Trihexyphenidyl

drug
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Also known as Apo-trihexNSC-12268TrihexifenidiloTrihexyphenidyleSID90341555SID50105266TRIHEXYPHENIDYL HYDROCHLORIDE

Summary

Trihexyphenidyl (CHEMBL1490) is an approved small molecule (ATC N04AA01) targeting CHRM1; indicated across 2 conditions including parkinson disease and dystonic disorder.

At a glance

  • Status: Approved (max clinical phase 4)
  • Modality: Small molecule
  • ATC class: N04AA01
  • Targets: 1 (CHRM1)
  • Indications: 2 conditions
  • Clinical trials: 4
  • Chemistry: 301.5 Da · C20H31NO

Identifiers

Drug identity and classification

FieldValue
ChEMBL IDCHEMBL1490
NameTrihexyphenidyl
TypeSmall molecule
Max phase4
FDA approvedyes
PubChem CID5572
ATCN04AA01
Molecular formulaC20H31NO
Molecular weight301.5
InChIKeyHWHLPVGTWGOCJO-UHFFFAOYSA-N

SMILES: C1CCC(CC1)C(CCN2CCCCC2)(C3=CC=CC=C3)O

IUPAC name: 1-cyclohexyl-1-phenyl-3-piperidin-1-ylpropan-1-ol

Also known as: Apo-trihex, NSC-12268, Trihexifenidilo, Trihexyphenidyl, Trihexyphenidyle, trihexyphenidyl, SID90341555, SID50105266, TRIHEXYPHENIDYLE, TRIHEXYPHENIDYL, TRIHEXYPHENIDYL HYDROCHLORIDE

Parent form; salt/anhydrous children: CHEMBL1092

Patent coverage: 3,454 distinct patent families (12,556 SureChEMBL compound mentions), from 1 matched compound structure(s). Mentions count patents naming the compound (not distinct inventions), so promiscuous / reference molecules inflate the mention figure — families are the dedup metric.

Targets

Targets

Primary targets (GtoPdb curated mechanism): the Cancer dependency column is the DepMap CRISPR fitness signal (% of screened cell lines dependent on the target).

GeneTargetActionpAffinityCancer dependencyUniProt
CHRM1M1 receptorAntagonist8.870.2%P11229

Broader ChEMBL bioactivity targets: 10 (assay-derived). Sample: Muscarinic acetylcholine receptor M4, Muscarinic acetylcholine receptor M5, Muscarinic acetylcholine receptor M2, 5-hydroxytryptamine receptor 1A, Muscarinic acetylcholine receptor M1, Mu-type opioid receptor, Voltage-gated inwardly rectifying potassium channel KCNH2, Muscarinic acetylcholine receptor M3, Sigma non-opioid intracellular receptor 1, Cytochrome P450 2D6.

Bioactivity

ChEMBL activities: 15 potent at pChembl ≥ 5 of 18 total. Top 100 by potency (10 = 0.1 nM, 6 = 1 µM):

TargetpChemblTypeValueUnitActivity ID
CHRM49.12Ki0.76nMCHEMBL_ACT_7782836
CHRM18.87Ki1.35nMCHEMBL_ACT_7782830
CHRM18.52AC503nMCHEMBL_ACT_25210174
CHRM38.5Ki3.15nMCHEMBL_ACT_7782834
CHRM48.26IC505.48nMCHEMBL_ACT_7782835
CHRM18.25IC505.61nMCHEMBL_ACT_7782829
CHRM58.06Ki8.68nMCHEMBL_ACT_7782838
CHRM27.92Ki12nMCHEMBL_ACT_7782832
CHRM57.92IC5012nMCHEMBL_ACT_7782837
CHRM37.82IC5015nMCHEMBL_ACT_7782833
CHRM27.8AC5016nMCHEMBL_ACT_25195689
CHRM27.47IC5034nMCHEMBL_ACT_7782831
SIGMAR17.35Ki45nMCHEMBL_ACT_7783590
SIGMAR16.97IC50108nMCHEMBL_ACT_7783589
CYP2D65.61IC502450nMCHEMBL_ACT_7782761

Target pathways

Aggregated over 1 target gene(s): CHRM1.

Top Reactome pathways

8 total, by targets touching each:

PathwayTargetsGenes
Signal Transduction1CHRM1
Signaling by GPCR1CHRM1
Class A/1 (Rhodopsin-like receptors)1CHRM1
Amine ligand-binding receptors1CHRM1
GPCR downstream signalling1CHRM1
Muscarinic acetylcholine receptors1CHRM1
G alpha (q) signalling events1CHRM1
GPCR ligand binding1CHRM1

Dominant GO biological processes

GO termTargets
signal transduction1
G protein-coupled receptor signaling pathway1
G protein-coupled receptor signaling pathway, coupled to cyclic nucleotide second messenger1
adenylate cyclase-inhibiting G protein-coupled acetylcholine receptor signaling pathway1
phospholipase C-activating G protein-coupled receptor signaling pathway1
phospholipase C-activating G protein-coupled acetylcholine receptor signaling pathway1
G protein-coupled acetylcholine receptor signaling pathway1
chemical synaptic transmission1
neuromuscular synaptic transmission1
nervous system development1
regulation of locomotion1
positive regulation of monoatomic ion transport1
saliva secretion1
cognition1
regulation of postsynaptic membrane potential1

Indications & clinical

Indications

1 approved indication. FDA phase 4, plus an anticancer drug’s labelled cancer uses (which ChEMBL often logs at phase 3).

IndicationPhaseMONDOEFO
Parkinson disease4MONDO:0005180MONDO:0005180

1 disease in clinical trials (phase 1–3, investigational — not approved indications). Highest ChEMBL trial phase per disease; a non-cancer approved use is occasionally logged at phase 3 here.

Disease (in trials)PhaseMONDOEFO
dystonic disorder2MONDO:0003441MONDO:0003441

Clinical trials

Total trials: 4.

Phase distribution

PhaseTrials
PHASE41
PHASE21
EARLY_PHASE11
PHASE11

Top trials by phase / activity

NCTPhaseStatusTitle
NCT04523935PHASE4COMPLETEDExcessive Crying in Children With Cerebral Palsy and Communication Deficits
NCT00122044PHASE2COMPLETEDChildhood Hypertonia of Central Origin: A Trial of Anticholinergic Treatment Effects
NCT06554288PHASE1RECRUITINGPharmacogenomic Contributions to Trihexyphenidyl Biotransformation and Response in Children With Dystonic Cerebral Palsy
NCT03430596EARLY_PHASE1COMPLETEDa Pilot Study of Pramipexole to Treat Extrapyramidal Symptoms Induced by Antipsychotics

Clinical evidence (CIViC)

No CIViC predictive evidence (expected for non-precision-medicine drugs).

Pharmacology

Pharmacogenomics

No CPIC/DPWG dosing guideline, but PharmGKB curates 0 clinical and 1 variant annotation(s) for this drug (gene-keyed; see PharmGKB).

Molecules sharing ≥1 of this drug’s curated primary targets, merged from two biobtree sources and ranked by shared-target count, then clinical phase: ChEMBL clinical-stage candidates (development phase ≥2) and PubChem drug-class bioactivity (approved / known drugs acting on the target). Deduplicated by drug name; the drug’s own salt forms are excluded. Note: for a drug with few primary targets a shared-target match can reflect off-target / promiscuous binding rather than the same therapeutic mechanism — the phase ordering surfaces bona-fide therapeutics first.

438 molecules share ≥1 primary target. Top 100 by shared-target count:

MoleculeSourceStatusShared targets
GENTIAN VIOLETChEMBL + PubChemPhase 4 (approved)CHRM1
LINAGLIPTINChEMBL + PubChemPhase 4 (approved)CHRM1
PIMAVANSERINChEMBL + PubChemPhase 4 (approved)CHRM1
REGORAFENIBChEMBL + PubChemPhase 4 (approved)CHRM1
VORAPAXARChEMBL + PubChemPhase 4 (approved)CHRM1
ACETYLCHOLINEChEMBLPhase 4 (approved)CHRM1
ACETYLCHOLINE CHLORIDEChEMBLPhase 4 (approved)CHRM1
ACLIDINIUM BROMIDEChEMBLPhase 4 (approved)CHRM1
AMBENONIUMChEMBLPhase 4 (approved)CHRM1
AMDINOCILLIN PIVOXILChEMBLPhase 4 (approved)CHRM1
AMIODARONEChEMBLPhase 4 (approved)CHRM1
AMITRIPTYLINEChEMBLPhase 4 (approved)CHRM1
AMLODIPINEChEMBLPhase 4 (approved)CHRM1
AMODIAQUINEChEMBLPhase 4 (approved)CHRM1
AMOROLFINEChEMBLPhase 4 (approved)CHRM1
AMOXAPINEChEMBLPhase 4 (approved)CHRM1
AMSACRINEChEMBLPhase 4 (approved)CHRM1
ANISOTROPINEChEMBLPhase 4 (approved)CHRM1
ARIPIPRAZOLEChEMBLPhase 4 (approved)CHRM1
ASTEMIZOLEChEMBLPhase 4 (approved)CHRM1
ATOMOXETINEChEMBLPhase 4 (approved)CHRM1
ATROPINEChEMBLPhase 4 (approved)CHRM1
AZATADINEChEMBLPhase 4 (approved)CHRM1
AZELASTINEChEMBLPhase 4 (approved)CHRM1
BALSALAZIDEChEMBLPhase 4 (approved)CHRM1
BAZEDOXIFENEChEMBLPhase 4 (approved)CHRM1
BECLOMETHASONE DIPROPIONATEChEMBLPhase 4 (approved)CHRM1
BENPERIDOLChEMBLPhase 4 (approved)CHRM1
BENZTROPINEChEMBLPhase 4 (approved)CHRM1
BENZYDAMINEChEMBLPhase 4 (approved)CHRM1
BEPRIDILChEMBLPhase 4 (approved)CHRM1
BETAMETHASONE PHOSPHORIC ACIDChEMBLPhase 4 (approved)CHRM1
BETHANECHOLChEMBLPhase 4 (approved)CHRM1
BEXAROTENEChEMBLPhase 4 (approved)CHRM1
BIPERIDENChEMBLPhase 4 (approved)CHRM1
BITHIONOLChEMBLPhase 4 (approved)CHRM1
BROMOCRIPTINEChEMBLPhase 4 (approved)CHRM1
BROMODIPHENHYDRAMINEChEMBLPhase 4 (approved)CHRM1
BROMPERIDOLChEMBLPhase 4 (approved)CHRM1
BROMPHENIRAMINEChEMBLPhase 4 (approved)CHRM1
BUDESONIDEChEMBLPhase 4 (approved)CHRM1
BUTRIPTYLINEChEMBLPhase 4 (approved)CHRM1
CABOZANTINIBChEMBLPhase 4 (approved)CHRM1
CARBACHOLChEMBLPhase 4 (approved)CHRM1
CARBAMOYLCHOLINEChEMBLPhase 4 (approved)CHRM1
CARBETAPENTANEChEMBLPhase 4 (approved)CHRM1
CARIPRAZINEChEMBLPhase 4 (approved)CHRM1
CASPOFUNGINChEMBLPhase 4 (approved)CHRM1
CERIVASTATINChEMBLPhase 4 (approved)CHRM1
CEVIMELINEChEMBLPhase 4 (approved)CHRM1
CHLORMADINONEChEMBLPhase 4 (approved)CHRM1
CHLOROQUINEChEMBLPhase 4 (approved)CHRM1
CHLORPHENIRAMINEChEMBLPhase 4 (approved)CHRM1
CHLORPROMAZINEChEMBLPhase 4 (approved)CHRM1
CHLORPROTHIXENEChEMBLPhase 4 (approved)CHRM1
CICLOPIROXChEMBLPhase 4 (approved)CHRM1
CINACALCETChEMBLPhase 4 (approved)CHRM1
CINNARIZINEChEMBLPhase 4 (approved)CHRM1
CITALOPRAMChEMBLPhase 4 (approved)CHRM1
CLEMASTINEChEMBLPhase 4 (approved)CHRM1
CLIDINIUMChEMBLPhase 4 (approved)CHRM1
CLOFAZIMINEChEMBLPhase 4 (approved)CHRM1
CLOMIPHENEChEMBLPhase 4 (approved)CHRM1
CLOMIPRAMINEChEMBLPhase 4 (approved)CHRM1
CLOTRIMAZOLEChEMBLPhase 4 (approved)CHRM1
CLOZAPINEChEMBLPhase 4 (approved)CHRM1
COBIMETINIBChEMBLPhase 4 (approved)CHRM1
CRISABOROLEChEMBLPhase 4 (approved)CHRM1
CYCLIZINEChEMBLPhase 4 (approved)CHRM1
CYCLOBENZAPRINEChEMBLPhase 4 (approved)CHRM1
CYCLOFENILChEMBLPhase 4 (approved)CHRM1
CYCLOPENTOLATEChEMBLPhase 4 (approved)CHRM1
CYCLOTHIAZIDEChEMBLPhase 4 (approved)CHRM1
CYPROHEPTADINEChEMBLPhase 4 (approved)CHRM1
DACOMITINIBChEMBLPhase 4 (approved)CHRM1
DALFAMPRIDINEChEMBLPhase 4 (approved)CHRM1
DARIFENACINChEMBLPhase 4 (approved)CHRM1
DAUNORUBICINChEMBLPhase 4 (approved)CHRM1
DELAVIRDINEChEMBLPhase 4 (approved)CHRM1
DEQUALINIUMChEMBLPhase 4 (approved)CHRM1
DESIPRAMINEChEMBLPhase 4 (approved)CHRM1
DESLORATADINEChEMBLPhase 4 (approved)CHRM1
DESOXIMETASONEChEMBLPhase 4 (approved)CHRM1
DEXAMETHASONE PHOSPHORIC ACIDChEMBLPhase 4 (approved)CHRM1
DEXBROMPHENIRAMINEChEMBLPhase 4 (approved)CHRM1
DEXCHLORPHENIRAMINEChEMBLPhase 4 (approved)CHRM1
DICYCLOMINEChEMBLPhase 4 (approved)CHRM1
DIETHYLSTILBESTROLChEMBLPhase 4 (approved)CHRM1
DIMENHYDRINATEChEMBLPhase 4 (approved)CHRM1
DIPHEMANILChEMBLPhase 4 (approved)CHRM1
DIPHENHYDRAMINEChEMBLPhase 4 (approved)CHRM1
DIPHENIDOLChEMBLPhase 4 (approved)CHRM1
DIPHENYLPYRALINEChEMBLPhase 4 (approved)CHRM1
DISULFIRAMChEMBLPhase 4 (approved)CHRM1
DONEPEZILChEMBLPhase 4 (approved)CHRM1
DOTHIEPINChEMBLPhase 4 (approved)CHRM1
DOXAZOSINChEMBLPhase 4 (approved)CHRM1
DOXEPINChEMBLPhase 4 (approved)CHRM1
DOXORUBICINChEMBLPhase 4 (approved)CHRM1
DRONEDARONEChEMBLPhase 4 (approved)CHRM1