Sporadic infantile bilateral striatal necrosis

disease
On this page

Also known as ABSNacute bilateral striatal necrosissporadic IBSNsporadic infantile striatonigral degenerationsporadic infantile striatonigral necrosis

Summary

Sporadic infantile bilateral striatal necrosis (MONDO:0016394) is a disease. A subtype of infantile bilateral striatal necrosis — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • Prevalence: 1-9 / 1 000 000 (Europe) [Orphanet-validated]
  • Phenotypes (HPO): 38

Clinical features

Epidemiology

Prevalence records

1 prevalence record(s), Orphanet:

TypeClassValueGeographyValidation
Point prevalence1-9 / 1 000 000EuropeValidated

Signs & symptoms

Clinical features (HPO)

38 HPO clinical features (Orphanet curated; top 38 by frequency):

HPO IDTermFrequency
HP:0030215Inappropriate cryingFrequent (30-79%)
HP:0100022Abnormality of movementFrequent (30-79%)
HP:0000273Facial grimacingFrequent (30-79%)
HP:0001250SeizureFrequent (30-79%)
HP:0001260DysarthriaFrequent (30-79%)
HP:0001328Specific learning disabilityFrequent (30-79%)
HP:0002015DysphagiaFrequent (30-79%)
HP:0002533Abnormal posturingFrequent (30-79%)
HP:0002788Recurrent upper respiratory tract infectionsFrequent (30-79%)
HP:0008936Axial hypotoniaFrequent (30-79%)
HP:0000020Urinary incontinenceOccasional (5-29%)
HP:0000298Mask-like faciesOccasional (5-29%)
HP:0000338Hypomimic faceOccasional (5-29%)
HP:0000736Short attention spanOccasional (5-29%)
HP:0001288Gait disturbanceOccasional (5-29%)
HP:0001300ParkinsonismOccasional (5-29%)
HP:0001332DystoniaOccasional (5-29%)
HP:0001347HyperreflexiaOccasional (5-29%)
HP:0002033Poor suckOccasional (5-29%)
HP:0002066Gait ataxiaOccasional (5-29%)
HP:0002067BradykinesiaOccasional (5-29%)
HP:0002072ChoreaOccasional (5-29%)
HP:0002300MutismOccasional (5-29%)
HP:0002301HemiplegiaOccasional (5-29%)
HP:0002307DroolingOccasional (5-29%)
HP:0002322Resting tremorOccasional (5-29%)
HP:0002465Poor speechOccasional (5-29%)
HP:0003487Babinski signOccasional (5-29%)
HP:0004372Reduced consciousness/confusionOccasional (5-29%)
HP:0005366Recurrent streptococcus pneumoniae infectionsOccasional (5-29%)
HP:0007158Progressive extrapyramidal muscular rigidityOccasional (5-29%)
HP:0007185Loss of consciousnessOccasional (5-29%)
HP:0007359Focal-onset seizureOccasional (5-29%)
HP:0008947Floppy infantOccasional (5-29%)
HP:0011151Obtundation statusOccasional (5-29%)
HP:0025439PharyngitisOccasional (5-29%)
HP:0030187TitubationOccasional (5-29%)
HP:0040288Nasogastric tube feedingOccasional (5-29%)

Identifiers

Disease identifiers

FieldValue
Canonical namesporadic infantile bilateral striatal necrosis
Mondo IDMONDO:0016394
Orphanet225147
ICD-111174703901
UMLSC4087175
MedGen1672494
GARD0020549
Is cancer (heuristic)no

Also known as: ABSN · acute bilateral striatal necrosis · sporadic IBSN · sporadic infantile striatonigral degeneration · sporadic infantile striatonigral necrosis

Disease family

This is a subtype of infantile bilateral striatal necrosis. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by body system or component › nervous system disordercentral nervous system disorderneurodegenerative diseaseinfantile bilateral striatal necrosissporadic infantile bilateral striatal necrosis

Related subtypes (1): familial infantile bilateral striatal necrosis

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

No tiered GWAS variants or ClinVar records for this disease.

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

No druggable-target or therapeutic data for this disease’s cohort.

Clinical trials & evidence

Clinical trials

Clinical trials: 0.

No linked Atlas pages yet — the cross-entity mesh grows as the corpus expands.