Nodular goiter

disease
On this page

Also known as goiter, nodularnodular goiter (disease)nodular goitre (disease)nodular goitre NOS

Summary

Nodular goiter (MONDO:0006869) is a disease with 239 GWAS associations across 14 studies and 12 clinical trials. Top therapeutic interventions include remifentanil and iodide. A subtype of goiter — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • GWAS associations: 239
  • Clinical trials: 12

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namenodular goiter
Mondo IDMONDO:0006869
EFOEFO:1001062
MeSHD006044
DOIDDOID:13197
NCITC131437
SNOMED CT419153005
UMLSC0018023
MedGen42271
MedDRA10018495
Is cancer (heuristic)no

Also known as: goiter, nodular · nodular goiter · nodular goiter (disease) · nodular goitre (disease) · nodular goitre NOS

Data availability: 239 GWAS associations (14 studies) · 1 HPO phenotype.

Disease family

This is a subtype of goiter. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by body system or component › endocrine system disorderthyroid gland disordergoiternodular goiter

Related subtypes (6): toxic diffuse goiter, dyshormonogenic goiter, nontoxic goiter, endemic goiter, lingual goiter, substernal goiter

Subtypes (1): multinodular goiter

Genetics & variants

GWAS landscape

239 GWAS associations across 14 studies. Top hits map to 28 distinct genes (as reported by GWAS).

Top associations by p-value

rsIDp-valueGeneRisk alleleOdds ratio
rs15619626e-292PTCSC2T0.42
rs174779234e-279FAM227BC0.24
rs9254882e-269PTCSC2A0.44
rs10072022e-159LNCNEF - LINC01747G0.18
rs12039461e-146LNCNEF - LINC01747C0.21
rs574814452e-139DIRC3G0.24
rs124612061e-117INSRC0.17
rs24393041e-112NRG1G0.17
rs587221864e-104MAFTRR, LINC01229T0.14
rs124315029e-104ITPK1A0.17
rs109174697e-101MICOS10G0.16
rs21834517e-99LINC00609G0.15
rs796768424e-97TGT0.43
rs1169093742e-93LINC00609 - MBIPT0.35
rs121010807e-89ITPK1T0.18
rs125891241e-83LINC00609A0.18
rs37587233e-82PRDM11C0.13
rs3346998e-81NFIAG0.23
rs110383571e-76PRDM11A0.14
rs667603201e-66SCIRTT0.12
rs45789732e-66LINC00887T0.14
rs99717704e-63MSRB3-AS1C0.24
rs107998244e-58MICOS10A0.15
rs6757633e-48LINC02869G0.09
rs16907898e-48LINC02869T0.1
rs1426988379e-48TGA1.06
rs77252183e-44TERTA0.11
rs132950815e-44PTCSC2C0.11
rs92964221e-42SCIRT, LINC01512C0.11
rs784550891e-41EPB41L4AA0.22

Top studies (by case count)

StudyLead authorYearCasesControlsTitle
GCST90627740White SL202650,6031,756,950Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627765White SL202645,3621,686,534Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627737White SL20269,845198,496Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627758White SL20268,2530Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627773White SL20267,0710Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627738White SL20264,102115,168Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627739White SL20262,145262,896Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627757White SL20266410Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627756White SL20264510Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.
GCST90627741White SL202600Global multi-ancestry genome-wide analyses identify genes and biological pathways associated with thyroid cancer and benign thyroid diseases.

Variant details and genetic-evidence tiers

Tier distribution (top 50 variants)

TierVariants
Tier 1: coding1
Tier 2: splice/UTR0
Tier 3: regulatory1
Tier 4: intronic/intergenic48

MAF distribution

BucketVariants
common (>=0.05)47
low_freq (0.01-0.05)2
rare (<0.01)1
unknown0

Functional consequences

ConsequenceCount
intron_variant40
intergenic_variant5
non_coding_transcript_exon_variant3
missense_variant1
TF_binding_site_variant1

Top variants

rsIDChrPosAllelesMAFConsequenceGenep-valueTier
rs1561962997783937C>G,T0.322intron_variantPTCSC26e-292Tier 4: intronic/intergenic
rs174779231549418988T>C0.24intron_variantFAM227B4e-279Tier 4: intronic/intergenic
rs925488997784109G>A0.349intron_variantPTCSC22e-269Tier 4: intronic/intergenic
rs10072022022608882T>A,C,G0.253intergenic_variantLNCNEF - LINC017472e-159Tier 4: intronic/intergenic
rs12039462022620340A>C0.228intergenic_variantLNCNEF - LINC017471e-146Tier 4: intronic/intergenic
rs574814452217431651A>G0.297intron_variantDIRC32e-139Tier 4: intronic/intergenic
rs12461206197235439A>C,T0.228intron_variantINSR1e-117Tier 4: intronic/intergenic
rs2439304832572853A>G,T0.473intron_variantNRG11e-112Tier 4: intronic/intergenic
rs587221861679717694C>A,T0.292intron_variantMAFTRR, LINC012294e-104Tier 4: intronic/intergenic
rs124315021493097919G>A0.175intron_variantITPK19e-104Tier 4: intronic/intergenic
rs10917469119517082A>G,T0.162intron_variantMICOS107e-101Tier 4: intronic/intergenic
rs21834511436095227T>G0.499intron_variantLINC006097e-99Tier 4: intronic/intergenic
rs796768428132871660G>A,T0.02intron_variantTG4e-97Tier 4: intronic/intergenic
rs1169093741436269155C>T0.029non_coding_transcript_exon_variantLINC00609 - MBIP2e-93Tier 4: intronic/intergenic
rs121010801493096510C>T0.2intron_variantITPK17e-89Tier 4: intronic/intergenic
rs125891241436094718G>A0.432intron_variantLINC006091e-83Tier 4: intronic/intergenic
rs37587231145221961T>C0.26intron_variantPRDM113e-82Tier 4: intronic/intergenic
rs334699161154824A>C,G,T0.067intron_variantNFIA8e-81Tier 4: intronic/intergenic
rs110383571145216307T>A,C,G0.282intron_variantPRDM111e-76Tier 4: intronic/intergenic
rs66760320643938518C>T0.264intron_variantSCIRT1e-66Tier 4: intronic/intergenic
rs45789733194200845C>T0.214non_coding_transcript_exon_variantLINC008872e-66Tier 4: intronic/intergenic
rs99717701265639270G>A,C,T0.159intron_variantMSRB3-AS14e-63Tier 4: intronic/intergenic
rs10799824119514680G>A0.148intron_variantMICOS104e-58Tier 4: intronic/intergenic
rs6757631218508777A>C,G,T0.39intron_variantLINC028693e-48Tier 4: intronic/intergenic
rs16907891218524685C>A,T0.481intron_variantLINC028698e-48Tier 4: intronic/intergenic
rs1426988378132869781G>A0.001missense_variantTG9e-48Tier 1: coding
rs772521851282299G>A,T0.373intron_variantTERT3e-44Tier 4: intronic/intergenic
rs13295081997796729T>A,C0.337intron_variantPTCSC25e-44Tier 4: intronic/intergenic
rs9296422643938079G>A,C0.24non_coding_transcript_exon_variantSCIRT, LINC015121e-42Tier 4: intronic/intergenic
rs784550895112143173C>A0.116TF_binding_site_variantEPB41L4A1e-41Tier 3: regulatory

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

Drugs indicated for this disease

No approved or late-stage (phase ≥3) drug is indicated for this disease; the following are in earlier-phase trials only.

Earlier-phase candidates (phase 2, investigational — efficacy not yet established): Thyrotropin Alfa.

Clinical trials & evidence

Clinical trials

Clinical trials: 12.

Phase distribution (across all retrieved trials)

PhaseTrials
Not specified9
PHASE42
PHASE21

Top trials by phase / activity

NCTPhaseStatusTitle
NCT00277589PHASE4COMPLETEDLISA-study : Levothyroxin in Nodular Goiter
NCT01761149PHASE4UNKNOWNEffect of Higher Doses of Remifentanil on Postoperative Pain in Patients Undergoing Thyroidectomy
NCT00275171PHASE2COMPLETEDrhTSH, Radioiodine Uptake and Goiter Reduction Following 131I Therapy in Patients With Benign Nontoxic Nodular Goiter
NCT06537141Not specifiedNOT_YET_RECRUITINGRole of Embolization of Thyroid Arteries as a Treatment for Different Thyroid Disorders
NCT07258199Not specifiedENROLLING_BY_INVITATIONTACE Treats Nodular Goiter
NCT00615537Not specifiedCOMPLETEDPilot Study on Laser Ablation of Symptomatic Benign Thyroid Masses
NCT01102127Not specifiedCOMPLETEDElastography in Thyroid Nodules
NCT01588288Not specifiedCOMPLETEDGalectin 3 Dosage in Diagnosis of Nodular and Multinodular Goiter
NCT02205801Not specifiedCOMPLETEDStudy of the Efficacy of Local Analgesia as an Adjunct to General Anesthesia in Thyroidectomy and Parathyroidectomy
NCT03072654Not specifiedCOMPLETEDTracheal Anatomy After Thyroidectomy
NCT06067594Not specifiedCOMPLETEDCalcitonin in Needle Wash Using Electrochemiluminescence Method For Diagnosis Of Medullary Thyroid Carcinoma.
NCT06924242Not specifiedCOMPLETEDThyroid Cancer in Surgical Treated Multinodular Goiter

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
REMIFENTANIL41
IODIDE-11