Wilms tumor 2

disease
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Also known as familial Wilms tumor 2familial Wilms tumour 2FWT2Wilms tumor 2, autosomal dominant, somatic mutationWilms tumor type 2Wilms tumour 2, autosomal dominant, somatic mutationWilms tumour type 2WT2

Summary

Wilms tumor 2 (MONDO:0008680) is a cancer with 2 cohort genes.

At a glance

  • Classification: Cancer
  • Cohort genes: 2
  • ClinVar variants: 2

Clinical features

No curated clinical features (Orphanet) for this disease.

Identifiers

Disease identifiers

FieldValue
Canonical nameWilms tumor 2
Mondo IDMONDO:0008680
MeSHC536853
OMIM194071
UMLSC3887743
MedGen854562
GARD0008559
Is cancer (heuristic)yes

Also known as: familial Wilms tumor 2 · familial Wilms tumour 2 · FWT2 · Wilms tumor 2 · Wilms tumor 2, autosomal dominant, somatic mutation · Wilms tumor type 2 · Wilms tumour 2, autosomal dominant, somatic mutation · Wilms tumour type 2 · WT2

Data availability: 2 ClinVar variants.

Disease family

Classification path: disease › human disease › disease by etiologic mechanism › disease of genetic or genomic mechanism › hereditary diseasehereditary Wilms tumorWilms tumor 2

Related subtypes (6): Wilms tumor 1, Wilms tumor 3, Wilms tumor 4, Wilms tumor 5, Wilms tumor 6, Wilms tumor 7

Genetics & variants

GWAS landscape

No GWAS associations recorded — common-variant (GWAS) studies don’t cover this disease (typical for Mendelian / rare diseases). See the curated gene cohort and Mendelian overlap below.

Variant details and genetic-evidence tiers

ClinVar germline variants

2 retrieved; paginated sample, class counts are floors:

2 pathogenic

ClinVarVariant (HGVS)GeneClassificationReview
162493NR_002196.1(H19):n.-7080_-1781delH19Pathogenicno assertion criteria provided
162494GRCh38/hg38 11p15.5(chr11:2000799-2001783)x3MRPL23Pathogenicno assertion criteria provided

Genes & proteins

Mendelian disease overlap and somatic drivers

GenCC: 0 · Orphanet: 6 · OMIM-shared: 0 · Dual-evidence (GWAS+Mendelian): 0

Orphanet rare-disease linkage (cohort genes)

GeneOrphanet IDRare disease
H19Orphanet:2128Isolated hemihyperplasia
H19Orphanet:231117Beckwith-Wiedemann syndrome due to imprinting defect of 11p15
H19Orphanet:231127Beckwith-Wiedemann syndrome due to 11p15 microdeletion
H19Orphanet:231140Silver-Russell syndrome due to an imprinting defect of 11p15
H19Orphanet:231144Silver-Russell syndrome due to 11p15 microduplication
H19Orphanet:654Nephroblastoma

Cohort genes → proteins

2 cohort genes, 1 distinct canonical proteins.

Evidence partition

SubsetGenes
multi_evidence2

Cohort genes (full)

SymbolHGNCEnsemblUniProtNameEvidence
MRPL23HGNC:10322ENSG00000214026Q16540Large ribosomal subunit protein uL23mclinvar
H19HGNC:4713ENSG00000130600H19 imprinted maternally expressed transcriptclinvar

Protein-family classification

Druggable: 0 · Difficult: 0 · Unknown: 2 · Druggable fraction: 0.0

Family distribution

Cohort families vs a genome-wide background (hypergeometric, BH-FDR; fold = observed/expected). Counts kept; sorted by enrichment, so the catch-all Other/Unknown bucket no longer leads.

FamilyGenesFoldFDR
Other/Unknown21.8×0.312

Per-gene assignment

SymbolFamilyDruggable?ECInterPro (top 3)
MRPL23Other/UnknownnoNucleotide-bd_a/b_plait_sf, Ribosomal_uL23/eL15/eS24_sf, Ribosomal_uL23-like
H19Other/Unknownno

Expression context

Cohort genes with no expression data: 0.

2 cohort genes are a single-cell marker in ≥1 SCXA experiment.

Breadth distribution (Bgee present_calls)

BucketGenes
narrow (1-5 tissues)0
moderate (6-20)0
broad (>20)2
unknown0

Top tissues across cohort

TissueCohort genes
apex of heart1
olfactory segment of nasal mucosa1
right uterine tube1
adrenal tissue1
hindlimb stylopod muscle1
placenta1

Per-gene tissue summary (top 30)

SymbolBgee breadthFANTOM5 breadthSCXATop tissues
MRPL23134ubiquitousmarkerolfactory segment of nasal mucosa, apex of heart, right uterine tube
H19134broadmarkerplacenta, adrenal tissue, hindlimb stylopod muscle

Protein interactions among cohort

Intra-cohort edges: 0.

Hub genes (top 10 by interactor count)

SymbolInteractor count
MRPL232,519
H190

Structural data

PDB: 1 · AlphaFold-only: 0 · No structure: 1

Cohort genes with PDB structures (top 30)

SymbolUniProtPDB entries
MRPL23Q1654086

Function

Pathway analysis

Distinct Reactome pathways touched by cohort: 7. Enrichment computed across 2 evidence-associated genes (1 with Reactome annotation).

Pathways by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

PathwayCohort genesFoldFDRSample cohort genes
Mitochondrial translation1137.6×0.013MRPL23
Mitochondrial translation initiation1126.9×0.013MRPL23
Mitochondrial translation elongation1126.9×0.013MRPL23
Mitochondrial ribosome-associated quality control1122.8×0.013MRPL23
Mitochondrial translation termination1109.8×0.013MRPL23
Translation162.1×0.019MRPL23
Metabolism of proteins112.4×0.081MRPL23

GO biological processes by enrichment

Over-representation of cohort genes vs the genome-wide background (hypergeometric test, Benjamini-Hochberg FDR; fold = observed/expected over 1 annotated cohort genes). Counts and members are kept as ground-truth; sorted by enrichment.

GO termCohort genesFoldFDRSample cohort genes
mitochondrial translation1173.7×0.010MRPL23
translation1102.8×0.010MRPL23

Therapeutics

Drug target analysis

Approved (phase 4): 0 · Phase ≥3: 0 · Phased (≥1): 0 · Undrugged: 2

Druggability breadth: 0 of 2 evidence-associated genes (0%) have a ChEMBL target (buckets above are over the deeply-mined display cohort).

Top cohort targets by molecule count

SymbolMoleculesMax phase
MRPL2300
H1900

Bioactivity and enzyme data

Enzyme cohort genes (≥1 EC): 0.

Pharmacogenomics

Cohort genes with a PharmGKB record: 2; with CPIC/DPWG dosing guidelines: 0.

No cohort gene has a CPIC/DPWG genotype-guided dosing guideline (PharmGKB).

Drug repurposing candidates

0 approved/phased drugs hit cohort targets but don’t yet appear in disease-level clinical trials. Target-inhibition rationale is strongest for cancer driver genes; a bioactivity hit is a screening signal, not a treatment claim.

Druggability pyramid

Cohort genes binned by druggability tier (high → low):

TierDefinitionGenesSymbols
AApproved (phase 4 drug)0
BPhased (≥1) drug, not yet approved0
CDruggable family + PDB, no drug0
DDruggable family + AlphaFold only, no drug0
EDifficult family or no structure, no drug2MRPL23, H19

Undrugged target profiles

2 cohort genes are undrugged. Ranked by ‘starting-point quality’ (assay depth + drugged-partner adjacency).

SymbolChEMBL assaysDrugged partners (top 3)
MRPL230
H190

Clinical trials & evidence

Clinical trials

Clinical trials: 0.