Qualitative or quantitative defects of delta-sarcoglycan

disease
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Also known as delta-sarcoglycanopathy

Summary

Qualitative or quantitative defects of delta-sarcoglycan (MONDO:0016144) is a disease with 1 cohort gene.

At a glance

  • Cohort genes: 1
  • ClinVar variants: 197

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namequalitative or quantitative defects of delta-sarcoglycan
Mondo IDMONDO:0016144
Orphanet207070
UMLSC5680806
MedGen1826098
GARD0020393
Is cancer (heuristic)no

Also known as: delta-sarcoglycanopathy

Data availability: 197 ClinVar variants.

Disease family

An umbrella term covering 2 Mondo subtypes.

Classification path: disease › human disease › disease by body system or component › nervous system disorderqualitative or quantitative protein defects in neuromuscular diseasessarcoglycanopathyqualitative or quantitative defects of delta-sarcoglycan

Related subtypes (3): qualitative or quantitative defects of alpha-sarcoglycan, qualitative or quantitative defects of beta-sarcoglycan, qualitative or quantitative defects of gamma-sarcoglycan

Subtypes (2): autosomal recessive limb-girdle muscular dystrophy type 2F, dilated cardiomyopathy 1L

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

197 retrieved; paginated sample, class counts are floors:

124 uncertain significance, 26 benign/likely benign, 19 benign, 15 conflicting classifications of pathogenicity, 13 likely benign

ClinVarVariant (HGVS)GeneClassificationReview
165222NC_000005.10:g.156326924T>CSGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
179031NM_000337.6(SGCD):c.-44+11G>ASGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
196255NM_000337.6(SGCD):c.92G>A (p.Arg31Gln)SGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
352330NM_000337.5(SGCD):c.-135C>TSGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
352331NM_000337.6(SGCD):c.-30G>ASGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
352335NM_000337.6(SGCD):c.510G>A (p.Glu170=)SGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
378577NM_000337.6(SGCD):c.717G>A (p.Ala239=)SGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
43358NM_000337.6(SGCD):c.848A>G (p.Gln283Arg)SGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
464023NM_000337.6(SGCD):c.832G>A (p.Ala278Thr)SGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
48112NC_000005.10:g.156326904C>GSGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
48113NC_000005.10:g.156326864A>TSGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
48115NM_000337.6(SGCD):c.123C>G (p.Leu41=)SGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
48116NM_000337.6(SGCD):c.213G>A (p.Arg71=)SGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
506908NM_000337.6(SGCD):c.3+14G>ASGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
904489NM_000337.6(SGCD):c.699+15G>ASGCDConflicting classifications of pathogenicitycriteria provided, conflicting classifications
352332NM_000337.6(SGCD):c.193-10T>ASGCDUncertain significancecriteria provided, single submitter
352333NM_000337.6(SGCD):c.383-14T>CSGCDUncertain significancecriteria provided, single submitter
352336NM_000337.6(SGCD):c.716C>T (p.Ala239Val)SGCDUncertain significancecriteria provided, multiple submitters, no conflicts
352337NM_000337.6(SGCD):c.*148G>ASGCDUncertain significancecriteria provided, single submitter
352339NM_000337.6(SGCD):c.*158G>ASGCDUncertain significancecriteria provided, multiple submitters, no conflicts
352340NM_000337.6(SGCD):c.*317C>TSGCDUncertain significancecriteria provided, single submitter
352343NM_000337.6(SGCD):c.*557A>CSGCDUncertain significancecriteria provided, single submitter
352344NM_000337.6(SGCD):c.*560C>TSGCDUncertain significancecriteria provided, single submitter
352345NM_000337.6(SGCD):c.*753C>TSGCDUncertain significancecriteria provided, multiple submitters, no conflicts
352346NM_000337.6(SGCD):c.*767A>TSGCDUncertain significancecriteria provided, single submitter
352349NM_000337.6(SGCD):c.*906C>TSGCDUncertain significancecriteria provided, multiple submitters, no conflicts
352355NM_000337.6(SGCD):c.*1719G>ASGCDUncertain significancecriteria provided, multiple submitters, no conflicts
352357NM_000337.6(SGCD):c.*1856A>TSGCDUncertain significancecriteria provided, multiple submitters, no conflicts
352358NM_000337.6(SGCD):c.*1871G>ASGCDUncertain significancecriteria provided, single submitter
352360NM_000337.6(SGCD):c.*2316G>ASGCDUncertain significancecriteria provided, single submitter

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 0 · Orphanet: 2 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
SGCDOrphanet:154Familial isolated dilated cardiomyopathy
SGCDOrphanet:219Delta-sarcoglycan-related limb-girdle muscular dystrophy R6

Cohort genes → proteins

1 cohort genes, 1 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence1

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
SGCDHGNC:10807ENSG00000170624Q92629Delta-sarcoglycanclinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
SGCDDelta-sarcoglycanComponent of the sarcoglycan complex, a subcomplex of the dystrophin-glycoprotein complex which forms a link between the F-actin cytoskeleton and the extracellular matrix.

Protein-family classification

Druggable: 0 · Difficult: 0 · Unknown: 1 · Druggable fraction: 0.0

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Other/Unknown11.8×0.558

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
SGCDOther/UnknownnoSarcoglycan, Sarcoglycan_gamma/delta/zeta

Expression context

Cohort genes with no expression data: 0.

1 cohort gene are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)1
unknown0

Top tissues across cohort

TissueCohort genes
heart right ventricle1
left ventricle myocardium1
skeletal muscle tissue of rectus abdominis1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
SGCD247broadmarkerleft ventricle myocardium, skeletal muscle tissue of rectus abdominis, heart right ventricle

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
SGCD1,102

Structural data

PDB: 0 · AlphaFold-only: 1 · No structure: 0

AlphaFold-only cohort genes (top 30 by pLDDT)

SymbolUniProtpLDDT
SGCDQ9262981.43

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 3. Enrichment computed across 1 evidence-associated genes (1 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Formation of the dystrophin-glycoprotein complex (DGC)1308.6×0.010SGCD
Non-integrin membrane-ECM interactions1154.3×0.010SGCD
Extracellular matrix organization163.1×0.016SGCD

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
coronary vasculature morphogenesis18426.0×0.001SGCD
cardiac muscle cell contraction11685.2×0.002SGCD
protein-containing complex localization1991.3×0.002SGCD
cardiac muscle tissue development1887.0×0.002SGCD
heart contraction1766.0×0.002SGCD
cardiac muscle cell development1624.1×0.002SGCD
calcium ion homeostasis1443.5×0.003SGCD
calcium-mediated signaling1183.2×0.006SGCD
muscle organ development1166.8×0.006SGCD

Therapeutics

Drug target analysis

Approved (phase 4): 0 · Phase ≥3: 0 · Phased (≥1): 0 · Undrugged: 1

Druggability breadth: 0 of 1 evidence-associated genes (0%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Top cohort targets by molecule count

SymbolMoleculesMax phase
SGCD00

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Pharmacogenomics

Cohort genes with a PharmGKB record: 1; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

0 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)0
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug1SGCD

Undrugged target profiles

1 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
SGCD0

Clinical trials & evidence

Clinical trials

Clinical trials: 0.