Pulmonary hemosiderosis

disease
On this page

Also known as alveolar hypoventilation syndromeIdiopathic Pulmonary Hemosiderosispulmonary siderosis

Summary

Pulmonary hemosiderosis (MONDO:0008346) is a disease and 2 clinical trials. Top therapeutic interventions include leflunomide. A subtype of hemosiderosis — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • Prevalence: <1 / 1 000 000 (Europe) [Orphanet-validated]
  • Phenotypes (HPO): 29
  • Clinical trials: 2

Clinical features

Epidemiology

Prevalence records

1 prevalence record(s), Orphanet:

TypeClassValueGeographyValidation
Annual incidence<1 / 1 000 0000.0425EuropeValidated

Signs & symptoms

Clinical features (HPO)

29 HPO clinical features (Orphanet curated; top 29 by frequency):

HPO IDTermFrequency
HP:0001891Iron deficiency anemiaVery frequent (80-99%)
HP:0000980PallorFrequent (30-79%)
HP:0001433HepatosplenomegalyFrequent (30-79%)
HP:0002105HemoptysisFrequent (30-79%)
HP:0002113Pulmonary infiltratesFrequent (30-79%)
HP:0012378FatigueFrequent (30-79%)
HP:0012735CoughFrequent (30-79%)
HP:0025179Ground-glass opacification on pulmonary HRCTFrequent (30-79%)
HP:0001508Failure to thriveOccasional (5-29%)
HP:0001640CardiomegalyOccasional (5-29%)
HP:0001945FeverOccasional (5-29%)
HP:0002091Restrictive ventilatory defectOccasional (5-29%)
HP:0002094DyspneaOccasional (5-29%)
HP:0002206Pulmonary fibrosisOccasional (5-29%)
HP:0002240HepatomegalyOccasional (5-29%)
HP:0002878Respiratory failureOccasional (5-29%)
HP:0002923Rheumatoid factor positiveOccasional (5-29%)
HP:0003262Smooth muscle antibody positivityOccasional (5-29%)
HP:0003453Antineutrophil antibody positivityOccasional (5-29%)
HP:0003493Antinuclear antibody positivityOccasional (5-29%)
HP:0012393AllergyOccasional (5-29%)
HP:0025390Reticular pattern on pulmonary HRCTOccasional (5-29%)
HP:0025392Nodular pattern on pulmonary HRCTOccasional (5-29%)
HP:0025420Diffuse alveolar hemorrhageOccasional (5-29%)
HP:0030057Autoimmune antibody positivityOccasional (5-29%)
HP:0030148Heart murmurOccasional (5-29%)
HP:0030830CracklesOccasional (5-29%)
HP:0000099GlomerulonephritisVery rare (<1-4%)
HP:0100327Cow milk allergyVery rare (<1-4%)

Identifiers

Disease identifiers

FieldValue
Canonical namepulmonary hemosiderosis
Mondo IDMONDO:0008346
MeSHD012806
OMIM178550
Orphanet99931
DOIDDOID:10328, DOID:12118
ICD-10-CMJ84.03
ICD-111542272036
SNOMED CT40527005
UMLSC0020807
MedGen9403
GARD0006763
NORD91174
Is cancer (heuristic)no

Also known as: alveolar hypoventilation syndrome · Idiopathic Pulmonary Hemosiderosis · idiopathic pulmonary hemosiderosis · pulmonary hemosiderosis · pulmonary siderosis

Disease family

This is a subtype of hemosiderosis. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by developmental or physiological process › metabolic diseasemineral metabolism diseaseiron metabolism diseasehemosiderosispulmonary hemosiderosis

Related subtypes (2): ocular siderosis, hereditary hemochromatosis

Subtypes (2): hemosiderosis, pulmonary, with deficiency of gamma-a globulin, Lane Hamilton syndrome

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

No tiered GWAS variants or ClinVar records for this disease.

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

No druggable-target or therapeutic data for this disease’s cohort.

Clinical trials & evidence

Clinical trials

Clinical trials: 2.

Phase distribution (across all retrieved trials)

PhaseTrials
PHASE1/PHASE21
EARLY_PHASE11

Top trials by phase / activity

NCTPhaseStatusTitle
NCT05937191PHASE1/PHASE2RECRUITINGLeflunomide for Idiopathic Pulmonary Hemosiderosis in Children
NCT02985346EARLY_PHASE1UNKNOWNEfficacy of Bone Marrow Mesenchymal Stem Cell in Pulmonary Hemosiderosis

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
LEFLUNOMIDE41