Tasimelteon

drug
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Also known as BMS-214,778BMS-214778HetliozHetlioz lqVEC-162

Summary

Tasimelteon (CHEMBL2103822) is an approved small-molecule melatonin receptor agonist (ATC N05CH03) targeting MTNR1A and MTNR1B; indicated across 9 conditions including sleep-wake disorder and circadian rhythm sleep disorder.

At a glance

  • Status: Approved (max clinical phase 4)
  • Modality: Small molecule
  • ATC class: N05CH03
  • Targets: 2 (MTNR1A, MTNR1B)
  • Indications: 9 conditions
  • Clinical trials: 25
  • Chemistry: 245.32 Da · C15H19NO2

Identifiers

Drug identity and classification

FieldValue
ChEMBL IDCHEMBL2103822
NameTasimelteon
TypeSmall molecule
Max phase4
FDA approvedyes
PubChem CID10220503
ChEBICHEBI:79042
ATCN05CH03
Molecular formulaC15H19NO2
Molecular weight245.32
InChIKeyPTOIAAWZLUQTIO-GXFFZTMASA-N

SMILES: CCC(=O)NC[C@@H]1C[C@H]1C2=C3CCOC3=CC=C2

IUPAC name: N-[[(1R,2R)-2-(2,3-dihydro-1-benzofuran-4-yl)cyclopropyl]methyl]propanamide

ChEBI definition: A member of the class of 1-benzofurans that is propionamide in which one of the amide hydrogens is replaced by a [(1R,2R)-2-(2,3-dihydro-1-benzofuran-4-yl)cyclopropyl]methyl group. A melatonin receptor agonist used for the treatment of non-24-hour sleep-wake disorder.

Pharmacological roles (ChEBI): melatonin receptor agonist.

Also known as: BMS-214,778, BMS-214778, Hetlioz, Hetlioz lq, Tasimelteon, VEC-162, TASIMELTEON

Patent coverage: 185 distinct patent families (516 SureChEMBL compound mentions), from 2 matched compound structure(s). One matched structure accounts for 375 (73%) of the total. Mentions count patents naming the compound (not distinct inventions), so promiscuous / reference molecules inflate the mention figure — families are the dedup metric.

Targets

Targets

Primary targets (GtoPdb curated mechanism): the Cancer dependency column is the DepMap CRISPR fitness signal (% of screened cell lines dependent on the target).

GeneTargetActionpAffinityCancer dependencyUniProt
MTNR1AMT1 receptorFull agonist9.50%P48039
MTNR1BMT2 receptorFull agonist10.20.2%P49286

Broader ChEMBL bioactivity targets: 1 (assay-derived). Sample: Melatonin receptor type 1B.

Bioactivity

ChEMBL activities: 1 potent at pChembl ≥ 5 of 1 total. Top 30 by potency (10 = 0.1 nM, 6 = 1 µM):

TargetpChemblTypeValueUnitActivity ID
MTNR1B10.15Ki0.07nMCHEMBL_ACT_25521263

Target pathways

Aggregated over 2 target gene(s): MTNR1A, MTNR1B.

Top Reactome pathways

6 total, by targets touching each:

PathwayTargetsGenes
Signal Transduction2MTNR1A, MTNR1B
Signaling by GPCR2MTNR1A, MTNR1B
Class A/1 (Rhodopsin-like receptors)2MTNR1A, MTNR1B
GPCR downstream signalling2MTNR1A, MTNR1B
G alpha (i) signalling events2MTNR1A, MTNR1B
GPCR ligand binding2MTNR1A, MTNR1B

Dominant GO biological processes

GO termTargets
G protein-coupled receptor signaling pathway2
G protein-coupled receptor signaling pathway, coupled to cyclic nucleotide second messenger2
signal transduction2
adenylate cyclase-inhibiting G protein-coupled receptor signaling pathway1
mating behavior1
circadian rhythm1
chemical synaptic transmission1
negative regulation of receptor guanylyl cyclase signaling pathway1
glucose homeostasis1
camera-type eye development1
negative regulation of neuron apoptotic process1
negative regulation of vasoconstriction1
positive regulation of circadian sleep/wake cycle, non-REM sleep1
negative regulation of insulin secretion1
regulation of insulin secretion1

Indications & clinical

Indications

9 indications (4 at ChEMBL trial phase 4). Phase below is the highest clinical-trial phase recorded for this drug against each disease — not the molecule’s overall approval status (that is in the Summary).

IndicationTrial phaseMONDOEFO
sleep-wake disorder4MONDO:0003406MONDO:0003406
circadian rhythm sleep disorder4MONDO:0024361MONDO:0024361
Smith-Magenis syndrome4MONDO:0008434Orphanet:68335
insomnia3MONDO:0013600EFO:0004698
major depressive disorder2MONDO:0002009MONDO:0002009
liver disorder1MONDO:0005154EFO:0001421
kidney disorder1MONDO:0005240EFO:0003086
REM sleep behavior disorder0MONDO:0005937EFO:0007462

1 further indication record had no mapped disease name (EFO/MeSH-only) or were duplicates, and are omitted.

Clinical trials

Total trials: 25.

Phase distribution

PhaseTrials
PHASE310
PHASE110
PHASE2/PHASE32
PHASE22
EARLY_PHASE11

Top trials by phase / activity

NCTPhaseStatusTitle
NCT04652882PHASE3RECRUITINGEvaluating the Effects of Tasimelteon vs. Placebo in Delayed Sleep-Wake Phase Disorder (DSWPD)
NCT06701396PHASE3RECRUITINGEvaluating the Effects of Tasimelteon Vs. Placebo in Delayed Sleep-Wake Phase Disorder (DSWPD) and the CRY1Δ11 Variant
NCT06953869PHASE3RECRUITINGEvaluating the Effects of Tasimelteon vs. Placebo in Treating Pediatric Insomnia
NCT00291187PHASE3COMPLETEDVEC-162 Study in Healthy Adult Volunteers in a Model of Insomnia
NCT00548340PHASE3COMPLETEDVEC-162 Study in Adult Patients With Primary Insomnia
NCT01163032PHASE3COMPLETEDEfficacy and Safety of Tasimelteon Compared With Placebo in Totally Blind Subjects With Non-24-Hour Sleep-Wake Disorder
NCT01218789PHASE3UNKNOWNSafety Study of Tasimelteon for Treatment of Non-24-Hour-Sleep-Wake Disorder in Blind Individuals With No Light Perception
NCT01428661PHASE2/PHASE3COMPLETEDMelatonin Agonist Effects of Tasimelteon Versus Placebo in Patients With Major Depressive Disorder
NCT01429116PHASE3COMPLETEDTasimelteon for the Treatment of Non-24-hour Sleep-Wake Disorder (N24HSWD) in Blind Individuals With no Light Perception
NCT01430754PHASE3COMPLETEDWithdrawal Study to Demonstrate the Maintenance Effect in the Treatment of Non-24-Hour Sleep-Wake Disorder
NCT02231008PHASE2/PHASE3COMPLETEDEvaluating the Effects of Tasimelteon vs Placebo on Sleep Disturbances in SMS
NCT03373201PHASE3COMPLETEDEvaluating the Effects of Tasimelteon vs. Placebo on Jet Lag Type Insomnia
NCT00490945PHASE2COMPLETEDSafety and Efficacy of VEC-162 on Circadian Rhythm in Healthy Adult Volunteers
NCT03291041PHASE2COMPLETEDA Proof of Concept Study to Evaluate the Effects of Tasimelteon and Placebo in Travelers With Jet Lag Disorder
NCT01271387PHASE1COMPLETEDPharmacokinetics of Tasimelteon in Subjects With Mild or Moderate Hepatic Impairment
NCT01402076PHASE1COMPLETEDA Study to Assess the Effect Tasimelteon on the Cytochrome P450 3A4 and 2C8 Enzymes in Healthy Subjects
NCT01477619PHASE1COMPLETEDEffects of Smoking, Age and Body Size on Pharmacokinetics, Safety and Tolerability on Tasimelteon in Healthy Subjects
NCT01526746PHASE1COMPLETEDPharmacokinetics of Tasimelteon in Subjects With Renal Impairment and Matched Control Subjects With Relatively Normal Renal Function
NCT01540500PHASE1COMPLETEDPharmacokinetics of Tasimelteon Alone and in Combination With CYP1A2 Inhibitor, Fluvoxamine
NCT01578057PHASE1COMPLETEDEvaluation of the Pharmacodynamic and Pharmacokinetic Interactions of Tasimelteon and Ethanol
NCT01637636PHASE1COMPLETEDPharmacokinetics of Tasimelteon Alone and in Combination With a CYP3A4 Inhibitor, Ketoconazole, or a CYP3A4 Inducer, Rifampin.
NCT02776215PHASE1COMPLETEDStudy of the Pharmacokinetics and Safety of Tasimelteon in Children and Adolescents
NCT05572281PHASE1COMPLETEDBioequivalence Study Between Tasimelteon Capsule Formulation and Liquid Suspension Formulation in Healthy Volunteers
NCT06323655PHASE1COMPLETEDEvaluation of Next-Day Residual Effects of Tasimelteon Compared With Placebo and Active Control in Healthy Subjects
NCT05922995EARLY_PHASE1TERMINATEDThe Effects of Tasimelteon in Participants With REM Behavior Disorder (RBD)

Clinical evidence (CIViC)

No CIViC predictive evidence (expected for non-precision-medicine drugs).

Pharmacology

Pharmacogenomics

No CPIC/DPWG dosing guideline or drug-level clinical/variant annotations in PharmGKB for this molecule.

Molecules sharing ≥1 of this drug’s curated primary targets, merged from two biobtree sources and ranked by shared-target count, then clinical phase: ChEMBL clinical-stage candidates (development phase ≥2) and PubChem drug-class bioactivity (approved / known drugs acting on the target). Deduplicated by drug name; the drug’s own salt forms are excluded. Note: for a drug with few primary targets a shared-target match can reflect off-target / promiscuous binding rather than the same therapeutic mechanism — the phase ordering surfaces bona-fide therapeutics first.

6 molecules share ≥1 primary target. Top 6 by shared-target count:

MoleculeSourceStatusShared targets
AGOMELATINEChEMBLPhase 4 (approved)MTNR1A, MTNR1B
CIANIDANOLChEMBLPhase 4 (approved)MTNR1A, MTNR1B
DOPAMINEChEMBLPhase 4 (approved)MTNR1A, MTNR1B
MELATONINChEMBLPhase 4 (approved)MTNR1A, MTNR1B
RAMELTEONChEMBLPhase 4 (approved)MTNR1A, MTNR1B
MEBUFOTENINChEMBLPhase 2MTNR1A, MTNR1B