Etelcalcetide

drug
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Also known as EtelcalcetidaKAI-4169ONO-5163TelcalcetideVelcalcetide

Summary

Etelcalcetide (CHEMBL3545184) is an approved protein (ATC H05BX04) targeting CASR; indicated across 3 conditions including secondary hyperparathyroidism and parathyroid gland disorder.

At a glance

  • Status: Approved (max clinical phase 4)
  • Modality: Protein
  • ATC class: H05BX04
  • Targets: 1 (CASR)
  • Indications: 3 conditions
  • Clinical trials: 18
  • Chemistry: 1048.3 Da · C38H73N21O10S2

Identifiers

Drug identity and classification

FieldValue
ChEMBL IDCHEMBL3545184
NameEtelcalcetide
TypeProtein
Max phase4
FDA approvedyes
PubChem CID71511839
ATCH05BX04
Molecular formulaC38H73N21O10S2
Molecular weight1048.3
InChIKeyANIAZGVDEUQPRI-ZJQCGQFWSA-N

SMILES: C[C@H](C(=O)N[C@H](CCCN=C(N)N)C(=O)N)NC(=O)[C@@H](CCCN=C(N)N)NC(=O)[C@@H](CCCN=C(N)N)NC(=O)[C@@H](CCCN=C(N)N)NC(=O)[C@@H](C)NC(=O)[C@@H](CSSC[C@@H](C(=O)O)N)NC(=O)C

IUPAC name: (2R)-3-[[(2S)-2-acetamido-3-[[(2R)-1-[[(2R)-1-[[(2R)-1-[[(2R)-1-[[(2R)-1-[[(2R)-1-amino-5-(diaminomethylideneamino)-1-oxopentan-2-yl]amino]-1-oxopropan-2-yl]amino]-5-(diaminomethylideneamino)-1-oxopentan-2-yl]amino]-5-(diaminomethylideneamino)-1-oxopentan-2-yl]amino]-5-(diaminomethylideneamino)-1-oxopentan-2-yl]amino]-1-oxopropan-2-yl]amino]-3-oxopropyl]disulfanyl]-2-aminopropanoic acid

Also known as: Etelcalcetida, Etelcalcetide, KAI-4169, ONO-5163, Telcalcetide, Velcalcetide, ETELCALCETIDE

Parent form; salt/anhydrous children: CHEMBL3545183

Patent coverage: 265 distinct patent families (575 SureChEMBL compound mentions), from 2 matched compound structure(s). One matched structure accounts for 469 (82%) of the total. Mentions count patents naming the compound (not distinct inventions), so promiscuous / reference molecules inflate the mention figure — families are the dedup metric.

Targets

Targets

Primary targets (GtoPdb curated mechanism): the Cancer dependency column is the DepMap CRISPR fitness signal (% of screened cell lines dependent on the target).

GeneTargetActionpAffinityCancer dependencyUniProt
CASRCaS receptorPositive4.60.1%P41180

Bioactivity

No ChEMBL bioactivity rows at pChembl ≥ 5 (expected for biologics / antibodies).

Target pathways

Aggregated over 1 target gene(s): CASR.

Top Reactome pathways

7 total, by targets touching each:

PathwayTargetsGenes
Signal Transduction1CASR
Signaling by GPCR1CASR
GPCR downstream signalling1CASR
G alpha (q) signalling events1CASR
G alpha (i) signalling events1CASR
Class C/3 (Metabotropic glutamate/pheromone receptors)1CASR
GPCR ligand binding1CASR

Dominant GO biological processes

GO termTargets
ossification1
response to ischemia1
detection of calcium ion1
intracellular calcium ion homeostasis1
G protein-coupled receptor signaling pathway1
adenylate cyclase-inhibiting G protein-coupled receptor signaling pathway1
phospholipase C-activating G protein-coupled receptor signaling pathway1
JNK cascade1
chemosensory behavior1
positive regulation of cell population proliferation1
anatomical structure morphogenesis1
positive regulation of gene expression1
positive regulation of insulin secretion1
bile acid secretion1
cellular response to hepatocyte growth factor stimulus1

Indications & clinical

Indications

3 indications (2 at ChEMBL trial phase 4). Phase below is the highest clinical-trial phase recorded for this drug against each disease — not the molecule’s overall approval status (that is in the Summary).

IndicationTrial phaseMONDOEFO
secondary hyperparathyroidism4MONDO:0006964EFO:1001173
parathyroid gland disorder4MONDO:0001223EFO:0005754
chronic kidney disease1MONDO:0005300EFO:0003884

Clinical trials

Total trials: 18.

Phase distribution

PhaseTrials
PHASE39
PHASE25
PHASE14

Top trials by phase / activity

NCTPhaseStatusTitle
NCT03633708PHASE3RECRUITINGA Trial of Etelcalcetide in Pediatric Participants With Secondary Hyperparathyroidism and Chronic Kidney Disease on Hemodialysis
NCT03969329PHASE3RECRUITINGA Phase 3 Study of Etelcalcetide in Children With Secondary Hyperparathyroidism Receiving Hemodialysis
NCT01785849PHASE3COMPLETEDEfficacy and Safety of Etelcalcetide (AMG 416) in the Treatment of Secondary Hyperparathyroidism (SHPT) in Patients With Chronic Kidney Disease on Hemodialysis
NCT01785875PHASE3COMPLETEDExtension Study of Etelcalcetide in the Treatment of Secondary Hyperparathyroidism (SHPT) in Patients With Chronic Kidney Disease (CKD) on Hemodialysis
NCT01788046PHASE3COMPLETEDEfficacy and Safety of Etelcalcetide (AMG 416) in the Treatment of Secondary Hyperparathyroidism (SHPT) in Patients With Chronic Kidney Disease (CKD) on Hemodialysis
NCT01896232PHASE3COMPLETEDHead-to-Head Study of Etelcalcetide (AMG 416) and Cinacalcet
NCT01932970PHASE3COMPLETEDStudy to Assess the Impact on Calcium Levels When Hemodialysis Patients With Secondary Hyperparathyroidism (SHPT) Switch From Cinacalcet to Etelcalcetide
NCT02102204PHASE3COMPLETEDExtension Study of Etelcalcetide for Treatment of Secondary Hyperparathyroidism in Patients With Chronic Kidney Disease on Hemodialysis
NCT03299244PHASE3COMPLETEDHead-to-Head Study of Etelcalcetide and Cinacalcet in Asian Hemodialysis Patients With Secondary Hyperparathyroidism (SHPT)
NCT01254565PHASE2COMPLETEDSafety, Tolerability and Efficacy of Etelcalcetide in Hemodialysis Patients With Secondary Hyperparathyroidism
NCT01414114PHASE2COMPLETEDEtelcalcetide to Treat Secondary Hyperparathyroidism in Hemodialysis Patients With Chronic Kidney Disease-Mineral and Bone Disorder
NCT01576146PHASE2TERMINATEDOpen-label Study to Assess the Long-term Safety and Efficacy of Etelcalcetide (Also Known as AMG 416 or KAI-4169) in Patients With Secondary Hyperparathyroidism
NCT03795558PHASE2COMPLETEDA Study to Investigate the Influence of PTH-lowering by Etelcalcetide (Parsabiv®) on the Calcification Propensity of Serum in Dialysis Patients
NCT03960437PHASE2COMPLETEDThe Effect of Etelcalcetide on CKD-MBD
NCT01134549PHASE1COMPLETEDSafety, Tolerability and Pharmacokinetics of Etelcalcetide in Healthy Male Volunteers
NCT01134562PHASE1COMPLETEDSafety, Tolerability and Pharmacokinetics of Etelcalcetide in Hemodialysis Patients With Secondary Hyperparathyroidism
NCT02833857PHASE1COMPLETEDA Single-dose Study in Paediatric Patients Aged 2 to Less Than 18 Years With Secondary Hyperparathyroidism (sHPT) Receiving Haemodialysis
NCT03283098PHASE1COMPLETEDA Phase 1 Study to Evaluate PK, Safety and Tolerability of AMG 416

Clinical evidence (CIViC)

No CIViC predictive evidence (expected for non-precision-medicine drugs).

Pharmacology

Pharmacogenomics

No PharmGKB pharmacogenomic data curated for this drug.

Molecules sharing ≥1 of this drug’s curated primary targets, merged from two biobtree sources and ranked by shared-target count, then clinical phase: ChEMBL clinical-stage candidates (development phase ≥2) and PubChem drug-class bioactivity (approved / known drugs acting on the target). Deduplicated by drug name; the drug’s own salt forms are excluded. Note: for a drug with few primary targets a shared-target match can reflect off-target / promiscuous binding rather than the same therapeutic mechanism — the phase ordering surfaces bona-fide therapeutics first.

8 molecules share ≥1 primary target. Top 8 by shared-target count:

MoleculeSourceStatusShared targets
CINACALCETChEMBL + PubChemPhase 4 (approved)CASR
ENCALERETChEMBLPhase 3CASR
EVOCALCETChEMBLPhase 3CASR
FENDILINEChEMBLPhase 2CASR
RONACALERETChEMBLPhase 2CASR
SB-423562ChEMBLPhase 2CASR
TECALCETChEMBLPhase 2CASR
tryptophanPubChemApprovedCASR