Toxic multinodular goitre

disease
On this page

Also known as MNGPlummer diseasePlummer's diseaseTMNGToxic goiterToxic goitretoxic nodular goitertoxic nodular goitre

Summary

Toxic multinodular goitre (MONDO:0001252) is a disease with 59 GWAS associations across 7 studies and 3 clinical trials. Top therapeutic interventions include methimazole. A subtype of primary hyperthyroidism — broader associated-gene and molecular evidence is on the parent page (see Disease family below).

At a glance

  • GWAS associations: 59
  • Clinical trials: 3

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical nametoxic multinodular goitre
Mondo IDMONDO:0001252
EFOEFO:0009191
DOIDDOID:11277
ICD-11999910988
NCITC35171
SNOMED CT57777000
UMLSC0342127
MedGen137963
Is cancer (heuristic)no

Also known as: MNG · Plummer disease · Plummer’s disease · TMNG · Toxic goiter · Toxic goitre · toxic nodular goiter · toxic nodular goitre

Data availability: 59 GWAS associations (7 studies).

Disease family

Classification path: disease › human disease › disease by body system or component › endocrine system disorderthyroid gland disorderhyperthyroidism › primary hyperthyroidism › toxic multinodular goitre

Related subtypes (2): Graves disease, toxic thyroid adenoma

Genetics & variants

GWAS landscape

59 GWAS associations across 7 studies. Top hits map to 22 distinct genes (as reported by GWAS).

Top associations by p-value

rsIDp-valueGeneRisk alleleOdds ratio
rs733982643e-108FAM227BT0.26
rs12039301e-86LNCNEF - LINC01747A0.23
rs174779232e-81FAM227BT0.25
rs99717701e-65MSRB3-AS1?
rs109174693e-47MICOS10A0.19
rs3347006e-44NFIAA0.26
rs124612067e-41INSRA0.19
rs735750864e-37MAFTRR, LINC01229T0.14
rs124315022e-36ITPK1G0.2
rs667603201e-31SCIRTC0.13
rs1169093741e-31LINC00609 - MBIPC0.39
rs1426988373e-31TGG1.16
chr14:935853314e-31G0.18
rs37587233e-30PRDM11T0.13
rs43387404e-29FGF7, FAM227BT0.3
chr8:1338836717e-29C0.43
rs107998242e-28MICOS10G0.25
chr11:452378585e-28T0.14
chr1:616190566e-27C0.28
rs45789732e-24LINC00887C0.13
rs12039255e-21LNCNEF - LINC01747G0.19
chr1:2186529907e-21A0.12
rs5553104828e-21LINC01603C0.1
rs735750853e-20LINC01229, MAFTRRG0.2
rs6757632e-18LINC02869A0.1
rs9254882e-17PTCSC2G0.23
chr20:558942998e-17T0.17
chr12:660442841e-16G0.18
rs72077814e-16BCAS3A0.15
rs60856571e-14CASC20 - LINC01713A0.1

Top studies (by case count)

StudyLead authorYearCasesControlsTitle
GCST90475638Verma A202415,286431,005Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90651136Liu TY20257,924212,391Diversity and longitudinal records: Genetic architecture of disease associations and polygenic risk in the Taiwanese Han population.
GCST90475637Verma A20245,733114,463Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90479862Verma A20245,733114,463Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90475636Verma A20241,42057,947Diversity and scale: Genetic architecture of 2068 traits in the VA Million Veteran Program.
GCST90435685Zhou W20181,143391,429Efficiently controlling for case-control imbalance and sample relatedness in large-scale genetic association studies.
GCST90435686Zhou W2018472391,429Efficiently controlling for case-control imbalance and sample relatedness in large-scale genetic association studies.

Variant details and genetic-evidence tiers

Tier distribution (top 50 variants)

TierVariants
Tier 1: coding1
Tier 2: splice/UTR0
Tier 3: regulatory0
Tier 4: intronic/intergenic46

MAF distribution

BucketVariants
common (>=0.05)44
low_freq (0.01-0.05)2
rare (<0.01)1
unknown0

Functional consequences

ConsequenceCount
intron_variant26
unknown15
intergenic_variant3
non_coding_transcript_exon_variant2
missense_variant1

Top variants

rsIDChrPosAllelesMAFConsequenceGenep-valueTier
rs733982641549414220T>C0.22intron_variantFAM227B3e-108Tier 4: intronic/intergenic
rs12039302022610197A>G,T0.292intergenic_variantLNCNEF - LINC017471e-86Tier 4: intronic/intergenic
rs174779231549418988T>C0.248intron_variantFAM227B2e-81Tier 4: intronic/intergenic
rs99717701265639270G>A,C,T0.05intron_variantMSRB3-AS11e-65Tier 4: intronic/intergenic
rs10917469119517082A>G,T0.167intron_variantMICOS103e-47Tier 4: intronic/intergenic
rs334700161153791A>C,G,T0.085intron_variantNFIA6e-44Tier 4: intronic/intergenic
rs12461206197235439A>C,T0.196intron_variantINSR7e-41Tier 4: intronic/intergenic
rs735750861679714588T>A,C0.296intron_variantMAFTRR, LINC012294e-37Tier 4: intronic/intergenic
rs124315021493097919G>A0.159intron_variantITPK12e-36Tier 4: intronic/intergenic
rs66760320643938518C>T0.277intron_variantSCIRT1e-31Tier 4: intronic/intergenic
rs1169093741436269155C>T0.024non_coding_transcript_exon_variantLINC00609 - MBIP1e-31Tier 4: intronic/intergenic
rs1426988378132869781G>A0.001missense_variantTG3e-31Tier 1: coding
chr14:935853310.1974e-31Tier 4: intronic/intergenic
rs37587231145221961T>C0.252intron_variantPRDM113e-30Tier 4: intronic/intergenic
rs43387401549443100T>C0.13intron_variantFGF7, FAM227B4e-29Tier 4: intronic/intergenic
chr8:1338836710.0247e-29Tier 4: intronic/intergenic
rs10799824119514680G>A0.241intron_variantMICOS102e-28Tier 4: intronic/intergenic
chr11:452378580.2775e-28Tier 4: intronic/intergenic
chr1:616190560.1726e-27Tier 4: intronic/intergenic
rs45789733194200845C>T0.21non_coding_transcript_exon_variantLINC008872e-24Tier 4: intronic/intergenic
rs12039252022608135G>A,C0.493intergenic_variantLNCNEF - LINC017475e-21Tier 4: intronic/intergenic
chr1:2186529900.4037e-21Tier 4: intronic/intergenic
rs555310482869445688C>A,T0.339intron_variantLINC016038e-21Tier 4: intronic/intergenic
rs735750851679714179G>C0.264intron_variantLINC01229, MAFTRR3e-20Tier 4: intronic/intergenic
rs6757631218508777A>C,G,T0.38intron_variantLINC028692e-18Tier 4: intronic/intergenic
rs925488997784109G>A0.209intron_variantPTCSC22e-17Tier 4: intronic/intergenic
chr20:558942990.4448e-17Tier 4: intronic/intergenic
chr12:660442840.2981e-16Tier 4: intronic/intergenic
rs72077811761253946A>C0.084intron_variantBCAS34e-16Tier 4: intronic/intergenic
rs6085657206702192A>C,G0.389intergenic_variantCASC20 - LINC017131e-14Tier 4: intronic/intergenic

Genes & proteins

No associated-gene cohort resolved for this disease. Atlas builds the molecular and therapeutic sections — associated genes, protein families, druggability, pathways, interactions, and drug associations — by aggregating over a disease’s associated genes (resolved via GWAS / GenCC / ClinVar / CIViC), and none resolved here. This is expected for antibody-mediated, autoimmune, or otherwise non-gene-defined conditions; the curated evidence for this disease is its clinical features, GWAS susceptibility, and clinical trials (above).

Function

No pathway enrichment — requires an associated-gene cohort.

Therapeutics

No druggable-target or therapeutic data for this disease’s cohort.

Clinical trials & evidence

Clinical trials

Clinical trials: 3.

Phase distribution (across all retrieved trials)

PhaseTrials
PHASE42
Not specified1

Top trials by phase / activity

NCTPhaseStatusTitle
NCT00150124PHASE4COMPLETEDBlock-replacement Therapy During Radioiodine Therapy
NCT00150137PHASE4COMPLETEDAntithyroid Drugs During Radioiodine Therapy
NCT05774535Not specifiedWITHDRAWNProspective, Observational Study on the Carotid Intima-media Thickness in Patients Undergoing Thyroid Surgery

Drugs tested across these trials (top 30)

MoleculeMax phaseTrials referencing
METHIMAZOLE42