Hypotrichosis 7

disease
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Also known as alopecia universalis congenita, Mari typehypotrichosis caused by mutation in LIPHhypotrichosis type 7hypotrichosis, localized, autosomal recessive 2HYPT7LAH2LIPH hypotrichosisMari type alopecia universalis congenitatotal hypotrichosis, Mari typetotal Mari type hypotrichosis,woolly hair, autosomal recessive 2 with or without hypotrichosiswoolly hair, autosomal recessive 2, with or without hypotrichosiswooly hair, autosomal recessive 2 with or without hypotrichosis

Summary

Hypotrichosis 7 (MONDO:0011452) is a disease caused by LIPH (GenCC Definitive), with 1 cohort gene.

At a glance

  • Causal gene: LIPH (GenCC Definitive)
  • Cohort genes: 1
  • ClinVar variants: 14

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namehypotrichosis 7
Mondo IDMONDO:0011452
MeSHC536973
OMIM604379
DOIDDOID:0110704
UMLSC1836672
MedGen322969
GARD0008178
Is cancer (heuristic)no

Also known as: alopecia universalis congenita, Mari type · hypotrichosis 7 · hypotrichosis caused by mutation in LIPH · hypotrichosis type 7 · hypotrichosis, localized, autosomal recessive 2 · HYPT7 · LAH2 · Lah2 · LIPH hypotrichosis · Mari type alopecia universalis congenita · total hypotrichosis, Mari type · total Mari type hypotrichosis, · woolly hair, autosomal recessive 2 with or without hypotrichosis · woolly hair, autosomal recessive 2, with or without hypotrichosis · wooly hair, autosomal recessive 2 with or without hypotrichosis

Data availability: 14 ClinVar variants · 3 GenCC gene-disease records.

Disease family

Classification path: disease › human disease › disease by body system or component › integumentary system disorder › disorder of pilosebaceous unithypotrichosishypotrichosis 7

Related subtypes (18): hypotrichosis of eyelid, hypotrichosis 2, hypotrichosis 8, congenital hypotrichosis with juvenile macular dystrophy, hypotrichosis 1, hypotrichosis 6, hypotrichosis 3, hypotrichosis 9, hypotrichosis 10, hypotrichosis 11, hypotrichosis 12, hypotrichosis 13, Marie Unna hereditary hypotrichosis, Basaran Yilmaz syndrome, congenital hypotrichosis milia, hypotrichosis 14, hypotrichosis 15, hypotrichosis 16

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

14 retrieved; paginated sample, class counts are floors:

5 pathogenic, 4 uncertain significance, 3 pathogenic/likely pathogenic, 2 likely pathogenic

ClinVarVariant (HGVS)GeneClassificationReview
225403NM_139248.3(LIPH):c.736T>A (p.Cys246Ser)LIPHPathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
280138NM_139248.3(LIPH):c.328C>T (p.Arg110Ter)LIPHPathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
30669NM_139248.3(LIPH):c.742C>A (p.His248Asn)LIPHPathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
3301NG_012183.1:g.(2711_2742)_(3942_3973)delLIPHPathogenicno assertion criteria provided
3302NM_139248.3(LIPH):c.346_350del (p.Ile116fs)LIPHPathogenicno assertion criteria provided
3303NM_139248.3(LIPH):c.659_660del (p.Ile220fs)LIPHPathogeniccriteria provided, multiple submitters, no conflicts
3304NM_139248.3(LIPH):c.886+405_1094+962delLIPHPathogenicno assertion criteria provided
3306NM_139248.3(LIPH):c.280_369dup (p.Lys123_Thr124insGlyLeuLeuSerValGluAspMetAsnValValValValAspTrpAsnArgGlyAlaThrThrLeuIleTyrThrHisAlaSerSerLys)LIPHPathogeniccriteria provided, multiple submitters, no conflicts
3391346NM_139248.3(LIPH):c.263del (p.Met88fs)LIPHLikely pathogeniccriteria provided, single submitter
3775180NM_139248.3(LIPH):c.686delinsGTAGAACCCAACCTGGCT (p.Asp229fs)LIPHLikely pathogeniccriteria provided, single submitter
3064369NM_139248.3(LIPH):c.899A>C (p.Asp300Ala)LIPHUncertain significancecriteria provided, single submitter
3359263NM_139248.3(LIPH):c.482G>A (p.Gly161Glu)LIPHUncertain significancecriteria provided, single submitter
3891578NM_139248.3(LIPH):c.614A>G (p.His205Arg)LIPHUncertain significancecriteria provided, single submitter
4073584NM_139248.3(LIPH):c.1301_1302insA (p.Met434fs)LIPHUncertain significancecriteria provided, single submitter

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 5 · Orphanet: 2 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

GenCC gene–disease validity (cohort genes)

the Disease column is the GenCC-asserted condition — a cohort gene’s strongest validity may be for a related predisposition syndrome.

GeneClassificationInheritanceDiseaseRecords
LIPHDefinitiveAutosomal recessivehypotrichosis 75

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
LIPHOrphanet:170Woolly hair
LIPHOrphanet:55654Hypotrichosis simplex

Cohort genes → proteins

1 cohort genes, 1 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence1

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
LIPHHGNC:18483ENSG00000163898Q8WWY8Lipase member Hgencc,clinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
LIPHLipase member HHydrolyzes specifically phosphatidic acid (PA) to produce 2-acyl lysophosphatidic acid (LPA; a potent bioactive lipid mediator) and fatty acid.

Protein-family classification

Druggable: 1 · Difficult: 0 · Unknown: 0 · Druggable fraction: 1.0

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Enzyme (other)112.0×0.083

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
LIPHEnzyme (other)yes3.1.1.32TAG_lipase, Lipase, Lipase_LIPH

Expression context

Cohort genes with no expression data: 0.

1 cohort gene are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)1
unknown0

Top tissues across cohort

TissueCohort genes
buccal mucosa cell1
pancreatic ductal cell1
rectum1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
LIPH187broadmarkerbuccal mucosa cell, rectum, pancreatic ductal cell

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
LIPH635

Structural data

PDB: 0 · AlphaFold-only: 1 · No structure: 0

AlphaFold-only cohort genes (top 30 by pLDDT)

SymbolUniProtpLDDT
LIPHQ8WWY890.89

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 5. Enrichment computed across 1 evidence-associated genes (1 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Glycerophospholipid biosynthesis1335.9×0.008LIPH
Synthesis of PA1292.8×0.008LIPH
Phospholipid metabolism1200.3×0.008LIPH
Metabolism of lipids131.6×0.040LIPH
Metabolism111.6×0.086LIPH

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
phosphatidic acid biosynthetic process1510.7×0.004LIPH
lipid catabolic process1244.2×0.004LIPH

Therapeutics

Drug target analysis

Approved (phase 4): 0 · Phase ≥3: 0 · Phased (≥1): 0 · Undrugged: 1

Druggability breadth: 0 of 1 evidence-associated genes (0%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Top cohort targets by molecule count

SymbolMoleculesMax phase
LIPH00

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 1.

Cohort enzymes (BRENDA EC)

SymbolEC numbersNames
LIPH3.1.1.32phospholipase A1

Pharmacogenomics

Cohort genes with a PharmGKB record: 1; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

0 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)0
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug1LIPH
EDifficult family or no structure, no drug0

Undrugged target profiles

1 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
LIPH0

Clinical trials & evidence

Clinical trials

Clinical trials: 0.