Hereditary sensory and autonomic neuropathy type 7

disease
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Also known as autosomal dominant hereditary sensory and autonomic neuropathy caused by mutation in SCN11ACIP with hyperhidrosis and gastrointestinal dysfunctioncongenital insensitivity to pain with hyperhidrosis and gastrointestinal dysfunctionhereditary sensory and autonomic neuropathy type VIIhereditary sensory and autonomic neuropathy with hyperhidrosis and gastrointestinal dysfunctionHSAN VIIHSAN with hyperhidrosis and gastrointestinal dysfunctionHSAN7neuropathy, hereditary sensory and autonomic, type VIISCN11A autosomal dominant hereditary sensory and autonomic neuropathy

Summary

Hereditary sensory and autonomic neuropathy type 7 (MONDO:0014244) is a disease caused by SCN11A (GenCC Definitive), with 2 cohort genes.

At a glance

  • Prevalence: <1 / 1 000 000 (Worldwide) [Orphanet-validated]
  • Causal gene: SCN11A (GenCC Definitive)
  • Cohort genes: 2
  • ClinVar variants: 1,383

Clinical features

Epidemiology

Prevalence records

2 prevalence record(s), Orphanet:

TypeClassValueGeographyValidation
Cases/families3WorldwideValidated
Point prevalence<1 / 1 000 000WorldwideValidated

Identifiers

Disease identifiers

FieldValue
Canonical namehereditary sensory and autonomic neuropathy type 7
Mondo IDMONDO:0014244
OMIM615548
Orphanet391397
DOIDDOID:0070149
NCITC125388
UMLSC3809882
MedGen816212
GARD0012732
Is cancer (heuristic)no

Also known as: autosomal dominant hereditary sensory and autonomic neuropathy caused by mutation in SCN11A · CIP with hyperhidrosis and gastrointestinal dysfunction · congenital insensitivity to pain with hyperhidrosis and gastrointestinal dysfunction · hereditary sensory and autonomic neuropathy type VII · hereditary sensory and autonomic neuropathy with hyperhidrosis and gastrointestinal dysfunction · HSAN VII · HSAN with hyperhidrosis and gastrointestinal dysfunction · HSAN7 · neuropathy, hereditary sensory and autonomic, type VII · SCN11A autosomal dominant hereditary sensory and autonomic neuropathy

Data availability: 1,383 ClinVar variants · 4 GenCC gene-disease records · 2 cell lines.

Disease family

Classification path: disease › human disease › disease by body system or component › nervous system disorderperipheral nervous system disorderperipheral neuropathysensory peripheral neuropathyhereditary sensory and autonomic neuropathyhereditary sensory and autonomic neuropathy type 7

Related subtypes (12): polyneuropathy-hand defect syndrome, hereditary sensory and autonomic neuropathy type 4, neuropathy, hereditary sensory, atypical, X-linked hereditary sensory and autonomic neuropathy with hearing loss, hereditary sensory neuropathy X-linked, hereditary sensory and autonomic neuropathy type 5, hereditary sensory and autonomic neuropathy type 6, congenital insensitivity to pain-hypohidrosis syndrome, congenital insensitivity to pain with hyperhidrosis, hereditary sensory and autonomic neuropathy type 1, cold-induced sweating syndrome - hyperthermia spectrum, hereditary sensory and autonomic neuropathy type 2

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

600 retrieved; paginated sample, class counts are floors:

347 uncertain significance, 206 likely benign, 24 conflicting classifications of pathogenicity, 18 benign, 5 benign/likely benign

ClinVarVariant (HGVS)GeneClassificationReview
1001012NM_001349253.2(SCN11A):c.4414C>T (p.Arg1472Ter)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1002213NM_001349253.2(SCN11A):c.3010G>A (p.Gly1004Arg)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1014224NM_001349253.2(SCN11A):c.4978G>A (p.Ala1660Thr)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1017449NM_001349253.2(SCN11A):c.3467G>A (p.Arg1156His)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1039827NM_001349253.2(SCN11A):c.4640T>C (p.Ile1547Thr)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1056448NM_001349253.2(SCN11A):c.89G>A (p.Arg30Gln)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1060572NM_001349253.2(SCN11A):c.1913G>A (p.Arg638His)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1142743NM_001349253.2(SCN11A):c.4057-6delSCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1352340NM_001349253.2(SCN11A):c.2222C>T (p.Pro741Leu)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1397095NM_001349253.2(SCN11A):c.923C>T (p.Pro308Leu)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1463207NM_001349253.2(SCN11A):c.2404-6T>CSCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1476674NM_001349253.2(SCN11A):c.4081G>A (p.Asp1361Asn)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1516982NM_001349253.2(SCN11A):c.2518C>T (p.Arg840Cys)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1542161NM_001349253.2(SCN11A):c.970A>G (p.Ile324Val)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
157599NM_001349253.2(SCN11A):c.3473T>C (p.Leu1158Pro)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
157600NM_001349253.2(SCN11A):c.1142T>C (p.Ile381Thr)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1675178NM_001349253.2(SCN11A):c.3366G>A (p.Trp1122Ter)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1685430NM_001349253.2(SCN11A):c.712+1G>ASCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1737551NM_001349253.2(SCN11A):c.4070G>C (p.Gly1357Ala)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1798487NM_001349253.2(SCN11A):c.298A>G (p.Ile100Val)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1805943NM_001349253.2(SCN11A):c.4894A>G (p.Lys1632Glu)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1928733NM_001349253.2(SCN11A):c.4322T>C (p.Ile1441Thr)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
2379025NM_001349253.2(SCN11A):c.1912C>T (p.Arg638Cys)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
2922596NM_001349253.2(SCN11A):c.2479G>T (p.Ala827Ser)SCN11AConflicting classifications of pathogenicitycriteria provided, conflicting classifications
1055871NM_001349253.2(SCN11A):c.3693C>A (p.Phe1231Leu)LOC126806652Uncertain significancecriteria provided, single submitter
1374373NM_001349253.2(SCN11A):c.3509C>T (p.Ala1170Val)LOC126806652Uncertain significancecriteria provided, multiple submitters, no conflicts
1489622NM_001349253.2(SCN11A):c.3655A>G (p.Ile1219Val)LOC126806652Uncertain significancecriteria provided, single submitter
1503941NM_001349253.2(SCN11A):c.3746C>T (p.Ala1249Val)LOC126806652Uncertain significancecriteria provided, multiple submitters, no conflicts
1517780NM_001349253.2(SCN11A):c.3578G>T (p.Cys1193Phe)LOC126806652Uncertain significancecriteria provided, single submitter
1715954NM_001349253.2(SCN11A):c.3745G>C (p.Ala1249Pro)LOC126806652Uncertain significancecriteria provided, single submitter

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 8 · Orphanet: 12 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

GenCC gene–disease validity (cohort genes)

the Disease column is the GenCC-asserted condition — a cohort gene’s strongest validity may be for a related predisposition syndrome.

GeneClassificationInheritanceDiseaseRecords
SCN11ADefinitiveAutosomal dominanthereditary sensory and autonomic neuropathy type 78

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
SCN11AOrphanet:306577Hereditary sodium channelopathy-related small fibers neuropathy
SCN11AOrphanet:391392Familial episodic pain syndrome with predominantly lower limb involvement
SCN11AOrphanet:391397Hereditary sensory and autonomic neuropathy type 7
SCN11AOrphanet:46348Paroxysmal extreme pain disorder
SCN11AOrphanet:88642Congenital insensitivity to pain-anosmia-neuropathic arthropathy
SCN11AOrphanet:90026Primary erythromelalgia
SCN10AOrphanet:101016Romano-Ward syndrome
SCN10AOrphanet:130Brugada syndrome
SCN10AOrphanet:306577Hereditary sodium channelopathy-related small fibers neuropathy
SCN10AOrphanet:46348Paroxysmal extreme pain disorder
SCN10AOrphanet:88642Congenital insensitivity to pain-anosmia-neuropathic arthropathy
SCN10AOrphanet:90026Primary erythromelalgia

Cohort genes → proteins

2 cohort genes, 2 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence2

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
SCN11AHGNC:10583ENSG00000168356Q9UI33Sodium channel protein type 11 subunit alphagencc,clinvar
SCN10AHGNC:10582ENSG00000185313Q9Y5Y9Sodium channel protein type 10 subunit alphaclinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
SCN11ASodium channel protein type 11 subunit alphaSodium channel mediating the voltage-dependent sodium ion permeability of excitable membranes.
SCN10ASodium channel protein type 10 subunit alphaTetrodotoxin-resistant channel that mediates the voltage-dependent sodium ion permeability of excitable membranes.

Protein-family classification

Druggable: 2 · Difficult: 0 · Unknown: 0 · Druggable fraction: 1.0

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Ion channel2111.5×8e-05

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
SCN11AIon channelyesNa_channel_asu, Ion_trans_dom, Na_trans_assoc_dom
SCN10AIon channelyesNa_channel_asu, Ion_trans_dom, Na_trans_assoc_dom

Expression context

Cohort genes with no expression data: 0.

2 cohort genes are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)2
unknown0

Top tissues across cohort

TissueCohort genes
buccal mucosa cell1
dorsal root ganglion1
male germ line stem cell (sensu Vertebrata) in testis1
diaphragm1
olfactory bulb1
type B pancreatic cell1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
SCN11A166broadmarkerbuccal mucosa cell, dorsal root ganglion, male germ line stem cell (sensu Vertebrata) in testis
SCN10A21markertype B pancreatic cell, olfactory bulb, diaphragm

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
SCN10A1,802
SCN11A1,202

Structural data

PDB: 1 · AlphaFold-only: 1 · No structure: 0

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
SCN10AQ9Y5Y98

AlphaFold-only cohort genes (top 30 by pLDDT)

SymbolUniProtpLDDT
SCN11AQ9UI3369.66

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 8. Enrichment computed across 2 evidence-associated genes (2 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 2 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Interaction between L1 and Ankyrins2368.4×3e-05SCN11A, SCN10A
Phase 0 - rapid depolarisation2346.1×3e-05SCN11A, SCN10A
L1CAM interactions2120.2×2e-04SCN11A, SCN10A
Cardiac conduction2108.8×2e-04SCN11A, SCN10A
Muscle contraction277.2×3e-04SCN11A, SCN10A
Axon guidance245.1×6e-04SCN11A, SCN10A
Nervous system development242.9×6e-04SCN11A, SCN10A
Developmental Biology214.5×0.005SCN11A, SCN10A

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 2 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
membrane depolarization during action potential21685.2×1e-05SCN11A, SCN10A
cardiac muscle cell action potential involved in contraction2702.2×4e-05SCN11A, SCN10A
sodium ion transmembrane transport2203.0×3e-04SCN11A, SCN10A
reflex18426.0×0.001SCN11A
small intestine smooth muscle contraction18426.0×0.001SCN11A
thermosensory behavior14213.0×0.001SCN11A
behavioral response to acetic acid induced pain14213.0×0.001SCN11A
bundle of His cell action potential14213.0×0.001SCN10A
response to high light intensity12808.7×0.001SCN11A
micturition12808.7×0.001SCN11A
behavioral response to formalin induced pain12808.7×0.001SCN11A
action potential initiation12808.7×0.001SCN11A
thigmotaxis12106.5×0.001SCN11A
AV node cell action potential12106.5×0.001SCN10A
response to nitric oxide11685.2×0.002SCN11A
calcitonin gene-related peptide receptor signaling pathway11404.3×0.002SCN11A
skeletal muscle organ development11053.2×0.002SCN11A
regulation of atrial cardiac muscle cell membrane depolarization1936.2×0.002SCN10A
sensory perception of itch1936.2×0.002SCN11A
acute inflammatory response1842.6×0.002SCN11A
chronic inflammatory response1842.6×0.002SCN11A
sensory perception1702.2×0.002SCN10A
response to prostaglandin E1702.2×0.002SCN11A
artery development1702.2×0.002SCN11A
cAMP/PKA signal transduction1702.2×0.002SCN11A
detection of mechanical stimulus involved in sensory perception of pain1561.7×0.003SCN11A
cellular response to cold1526.6×0.003SCN11A
regulation of cardiac muscle contraction1443.5×0.003SCN10A
detection of temperature stimulus involved in sensory perception of pain1421.3×0.004SCN11A
response to auditory stimulus1366.4×0.004SCN11A

Therapeutics

Drug target analysis

Approved (phase 4): 2 · Phase ≥3: 2 · Phased (≥1): 2 · Undrugged: 0

Druggability breadth: 2 of 2 evidence-associated genes (100%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Genes with an approved drug

The molecule shown is one approved compound that hits the gene — not necessarily a drug of choice or one indicated for this disease.

SymbolExample approved molecule
SCN11AIMIPRAMINE
SCN10AIMIPRAMINE

Top cohort targets by molecule count

SymbolMoleculesMax phase
SCN10A214
SCN11A154

Drugs targeting cohort genes (top 30)

MoleculeMax phaseTargets in cohort
IMIPRAMINE4SCN10A, SCN11A
SERTINDOLE4SCN10A, SCN11A
PIMOZIDE4SCN10A, SCN11A
NIFEDIPINE4SCN10A, SCN11A
DILTIAZEM4SCN10A, SCN11A
MIBEFRADIL4SCN10A, SCN11A
HALOPERIDOL4SCN10A, SCN11A
MEXILETINE4SCN10A, SCN11A
AMITRIPTYLINE4SCN10A, SCN11A
AMIODARONE4SCN10A, SCN11A
CHLORPROMAZINE4SCN10A, SCN11A
LAMOTRIGINE4SCN10A
TEDISAMIL3SCN10A, SCN11A
NITRENDIPINE3SCN10A, SCN11A
AJMALINE3SCN10A, SCN11A
VIXOTRIGINE3SCN10A
ELECLAZINE3SCN10A
CIFENLINE2SCN10A, SCN11A
PF-045310832SCN10A
FUNAPIDE2SCN10A
PF-063055911SCN10A

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Cohort genes with ChEMBL bioactivity (full, sorted by assay count)

SymbolAssaysType breakdown
SCN10A144Binding:124, Functional:16, ADMET:4
SCN11A33Functional:16, Binding:15, ADMET:2

Cohort genes with high screening signal

≥100 ChEMBL assays — a studied-ness signal; see Therapeutics for approved-drug status.

SymbolChEMBL assays
SCN10A144

Pharmacogenomics

Cohort genes with a PharmGKB record: 2; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

21 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

CompoundMax phaseCohort target (bioactivity)
IMIPRAMINE4SCN10A, SCN11A
SERTINDOLE4SCN10A, SCN11A
PIMOZIDE4SCN10A, SCN11A
NIFEDIPINE4SCN10A, SCN11A
DILTIAZEM4SCN10A, SCN11A
MIBEFRADIL4SCN10A, SCN11A
HALOPERIDOL4SCN10A, SCN11A
MEXILETINE4SCN10A, SCN11A
AMITRIPTYLINE4SCN10A, SCN11A
AMIODARONE4SCN10A, SCN11A
CHLORPROMAZINE4SCN10A, SCN11A
LAMOTRIGINE4SCN10A
TEDISAMIL3SCN10A, SCN11A
NITRENDIPINE3SCN10A, SCN11A
AJMALINE3SCN10A, SCN11A
VIXOTRIGINE3SCN10A
ELECLAZINE3SCN10A
CIFENLINE2SCN10A, SCN11A
PF-045310832SCN10A
FUNAPIDE2SCN10A
PF-063055911SCN10A

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)2SCN11A, SCN10A
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug0

Undrugged target profiles

0 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

Clinical trials & evidence

Clinical trials

Clinical trials: 0.