Potassium deficiency disease

disease
On this page

Also known as hypokalemia

Summary

Potassium deficiency disease (MONDO:0003019) is a disease with 19 GWAS associations across 6 studies and 17 clinical trials. Top therapeutic interventions include hydrochlorothiazide, potassium chloride, and potassium. A subtype of mineral metabolism disease — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • GWAS associations: 19
  • Clinical trials: 17

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namepotassium deficiency disease
Mondo IDMONDO:0003019
MeSHD007008
DOIDDOID:4500
ICD-10-CME87.6
NCITC34939
SNOMED CT43339004
UMLSC1514284
MedGen271346
Is cancer (heuristic)no

Also known as: hypokalemia

Data availability: 19 GWAS associations (6 studies) · 1 HPO phenotype.

Disease family

This is a subtype of mineral metabolism disease. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by developmental or physiological process › metabolic diseasemineral metabolism diseasepotassium deficiency disease

Related subtypes (12): iron metabolism disease, phosphorus metabolism disease, calcium metabolic disease, spondyloepiphyseal dysplasia with congenital joint dislocations, diastrophic dysplasia, multiple epiphyseal dysplasia type 4, atelosteogenesis type II, achondrogenesis type IB, chondrodysplasia with joint dislocations, gPAPP type, spondyloepimetaphyseal dysplasia, PAPSS2 type, acquired mineral metabolism disease, sulfur metabolism disease

Subtypes (1): hypokalemic periodic paralysis

Genetics & variants

GWAS landscape

19 GWAS associations across 6 studies. Top hits map to 9 distinct genes (as reported by GWAS).

Top associations by p-value

rsIDp-valueGeneRisk alleleOdds ratio
rs65636243e-32B3GLCT - RXFP2T0.1
chr13:321797333e-27G0.1
rs8803156e-20CASZ1T0.08
rs607725262e-19HOTTIPC0.12
rs5695506e-18LSP1T0.08
rs49803792e-16LSP1C0.08
rs49180602e-14SH3PXD2AC0.09
rs26438263e-14RNU1-96P - Y_RNAC0.07
rs350214744e-14KCNK3C0.07
rs108571479e-13PRDM8 - FGF5A0.07
chr7:273223522e-12T0.17
rs801766688e-12TARIDA0.18
rs77267952e-11FBN2T0.06
rs170386483e-11LEF1C0.28
rs10324668e-07ATL1?

Top studies (by case count)

StudyLead authorYearCasesControlsTitle
GCST90475755Verma A202423,659402,078Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90475754Verma A202410,895101,696Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90479944Verma A202410,895101,696Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90477411Verma A20242,76353,922Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90652206Liu TY20252,531219,134Diversity and longitudinal records: Genetic architecture of disease associations and polygenic risk in the Taiwanese Han population.
GCST90435774Zhou W20181,430401,506Efficiently controlling for case-control imbalance and sample relatedness in large-scale genetic association studies.

Variant details and genetic-evidence tiers

Tier distribution (top 50 variants)

TierVariants
Tier 1: coding0
Tier 2: splice/UTR0
Tier 3: regulatory1
Tier 4: intronic/intergenic14

MAF distribution

BucketVariants
common (>=0.05)14
low_freq (0.01-0.05)1
rare (<0.01)0
unknown0

Functional consequences

ConsequenceCount
intron_variant9
intergenic_variant2
unknown2
non_coding_transcript_exon_variant1
regulatory_region_variant1

Top variants

rsIDChrPosAllelesMAFConsequenceGenep-valueTier
rs65636241331619754T>A,C,G0.447intergenic_variantB3GLCT - RXFP23e-32Tier 4: intronic/intergenic
chr13:321797330.4423e-27Tier 4: intronic/intergenic
rs880315110736809T>C,G0.325intron_variantCASZ16e-20Tier 4: intronic/intergenic
rs60772526727206377C>G,T0.123non_coding_transcript_exon_variantHOTTIP2e-19Tier 4: intronic/intergenic
rs569550111865838T>G0.361intron_variantLSP16e-18Tier 4: intronic/intergenic
rs4980379111867384C>A,T0.363intron_variantLSP12e-16Tier 4: intronic/intergenic
rs491806010103846529C>A,G,T0.106intron_variantSH3PXD2A2e-14Tier 4: intronic/intergenic
rs2643826327521497C>T0.471regulatory_region_variantRNU1-96P - Y_RNA3e-14Tier 3: regulatory
rs35021474226693976C>G,T0.459intron_variantKCNK34e-14Tier 4: intronic/intergenic
rs10857147480259918A>T0.249intergenic_variantPRDM8 - FGF59e-13Tier 4: intronic/intergenic
chr7:273223520.052e-12Tier 4: intronic/intergenic
rs801766686133748827A>G0.103intron_variantTARID8e-12Tier 4: intronic/intergenic
rs77267955128529392T>A,C0.366intron_variantFBN22e-11Tier 4: intronic/intergenic
rs170386484108140367C>T0.032intron_variantLEF13e-11Tier 4: intronic/intergenic
rs10324661450607743A>C,G0.05intron_variantATL18e-07Tier 4: intronic/intergenic

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

No druggable-target or therapeutic data for this disease’s cohort.

Clinical trials & evidence

Clinical trials

Clinical trials: 17.

Phase distribution (across all retrieved trials)

PhaseTrials
PHASE48
Not specified8
PHASE1/PHASE21

Top trials by phase / activity

NCTPhaseStatusTitle
NCT03833089PHASE4ACTIVE_NOT_RECRUITINGTargeted Potassium Levels for Prevention of ICD Therapy
NCT06736184PHASE4NOT_YET_RECRUITINGthe Cardioprotective Effects of Improving Potassium Variability in Maintenance Hemodialysis Patients
NCT00605202PHASE4COMPLETEDEffect of Licorice and Hydrochlorothiazide on Plasma Potassium
NCT00718068PHASE4COMPLETEDSafety of Continuous Potassium Chloride Infusion in Critical Care
NCT02015962PHASE4UNKNOWNComparison of Enteral Versus Intravenous Potassium Supplementation
NCT02082717PHASE4TERMINATEDThe Impact of Neut During Potassium Chloride Replacement on Pain and Incidence of Phlebitis
NCT02721095PHASE4UNKNOWNEfficacy of KCl Plus 0.9%NaCl Compare With KCl Plus 0.45%NaCl
NCT02926989PHASE4COMPLETEDIntravenous Fluids in Hospitalised Children
NCT02709031PHASE1/PHASE2UNKNOWNCicletanine in Hypertension With Diabetes: Added Magnesium Preserves Potassium and Sodium
NCT04278404Not specifiedRECRUITINGPharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)
NCT06569589Not specifiedRECRUITINGTissue Sodium Quantification in Patients With Primary Aldosteronism: See Sodium to Treat
NCT01431326Not specifiedCOMPLETEDPharmacokinetics of Understudied Drugs Administered to Children Per Standard of Care
NCT01572454Not specifiedCOMPLETEDComparison of Dexmedetomidine and Remifentanil Infusion During CABG
NCT04426994Not specifiedCOMPLETEDHypomagnesemia Associated With Proton-Pump Inhibitor Use
NCT04428827Not specifiedUNKNOWNOutcome of Patients With Primary Aldosteronism
NCT05118022Not specifiedCOMPLETEDArtificial Intelligence Identified Dyskalemia Using Electrocardiogram (AIDE)
NCT05184998Not specifiedCOMPLETEDDescription of the Clinical Outcomes of Hospitalized Patients With Heart Failure With Different Serum Potassium Levels

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
HYDROCHLOROTHIAZIDE41
POTASSIUM CHLORIDE41
POTASSIUM32
BLOOD, WHOLE31
LICORICE31
MAGNESIUM31
CICLETANINE21