Renal dysplasia, cystic, susceptibility to

disease
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Also known as CYSRDdiffuse cystic renal dysplasiarenal dysplasia diffuse cystic

Summary

Renal dysplasia, cystic, susceptibility to (MONDO:0011037) is a disease with 3 cohort genes.

At a glance

  • Cohort genes: 3
  • ClinVar variants: 127

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical namerenal dysplasia, cystic, susceptibility to
Mondo IDMONDO:0011037
MeSHC537755
OMIM601331
DOIDDOID:0111682
UMLSC3275898
MedGen477529
Is cancer (heuristic)no

Also known as: CYSRD · diffuse cystic renal dysplasia · renal dysplasia diffuse cystic · renal dysplasia, cystic, susceptibility to

Data availability: 127 ClinVar variants · 3 GenCC gene-disease records.

Disease family

Classification path: disease susceptibility › inherited disease susceptibilityrenal dysplasia, cystic, susceptibility to

Related subtypes (283): microvascular complications of diabetes, susceptibility, Mycobacterium tuberculosis, susceptibility, bacteremia, susceptibility, pregnancy loss, recurrent, susceptibility, autoimmune thyroid disease, susceptibility to, susceptibility to HIV infection, appendicitis, proneness to, atherosclerosis susceptibility, multiple sclerosis, susceptibility to, dyslexia, susceptibility to, 1, endometriosis, susceptibility to, 1, osteoarthritis susceptibility 2, essential hypertension, genetic, osteoarthritis susceptibility 1, otitis media, susceptibility to, pelvic organ prolapse, susceptibility to, pulmonary edema of mountaineers, susceptibility to, sarcoidosis, susceptibility to, 1, strabismus, susceptibility to, thyrotoxic periodic paralysis, susceptibility to, 1, predisposition to invasive fungal disease due to CARD9 deficiency, celiac disease, susceptibility to, 1, hemolytic uremic syndrome, atypical, susceptibility to, 1, hypervitaminosis a, susceptibility to, kuru, susceptibility to, leprosy, susceptibility to, 3, nonarteritic anterior ischemic optic neuropathy, susceptibility to, diabetes mellitus, insulin-dependent, X-linked, susceptibility to, coronary heart disease, susceptibility to, 3, dyslexia, susceptibility to, 9, systemic lupus erythematosus, susceptibility to, 15, Leber optic atrophy, susceptibility to, dyslexia, susceptibility to, 2, Helicobacter pylori infection, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 1, inherited susceptibility to asthma, systemic lupus erythematosus, susceptibility to, 1, leishmaniasis, tegumentary, susceptibility to, xanthomatosis, susceptibility to, hyperlipidemia, combined, 1, urinary tract infections, recurrent, susceptibility to, hypertension, essential, susceptibility to, 1, hepatic fibrosis, severe, susceptibility to, due to Schistosoma mansoni infection, dyslexia, susceptibility to, 3, Ascaris lumbricoides infection, susceptibility to, hypertension, essential, susceptibility to, 2, epilepsy, idiopathic generalized, susceptibility to, 7, systemic lupus erythematosus, susceptibility to, 2, systemic lupus erythematosus, susceptibility to, 3, nephrolithiasis, uric acid, susceptibility to, atrioventricular septal defect, susceptibility to, 2, vitiligo-associated multiple autoimmune disease susceptibility 1, polysubstance abuse, susceptibility to, dyslexia, susceptibility to, 6, glaucoma, normal tension, susceptibility to, anorexia nervosa, susceptibility to, 1, stroke, susceptibility to, 1, dyslexia, susceptibility to, 5, epilepsy, idiopathic generalized, susceptibility to, 2, familial meningioma, celiac disease, susceptibility to, 5, systemic lupus erythematosus with hemolytic anemia, susceptibility to, 1, hypertension, essential, susceptibility to, 3, coronary heart disease, susceptibility to, 1, bulimia nervosa, susceptibility to, 1, leprosy, susceptibility to, 2, epilepsy, idiopathic generalized, susceptibility to, 9, Parkinson disease 11, autosomal dominant, susceptibility to, focal segmental glomerulosclerosis 3, susceptibility to, autoimmune disease, susceptibility to, 1, osteoarthritis susceptibility 3, systemic lupus erythematosus with nephritis, susceptibility to, 1, systemic lupus erythematosus with nephritis, susceptibility to, 2, systemic lupus erythematosus with nephritis, susceptibility to, 3, coronary heart disease, susceptibility to, 2, coronary heart disease, susceptibility to, 4, autoimmune disease, susceptibility to, 2, autoimmune disease, susceptibility to, 3, systemic lupus erythematosus, susceptibility to, 4, myocardial infarction, susceptibility to, major depressive disorder 1, legionnaire disease, susceptibility to, myocardial infarction, susceptibility to, 2, major depressive disorder 2, hypertension, essential, susceptibility to, 4, epilepsy, idiopathic generalized, susceptibility to, 3, myoclonic epilepsy, juvenile, susceptibility to, 3, orofacial cleft 6, susceptibility to, coronary heart disease, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 1, attention deficit-hyperactivity disorder, susceptibility to, 2, attention deficit-hyperactivity disorder, susceptibility to, 3, attention deficit-hyperactivity disorder, susceptibility to, 4, Alzheimer disease 9, susceptibility to respiratory infections associated with CD8alpha chain mutation, dyslexia, susceptibility to, 8, autoimmune disease, susceptibility to, 4, hepatitis C virus, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 4, celiac disease, susceptibility to, 4, celiac disease, susceptibility to, 2, celiac disease, susceptibility to, 3, leprosy, susceptibility to, 1, systemic lupus erythematosus, susceptibility to, 5, systemic lupus erythematosus, susceptibility to, 6, opioid dependence, susceptibility to, 1, systemic lupus erythematosus, susceptibility to, 7, systemic lupus erythematosus, susceptibility to, 8, hypertension, essential, susceptibility to, 5, hypertension, essential, susceptibility to, 6, Parkinson disease 13, autosomal dominant, susceptibility to, West Nile virus, susceptibility to, hepatitis B virus, susceptibility to, Buruli ulcer, susceptibility to, osteoarthritis susceptibility 4, systemic lupus erythematosus, susceptibility to, 9, coronary heart disease, susceptibility to, 7, hypertension, essential, susceptibility to, 7, leprosy, susceptibility to, 4, hypertension, essential, susceptibility to, 8, epilepsy, idiopathic generalized, susceptibility to, 13, coronary heart disease, susceptibility to, 8, myoclonic epilepsy, juvenile, susceptibility to, 4, susceptibility to visceral leishmaniasis, 2, susceptibility to visceral leishmaniasis, 3, celiac disease, susceptibility to, 6, epilepsy, idiopathic generalized, susceptibility to, 5, epilepsy, childhood absence, susceptibility to, 6, celiac disease, susceptibility to, 7, celiac disease, susceptibility to, 8, celiac disease, susceptibility to, 9, celiac disease, susceptibility to, 10, celiac disease, susceptibility to, 11, celiac disease, susceptibility to, 12, celiac disease, susceptibility to, 13, coronary heart disease, susceptibility to, 9, systemic lupus erythematosus, susceptibility to, 10, systemic lupus erythematosus, susceptibility to, 11, systemic lupus erythematosus, susceptibility to, 12, epilepsy, childhood absence, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 5, attention deficit-hyperactivity disorder, susceptibility to, 6, systemic lupus erythematosus, susceptibility to, 13, sarcoidosis, susceptibility to, 2, sarcoidosis, susceptibility to, 3, osteoarthritis susceptibility 5, osteoarthritis susceptibility 6, focal segmental glomerulosclerosis 4, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 8, herpes simplex encephalitis, susceptibility to, 2, attention deficit-hyperactivity disorder, susceptibility to, 7, epilepsy, idiopathic generalized, susceptibility to, 10, pelvic organ prolapse, susceptibility to, 2, systemic lupus erythematosus, susceptibility to, 14, leprosy, susceptibility to, 5, thyrotoxic periodic paralysis, susceptibility to, 2, hearing loss, cisplatin-induced, susceptibility to, susceptibility to mononeuropathy of the median nerve, mild, fatty liver disease, nonalcoholic, susceptibility to, 2, leprosy, susceptibility to, 6, autoimmune disease, susceptibility to, 6, Parkinson disease 5, autosomal dominant, susceptibility to, aspergillosis, susceptibility to, sick sinus syndrome 3, susceptibility to, Parkinson disease 18, autosomal dominant, susceptibility to, epilepsy, juvenile myoclonic, susceptibility to, 9, dengue virus, susceptibility to, coronary heart disease, susceptibility to, 6, podoconiosis, susceptibility to, peripartum cardiomyopathy, susceptibility to, influenza, severe, susceptibility to, thyrotoxic periodic paralysis, susceptibility to, 3, human herpesvirus 8, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 12, herpes simplex encephalitis, susceptibility to, 3, herpes simplex encephalitis, susceptibility to, 4, pulmonary hypertension, neonatal, susceptibility to, craniosynostosis 5, susceptibility to, melioidosis, susceptibility to, chronic mountain sickness, susceptibility to, herpes simplex encephalitis, susceptibility to, 7, epilepsy, idiopathic generalized, susceptibility to, 14, hereditary neoplastic syndrome, autosomal recessive Mendelian susceptibility to mycobacterial diseases due to partial IFNgammaR1 deficiency, autosomal recessive Mendelian susceptibility to mycobacterial diseases due to partial IFNgammaR2 deficiency, susceptibility to localized juvenile periodontitis, inherited susceptibility to mycobacterial diseases, neural tube defects, susceptibility to, multiple system atrophy 1, susceptibility to, nephrolithiasis susceptibility caused by SLC26A1, myoclonic epilepsy, juvenile, susceptibility to, 1, epilepsy, childhood absence, susceptibility to, 1, autism, susceptiblity to, susceptibility to visceral leishmaniasis, 1, malaria, susceptibility to, spondyloarthropathy, susceptibility to, herpes simplex encephalitis, susceptibility to, 1, epilepsy, idiopathic generalized, susceptibility to, 18, epilepsy, idiopathic generalized, susceptibility to, 15, hepatitis, fulminant viral, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 16, autosomal recessive mendelian susceptibility to mycobacterial diseases due to partial jak1 deficiency, aortic aneurysm, familial thoracic 11, susceptibility to, craniosynostosis 7, amyotrophic lateral sclerosis, susceptibility to, 24, amyotrophic lateral sclerosis, susceptibility to, 25, epilepsy, juvenile myoclonic, susceptibility to, 10, susceptibility to angioedema induced by ACE inhibitors, epidermodysplasia verruciformis, susceptibility to, exfoliation syndrome, susceptibility to, basal cell carcinoma, susceptibility to, graft-versus-host disease, susceptibility to, narcolepsy, susceptibility to, pulmonary disease, chronic obstructive, susceptibility to, restless legs syndrome, susceptibility to, psoriasis, susceptibility to, age related macular degeneration, susceptibility to, allergic rhinitis, susceptibility to, dermatitis, atopic, susceptibility to, Hirschsprung disease, susceptibility to, diabetes mellitus, ketosis-prone, schizophrenia, susceptibility to, radioulnar synostosis, nonsyndromic, susceptibility to, lumbar disk herniation, susceptibility to, lumbar disk degeneration, susceptibility to, psoriatic arthritis, susceptibility to, migraine with or without aura, susceptibility to, Alzheimer disease, susceptibility to, mitochondrial, Asperger syndrome, susceptibility to, tobacco addiction, susceptibility to, lipodystrophy, partial, acquired, susceptibility to, Graves disease, susceptibility to, 1, epilepsy, idiopathic generalized, susceptibility to, 17, breast-ovarian cancer, familial, susceptibility to, blepharospasm, benign essential, susceptibility to, hemorrhage, intracerebral, susceptibility to, IgA nephropathy, susceptibility to, hemolytic uremic syndrome, atypical, susceptibility to, 7, vitiligo-associated multiple autoimmune disease susceptibility 6, delayed sleep phase syndrome, susceptibility to, encephalitis, acute, infection-induced, susceptibility to, malignant hyperthermia, susceptibility to, multicentric Castleman disease, susceptibility to, pelvic organ prolapse, susceptibility to, 1, amyotrophic lateral sclerosis, susceptibility to, 13, Graves disease, susceptibility to, X-linked 2, autoimmune thyroid disease, susceptibility to, 5, atrioventricular septal defect, susceptibility to, 1, epilepsy, juvenile myoclonic, susceptibility to, 6, autoimmune disease, susceptibility to, 5, epilepsy, idiopathic generalized, susceptibility to, 6, seasonal affective disorder, susceptibility to, ventricular fibrillation during myocardial infarction, susceptibility to, UV-induced skin damage, susceptibility to, antisocial behavior, susceptibility to, aplastic anemia, susceptibility to, cardiomyopathy, familial hypertrophic, 4, susceptibility to, cirrhosis, noncryptogenic, susceptibility to, coronary artery disease, severe, susceptibility to, dengue fever, susceptibility to, dengue hemorrhagic fever, susceptibility to, dengue shock syndrome, susceptibility to, dyslexia, susceptibility to, 4, dyslexia, susceptibility to, 7, efavirenz central nervous system toxicity, susceptibility to, obesity, susceptibility to, bleeding disorder, platelet-type, 13, susceptibility to, Schistosoma mansoni infection, susceptibility/resistance to, Parkinson disease 24, autosomal dominant, susceptibility to, iron overload, susceptibility to, hydrocephalus, congenital, 5, susceptibility to, hearing loss, noise-induced, susceptibility to, hyperemesis gravidarum, susceptibility to, Parkinson disease 26, autosomal dominant, susceptibility to, epilepsy, idiopathic generalized, susceptibility to, 19, polycystic kidney disease 9, susceptibility to, rhabdomyolysis, susceptibility to, scoliosis, isolated, susceptibility to, dystonia 38, susceptibility to, gallbladder disease 4, epilepsy, juvenile absence, susceptibility to, GBA1-related Parkinson disease, susceptibility, SH2B3-related immune system disorder

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

127 retrieved; paginated sample, class counts are floors:

109 uncertain significance, 8 conflicting classifications of pathogenicity, 3 likely pathogenic, 2 benign/likely benign, 2 likely benign, 1 pathogenic, 1 benign, 1 risk factor

ClinVarVariant (HGVS)GeneClassificationReview
1048654NM_001080512.3(BICC1):c.93del (p.Glu32fs)BICC1Pathogeniccriteria provided, single submitter
3066390NM_001080512.3(BICC1):c.2229_2230insGA (p.Lys744fs)BICC1Likely pathogeniccriteria provided, single submitter
3234043NM_001080512.3(BICC1):c.1827del (p.Glu609fs)BICC1Likely pathogeniccriteria provided, single submitter
3236040NM_001080512.3(BICC1):c.1179+1G>TBICC1Likely pathogeniccriteria provided, single submitter
31153NM_001080512.3(BICC1):c.259C>T (p.Gln87Ter)BICC1risk factorno assertion criteria provided
1357855NM_001080512.3(BICC1):c.2828C>T (p.Ser943Leu)BICC1Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
2510105NM_001080512.3(BICC1):c.706A>C (p.Asn236His)BICC1Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
3236256NM_001080512.3(BICC1):c.1204C>T (p.Arg402Ter)BICC1Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
3596080NM_001080512.3(BICC1):c.1453T>A (p.Leu485Met)BICC1Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
3596120NM_001080512.3(BICC1):c.1540A>G (p.Ile514Val)BICC1Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
3596143NM_001080512.3(BICC1):c.1684G>A (p.Glu562Lys)BICC1Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
3596297NM_001080512.3(BICC1):c.2840G>A (p.Arg947His)BICC1Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
383742NM_001080512.3(BICC1):c.994G>A (p.Val332Ile)BICC1Conflicting classifications of pathogenicitycriteria provided, conflicting classifications
1328413NM_000789.4(ACE):c.417+5G>AACEUncertain significancecriteria provided, single submitter
1328412NM_000685.5(AGTR1):c.377G>C (p.Arg126Pro)AGTR1Uncertain significancecriteria provided, single submitter
1181881NM_001080512.3(BICC1):c.707A>G (p.Asn236Ser)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
1312346NM_001080512.3(BICC1):c.1910C>A (p.Ser637Tyr)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
1383883NM_001080512.3(BICC1):c.41C>T (p.Ser14Leu)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
1709315NM_001080512.3(BICC1):c.129C>G (p.Ser43Arg)BICC1Uncertain significancecriteria provided, single submitter
1711182NM_001080512.3(BICC1):c.1858+1G>TBICC1Uncertain significancecriteria provided, single submitter
1973759NM_001080512.3(BICC1):c.1675A>G (p.Met559Val)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2064075NM_001080512.3(BICC1):c.1996A>G (p.Thr666Ala)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2145086NM_001080512.3(BICC1):c.826G>T (p.Ala276Ser)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2159993NM_001080512.3(BICC1):c.2563A>G (p.Met855Val)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2176158NM_001080512.3(BICC1):c.1150A>G (p.Ile384Val)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2183790NM_001080512.3(BICC1):c.2010C>G (p.His670Gln)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2227409NM_001080512.3(BICC1):c.1997C>T (p.Thr666Met)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2374068NM_001080512.3(BICC1):c.790G>T (p.Val264Leu)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2380399NM_001080512.3(BICC1):c.2534C>A (p.Thr845Lys)BICC1Uncertain significancecriteria provided, multiple submitters, no conflicts
2443049NM_001080512.3(BICC1):c.1725+3_1725+6dupBICC1Uncertain significancecriteria provided, single submitter

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 3 · Orphanet: 3 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

GenCC gene–disease validity (cohort genes)

the Disease column is the GenCC-asserted condition — a cohort gene’s strongest validity may be for a related predisposition syndrome.

GeneClassificationInheritanceDiseaseRecords
BICC1ModerateAutosomal dominantrenal dysplasia, cystic, susceptibility to3

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
BICC1Orphanet:730Autosomal dominant polycystic kidney disease
ACEOrphanet:97369Renal tubular dysgenesis of genetic origin
AGTR1Orphanet:97369Renal tubular dysgenesis of genetic origin

Cohort genes → proteins

3 cohort genes, 3 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence3

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
BICC1HGNC:19351ENSG00000122870Q9H694Protein bicaudal C homolog 1gencc,clinvar
ACEHGNC:2707ENSG00000159640P12821Angiotensin-converting enzymeclinvar
AGTR1HGNC:336ENSG00000144891P30556Type-1 angiotensin II receptorclinvar

Cohort function summary

Lead sentence per gene, UniProt-curated.

SymbolProtein nameFunction (lead sentence)
BICC1Protein bicaudal C homolog 1Putative RNA-binding protein.
ACEAngiotensin-converting enzymeDipeptidyl carboxypeptidase that removes dipeptides from the C-terminus of a variety of circulating hormones, such as angiotensin I, bradykinin or enkephalins, thereby playing a key role in the regulation of blood pressure, electrolyte hom…
AGTR1Type-1 angiotensin II receptorReceptor for angiotensin II, a vasoconstricting peptide, which acts as a key regulator of blood pressure and sodium retention by the kidney.

Protein-family classification

Druggable: 2 · Difficult: 0 · Unknown: 1 · Druggable fraction: 0.67

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Protease112.2×0.180
GPCR18.0×0.180
Other/Unknown10.6×0.914

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
BICC1Other/UnknownnoSAM, KH_dom, KH_dom_type_1
ACEProteaseyes3.4.15.1Peptidase_M2
AGTR1GPCRyesATII_AT1_rcpt, ATII_rcpt, GPCR_Rhodpsn

Expression context

Cohort genes with no expression data: 0.

3 cohort genes are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)3
unknown0

Top tissues across cohort

TissueCohort genes
germinal epithelium of ovary1
parietal pleura1
renal medulla1
ileal mucosa1
left testis1
right testis1
placenta1
skin of hip1
subcutaneous adipose tissue1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
BICC1236ubiquitousmarkergerminal epithelium of ovary, renal medulla, parietal pleura
ACE177ubiquitousmarkerileal mucosa, right testis, left testis
AGTR1224markerskin of hip, placenta, subcutaneous adipose tissue

Protein interactions among cohort

Intra-cohort edges: 1.

Hub genes (top 10 by interactor count)

SymbolInteractor count
ACE3,659
AGTR12,651
BICC11,265

Intra-cohort edges

ABSources
ACEAGTR1string_interaction

Structural data

PDB: 3 · AlphaFold-only: 0 · No structure: 0

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
ACEP1282197
AGTR1P3055611
BICC1Q9H6943

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 14. Enrichment computed across 3 evidence-associated genes (2 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 2 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Metabolism of Angiotensinogen to Angiotensins1317.2×0.044ACE
Peptide hormone metabolism1135.9×0.051ACE
Cargo recognition for clathrin-mediated endocytosis152.4×0.060AGTR1
Clathrin-mediated endocytosis142.6×0.060AGTR1
Class A/1 (Rhodopsin-like receptors)137.1×0.060AGTR1
Peptide ligand-binding receptors137.1×0.060AGTR1
GPCR ligand binding132.1×0.060AGTR1
G alpha (q) signalling events128.7×0.060AGTR1
GPCR downstream signalling121.7×0.066AGTR1
Signaling by GPCR120.0×0.066AGTR1
Membrane Trafficking118.5×0.066AGTR1
Vesicle-mediated transport117.4×0.066AGTR1
Metabolism of proteins16.2×0.167ACE
Signal Transduction15.1×0.187AGTR1

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 3 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
regulation of systemic arterial blood pressure by renin-angiotensin22246.9×1e-05ACE, AGTR1
kidney development3140.4×1e-05BICC1, ACE, AGTR1
angiotensin-activated signaling pathway21021.3×2e-05ACE, AGTR1
regulation of vasoconstriction2535.0×7e-05ACE, AGTR1
blood vessel diameter maintenance2416.1×9e-05ACE, AGTR1
mononuclear cell proliferation15617.3×0.002ACE
regulation of renal output by angiotensin12808.7×0.002ACE
regulation of angiotensin metabolic process12808.7×0.002ACE
cell proliferation in bone marrow12808.7×0.002ACE
negative regulation of gap junction assembly12808.7×0.002ACE
renin-angiotensin regulation of aldosterone production11872.4×0.002AGTR1
maintenance of blood vessel diameter homeostasis by renin-angiotensin11872.4×0.002AGTR1
substance P catabolic process11872.4×0.002ACE
phospholipase C-activating angiotensin-activated signaling pathway11872.4×0.002AGTR1
regulation of hematopoietic stem cell proliferation11872.4×0.002ACE
regulation of renal sodium excretion11404.3×0.003AGTR1
antigen processing and presentation of peptide antigen via MHC class I11123.5×0.003ACE
hormone catabolic process1936.2×0.004ACE
bradykinin catabolic process1802.5×0.004ACE
regulation of smooth muscle cell migration1802.5×0.004ACE
positive regulation of cholesterol metabolic process1702.2×0.004AGTR1
positive regulation of blood vessel endothelial cell proliferation involved in sprouting angiogenesis1561.7×0.005AGTR1
amyloid-beta metabolic process1510.7×0.005ACE
neutrophil mediated immunity1468.1×0.005ACE
positive regulation of systemic arterial blood pressure1468.1×0.005ACE
angiotensin maturation1432.1×0.005ACE
low-density lipoprotein particle remodeling1351.1×0.006AGTR1
peptide catabolic process1351.1×0.006ACE
hormone metabolic process1295.6×0.007ACE
positive regulation of macrophage derived foam cell differentiation1280.9×0.007AGTR1

Therapeutics

Drug target analysis

Approved (phase 4): 2 · Phase ≥3: 2 · Phased (≥1): 2 · Undrugged: 1

Druggability breadth: 2 of 3 evidence-associated genes (67%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Genes with an approved drug

The molecule shown is one approved compound that hits the gene — not necessarily a drug of choice or one indicated for this disease.

SymbolExample approved molecule
ACETELMISARTAN
AGTR1IRBESARTAN

Top cohort targets by molecule count

SymbolMoleculesMax phase
AGTR1884
ACE314
BICC100

Drugs targeting cohort genes (top 30)

MoleculeMax phaseTargets in cohort
TELMISARTAN4ACE, AGTR1
MOEXIPRIL4ACE
RAMIPRIL4ACE
LISINOPRIL ANHYDROUS4ACE
SITAGLIPTIN4ACE
TRANDOLAPRIL4ACE
CAPTOPRIL4ACE
PERINDOPRIL4ACE
QUINAPRIL4ACE
LOSARTAN4ACE, AGTR1
FOSINOPRIL4ACE
IMIDAPRIL4ACE
ENALAPRILAT ANHYDROUS4ACE
ENALAPRIL4ACE
BENAZEPRIL4ACE
IRBESARTAN4AGTR1
SARALASIN4AGTR1
LOSARTAN POTASSIUM4AGTR1
CANDESARTAN CILEXETIL4AGTR1
CLOTRIMAZOLE4AGTR1
SIMVASTATIN4AGTR1
VALSARTAN4AGTR1
RIMONABANT4AGTR1
ARIPIPRAZOLE4AGTR1
PONATINIB4AGTR1
OXYMETHOLONE4AGTR1
OLMESARTAN MEDOXOMIL4AGTR1
NORGESTIMATE4AGTR1
ROCURONIUM4AGTR1
PYRVINIUM4AGTR1

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 1.

Cohort genes with ChEMBL bioactivity (full, sorted by assay count)

SymbolAssaysType breakdown
AGTR1421Binding:315, Functional:105, ADMET:1
ACE304Binding:288, Functional:8, ADMET:5, Unclassified:3

Cohort enzymes (BRENDA EC)

SymbolEC numbersNames
ACE3.4.15.1peptidyl-dipeptidase A

Cohort genes with high screening signal

≥100 ChEMBL assays — a studied-ness signal; see Therapeutics for approved-drug status.

SymbolChEMBL assays
ACE304
AGTR1421

Pharmacogenomics

Cohort genes with a PharmGKB record: 3; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Chemical tractability of cohort targets

30 approved/phased compounds have measured bioactivity against a cohort gene (and aren’t yet in disease-level trials). This is a research / tractability signal, NOT a therapeutic recommendation — a bioactivity row often reflects off-target or screening binding (e.g. promiscuous kinase inhibitors against a cohort kinase), implying no disease mechanism.

CompoundMax phaseCohort target (bioactivity)
TELMISARTAN4ACE, AGTR1
MOEXIPRIL4ACE
RAMIPRIL4ACE
LISINOPRIL ANHYDROUS4ACE
SITAGLIPTIN4ACE
TRANDOLAPRIL4ACE
CAPTOPRIL4ACE
PERINDOPRIL4ACE
QUINAPRIL4ACE
LOSARTAN4ACE, AGTR1
FOSINOPRIL4ACE
IMIDAPRIL4ACE
ENALAPRILAT ANHYDROUS4ACE
ENALAPRIL4ACE
BENAZEPRIL4ACE
IRBESARTAN4AGTR1
SARALASIN4AGTR1
LOSARTAN POTASSIUM4AGTR1
CANDESARTAN CILEXETIL4AGTR1
CLOTRIMAZOLE4AGTR1
SIMVASTATIN4AGTR1
VALSARTAN4AGTR1
RIMONABANT4AGTR1
ARIPIPRAZOLE4AGTR1
PONATINIB4AGTR1
OXYMETHOLONE4AGTR1
OLMESARTAN MEDOXOMIL4AGTR1
NORGESTIMATE4AGTR1
ROCURONIUM4AGTR1
PYRVINIUM4AGTR1

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)2ACE, AGTR1
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug1BICC1

Undrugged target profiles

1 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
BICC10

Clinical trials & evidence

Clinical trials

Clinical trials: 0.