Sinus histiocytosis with massive lymphadenopathy

disease
On this page

Also known as Destombes-RosaC/-Dorfman diseaseDestombes-Rosaï-Dorfman diseaseRDDRosaC/-Dorfman-Destombes diseaseRosai-Dorfman DiseaseRosaï-Dorfman-Destombes diseaseSHML

Summary

Sinus histiocytosis with massive lymphadenopathy (MONDO:0006412) is a disease and 8 clinical trials. Top therapeutic interventions include cobimetinib and mirdametinib. A subtype of non-Langerhans cell histiocytosis — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • Prevalence: <1 / 1 000 000 (Worldwide) [Orphanet-validated]
  • Phenotypes (HPO): 12
  • Clinical trials: 8

Clinical features

Epidemiology

Prevalence records

2 prevalence record(s), Orphanet:

TypeClassValueGeographyValidation
Cases/families1000WorldwideValidated
Point prevalence<1 / 1 000 000WorldwideValidated

Signs & symptoms

Clinical features (HPO)

12 HPO clinical features (Orphanet curated; top 12 by frequency):

HPO IDTermFrequency
HP:0001903AnemiaVery frequent (80-99%)
HP:0001945FeverVery frequent (80-99%)
HP:0002716LymphadenopathyVery frequent (80-99%)
HP:0002961DysgammaglobulinemiaVery frequent (80-99%)
HP:0001250SeizureOccasional (5-29%)
HP:0001482Subcutaneous noduleOccasional (5-29%)
HP:0002315HeadacheOccasional (5-29%)
HP:0002797OsteolysisOccasional (5-29%)
HP:0003401ParesthesiaOccasional (5-29%)
HP:0010550ParaplegiaOccasional (5-29%)
HP:0010783ErythemaOccasional (5-29%)
HP:0200034PapuleOccasional (5-29%)

Identifiers

Disease identifiers

FieldValue
Canonical namesinus histiocytosis with massive lymphadenopathy
Mondo IDMONDO:0006412
MeSHD015618
Orphanet158014
ICD-111908538383
NCITC36075
SNOMED CT34287003
UMLSC0019625
MedGen9266
GARD0007588
MedDRA10063397
NORD1676
Is cancer (heuristic)no

Also known as: Destombes-RosaC/-Dorfman disease · Destombes-Rosaï-Dorfman disease · RDD · RosaC/-Dorfman-Destombes disease · Rosai-Dorfman Disease · Rosai-Dorfman disease · Rosaï-Dorfman-Destombes disease · SHML · sinus histiocytosis with massive lymphadenopathy

Disease family

This is a subtype of non-Langerhans cell histiocytosis. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by body system or component › immune system disorder › lymphoid system disorder › lymphatic system disorderhistiocytosisnon-Langerhans cell histiocytosissinus histiocytosis with massive lymphadenopathy

Related subtypes (14): Niemann-Pick disease, hereditary progressive mucinous histiocytosis, sea-blue histiocyte syndrome, multicentric reticulohistiocytosis, generalized eruptive histiocytosis, benign cephalic histiocytosis, juvenile xanthogranuloma, xanthoma disseminatum, papular xanthoma, necrobiotic xanthogranuloma, indeterminate dendritic cell tumor, progressive nodular histiocytosis, Erdheim-Chester disease, xanthogranuloma

Subtypes (1): H syndrome

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

No tiered GWAS variants or ClinVar records for this disease.

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

Drugs indicated for this disease

No approved or late-stage (phase ≥3) drug is indicated for this disease; the following are in earlier-phase trials only.

Earlier-phase candidates (phase 2, investigational — efficacy not yet established): Dexamethasone, Lenalidomide.

Clinical trials & evidence

Clinical trials

Clinical trials: 8.

Phase distribution (across all retrieved trials)

PhaseTrials
PHASE24
Not specified2
PHASE41
EARLY_PHASE11

Top trials by phase / activity

NCTPhaseStatusTitle
NCT05284942PHASE4UNKNOWNCentral China Rosai-Dorfman Disease Registry
NCT04079179PHASE2RECRUITINGCobimetinib in Refractory Langerhans Cell Histiocytosis (LCH), and Other Histiocytic Disorders
NCT06153173PHASE2RECRUITINGMirdametinib in Histiocytic Disorders
NCT07187167PHASE2RECRUITINGEfficacy and Safety of the RD Regimen(Lenalidomide, Dexamethasone) for Rosai-Dorfman Disease
NCT04924647PHASE2UNKNOWNLenalidomide and Dexamethasone for Rosai-Dorfman Disease
NCT05093335EARLY_PHASE1RECRUITINGIn-Human CXCR4 Imaging of Hematologic and Solid Tumors Using [68Ga]-Pentixafor-PET
NCT02285582Not specifiedRECRUITINGInternational Rare Histiocytic Disorders Registry (IRHDR)
NCT05915208Not specifiedRECRUITINGHistiocytic Disorder Follow-up Study

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
COBIMETINIB41
MIRDAMETINIB21
CHEMBL453842501