c.160T>C (p.Tyr54His)KRT8Benigncriteria provided, multiple submitters, no conflicts
56169NM_002273.4(KRT8):c.1340C>T (p.Ala447Val)KRT8Likely benigncriteria provided, single submitter
66533NM_002273.4(KRT8):c.187A>G (p.Ile63Val)KRT8Benign/Likely benigncriteria provided, multiple submitters, no conflicts
1085729NM_002838.5(PTPRC):c.596A>G (p.Asn199Ser)PTPRCLikely benigncriteria provided, multiple submitters, no conflicts
1290650NM_002838.5(PTPRC):c.2848-4delPTPRCBenigncriteria provided, multiple submitters, no conflicts
378445NM_002838.5(PTPRC):c.1052A>G (p.Asn351Ser)PTPRCBenign/Likely benigncriteria provided, multiple submitters, no conflicts
516877NM_002838.5(PTPRC):c.2848-5_2848-4delPTPRCBenigncriteria provided, multiple submitters, no conflicts
56165NM_000224.3(KRT18):c.1230C>G (p.Thr410=)KRT18not providedno classification provided
56167NM_000224.3(KRT18):c.134G>C (p.Arg45Pro)KRT18not providedno classification provided
56168NM_002273.4(KRT8):c.1033G>T (p.Ala345Ser)KRT8not providedno classification provided
56166NM_000224.3(KRT18):c.282C>T (p.Tyr94=)LOC106096416not providedno classification provided

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 0 · Orphanet: 5 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
TLR3Orphanet:1930Herpes simplex virus encephalitis
IL10Orphanet:117Behçet disease
IL10Orphanet:238569Immune dysregulation-inflammatory bowel disease-arthritis-recurrent infections syndrome
IL10Orphanet:536Systemic lupus erythematosus
PTPRCOrphanet:169157T-B+ severe combined immunodeficiency due to CD45 deficiency

Cohort genes → proteins

6 cohort genes, 6 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence6

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
TLR3HGNC:11849ENSG00000164342O15455Toll-like receptor 3clinvar
CCR5HGNC:1606ENSG00000160791P51681C-C chemokine receptor type 5clinvar
IL10HGNC:5962ENSG00000136634P22301Interleukin-10clinvar
KRT18HGNC:6430ENSG00000111057P05783Keratin, type I cytoskeletal 18clinvar
KRT8HGNC:6446ENSG00000170421P05787Keratin, type II cytoskeletal 8clinvar
PTPRCHGNC:9666ENSG00000081237P08575Receptor-type tyrosine-protein phosphatase Cclinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
TLR3Toll-like receptor 3Key component of innate and adaptive immunity.
CCR5C-C chemokine receptor type 5Receptor for a number of inflammatory CC-chemokines including CCL3/MIP-1-alpha, CCL4/MIP-1-beta and RANTES and subsequently transduces a signal by increasing the intracellular calcium ion level.
IL10Interleukin-10Major immune regulatory cytokine that acts on many cells of the immune system where it has profound anti-inflammatory functions, limiting excessive tissue disruption caused by inflammation.
KRT18Keratin, type I cytoskeletal 18Required for the formation of KRT8/KRT18 filaments that are involved in ARHGEF40-mediated actin stress fiber formation and tensional force-induced stress fiber formation and reinforcement.
KRT8Keratin, type II cytoskeletal 8Required for the formation of KRT8/KRT18 filaments that are involved in ARHGEF40-mediated actin stress fiber formation and tensional force-induced stress fiber formation and reinforcement.
PTPRCReceptor-type tyrosine-protein phosphatase CProtein tyrosine-protein phosphatase required for T-cell activation through the antigen receptor.

Protein-family classification

Druggable: 2 · Difficult: 0 · Unknown: 4 · Druggable fraction: 0.33

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Phosphatase114.0×0.208
GPCR14.0×0.339
Other/Unknown41.2×0.458

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
TLR3Other/UnknownnoTIR_dom, Cys-rich_flank_reg_C, Leu-rich_rpt
CCR5GPCRyesGPCR_Rhodpsn, Chemokine_rcpt, Chemokine_CCR5
IL10Other/UnknownnoIL-10, 4_helix_cytokine-like_core, IL-10_CS
KRT18Other/UnknownnoKeratin_I, IF_conserved, IF_rod_dom
KRT8Other/UnknownnoKeratin_II, IF_conserved, Keratin_2_head
PTPRCPhosphataseyesPTP_cat, Tyr_Pase_dom, Tyr_Pase_cat

Expression context

Cohort genes with no expression data: 0.

6 cohort genes are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)6
unknown0

Top tissues across cohort

TissueCohort genes
endometrium epithelium2
jejunal mucosa1
palpebral conjunctiva1
placenta1
epithelium of nasopharynx1
olfactory bulb1
type B pancreatic cell1
cartilage tissue1
gall bladder1
vermiform appendix1
colonic mucosa1
mucosa of sigmoid colon1
duodenum1
mucosa of transverse colon1
leukocyte1
monocyte1
mononuclear cell1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
TLR3232ubiquitousmarkerjejunal mucosa, palpebral conjunctiva, placenta
CCR5194broadmarkertype B pancreatic cell, olfactory bulb, epithelium of nasopharynx
IL10158broadmarkervermiform appendix, gall bladder, cartilage tissue
KRT18250ubiquitousmarkerendometrium epithelium, mucosa of sigmoid colon, colonic mucosa
KRT8159ubiquitousmarkermucosa of transverse colon, endometrium epithelium, duodenum
PTPRC277broadmarkermonocyte, mononuclear cell, leukocyte

Protein interactions among cohort

Intra-cohort edges: 2.

Hub genes (top 10 by interactor count)

SymbolInteractor count
PTPRC6,849
IL106,185
KRT184,409
TLR34,305
KRT83,915
CCR53,406

Intra-cohort edges

ABSources
KRT18KRT8intact, string_interaction
KRT8PTPRCstring_interaction

Structural data

PDB: 5 · AlphaFold-only: 1 · No structure: 0

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
CCR5P5168126
TLR3O1545520
IL10P223019
PTPRCP085756
KRT8P057873

AlphaFold-only cohort genes (top 30 by pLDDT)

SymbolUniProtpLDDT
KRT18P0578380.18

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 45. Enrichment computed across 6 evidence-associated genes (6 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 6 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Developmental Lineage of Mammary Gland Alveolar Cells2211.5×0.002KRT18, KRT8
Developmental Lineage of Mammary Gland Luminal Epithelial Cells2152.3×0.002KRT18, KRT8
Interleukin-10 signaling277.7×0.004CCR5, IL10
TLR3 deficiency - HSE11903.3×0.006TLR3
UNC93B1 deficiency - HSE1951.7×0.008TLR3
TICAM1 deficiency - HSE1951.7×0.008TLR3
TRAF3 deficiency - HSE1634.4×0.010TLR3
Binding and entry of HIV virion1475.8×0.011CCR5
Formation of the cornified envelope229.3×0.011KRT18, KRT8
TLR3-mediated TICAM1-dependent programmed cell death1317.2×0.014TLR3
Early Phase of HIV Life Cycle1271.9×0.015CCR5
Keratinization218.6×0.017KRT18, KRT8
CD163 mediating an anti-inflammatory response1190.3×0.018IL10
TICAM1,TRAF6-dependent induction of TAK1 complex1173.0×0.019TLR3
Regulation of TBK1, IKKε-mediated activation of IRF3, IRF7 upon TLR3 ligation1158.6×0.019TLR3
Trafficking and processing of endosomal TLR1135.9×0.019TLR3
TICAM1-dependent activation of IRF3/IRF71135.9×0.019TLR3
RIP-mediated NFkB activation via ZBP11112.0×0.022TLR3
TICAM1, RIP1-mediated IKK complex recruitment1100.2×0.022TLR3
Other semaphorin interactions1100.2×0.022PTPRC
Phosphorylation of CD3 and TCR zeta chains190.6×0.024PTPRC
Gene and protein expression by JAK-STAT signaling after Interleukin-12 stimulation150.1×0.040IL10
FCGR3A-mediated IL10 synthesis148.8×0.040IL10
Toll Like Receptor 3 (TLR3) Cascade132.3×0.057TLR3
Chemokine receptors bind chemokines131.2×0.057CCR5
HIV Life Cycle126.8×0.063CCR5
RSV-host interactions126.1×0.063TLR3
Signaling by ALK fusions and activated point mutants125.0×0.063IL10
HIV Infection119.8×0.077CCR5
Interleukin-4 and Interleukin-13 signaling117.1×0.085IL10

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 6 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
extrinsic apoptotic signaling pathway4204.3×3e-07TLR3, KRT18, KRT8, PTPRC
hepatocyte apoptotic process2351.1×0.001KRT18, KRT8
positive regulation of immunoglobulin production2160.5×0.003IL10, PTPRC
B cell proliferation2160.5×0.003IL10, PTPRC
tumor necrosis factor-mediated signaling pathway2110.1×0.005KRT18, KRT8
negative regulation of chronic inflammatory response to antigenic stimulus12808.7×0.006IL10
type III interferon production12808.7×0.006TLR3
plasma membrane raft distribution12808.7×0.006PTPRC
positive regulation of antigen receptor-mediated signaling pathway12808.7×0.006PTPRC
negative regulation of cytokine activity12808.7×0.006IL10
regulation of response to wounding12808.7×0.006IL10
B cell differentiation273.0×0.006IL10, PTPRC
chronic inflammatory response to antigenic stimulus11404.3×0.007IL10
negative regulation of interleukin-18 production11404.3×0.007IL10
positive regulation of type III interferon production11404.3×0.007TLR3
negative regulation of interleukin-4-mediated signaling pathway11404.3×0.007PTPRC
positive regulation of hematopoietic stem cell migration11404.3×0.007PTPRC
MAPK cascade251.1×0.007CCR5, PTPRC
positive regulation of tumor necrosis factor production251.1×0.007TLR3, PTPRC
regulation of dendritic cell cytokine production1936.2×0.008TLR3
response to inactivity1936.2×0.008IL10
response to carbon monoxide1936.2×0.008IL10
response to dsRNA1936.2×0.008TLR3
alpha-beta T cell proliferation1936.2×0.008PTPRC
response to other organism1936.2×0.008KRT8
positive regulation of B cell apoptotic process1702.2×0.008IL10
negative regulation of cell adhesion involved in substrate-bound cell migration1702.2×0.008PTPRC
detection of virus1702.2×0.008TLR3
negative regulation of myeloid dendritic cell activation1702.2×0.008IL10
regulation of interleukin-8 production1702.2×0.008PTPRC

Therapeutics

Drug target analysis

Approved (phase 4): 1 · Phase ≥3: 1 · Phased (≥1): 1 · Undrugged: 5

Druggability breadth: 5 of 6 evidence-associated genes (83%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Genes with an approved drug

The molecule shown is one approved compound that hits the gene — not necessarily a drug of choice or one indicated for this disease.

SymbolExample approved molecule
CCR5TERFENADINE

Top cohort targets by molecule count

SymbolMoleculesMax phase
CCR5154
TLR300
IL1000
KRT1800
KRT800
PTPRC00

Drugs targeting cohort genes (top 30)

MoleculeMax phaseTargets in cohort
TERFENADINE4CCR5
ABAMETAPIR4CCR5
MARAVIROC4CCR5
DISULFIRAM4CCR5
APLAVIROC3CCR5
APLAVIROC HYDROCHLORIDE3CCR5
CENICRIVIROC3CCR5
VICRIVIROC3CCR5
INCB-94712CCR5
AZD56722CCR5
JNJ-17166864 CATION2CCR5
BMS-7416722CCR5
BMS-8131602CCR5
ANCRIVIROC2CCR5
CENICRIVIROC MESYLATE1CCR5

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Cohort genes with ChEMBL bioactivity (full, sorted by assay count)

SymbolAssaysType breakdown
CCR5409Binding:243, Functional:166
PTPRC111Binding:110, ADMET:1
TLR355Binding:52, Functional:3
KRT181Binding:1

Cohort genes with high screening signal

≥100 ChEMBL assays — a studied-ness signal; see Therapeutics for approved-drug status.

SymbolChEMBL assays
CCR5409
PTPRC111

Pharmacogenomics

Cohort genes with a PharmGKB record: 6; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

15 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

CompoundMax phaseCohort target (bioactivity)
TERFENADINE4CCR5
ABAMETAPIR4CCR5
MARAVIROC4CCR5
DISULFIRAM4CCR5
APLAVIROC3CCR5
APLAVIROC HYDROCHLORIDE3CCR5
CENICRIVIROC3CCR5
VICRIVIROC3CCR5
INCB-94712CCR5
AZD56722CCR5
JNJ-17166864 CATION2CCR5
BMS-7416722CCR5
BMS-8131602CCR5
ANCRIVIROC2CCR5
CENICRIVIROC MESYLATE1CCR5

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)1CCR5
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug1PTPRC
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug4TLR3, IL10, KRT18, KRT8

Undrugged target profiles

5 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
PTPRC111
TLR355
IL100
KRT181
KRT80

Clinical trials & evidence

Clinical trials

Clinical trials: 0.