Lichen sclerosus et atrophicus

disease
On this page

Also known as lichen sclerosislichen sclerosis et atrophicuslichen sclerosusLSA

Summary

Lichen sclerosus et atrophicus (MONDO:0007899) is a disease with 28 GWAS associations across 5 studies and 21 clinical trials. Top therapeutic interventions include clobetasol propionate, betamethasone dipropionate, and pimecrolimus. A subtype of dermatitis — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • GWAS associations: 28
  • Clinical trials: 21

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namelichen sclerosus et atrophicus
Mondo IDMONDO:0007899
MeSHD018459
OMIM151590
Orphanet33409
ICD-10-CML90.0
NCITC26817
SNOMED CT25674000
UMLSC0023652
MedGen7338
Is cancer (heuristic)no

Also known as: lichen sclerosis · lichen sclerosis et atrophicus · lichen sclerosus · lichen sclerosus et atrophicus · LSA

Data availability: 28 GWAS associations (5 studies).

Disease family

This is a subtype of dermatitis. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by body system or component › integumentary system disorder › skin disorderdermatitislichen sclerosus et atrophicus

Related subtypes (32): spongiotic dermatitis, atopic eczema, psoriasis, contact dermatitis, urticaria, acneiform dermatitis, acrodermatitis, folliculitis, granuloma annulare, granulomatous dermatitis, lichen planus, neurodermatitis, neurotic excoriation, parapsoriasis, pityriasis rosea, seborrheic dermatitis, acanthosis nigricans, dermatosis papulosa nigra, vitiligo, acne, porphyria cutanea tarda, dermatomyositis, acute generalized exanthematous pustulosis, hydroa vacciniforme, autoimmune bullous skin disease, cutaneous vasculitis, skin infection, intertrigo, lipodermatosclerosis, exfoliative dermatitis, radiodermatitis, food dermatitis

Subtypes (1): vulvar lichen sclerosus

Genetics & variants

GWAS landscape

28 GWAS associations across 5 studies. Top hits map to 12 distinct genes (as reported by GWAS).

Top associations by p-value

rsIDp-valueGeneRisk alleleOdds ratio
rs126618062e-83HLA-DRB1 - HLA-DQA1A0.42
rs1124575252e-79HLA-DRA - HLA-DRB9A2.43
HLA-DRB1*12:018e-63?2.54
rs29496612e-17CD247T0.85
rs67325652e-15ACOXLA1.15
rs767156268e-12IL4R - IL21RT0.74
rs2004405992e-11TYMSP2 - ZBTB32A0.69
rs107957911e-10IL2RA - RPL32P23A0.9
rs1409522211e-10IGFLR1T0.73
rs47665783e-10ATXN2A0.89
rs79688082e-09LRRC43T1.11
rs5398705763e-09RN7SL335P - BLTP1T1.2
rs10421214e-09HLA-DPB1, HLA-DPA1T0.76
rs2289552e-08IL2RBT0.91
rs1876616783e-08ROCR, LINC01152T5.74
rs793760894e-08IFITM3P8 - NASPP1A1.22
rs68877835e-08MIR3142HGT1.11
rs14945645e-08SPEF2 - IL7RT0.91
rs802491974e-07MIMT1 - RPL7AP69A1.81
rs75907367e-07QPCT - CDC42EP3-AS1T0.4
rs4400948e-07TMEM63CT0.69

Top studies (by case count)

StudyLead authorYearCasesControlsTitle
GCST90824102Dand N20267,651738,739Genome-wide meta-analysis in lichen sclerosus identifies 14 genomic risk loci.
GCST90824100Dand N20266,681407,255Genome-wide meta-analysis in lichen sclerosus identifies 14 genomic risk loci.
GCST90824101Dand N2026970331,484Genome-wide meta-analysis in lichen sclerosus identifies 14 genomic risk loci.
GCST90080375Backman JD2021555387,375Exome sequencing and analysis of 454,787 UK Biobank participants.
GCST90084361Backman JD2021555387,375Exome sequencing and analysis of 454,787 UK Biobank participants.

Variant details and genetic-evidence tiers

Tier distribution (top 50 variants)

TierVariants
Tier 1: coding2
Tier 2: splice/UTR0
Tier 3: regulatory0
Tier 4: intronic/intergenic19

MAF distribution

BucketVariants
common (>=0.05)14
low_freq (0.01-0.05)6
rare (<0.01)1
unknown0

Functional consequences

ConsequenceCount
intron_variant9
intergenic_variant8
missense_variant2
unknown1
non_coding_transcript_exon_variant1

Top variants

rsIDChrPosAllelesMAFConsequenceGenep-valueTier
rs12661806632615763A>T0.023intergenic_variantHLA-DRB1 - HLA-DQA12e-83Tier 4: intronic/intergenic
rs112457525632447652G>A,C0.023intron_variantHLA-DRA - HLA-DRB92e-79Tier 4: intronic/intergenic
HLA-DRB1*12:010.0228e-63Tier 4: intronic/intergenic
rs29496611167455687C>A,G,T0.338intron_variantCD2472e-17Tier 4: intronic/intergenic
rs67325652110850255A>G,T0.392intron_variantACOXL2e-15Tier 4: intronic/intergenic
rs767156261627386721T>C0.058intergenic_variantIL4R - IL21R8e-12Tier 4: intronic/intergenic
rs2004405991935697580AAAG>A,AAAGAAG0.051intergenic_variantTYMSP2 - ZBTB322e-11Tier 4: intronic/intergenic
rs10795791106066377A>G0.475intergenic_variantIL2RA - RPL32P231e-10Tier 4: intronic/intergenic
rs1409522211935740387C>A,T0.047missense_variantIGFLR11e-10Tier 1: coding
rs476657812111466567T>A0.463intron_variantATXN23e-10Tier 4: intronic/intergenic
rs796880812122177244C>A,T0.44intergenic_variantLRRC432e-09Tier 4: intronic/intergenic
rs5398705764122115655C>A,G,T0.081intergenic_variantRN7SL335P - BLTP13e-09Tier 4: intronic/intergenic
rs1042121633080765C>A,G,T0.499missense_variantHLA-DPB1, HLA-DPA14e-09Tier 1: coding
rs2289552237136659C>T0.463intron_variantIL2RB2e-08Tier 4: intronic/intergenic
rs1876616781772040543C>T0.004non_coding_transcript_exon_variantROCR, LINC011523e-08Tier 4: intronic/intergenic
rs79376089860929420G>A0.057intron_variantIFITM3P8 - NASPP14e-08Tier 4: intronic/intergenic
rs68877835160495202T>G0.331intron_variantMIR3142HG5e-08Tier 4: intronic/intergenic
rs1494564535851729C>A,G,T0.314intron_variantSPEF2 - IL7R5e-08Tier 4: intronic/intergenic
rs802491971956911790G>A0.041intergenic_variantMIMT1 - RPL7AP694e-07Tier 4: intronic/intergenic
rs7590736237395613T>G0.011intergenic_variantQPCT - CDC42EP3-AS17e-07Tier 4: intronic/intergenic
rs4400941477236800T>C,G0.08intron_variantTMEM63C8e-07Tier 4: intronic/intergenic

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

No druggable-target or therapeutic data for this disease’s cohort.

Clinical trials & evidence

Clinical trials

Clinical trials: 21.

Phase distribution (across all retrieved trials)

PhaseTrials
Not specified17
PHASE32
PHASE22

Top trials by phase / activity

NCTPhaseStatusTitle
NCT07335588PHASE3RECRUITINGA 52-Week Trial to Investigate the Efficacy and Safety of Delgocitinib Cream in Adult Participants With Lichen Sclerosus
NCT05010421PHASE3COMPLETEDLaser vs Clobetasol for Lichen Sclerosus
NCT00393263PHASE2COMPLETEDClobetasol Versus Pimecrolimus for Vulvar Lichen Sclerosus
NCT05593445PHASE2COMPLETEDA Study to Evaluate the Efficacy and Safety of Ruxolitinib Cream in Participants With Lichen Sclerosus
NCT06135402Not specifiedRECRUITINGComparison of Laser Treatment With Clobetasol Therapy in Patients With Lichen Sclerosus
NCT06472765Not specifiedENROLLING_BY_INVITATIONVaginal Ecosystem and Network in the United States Study
NCT06984263Not specifiedRECRUITINGMale Lichen Sclerosus - Risk Factors, Treatment, and Impact on Quality of Life
NCT02223975Not specifiedSUSPENDEDEvaluation of the Role of Vibrational Spectroscopy in the Assessment of Vulval Disease
NCT02732145Not specifiedCOMPLETEDDiagnostic Accuracy of Three Rings Vulvoscopy for Detection of Vulvar Dermatosis
NCT02794363Not specifiedCOMPLETEDPlatelet Rich Plasma Injections for Vulvar Lichen Sclerosus
NCT02880904Not specifiedTERMINATEDVulvar Scarring Grading Scale for Lichen Sclerosus
NCT02881229Not specifiedTERMINATEDVulvar Mucosal Specialty Clinic Chart Review
NCT03063684Not specifiedCOMPLETEDFractional / Pixel CO2 Laser Treatment of Vulvar Atrophy and Lichen Sclerosus
NCT03419377Not specifiedCOMPLETEDLichen Sclerosus - the Influence on Quality of Life
NCT03525522Not specifiedUNKNOWNNd:Yttrium Aluminum Garnet Laser Treatment for Lichen Sclerosus
NCT03561428Not specifiedUNKNOWNBiomarkers of Lichen Sclerosus
NCT03665584Not specifiedCOMPLETEDMonaLisa Touch Laser for the Treatment of Vulvar Lichen Sclerosus
NCT04073082Not specifiedUNKNOWNSafety and Efficacy of Laser Therapy in Gynaecology
NCT04697563Not specifiedCOMPLETEDLaser Therapy in Women With Lichenoid Disorders
NCT05396261Not specifiedCOMPLETEDa Flexible Wound Dressing for the Management of Genital Skin Conditions
NCT05671263Not specifiedUNKNOWNGenital Lichen Sclerosus - Epidemiology, Comorbidities and the Role of Vulvar and Penile Microbiome

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
CLOBETASOL PROPIONATE43
BETAMETHASONE DIPROPIONATE41
PIMECROLIMUS41
CLOBETASOL33
DELGOCITINIB31
VEHICLE02
CHEMBL542120401