Paroxysmal cold hemoglobinuria

disease
On this page

Also known as Donath-Landsteiner hemolytic anaemiaDonath-Landsteiner hemolytic anemiaDonath-Landsteiner syndromehemoglobinuria paroxysmal coldPCH

Summary

Paroxysmal cold hemoglobinuria (MONDO:0019533) is a disease. A subtype of autoimmune hemolytic anemia, cold type — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • Prevalence: 1-9 / 1 000 000 (Europe)
  • Phenotypes (HPO): 11

Clinical features

Epidemiology

Prevalence records

1 prevalence record(s), Orphanet:

TypeClassValueGeographyValidation
Point prevalence1-9 / 1 000 000EuropeNot yet validated

Signs & symptoms

Clinical features (HPO)

11 HPO clinical features (Orphanet curated; top 11 by frequency):

HPO IDTermFrequency
HP:0001890Autoimmune hemolytic anemiaVery frequent (80-99%)
HP:0001945FeverVery frequent (80-99%)
HP:0002205Recurrent respiratory infectionsVery frequent (80-99%)
HP:0002315HeadacheVery frequent (80-99%)
HP:0002829ArthralgiaVery frequent (80-99%)
HP:0003418Back painVery frequent (80-99%)
HP:0003641HemoglobinuriaVery frequent (80-99%)
HP:0004844Coombs-positive hemolytic anemiaVery frequent (80-99%)
HP:0012086Abnormal urinary colorVery frequent (80-99%)
HP:0002014DiarrheaOccasional (5-29%)
HP:0002017Nausea and vomitingOccasional (5-29%)

Identifiers

Disease identifiers

FieldValue
Canonical nameparoxysmal cold hemoglobinuria
Mondo IDMONDO:0019533
Orphanet90035
ICD-11715111132
SNOMED CT127057004
UMLSC0086774
MedGen39693
GARD0007335
NORD1556
Is cancer (heuristic)no

Also known as: Donath-Landsteiner hemolytic anaemia · Donath-Landsteiner hemolytic anemia · Donath-Landsteiner syndrome · hemoglobinuria paroxysmal cold · PCH

Disease family

This is a subtype of autoimmune hemolytic anemia, cold type. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by body system or component › hematologic disorderautoimmune disorder of bloodautoimmune hemolytic anemiaautoimmune hemolytic anemia, cold typeparoxysmal cold hemoglobinuria

Related subtypes (1): cold agglutinin disease

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

No tiered GWAS variants or ClinVar records for this disease.

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

No druggable-target or therapeutic data for this disease’s cohort.

Clinical trials & evidence

Clinical trials

Clinical trials: 0.

No linked Atlas pages yet — the cross-entity mesh grows as the corpus expands.