Tenosynovial giant cell tumor, diffuse type

disease
On this page

Also known as diffuse giant cell neoplasm of tendon sheathdiffuse giant cell neoplasm of Tenosynoviumdiffuse giant cell neoplasm of the Tenosynoviumdiffuse giant cell tumor of tendon sheathdiffuse giant cell tumor of Tenosynoviumdiffuse giant cell tumor of the Tenosynoviumdiffuse giant cell tumour of tendon sheathdiffuse giant cell tumour of Tenosynoviumdiffuse giant cell tumour of the Tenosynoviumdiffuse pigmented villonodular synovitisdiffuse tenosynovial giant cell neoplasmdiffuse tenosynovial giant cell tumordiffuse tenosynovial giant cell tumourdiffuse-type GCTdiffuse-type giant cell tumordiffuse-type giant cell tumourlocalised pigmented villonodular synovitislocalized pigmented villonodular synovitispigmented villonodular synovitistenosynovial giant cell tumor diffuse type

Summary

Tenosynovial giant cell tumor, diffuse type (MONDO:0024686) is a cancer and 16 clinical trials. Top therapeutic interventions include nilotinib, pexidartinib, and vimseltinib. A subtype of tenosynovial giant cell tumor — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • Classification: Cancer
  • Prevalence: 1-5 / 10 000 (Europe) [Orphanet-validated]
  • Phenotypes (HPO): 24
  • Clinical trials: 16

Clinical features

Epidemiology

Prevalence records

1 prevalence record(s), Orphanet:

TypeClassValueGeographyValidation
Point prevalence1-5 / 10 00020EuropeValidated

Signs & symptoms

Clinical features (HPO)

24 HPO clinical features (Orphanet curated; top 24 by frequency):

HPO IDTermFrequency
HP:0002829ArthralgiaVery frequent (80-99%)
HP:0001369ArthritisFrequent (30-79%)
HP:0001376Limitation of joint mobilityFrequent (30-79%)
HP:0001386Joint swellingFrequent (30-79%)
HP:0001387Joint stiffnessFrequent (30-79%)
HP:0002797OsteolysisFrequent (30-79%)
HP:0002815Abnormality of the kneeFrequent (30-79%)
HP:0005261Joint hemorrhageFrequent (30-79%)
HP:0000372Abnormality of the auditory canalOccasional (5-29%)
HP:0000405Conductive hearing impairmentOccasional (5-29%)
HP:0001003Multiple lentiginesOccasional (5-29%)
HP:0001004LymphedemaOccasional (5-29%)
HP:0001384Abnormality of the hip jointOccasional (5-29%)
HP:0003019Abnormality of the wristOccasional (5-29%)
HP:0003028Abnormality of the anklesOccasional (5-29%)
HP:0003043Abnormality of the shoulderOccasional (5-29%)
HP:0009811Abnormality of the elbowOccasional (5-29%)
HP:0009911Abnormal temporal bone morphologyOccasional (5-29%)
HP:0031520Groin painOccasional (5-29%)
HP:0040090Abnormality of the tympanic membraneOccasional (5-29%)
HP:0000934ChondrocalcinosisVery rare (<1-4%)
HP:0005186Synovial hypertrophyVery rare (<1-4%)
HP:0005195Polyarticular arthropathyVery rare (<1-4%)
HP:0040161Localized osteoporosisVery rare (<1-4%)

Identifiers

Disease identifiers

FieldValue
Canonical nametenosynovial giant cell tumor, diffuse type
Mondo IDMONDO:0024686
MeSHD013586
Orphanet66627
DOIDDOID:2702, DOID:9898
ICD-10-CMM12.2
NCITC3401
SNOMED CT95412009
UMLSC0039106
MedGen11691
GARD0007396
NORD1916
Is cancer (heuristic)yes

Also known as: diffuse giant cell neoplasm of tendon sheath · diffuse giant cell neoplasm of Tenosynovium · diffuse giant cell neoplasm of the Tenosynovium · diffuse giant cell tumor of tendon sheath · diffuse giant cell tumor of Tenosynovium · diffuse giant cell tumor of the Tenosynovium · diffuse giant cell tumour of tendon sheath · diffuse giant cell tumour of Tenosynovium · diffuse giant cell tumour of the Tenosynovium · diffuse pigmented villonodular synovitis · diffuse tenosynovial giant cell neoplasm · diffuse tenosynovial giant cell tumor · diffuse tenosynovial giant cell tumour · diffuse-type GCT · diffuse-type giant cell tumor · diffuse-type giant cell tumour · localised pigmented villonodular synovitis · localized pigmented villonodular synovitis · pigmented villonodular synovitis · tenosynovial giant cell tumor diffuse type (+7 more)

Disease family

This is a subtype of tenosynovial giant cell tumor. Genetic, therapeutic, and trial evidence is largely curated at the broader-term level — see the parent page for the associated-gene cohort and molecular evidence.

Classification path: disease › human disease › disease by etiologic mechanism › cancer or benign tumorneoplastic disease or syndromeneoplasmgiant cell tumortenosynovial giant cell tumortenosynovial giant cell tumor, diffuse type

Related subtypes (2): tenosynovial giant cell tumor, localized type, malignant tenosynovial giant cell tumor

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

No tiered GWAS variants or ClinVar records for this disease.

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

Drugs indicated for this disease

0 approved, 4 in late-stage (phase 3) trials. Disease-direct ChEMBL indications, not inferred from the associated-gene cohort below.

DrugDevelopment status
EmactuzumabPhase 3 (in late-stage trials)
PexidartinibPhase 3 (in late-stage trials)
PimicotinibPhase 3 (in late-stage trials)
VimseltinibPhase 3 (in late-stage trials)

Earlier-phase candidates (phase 2, investigational — efficacy not yet established): Nilotinib.

Clinical trials & evidence

Clinical trials

Clinical trials: 16.

Phase distribution (across all retrieved trials)

PhaseTrials
PHASE26
PHASE34
Not specified3
PHASE1/PHASE22
PHASE11

Top trials by phase / activity

NCTPhaseStatusTitle
NCT05059262PHASE3ACTIVE_NOT_RECRUITINGStudy of Vimseltinib for Tenosynovial Giant Cell Tumor
NCT05417789PHASE3ACTIVE_NOT_RECRUITINGStudy of Emactuzumab for Tenosynovial Giant Cell Tumor (TGCT)
NCT05804045PHASE3ACTIVE_NOT_RECRUITINGStudy of Pimicotinib (ABSK021) for Tenosynovial Giant Cell Tumor (MANEUVER)
NCT02371369PHASE3COMPLETEDPhase 3 Study of Pexidartinib for Pigmented Villonodular Synovitis (PVNS) or Giant Cell Tumor of the Tendon Sheath (GCT-TS)
NCT03069469PHASE1/PHASE2ACTIVE_NOT_RECRUITINGStudy of Vimseltinib (DCC-3014) in Patients With Advanced Tumors and Tenosynovial Giant Cell Tumor
NCT01207492PHASE2COMPLETEDNilotinib in Patients With Relapsed or Metastatic Pigmented Villonodular Synovitis/Tenosynovial Giant Cell Tumor/Diffuse-Type Giant Cell Tumor
NCT01261429PHASE2COMPLETEDStudy of Nilotinib Efficacy in Pigmented Villo-Nodular Synovitis/ Tenosynovial Giant Cell Tumour (PVNS/TGCT)
NCT01643850PHASE2COMPLETEDMCS110 in Patients With Pigmented Villonodular Synovitis (PVNS)
NCT02471716PHASE1/PHASE2COMPLETEDStudy of Cabiralizumab in Patients With Pigmented Villonodular Synovitis / Diffuse Type Tenosynovial Giant Cell Tumor
NCT04731675PHASE2COMPLETEDAn Open-Label Study of Intra-articular AMB-05X Injections in Subjects With Tenosynovial Giant Cell Tumor of the Knee
NCT04938180PHASE2TERMINATEDA Phase 2 Study of Intravenous AMB-05X in Tenosynovial Giant Cell Tumor Patients
NCT05349643PHASE2COMPLETEDA Study to Evaluate Safety and Efficacy of AMB-05X Injections in Subjects With TGCT
NCT05277454PHASE1UNKNOWNClinical Study of HMPL-653 in Treatment of Advanced Malignant Solid Tumors and TGCT
NCT06709911Not specifiedNOT_YET_RECRUITINGA Comparative Study of the Efficacy of Multimodal Interventions for Tenosynovitis
NCT04952896Not specifiedCOMPLETEDClinical Study of Magnetic Resonance Imaging and Deep Learning of Joint Synovial Disease
NCT04955535Not specifiedCOMPLETEDScreening of Specific Genes for Pigmented Villous Nodular Synovitis

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
NILOTINIB43
PEXIDARTINIB41
VIMSELTINIB32
EMACTUZUMAB31
CABIRALIZUMAB21