Myocardial infarction, susceptibility to

disease
On this page

Also known as myocardial infarction, decreased susceptibility to

Summary

Myocardial infarction, susceptibility to (MONDO:0012039) is a disease with 15 cohort genes.

At a glance

  • Cohort genes: 15
  • ClinVar variants: 70

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namemyocardial infarction, susceptibility to
Mondo IDMONDO:0012039
OMIM608446
UMLSC1832662
MedGen318680
Is cancer (heuristic)no

Also known as: myocardial infarction, decreased susceptibility to · myocardial infarction, susceptibility to

Data availability: 70 ClinVar variants · 1 GenCC gene-disease record.

Disease family

Classification path: disease susceptibility › inherited disease susceptibilitymyocardial infarction, susceptibility to

Related subtypes (283): microvascular complications of diabetes, susceptibility, Mycobacterium tuberculosis, susceptibility, bacteremia, susceptibility, pregnancy loss, recurrent, susceptibility, autoimmune thyroid disease, susceptibility to, susceptibility to HIV infection, appendicitis, proneness to, atherosclerosis susceptibility, multiple sclerosis, susceptibility to, dyslexia, susceptibility to, 1, endometriosis, susceptibility to, 1, osteoarthritis susceptibility 2, essential hypertension, genetic, osteoarthritis susceptibility 1, otitis media, susceptibility to, pelvic organ prolapse, susceptibility to, pulmonary edema of mountaineers, susceptibility to, sarcoidosis, susceptibility to, 1, strabismus, susceptibility to, thyrotoxic periodic paralysis, susceptibility to, 1, predisposition to invasive fungal disease due to CARD9 deficiency, celiac disease, susceptibility to, 1, hemolytic uremic syndrome, atypical, susceptibility to, 1, hypervitaminosis a, susceptibility to, kuru, susceptibility to, leprosy, susceptibility to, 3, nonarteritic anterior ischemic optic neuropathy, susceptibility to, diabetes mellitus, insulin-dependent, X-linked, susceptibility to, coronary heart disease, susceptibility to, 3, dyslexia, susceptibility to, 9, systemic lupus erythematosus, susceptibility to, 15, Leber optic atrophy, susceptibility to, dyslexia, susceptibility to, 2, Helicobacter pylori infection, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 1, inherited susceptibility to asthma, renal dysplasia, cystic, susceptibility to, systemic lupus erythematosus, susceptibility to, 1, leishmaniasis, tegumentary, susceptibility to, xanthomatosis, susceptibility to, hyperlipidemia, combined, 1, urinary tract infections, recurrent, susceptibility to, hypertension, essential, susceptibility to, 1, hepatic fibrosis, severe, susceptibility to, due to Schistosoma mansoni infection, dyslexia, susceptibility to, 3, Ascaris lumbricoides infection, susceptibility to, hypertension, essential, susceptibility to, 2, epilepsy, idiopathic generalized, susceptibility to, 7, systemic lupus erythematosus, susceptibility to, 2, systemic lupus erythematosus, susceptibility to, 3, nephrolithiasis, uric acid, susceptibility to, atrioventricular septal defect, susceptibility to, 2, vitiligo-associated multiple autoimmune disease susceptibility 1, polysubstance abuse, susceptibility to, dyslexia, susceptibility to, 6, glaucoma, normal tension, susceptibility to, anorexia nervosa, susceptibility to, 1, stroke, susceptibility to, 1, dyslexia, susceptibility to, 5, epilepsy, idiopathic generalized, susceptibility to, 2, familial meningioma, celiac disease, susceptibility to, 5, systemic lupus erythematosus with hemolytic anemia, susceptibility to, 1, hypertension, essential, susceptibility to, 3, coronary heart disease, susceptibility to, 1, bulimia nervosa, susceptibility to, 1, leprosy, susceptibility to, 2, epilepsy, idiopathic generalized, susceptibility to, 9, Parkinson disease 11, autosomal dominant, susceptibility to, focal segmental glomerulosclerosis 3, susceptibility to, autoimmune disease, susceptibility to, 1, osteoarthritis susceptibility 3, systemic lupus erythematosus with nephritis, susceptibility to, 1, systemic lupus erythematosus with nephritis, susceptibility to, 2, systemic lupus erythematosus with nephritis, susceptibility to, 3, coronary heart disease, susceptibility to, 2, coronary heart disease, susceptibility to, 4, autoimmune disease, susceptibility to, 2, autoimmune disease, susceptibility to, 3, systemic lupus erythematosus, susceptibility to, 4, major depressive disorder 1, legionnaire disease, susceptibility to, myocardial infarction, susceptibility to, 2, major depressive disorder 2, hypertension, essential, susceptibility to, 4, epilepsy, idiopathic generalized, susceptibility to, 3, myoclonic epilepsy, juvenile, susceptibility to, 3, orofacial cleft 6, susceptibility to, coronary heart disease, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 1, attention deficit-hyperactivity disorder, susceptibility to, 2, attention deficit-hyperactivity disorder, susceptibility to, 3, attention deficit-hyperactivity disorder, susceptibility to, 4, Alzheimer disease 9, susceptibility to respiratory infections associated with CD8alpha chain mutation, dyslexia, susceptibility to, 8, autoimmune disease, susceptibility to, 4, hepatitis C virus, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 4, celiac disease, susceptibility to, 4, celiac disease, susceptibility to, 2, celiac disease, susceptibility to, 3, leprosy, susceptibility to, 1, systemic lupus erythematosus, susceptibility to, 5, systemic lupus erythematosus, susceptibility to, 6, opioid dependence, susceptibility to, 1, systemic lupus erythematosus, susceptibility to, 7, systemic lupus erythematosus, susceptibility to, 8, hypertension, essential, susceptibility to, 5, hypertension, essential, susceptibility to, 6, Parkinson disease 13, autosomal dominant, susceptibility to, West Nile virus, susceptibility to, hepatitis B virus, susceptibility to, Buruli ulcer, susceptibility to, osteoarthritis susceptibility 4, systemic lupus erythematosus, susceptibility to, 9, coronary heart disease, susceptibility to, 7, hypertension, essential, susceptibility to, 7, leprosy, susceptibility to, 4, hypertension, essential, susceptibility to, 8, epilepsy, idiopathic generalized, susceptibility to, 13, coronary heart disease, susceptibility to, 8, myoclonic epilepsy, juvenile, susceptibility to, 4, susceptibility to visceral leishmaniasis, 2, susceptibility to visceral leishmaniasis, 3, celiac disease, susceptibility to, 6, epilepsy, idiopathic generalized, susceptibility to, 5, epilepsy, childhood absence, susceptibility to, 6, celiac disease, susceptibility to, 7, celiac disease, susceptibility to, 8, celiac disease, susceptibility to, 9, celiac disease, susceptibility to, 10, celiac disease, susceptibility to, 11, celiac disease, susceptibility to, 12, celiac disease, susceptibility to, 13, coronary heart disease, susceptibility to, 9, systemic lupus erythematosus, susceptibility to, 10, systemic lupus erythematosus, susceptibility to, 11, systemic lupus erythematosus, susceptibility to, 12, epilepsy, childhood absence, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 6, systemic lupus erythematosus, susceptibility to, 13, sarcoidosis, susceptibility to, 2, sarcoidosis, susceptibility to, 3, osteoarthritis susceptibility 5, osteoarthritis susceptibility 6, focal segmental glomerulosclerosis 4, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 8, herpes simplex encephalitis, susceptibility to, 2, attention deficit-hyperactivity disorder, susceptibility to, 7, epilepsy, idiopathic generalized, susceptibility to, 10, pelvic organ prolapse, susceptibility to, 2, systemic lupus erythematosus, susceptibility to, 14, leprosy, susceptibility to, 5, thyrotoxic periodic paralysis, susceptibility to, 2, hearing loss, cisplatin-induced, susceptibility to, susceptibility to mononeuropathy of the median nerve, mild, fatty liver disease, nonalcoholic, susceptibility to, 2, leprosy, susceptibility to, 6, autoimmune disease, susceptibility to, 6, Parkinson disease 5, autosomal dominant, susceptibility to, aspergillosis, susceptibility to, sick sinus syndrome 3, susceptibility to, Parkinson disease 18, autosomal dominant, susceptibility to, epilepsy, juvenile myoclonic, susceptibility to, 9, dengue virus, susceptibility to, coronary heart disease, susceptibility to, 6, podoconiosis, susceptibility to, peripartum cardiomyopathy, susceptibility to, influenza, severe, susceptibility to, thyrotoxic periodic paralysis, susceptibility to, 3, human herpesvirus 8, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 12, herpes simplex encephalitis, susceptibility to, 3, herpes simplex encephalitis, susceptibility to, 4, pulmonary hypertension, neonatal, susceptibility to, craniosynostosis 5, susceptibility to, melioidosis, susceptibility to, chronic mountain sickness, susceptibility to, herpes simplex encephalitis, susceptibility to, 7, epilepsy, idiopathic generalized, susceptibility to, 14, hereditary neoplastic syndrome, autosomal recessive Mendelian susceptibility to mycobacterial diseases due to partial IFNgammaR1 deficiency, autosomal recessive Mendelian susceptibility to mycobacterial diseases due to partial IFNgammaR2 deficiency, susceptibility to localized juvenile periodontitis, inherited susceptibility to mycobacterial diseases, neural tube defects, susceptibility to, multiple system atrophy 1, susceptibility to, nephrolithiasis susceptibility caused by SLC26A1, myoclonic epilepsy, juvenile, susceptibility to, 1, epilepsy, childhood absence, susceptibility to, 1, autism, susceptiblity to, susceptibility to visceral leishmaniasis, 1, malaria, susceptibility to, spondyloarthropathy, susceptibility to, herpes simplex encephalitis, susceptibility to, 1, epilepsy, idiopathic generalized, susceptibility to, 18, epilepsy, idiopathic generalized, susceptibility to, 15, hepatitis, fulminant viral, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 16, autosomal recessive mendelian susceptibility to mycobacterial diseases due to partial jak1 deficiency, aortic aneurysm, familial thoracic 11, susceptibility to, craniosynostosis 7, amyotrophic lateral sclerosis, susceptibility to, 24, amyotrophic lateral sclerosis, susceptibility to, 25, epilepsy, juvenile myoclonic, susceptibility to, 10, susceptibility to angioedema induced by ACE inhibitors, epidermodysplasia verruciformis, susceptibility to, exfoliation syndrome, susceptibility to, basal cell carcinoma, susceptibility to, graft-versus-host disease, susceptibility to, narcolepsy, susceptibility to, pulmonary disease, chronic obstructive, susceptibility to, restless legs syndrome, susceptibility to, psoriasis, susceptibility to, age related macular degeneration, susceptibility to, allergic rhinitis, susceptibility to, dermatitis, atopic, susceptibility to, Hirschsprung disease, susceptibility to, diabetes mellitus, ketosis-prone, schizophrenia, susceptibility to, radioulnar synostosis, nonsyndromic, susceptibility to, lumbar disk herniation, susceptibility to, lumbar disk degeneration, susceptibility to, psoriatic arthritis, susceptibility to, migraine with or without aura, susceptibility to, Alzheimer disease, susceptibility to, mitochondrial, Asperger syndrome, susceptibility to, tobacco addiction, susceptibility to, lipodystrophy, partial, acquired, susceptibility to, Graves disease, susceptibility to, 1, epilepsy, idiopathic generalized, susceptibility to, 17, breast-ovarian cancer, familial, susceptibility to, blepharospasm, benign essential, susceptibility to, hemorrhage, intracerebral, susceptibility to, IgA nephropathy, susceptibility to, hemolytic uremic syndrome, atypical, susceptibility to, 7, vitiligo-associated multiple autoimmune disease susceptibility 6, delayed sleep phase syndrome, susceptibility to, encephalitis, acute, infection-induced, susceptibility to, malignant hyperthermia, susceptibility to, multicentric Castleman disease, susceptibility to, pelvic organ prolapse, susceptibility to, 1, amyotrophic lateral sclerosis, susceptibility to, 13, Graves disease, susceptibility to, X-linked 2, autoimmune thyroid disease, susceptibility to, 5, atrioventricular septal defect, susceptibility to, 1, epilepsy, juvenile myoclonic, susceptibility to, 6, autoimmune disease, susceptibility to, 5, epilepsy, idiopathic generalized, susceptibility to, 6, seasonal affective disorder, susceptibility to, ventricular fibrillation during myocardial infarction, susceptibility to, UV-induced skin damage, susceptibility to, antisocial behavior, susceptibility to, aplastic anemia, susceptibility to, cardiomyopathy, familial hypertrophic, 4, susceptibility to, cirrhosis, noncryptogenic, susceptibility to, coronary artery disease, severe, susceptibility to, dengue fever, susceptibility to, dengue hemorrhagic fever, susceptibility to, dengue shock syndrome, susceptibility to, dyslexia, susceptibility to, 4, dyslexia, susceptibility to, 7, efavirenz central nervous system toxicity, susceptibility to, obesity, susceptibility to, bleeding disorder, platelet-type, 13, susceptibility to, Schistosoma mansoni infection, susceptibility/resistance to, Parkinson disease 24, autosomal dominant, susceptibility to, iron overload, susceptibility to, hydrocephalus, congenital, 5, susceptibility to, hearing loss, noise-induced, susceptibility to, hyperemesis gravidarum, susceptibility to, Parkinson disease 26, autosomal dominant, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 19, polycystic kidney disease 9, susceptibility to, rhabdomyolysis, susceptibility to, scoliosis, isolated, susceptibility to, dystonia 38, susceptibility to, gallbladder disease 4, epilepsy, juvenile absence, susceptibility to, GBA1-related Parkinson disease, susceptibility, SH2B3-related immune system disorder

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

70 retrieved; paginated sample, class counts are floors:

16 pathogenic, 13 pathogenic/likely pathogenic, 11 uncertain significance, 9 likely pathogenic, 6 risk factor, 5 conflicting classifications of pathogenicity, 4 benign, 3 benign; risk factor, 1 benign/likely benign, 1 pathogenic/likely pathogenic; other, 1 likely benign

ClinVarVariant (HGVS)GeneClassificationReview
13564NM_000212.3(ITGB3):c.2248C>T (p.Arg750Ter)EFCAB13-DTPathogenicreviewed by expert panel
29694NM_000129.4(F13A1):c.603_606del (p.Arg202fs)F13A1Pathogeniccriteria provided, single submitter
3594056NM_000129.4(F13A1):c.523C>T (p.Arg175Ter)F13A1Pathogeniccriteria provided, single submitter
12076NM_019616.4(F7):c.995C>T (p.Ala332Val)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
12085NM_019616.4(F7):c.1099T>G (p.Cys367Gly)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
1677255NM_019616.4(F7):c.868G>A (p.Val290Met)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
1678759NM_019616.4(F7):c.505+78G>AF7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
1684389NM_019616.4(F7):c.517T>C (p.Cys173Arg)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
1691295NM_019616.4(F7):c.225+1G>CF7Pathogeniccriteria provided, multiple submitters, no conflicts
265135NM_019616.4(F7):c.1043G>T (p.Cys348Phe)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
2683442NM_019616.4(F7):c.739+1G>AF7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
3352537NM_019616.4(F7):c.1008G>A (p.Met336Ile)F7Pathogeniccriteria provided, single submitter
3382510NM_019616.4(F7):c.64G>A (p.Val22Ile)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
3575772NM_019616.4(F7):c.1157A>G (p.His386Arg)F7Pathogeniccriteria provided, single submitter
420159NM_019616.4(F7):c.1025G>A (p.Arg342Gln)F7Pathogenic/Likely pathogenic; othercriteria provided, multiple submitters, no conflicts
420160NM_019616.4(F7):c.1085C>T (p.Thr362Met)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
626999NM_019616.4(F7):c.1325del (p.Pro442fs)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
627178NM_019616.4(F7):c.413A>G (p.Gln138Arg)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
627309NM_019616.4(F7):c.364+1G>AF7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
627403NM_019616.4(F7):c.845C>T (p.Ala282Val)F7Pathogenic/Likely pathogeniccriteria provided, multiple submitters, no conflicts
13553NM_000212.3(ITGB3):c.719G>A (p.Arg240Gln)ITGB3Pathogenicreviewed by expert panel
13567NM_000212.3(ITGB3):c.428T>G (p.Leu143Trp)ITGB3Pathogenicreviewed by expert panel
1879043NM_000212.3(ITGB3):c.725G>A (p.Arg242Gln)ITGB3Pathogenicreviewed by expert panel
812736NM_000212.3(ITGB3):c.565C>T (p.Pro189Ser)ITGB3Pathogenicreviewed by expert panel
953028NM_000212.3(ITGB3):c.31T>C (p.Trp11Arg)ITGB3Pathogenicreviewed by expert panel
953050NM_000212.3(ITGB3):c.79+1G>AITGB3Pathogenicreviewed by expert panel
996178NM_000212.3(ITGB3):c.709_710del (p.Ser237fs)ITGB3Pathogenicreviewed by expert panel
996188NM_000212.3(ITGB3):c.431T>G (p.Met144Arg)ITGB3Pathogenicreviewed by expert panel
996193NM_000212.3(ITGB3):c.100C>T (p.Arg34Ter)ITGB3Pathogenicreviewed by expert panel
850886NM_000212.3(ITGB3):c.777+1G>ALOC130061044Pathogenicreviewed by expert panel

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 2 · Orphanet: 12 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

GenCC gene–disease validity (cohort genes)

the Disease column is the GenCC-asserted condition — a cohort gene’s strongest validity may be for a related predisposition syndrome.

GeneClassificationInheritanceDiseaseRecords
TNFSF4LimitedAutosomal dominantmyocardial infarction, susceptibility to2

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
TNFSF4Orphanet:2073Narcolepsy type 1
TNFSF4Orphanet:536Systemic lupus erythematosus
ACEOrphanet:97369Renal tubular dysgenesis of genetic origin
ESR1Orphanet:785Estrogen resistance syndrome
F13A1Orphanet:331Congenital factor XIII deficiency
F7Orphanet:327Congenital factor VII deficiency
GCLCOrphanet:33574Glutamate-cysteine ligase deficiency
GCLCOrphanet:586Cystic fibrosis
APOC3Orphanet:181428Familial Hyperalphalipoproteinemia
ITGB3Orphanet:140957Autosomal dominant macrothrombocytopenia
ITGB3Orphanet:849Glanzmann thrombasthenia
ITGB3Orphanet:853Fetal and neonatal alloimmune thrombocytopenia

Cohort genes → proteins

15 cohort genes, 14 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence15

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
TNFSF4HGNC:11934ENSG00000117586P23510Tumor necrosis factor ligand superfamily member 4gencc
ACEHGNC:2707ENSG00000159640P12821Angiotensin-converting enzymeclinvar
ESR1HGNC:3467ENSG00000091831P03372Estrogen receptorclinvar
F13A1HGNC:3531ENSG00000124491P00488Coagulation factor XIII A chainclinvar
F7HGNC:3544ENSG00000057593P08709Coagulation factor VIIclinvar
GCLCHGNC:4311ENSG00000001084P48506Glutamate–cysteine ligase catalytic subunitclinvar
GCLMHGNC:4312ENSG00000023909P48507Glutamate–cysteine ligase regulatory subunitclinvar
EFCAB13-DTHGNC:55338ENSG00000263293EFCAB13 divergent transcriptclinvar
APOC3HGNC:610ENSG00000110245P02656Apolipoprotein C-IIIclinvar
ITGB3HGNC:6156ENSG00000259207P05106Integrin beta-3clinvar
LGALS2HGNC:6562ENSG00000100079P05162Galectin-2clinvar
LRP8HGNC:6700ENSG00000157193Q14114Low-density lipoprotein receptor-related protein 8clinvar
LTAHGNC:6709ENSG00000226979P01374Lymphotoxin-alphaclinvar
OLR1HGNC:8133ENSG00000173391P78380Oxidized low-density lipoprotein receptor 1clinvar
PSMA6HGNC:9535ENSG00000100902P60900Proteasome subunit alpha type-6clinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
TNFSF4Tumor necrosis factor ligand superfamily member 4Cytokine that binds to TNFRSF4.
ACEAngiotensin-converting enzymeDipeptidyl carboxypeptidase that removes dipeptides from the C-terminus of a variety of circulating hormones, such as angiotensin I, bradykinin or enkephalins, thereby playing a key role in the regulation of blood pressure, electrolyte hom…
ESR1Estrogen receptorNuclear hormone receptor.
F13A1Coagulation factor XIII A chainFactor XIII is activated by thrombin and calcium ion to a transglutaminase that catalyzes the formation of gamma-glutamyl-epsilon-lysine cross-links between fibrin chains, thus stabilizing the fibrin clot.
F7Coagulation factor VIIInitiates the extrinsic pathway of blood coagulation.
GCLCGlutamate–cysteine ligase catalytic subunitCatalyzes the ATP-dependent ligation of L-glutamate and L-cysteine and participates in the first and rate-limiting step in glutathione biosynthesis.
APOC3Apolipoprotein C-IIIComponent of triglyceride-rich very low density lipoproteins (VLDL) and high density lipoproteins (HDL) in plasma.
ITGB3Integrin beta-3Integrin alpha-V/beta-3 (ITGAV:ITGB3) is a receptor for cytotactin, fibronectin, laminin, matrix metalloproteinase-2, osteopontin, osteomodulin, prothrombin, thrombospondin, vitronectin and von Willebrand factor.
LGALS2Galectin-2This protein binds beta-galactoside.
LRP8Low-density lipoprotein receptor-related protein 8Cell surface receptor for Reelin (RELN) and apolipoprotein E (apoE)-containing ligands.
LTALymphotoxin-alphaCytokine that in its homotrimeric form binds to TNFRSF1A/TNFR1, TNFRSF1B/TNFBR and TNFRSF14/HVEM.
OLR1Oxidized low-density lipoprotein receptor 1Receptor that mediates the recognition, internalization and degradation of oxidatively modified low density lipoprotein (oxLDL) by vascular endothelial cells.
PSMA6Proteasome subunit alpha type-6Component of the 20S core proteasome complex involved in the proteolytic degradation of most intracellular proteins.

Protein-family classification

Druggable: 6 · Difficult: 0 · Unknown: 9 · Druggable fraction: 0.4

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Nuclear receptor125.7×0.155
Protease24.9×0.155
Antibody/Immunoglobulin11.9×0.478
Enzyme (other)21.6×0.478
Other/Unknown91.1×0.478

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
TNFSF4Other/UnknownnoTNF_dom, Tumour_necrosis_fac-like_dom, TNF_CS
ACEProteaseyes3.4.15.1Peptidase_M2
ESR1Nuclear receptoryesNucl_hrmn_rcpt_lig-bd, Estr_rcpt, Znf_hrmn_rcpt
F13A1Antibody/Immunoglobulinyes2.3.2.13Transglutaminase_N, Transglutaminase-like, Transglutaminase_C
F7Proteaseyes3.4.21.21EGF-type_Asp/Asn_hydroxyl_site, GLA_domain, EGF
GCLCEnzyme (other)yes6.3.2.2GCS, Gln_synth/guanido_kin_cat_dom
GCLMEnzyme (other)yes6.3.2.2NADP_OxRdtase_dom, Gclm, NAD(P)_OxRdtase_dom_sf
EFCAB13-DTOther/Unknownno
APOC3Other/UnknownnoApo-CIII, Apo_CIII_sf
ITGB3Other/UnknownnoIntegrin_bsu_VWA, Integrin_bsu_tail, EGF_extracell
LGALS2Other/UnknownnoGalectin_CRD, ConA-like_dom_sf, Galectin-like
LRP8Other/UnknownnoLDLR_classB_rpt, EGF-type_Asp/Asn_hydroxyl_site, EGF
LTAOther/UnknownnoTNF_beta, TNF_dom, TNF
OLR1Other/UnknownnoC-type_lectin-like, C-type_lectin-like/link_sf, CTDL_fold
PSMA6Other/UnknownnoProteasome_asu_N, Proteasome_sua/b, Proteasome_alpha-type

Expression context

Cohort genes with no expression data: 0.

12 cohort genes are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)15
unknown0

Top tissues across cohort

TissueCohort genes
monocyte4
mononuclear cell4
primordial germ cell in gonad2
left testis2
right testis2
liver2
right lobe of liver2
bronchial epithelial cell2
islet of Langerhans2
male germ line stem cell (sensu Vertebrata) in testis2
ileal mucosa1
cervix epithelium1
mammalian vulva1
oviduct epithelium1
pericardium1
buccal mucosa cell1
olfactory segment of nasal mucosa1
right uterine tube1
epithelium of bronchus1
right lobe of thyroid gland1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
TNFSF4181broadmarkerprimordial germ cell in gonad, monocyte, mononuclear cell
ACE177ubiquitousmarkerileal mucosa, right testis, left testis
ESR1216broadmarkeroviduct epithelium, cervix epithelium, mammalian vulva
F13A1261broadmarkermonocyte, mononuclear cell, pericardium
F7156tissue_specificyesright lobe of liver, liver, buccal mucosa cell
GCLC291ubiquitousmarkerbronchial epithelial cell, right uterine tube, olfactory segment of nasal mucosa
GCLM284ubiquitousmarkerbronchial epithelial cell, islet of Langerhans, epithelium of bronchus
EFCAB13-DT155tissue_specificyesmale germ line stem cell (sensu Vertebrata) in testis, primordial germ cell in gonad, right lobe of thyroid gland
APOC3156tissue_specificmarkerjejunal mucosa, right lobe of liver, liver
ITGB3199ubiquitousmarkermonocyte, mononuclear cell, leukocyte
LGALS2197broadmarkergall bladder, monocyte, mononuclear cell
LRP8246ubiquitousyesganglionic eminence, pigmented layer of retina, cortical plate
LTA119broadmarkermale germ line stem cell (sensu Vertebrata) in testis, granulocyte, lymph node
OLR1202broadmarkerright lung, C1 segment of cervical spinal cord, bone marrow cell
PSMA6137ubiquitousmarkerleft testis, right testis, islet of Langerhans

Protein interactions among cohort

Intra-cohort edges: 2.

Hub genes (top 10 by interactor count)

SymbolInteractor count
ESR112,382
ACE3,659
ITGB33,274
F13A12,346
GCLM2,137
GCLC1,928
APOC31,895
LTA1,807
OLR11,742
LRP81,682

Intra-cohort edges

ABSources
GCLCGCLMbiogrid_interaction, intact, string_interaction
LGALS2LTAbiogrid_interaction, intact, string_interaction

Structural data

PDB: 12 · AlphaFold-only: 2 · No structure: 1

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
ESR1P03372478
PSMA6P60900171
ITGB3P05106123
F7P08709114
ACEP1282197
F13A1P0048815
OLR1P7838013
LGALS2P051624
LRP8Q141144
LTAP013743
TNFSF4P235101
APOC3P026561

AlphaFold-only cohort genes (top 30 by pLDDT)

SymbolUniProtpLDDT
GCLCP4850693.68
GCLMP4850791.24

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 164. Enrichment computed across 15 evidence-associated genes (13 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 13 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Defective GCLC causes HAGGSD2878.5×2e-04GCLC, GCLM
Glutathione synthesis and recycling2146.4×0.005GCLC, GCLM
Fibrin formation2135.2×0.005F13A1, ITGB3
NFE2L2 regulating anti-oxidant/detoxification enzymes283.7×0.010GCLC, GCLM
TNFs bind their physiological receptors260.6×0.014TNFSF4, LTA
Metabolism of fat-soluble vitamins258.6×0.014APOC3, LRP8
Visual phototransduction239.9×0.025APOC3, LRP8
Retinoid metabolism and transport238.2×0.025APOC3, LRP8
TNFR2 non-canonical NF-kB pathway227.9×0.037LTA, PSMA6
Regulation of RUNX2 expression and activity227.9×0.037ESR1, PSMA6
Metabolism of vitamins and cofactors217.9×0.080APOC3, LRP8
RUNX1 regulates estrogen receptor mediated transcription1146.4×0.084ESR1
RUNX1 regulates transcription of genes involved in WNT signaling1146.4×0.084ESR1
Transport of gamma-carboxylated protein precursors from the endoplasmic reticulum to the Golgi apparatus197.6×0.084F7
Gamma-carboxylation of protein precursors187.8×0.084F7
Removal of aminoterminal propeptides from gamma-carboxylated proteins187.8×0.084F7
Chylomicron assembly187.8×0.084APOC3
Chylomicron remodeling187.8×0.084APOC3
HDL remodeling187.8×0.084APOC3
Cell surface interactions at the vascular wall214.6×0.084ITGB3, OLR1
Sensory Perception214.6×0.084APOC3, LRP8
Platelet degranulation213.5×0.084F13A1, ITGB3
PECAM1 interactions167.6×0.103ITGB3
p130Cas linkage to MAPK signaling for integrins158.6×0.103ITGB3
TFAP2 (AP-2) family regulates transcription of growth factors and their receptors158.6×0.103ESR1
GRB2:SOS provides linkage to MAPK signaling for Integrins154.9×0.103ITGB3
Plasma lipoprotein assembly154.9×0.103APOC3
Platelet sensitization by LDL151.7×0.103LRP8
TNF receptor superfamily (TNFSF) members mediating non-canonical NF-kB pathway151.7×0.103LTA
Mechanical load activates signaling by PIEZO1 and integrins in osteocytes151.7×0.103ITGB3

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 14 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
response to human chorionic gonadotropin21203.7×9e-05GCLC, GCLM
cellular response to thyroxine stimulus21203.7×9e-05GCLC, GCLM
blood vessel diameter maintenance3133.8×1e-04ACE, GCLC, GCLM
obsolete cysteine metabolic process2601.9×2e-04GCLC, GCLM
response to nitrosative stress2601.9×2e-04GCLC, GCLM
regulation of mitochondrial depolarization2401.2×4e-04GCLC, GCLM
response to activity369.5×4e-04GCLC, GCLM, ITGB3
response to nutrient363.4×5e-04GCLC, GCLM, LTA
blood coagulation, fibrin clot formation2240.7×9e-04F13A1, ITGB3
glutathione biosynthetic process2218.9×9e-04GCLC, GCLM
negative regulation of low-density lipoprotein particle clearance2218.9×9e-04APOC3, ITGB3
response to xenobiotic stimulus419.7×9e-04GCLC, GCLM, LRP8, LTA
cellular response to follicle-stimulating hormone stimulus2200.6×9e-04GCLC, GCLM
glutamate metabolic process2160.5×0.001GCLC, GCLM
cellular response to hepatocyte growth factor stimulus2160.5×0.001GCLC, GCLM
blood coagulation337.2×0.001F13A1, F7, ITGB3
regulation of inflammatory response336.1×0.001TNFSF4, ESR1, PSMA6
lipoprotein metabolic process2133.8×0.002APOC3, OLR1
cellular response to fibroblast growth factor stimulus277.7×0.005GCLC, GCLM
response to carbon dioxide11203.7×0.007F7
negative regulation of high-density lipoprotein particle clearance11203.7×0.007APOC3
ammon gyrus development11203.7×0.007LRP8
mononuclear cell proliferation11203.7×0.007ACE
T-helper 2 cell activation11203.7×0.007TNFSF4
response to nitrogen dioxide11203.7×0.007TNFSF4
regulation of serotonin uptake11203.7×0.007ITGB3
positive regulation of CD4-positive, alpha-beta T cell costimulation11203.7×0.007TNFSF4
positive regulation of adenylate cyclase-inhibiting opioid receptor signaling pathway11203.7×0.007ITGB3
regulation of epithelial cell apoptotic process11203.7×0.007ESR1
response to Thyroid stimulating hormone11203.7×0.007F7

Therapeutics

Drug target analysis

Approved (phase 4): 5 · Phase ≥3: 6 · Phased (≥1): 7 · Undrugged: 8

Druggability breadth: 13 of 15 evidence-associated genes (87%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Genes with an approved drug

The molecule shown is one approved compound that hits the gene — not necessarily a drug of choice or one indicated for this disease.

SymbolExample approved molecule
ACETELMISARTAN
ESR1CANDESARTAN CILEXETIL
F7NIACINAMIDE
ITGB3EPTIFIBATIDE
PSMA6BORTEZOMIB

Top cohort targets by molecule count

SymbolMoleculesMax phase
ESR11624
ACE314
ITGB3184
F784
PSMA664
F13A113
GCLC11
TNFSF400
GCLM00
EFCAB13-DT00

Drugs targeting cohort genes (top 30)

MoleculeMax phaseTargets in cohort
TELMISARTAN4ACE
MOEXIPRIL4ACE
RAMIPRIL4ACE
LISINOPRIL ANHYDROUS4ACE
SITAGLIPTIN4ACE
TRANDOLAPRIL4ACE
CAPTOPRIL4ACE
PERINDOPRIL4ACE
QUINAPRIL4ACE
LOSARTAN4ACE
FOSINOPRIL4ACE
IMIDAPRIL4ACE
ENALAPRILAT ANHYDROUS4ACE
ENALAPRIL4ACE
BENAZEPRIL4ACE
CANDESARTAN CILEXETIL4ESR1
DIENESTROL4ESR1
BEXAROTENE4ESR1
VARENICLINE4ESR1
ACETOPHENAZINE4ESR1
ARIPIPRAZOLE4ESR1
RALOXIFENE HYDROCHLORIDE4ESR1
NORETHINDRONE4ESR1
TRIMETREXATE4ESR1
ESTRADIOL ACETATE4ESR1
ETHYLESTRENOL4ESR1
ETHYNODIOL DIACETATE4ESR1
CHLOROTRIANISENE4ESR1
ESTRADIOL CYPIONATE4ESR1
MESTRANOL4ESR1

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 5.

Cohort genes with ChEMBL bioactivity (full, sorted by assay count)

SymbolAssaysType breakdown
ESR12,435Binding:2037, Functional:363, ADMET:35
ITGB3771Binding:575, Functional:183, ADMET:13
ACE304Binding:288, Functional:8, ADMET:5, Unclassified:3
F7255Binding:237, Functional:17, ADMET:1
PSMA6175Binding:166, ADMET:6, Functional:3
F13A142Binding:42
GCLC14Binding:14
LGALS212Binding:12
GCLM3Binding:3
LTA3Binding:3
OLR12Binding:2
APOC31Binding:1

Cohort enzymes (BRENDA EC)

SymbolEC numbersNames
ACE3.4.15.1peptidyl-dipeptidase A
F13A12.3.2.13protein-glutamine gamma-glutamyltransferase
F73.4.21.21coagulation factor VIIa
GCLC6.3.2.2glutamate-cysteine ligase
GCLM6.3.2.2glutamate-cysteine ligase

Cohort genes with high screening signal

≥100 ChEMBL assays — a studied-ness signal; see Therapeutics for approved-drug status.

SymbolChEMBL assays
ACE304
ESR12,435
F7255
ITGB3771
PSMA6175

Pharmacogenomics

Cohort genes with a PharmGKB record: 14; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

30 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

CompoundMax phaseCohort target (bioactivity)
TELMISARTAN4ACE
MOEXIPRIL4ACE
RAMIPRIL4ACE
LISINOPRIL ANHYDROUS4ACE
SITAGLIPTIN4ACE
TRANDOLAPRIL4ACE
CAPTOPRIL4ACE
PERINDOPRIL4ACE
QUINAPRIL4ACE
LOSARTAN4ACE
FOSINOPRIL4ACE
IMIDAPRIL4ACE
ENALAPRILAT ANHYDROUS4ACE
ENALAPRIL4ACE
BENAZEPRIL4ACE
CANDESARTAN CILEXETIL4ESR1
DIENESTROL4ESR1
BEXAROTENE4ESR1
VARENICLINE4ESR1
ACETOPHENAZINE4ESR1
ARIPIPRAZOLE4ESR1
RALOXIFENE HYDROCHLORIDE4ESR1
NORETHINDRONE4ESR1
TRIMETREXATE4ESR1
ESTRADIOL ACETATE4ESR1
ETHYLESTRENOL4ESR1
ETHYNODIOL DIACETATE4ESR1
CHLOROTRIANISENE4ESR1
ESTRADIOL CYPIONATE4ESR1
MESTRANOL4ESR1

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)5ACE, ESR1, F7, ITGB3, PSMA6
BPhased (≥1) drug, not yet approved2F13A1, GCLC
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug1GCLM
EDifficult family or no structure, no drug7TNFSF4, EFCAB13-DT, APOC3, LGALS2, LRP8, LTA, OLR1

Undrugged target profiles

8 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
GCLM3GCLC
TNFSF40
EFCAB13-DT0
APOC31
LGALS212
LRP80
LTA3
OLR12

Clinical trials & evidence

Clinical trials

Clinical trials: 0.