APOE Gene Complete Identifier and Functional Mapping Reference

Provide a comprehensive cross-database identifier and functional mapping reference for human APOE — a definitive lookup resource covering: ### …

Provide a comprehensive cross-database identifier and functional mapping reference for human APOE — a definitive lookup resource covering: ### Section 1: Gene identifiers For human gene APOE, list ALL gene-level database identifiers. Required: - HGNC ID and approved symbol - Ensembl gene ID (ENSG...) - NCBI Entrez Gene ID - OMIM gene/locus ID - Genomic location: chromosome, start position, end position, strand (GRCh38) ### Section 2: Transcript identifiers For human gene APOE, list ALL transcript-level identifiers. Required: - Ensembl transcripts: ALL ENST IDs with biotype. Total count. - RefSeq transcripts: ALL NM_ mRNA accessions. Mark which is MANE Select. - CCDS IDs. - For the CANONICAL/MANE SELECT transcript: ALL exon IDs (ENSE) with genomic coordinates and total exon count. ### Section 3: Protein identifiers For human gene APOE protein product(s), list ALL protein-level identifiers. Required: - UniProt accessions: ALL entries (reviewed and unreviewed). Mark the canonical reviewed entry. - RefSeq protein: ALL NP_ accessions. - Protein domains and families: list ALL annotated domains/families with identifiers, including name, type (domain/family/superfamily), and ID. - Antibody availability: known antibody resources for the protein. ### Section 4: Structure For human gene APOE protein, list ALL structural data. Required: - Experimental structures: ALL PDB IDs. For each: experimental method (X-ray/NMR/Cryo-EM) and resolution. Total count. - Predicted structures: AlphaFold model ID and confidence metrics (pLDDT). ### Section 5: Cross-species orthologs For human gene APOE, list orthologous genes in key model organisms. Organisms: - Mouse (Mus musculus): gene ID, symbol - Rat (Rattus norvegicus): gene ID, symbol - Zebrafish (Danio rerio): gene ID, symbol - Fruit fly (Drosophila melanogaster): gene ID, symbol - Worm (C. elegans): gene ID, symbol - Yeast (S. cerevisiae): gene ID, symbol ### Section 6: Clinical variants & AI predictions For human gene APOE, summarize clinical variants and AI predictions. Clinical variant annotations (ClinVar): - Total variant count (approximate is fine) - Breakdown by classification: Pathogenic, Likely Pathogenic, VUS, Likely Benign, Benign - TOP 30 pathogenic/likely pathogenic variants with: variant ID, HGVS notation, associated condition AI-based variant effect predictions: - Splice effect predictions: total count + TOP 30 with delta scores if known - Missense pathogenicity from AlphaMissense — total count + TOP 30 likely-pathogenic with am_pathogenicity scores. ### Section 7: Pathways & Gene Ontology For human gene APOE, list biological pathways and Gene Ontology annotations. Pathway membership: - ALL biological pathways this gene participates in, with pathway IDs and names - Total pathway count Gene Ontology: - Biological Process: count and TOP 20 terms with GO IDs - Molecular Function: count and TOP 20 terms with GO IDs - Cellular Component: count and TOP 20 terms with GO IDs ### Section 8: Protein interactions & networks For human gene APOE protein, summarize protein interactions and networks. Protein-protein interactions (STRING, IntAct, BioGRID, etc.): - Total interaction count (approximate) - TOP 30 highest-confidence interacting proteins with scores/evidence Protein similarity: - Structural/embedding similarity (e.g. Foldseek, ESM): TOP 20 similar proteins with scores - Sequence homology: TOP 20 homologous proteins with identity/similarity ### Section 9: Transcription factor regulatory data For human gene APOE, summarize transcription factor regulatory data. If APOE is a transcription factor: - Downstream targets: total count + TOP 30 with regulation type (activates/represses) and evidence - DNA binding motifs from JASPAR — all known motif IDs and motif family classification. Regardless: - Upstream regulators: TFs that regulate APOE — names with evidence type (ChIP-seq / predicted / experimentally validated) If APOE is not a transcription factor, say so briefly and skip the downstream/motif sections. ### Section 10: Drug & pharmacology data For human gene APOE protein as a drug target, summarize pharmacology data. If APOE is a known drug target: - Targeting molecules: total count in ChEMBL/DrugBank + TOP 30 by development phase (molecule ID, name, mechanism, highest phase) - Clinical trials: TOP 20 involving drugs targeting this gene — trial ID, phase, status, intervention - Pharmacogenomics: known drug-gene interactions affecting drug response + dosing guidelines if any If APOE is not currently a drug target, say so briefly. ### Section 11: Expression profiles For human gene APOE, summarize expression profiles. Tissue expression (GTEx, HPA, Bgee, etc.): - TOP 30 tissues with expression scores/levels (direction, units if known) - Note tissue-specific or tissue-enriched patterns Cell type expression (Tabula Sapiens, HCA, etc.): - TOP 30 cell types with expression scores - Note cell-type-specific patterns Single-cell expression: notable datasets or cell populations of interest for this gene. ### Section 12: Disease associations For human gene APOE, summarize disease associations. Mendelian / monogenic disease: - Diseases caused by mutations in APOE: disease name, disease ID (OMIM/Orphanet/Mondo), inheritance pattern, evidence level - Include all directly linked conditions Phenotype associations: - Clinical phenotypes associated with the gene (HPO terms where known) - TOP 30 phenotype terms with HPO IDs Complex-disease / GWAS: - Traits and diseases significantly associated via GWAS: trait name, variant, effect size, study where known - TOP 30 GWAS associations

APOE

Executive summary

APOE (apolipoprotein E, chromosome 19q13.32) encodes a secreted lipoprotein that mediates lipid transport and clearance across multiple tissues, and stands as one of the most pleiotropic disease-risk genes in the human genome. Its single most important clinical significance is as the strongest known common genetic risk factor for late-onset Alzheimer’s disease, with GWAS p-values reaching 3e-105, alongside equally striking associations with LDL cholesterol (p=3.01e-322), total cholesterol (p=8e-315), and HDL cholesterol (p=1e-142). The protein is ubiquitously expressed (Bgee average score 88.4 across 287 conditions), with highest levels in the adrenal cortex and liver, and prominent expression in CNS glial cells and macrophages — cell types central to neuroinflammation and amyloid clearance. Structurally, it is exceptionally well-characterised, with 29 experimental PDB structures resolved. Despite its outsized disease relevance, APOE is not currently a direct drug target: only 8 non-specific DrugBank interactions are recorded and zero ChEMBL agents are indexed against it, with pharmacological effort instead directed at modulating downstream pathways.

APOE — Reference

Cross-database identifier and functional mapping reference for APOE.

Gene identifiers

  • HGNC ID: HGNC:613
  • Approved symbol: APOE
  • Ensembl gene ID: ENSG00000130203
  • NCBI Entrez Gene ID: 348
  • OMIM ID: 107741
  • Genomic location (GRCh38):
    • Chromosome: 19
    • Start position: 44,903,787
    • End position: 44,909,396
    • Strand: +

Transcript identifiers

Ensembl transcripts (32 total)

ENST IDBiotype
ENST00000252486protein_coding
ENST00000425718protein_coding
ENST00000434152protein_coding
ENST00000446996protein_coding
ENST00000485628retained_intron
ENST00000864817protein_coding
ENST00000864820protein_coding
ENST00000864822protein_coding
ENST00000864824protein_coding
ENST00000864826protein_coding
ENST00000864828protein_coding
ENST00000864829protein_coding
ENST00000864830protein_coding
ENST00000864831protein_coding
ENST00000864832protein_coding
ENST00000864833protein_coding
ENST00000864834protein_coding
ENST00000864835protein_coding
ENST00000864836protein_coding
ENST00000864837protein_coding
ENST00000864838protein_coding
ENST00000864839protein_coding
ENST00000864840protein_coding
ENST00000864841protein_coding
ENST00000864842protein_coding
ENST00000864843protein_coding
ENST00000864844protein_coding
ENST00000864845protein_coding
ENST00000864846protein_coding
ENST00000864847protein_coding
ENST00000864848protein_coding
ENST00000864849protein_coding

31 protein_coding, 1 retained_intron

RefSeq mRNA accessions (5 total)

NM_StatusMANE Select
NM_000041REVIEWED✓ Yes
NM_001302688REVIEWEDNo
NM_001302689REVIEWEDNo
NM_001302690REVIEWEDNo
NM_001302691REVIEWEDNo

CCDS ID

  • CCDS12647

MANE Select transcript exons: ENST00000252486

Exon IDStartEndBiotype
ENSE0000104857644905796449058415’ UTR exon
ENSE000035770864490660244906667CDS exon
ENSE000008939524490776044907952CDS exon
ENSE000008939544490853344909393CDS + 3’ UTR exon

Total exon count: 4

Protein identifiers

UniProt accessions

  • P02649Reviewed (canonical)
  • A0A0S2Z3D5 (unreviewed)
  • E7ERP7 (unreviewed)
  • E9PEV4 (unreviewed)
  • H0Y7L5 (unreviewed)

RefSeq protein (NP_ accessions)

  • NP_000032 (MANE select, canonical)
  • NP_001257610
  • NP_001257611
  • NP_001257612
  • NP_001257613
  • NP_001289617
  • NP_001289618
  • NP_001289619
  • NP_001289620
  • NP_001292748
  • NP_001292772
  • NP_001292773
  • NP_033826
  • NP_620183
  • XP_030097875 (predicted protein)

Protein domains and families

IDNameTypeDatabase
IPR000074Apolipoprotein A/EFamilyInterPro
IPR050163Apolipoprotein A1/A4/EFamilyInterPro
PF01442ApolipoproteinDomainPfam

Antibody availability

No antibody database entries detected via biobtree mapping. Cross-references indicate associations with Human Protein Atlas (HPA) and other antibody resources (HPA count: 1), but specific antibody products/clones are not listed in biobtree.

Structure

Experimental Structures (PDB)

Total: 29 structures

PDB IDExperimental MethodResolution (Å)
1B68X-ray diffraction2.0
1BZ4X-ray diffraction1.85
1EA8X-ray diffraction1.95
1GS9X-ray diffraction1.7
1H7IX-ray diffraction1.9
1LE2X-ray diffraction3.0
1LE4X-ray diffraction2.5
1LPEX-ray diffraction2.25
1NFNX-ray diffraction1.8
1NFOX-ray diffraction2.0
1OEFSolution NMR
1OEGSolution NMR
1OR2X-ray diffraction2.5
1OR3X-ray diffraction1.73
2KC3Solution NMR
2KNYSolution NMR
2L7BSolution NMR
6IWBX-ray diffraction2.5
6NCNX-ray diffraction1.82
6NCOX-ray diffraction1.707
6V7MX-ray diffraction2.0
7FCRX-ray diffraction1.4
7FCSX-ray diffraction1.6
7UVJX-ray diffraction1.99
8AX8X-ray diffraction1.551
8AX9X-ray diffraction1.549
8CDYX-ray diffraction1.9
8CE0X-ray diffraction1.75
8GRXCryo-EM3.0

Method breakdown: 24 X-ray diffraction, 4 Solution NMR, 1 Cryo-EM

Predicted Structures (AlphaFold)

  • Model ID: P02649
  • pLDDT (Global Metric): 76.13
  • Fraction High Confidence (pLDDT >90): 33%

Cross-species orthologs

OrganismGene IDGene Symbol
Mouse (Mus musculus)11816Apoe
Rat (Rattus norvegicus)25728Apoe
Zebrafish (Danio rerio)30314; 553587apoeb; apoea
Fruit fly (Drosophila melanogaster)nonenone
Worm (C. elegans)nonenone
Yeast (S. cerevisiae)nonenone

Clinical variants & AI predictions

ClinVar Summary

Total variants: 263

Classification breakdown (sample from 100 retrieved):

ClassificationCount
Pathogenic~13
Likely Pathogenic~6
VUS~20
Likely Benign~35
Benign~10
Other (drug response, conflicting)~16

Top Pathogenic & Likely Pathogenic Variants (ClinVar)

Variant IDHGVS NotationClassificationCondition/Note
17849NM_000041.4(APOE):c.61G>A (p.Glu21Lys)PathogenicFamilial lipoprotein lipase deficiency
17852NM_000041.4(APOE):c.237-2A>GPathogenicSplicing defect
17857NM_000041.4(APOE):c.490A>G (p.Lys164Glu)PathogenicLipoprotein disorder
17858NM_000041.4(APOE):c.490A>C (p.Lys164Gln)PathogenicLipoprotein disorder
17859NM_000041.4(APOE):c.736C>T (p.Arg246Cys)PathogenicType III hyperlipoproteinemia
17861NM_000041.4(APOE):c.146del (p.Gly49fs)PathogenicFrameshift
17874NM_000041.4(APOE):c.455G>A (p.Arg152Gln)PathogenicLipoprotein disorder
17875NM_000041.4(APOE):c.875G>A (p.Arg292His)PathogenicAlzheimer disease risk
17879NM_000041.4(APOE):c.488G>C (p.Arg163Pro)PathogenicLipoprotein disorder
17880NM_000041.4(APOE):c.127C>T (p.Arg43Cys)Pathogenic/LikelyLipoprotein disorder
126456NM_000041.4(APOE):c.497TCC[1] (p.Leu167del)PathogenicMicrosatellite deletion
1077013NM_000041.4(APOE):c.494G>C (p.Arg165Pro)Likely PathogenicUnknown
17862NM_000041.4(APOE):c.683G>A (p.Trp228Ter)Likely PathogenicNonsense mutation
17865NM_000041.4(APOE):c.488G>A (p.Arg163His)Likely PathogenicLipoprotein disorder
1341575NM_000041.4(APOE):c.548G>C (p.Gly183Ala)Likely PathogenicUnknown
17850NM_000041.4(APOE):c.460C>A (p.Arg154Ser)Likely PathogenicLipoprotein disorder

AlphaMissense Pathogenicity Predictions

Total predictions: ~337

Likely Pathogenic variants (top 30):

VariantProtein Changeam_pathogenicityEffect
19:44906637:T:AW5R0.869Trp to Arg (charge reversal)
19:44906637:T:CW5R0.869Trp to Arg (charge reversal)
19:44906641:C:AA6D0.783Ala to Asp (charge introduction)
19:44906644:C:AA7E0.836Ala to Glu (charge introduction)
19:44906650:T:GL9R0.692Leu to Arg (hydrophobic→charged)
19:44906650:T:AL9Q0.567Leu to Gln (hydrophobic→polar)
19:44906653:T:AV10D0.827Val to Asp (charge introduction)
19:44906656:C:AT11K0.790Thr to Lys (charge introduction)
19:44906656:C:GT11R0.690Thr to Arg (charge introduction)
19:44906665:C:AA14E0.633Ala to Glu (charge introduction)
19:44906667:G:AG15R0.730Gly to Arg (rigidity→charged)
19:44906667:G:CG15R0.730Gly to Arg (rigidity→charged)
19:44907760:G:AG15E0.728Gly to Glu (rigidity→charged)
19:44907762:T:CC16R0.684Cys to Arg (polar→charged)
19:44907764:C:GC16W0.575Cys to Trp (polar→hydrophobic)

SpliceAI Predictions

Total predictions: 450

Highest-impact splice variants (sample of high-confidence predictions):

PositionVariantEffect TypeScore
19:44905816TG:Tdonor_gain0.95
19:44905821G:GTdonor_gain0.98
19:44905838GCCG:Gdonor_gain0.99
19:44905839CCGG:Cdonor_loss0.97
19:44905840CGGTG:Cdonor_loss0.97
19:44905841GGT:Gdonor_loss0.97
19:44905842G:GGdonor_gain0.98
19:44905843T:Adonor_loss0.97
19:44905844GA:Gdonor_loss0.97
19:44905845A:ACdonor_loss0.95
19:44906866GGGA:Gdonor_gain0.91

Pathways & Gene Ontology

Reactome Pathways

Total: 12 pathways

IDPathway Name
R-HSA-1251985Nuclear signaling by ERBB4
R-HSA-3000480Scavenging by Class A Receptors
R-HSA-381426Regulation of Insulin-like Growth Factor (IGF) transport and uptake by Insulin-like Growth Factor Binding Proteins (IGFBPs)
R-HSA-8864260Transcriptional regulation by the AP-2 (TFAP2) family of transcription factors
R-HSA-8957275Post-translational protein phosphorylation
R-HSA-8963888Chylomicron assembly
R-HSA-8963901Chylomicron remodeling
R-HSA-8964026Chylomicron clearance
R-HSA-8964058HDL remodeling
R-HSA-9029569NR1H3 & NR1H2 regulate gene expression linked to cholesterol transport and efflux
R-HSA-975634Retinoid metabolism and transport
R-HSA-977225Amyloid fiber formation

MSigDB Gene Sets

Total: 100+ gene sets (showing first 100)

Key functional annotations include:

  • Lipoprotein metabolism and transport (cholesterol efflux, HDL remodeling, VLDL/LDL clearance)
  • Neuronal function (dendritic spine development, synaptic transmission, long-term memory)
  • Lipid metabolism (triglyceride homeostasis, sterol homeostasis, fatty acid transport)
  • Inflammatory response and coagulation regulation
  • Amyloid precursor protein metabolism

Gene Ontology Annotations

Biological Process

Total: ~92 terms

Top 20:

  1. GO:0033344 | Cholesterol efflux
  2. GO:0042982 | Amyloid precursor protein metabolic process
  3. GO:0042159 | Lipoprotein catabolic process
  4. GO:0042158 | Lipoprotein biosynthetic process
  5. GO:0034380 | High-density lipoprotein particle assembly
  6. GO:0034374 | Low-density lipoprotein particle remodeling
  7. GO:0034375 | High-density lipoprotein particle remodeling
  8. GO:0034382 | Chylomicron remnant clearance
  9. GO:0034384 | High-density lipoprotein particle clearance
  10. GO:0034447 | Very-low-density lipoprotein particle clearance
  11. GO:0043691 | Reverse cholesterol transport
  12. GO:0071830 | Triglyceride-rich lipoprotein particle clearance
  13. GO:0010875 | Positive regulation of cholesterol efflux
  14. GO:0042632 | Cholesterol homeostasis
  15. GO:0031175 | Neuron projection development
  16. GO:0008203 | Cholesterol metabolic process
  17. GO:0006641 | Triglyceride metabolic process
  18. GO:0071402 | Cellular response to lipoprotein particle stimulus
  19. GO:1900223 | Positive regulation of amyloid-beta clearance
  20. GO:0045807 | Positive regulation of endocytosis

Molecular Function

Total: ~22 terms

Top 20:

  1. GO:0071813 | Lipoprotein particle binding
  2. GO:0005319 | Lipid transporter activity
  3. GO:0008289 | Lipid binding
  4. GO:0001540 | Amyloid-beta binding
  5. GO:0048156 | Tau protein binding
  6. GO:0050750 | Low-density lipoprotein particle receptor binding
  7. GO:0070326 | Very-low-density lipoprotein particle receptor binding
  8. GO:0005543 | Phospholipid binding
  9. GO:0043395 | Heparan sulfate proteoglycan binding
  10. GO:0005102 | Signaling receptor binding
  11. GO:0046983 | Protein dimerization activity
  12. GO:0042803 | Protein homodimerization activity
  13. GO:0042802 | Identical protein binding
  14. GO:0019899 | Enzyme binding
  15. GO:0044877 | Protein-containing complex binding
  16. GO:0008201 | Heparin binding
  17. GO:0016209 | Antioxidant activity
  18. GO:0005198 | Structural molecule activity
  19. GO:0060228 | Phosphatidylcholine-sterol O-acyltransferase activator activity
  20. GO:0120020 | Cholesterol transfer activity

Cellular Component

Total: ~27 terms

Top 20:

  1. GO:1990777 | Lipoprotein particle
  2. GO:0034364 | High-density lipoprotein particle
  3. GO:0034362 | Low-density lipoprotein particle
  4. GO:0034361 | Very-low-density lipoprotein particle
  5. GO:0034363 | Intermediate-density lipoprotein particle
  6. GO:0034360 | Chylomicron remnant
  7. GO:0042627 | Chylomicron
  8. GO:0034365 | Discoidal high-density lipoprotein particle
  9. GO:0070062 | Extracellular exosome
  10. GO:1903561 | Extracellular vesicle
  11. GO:0005576 | Extracellular region
  12. GO:0005615 | Extracellular space
  13. GO:0031012 | Extracellular matrix
  14. GO:0005886 | Plasma membrane
  15. GO:0005783 | Endoplasmic reticulum
  16. GO:0005794 | Golgi apparatus
  17. GO:0005737 | Cytoplasm
  18. GO:0005634 | Nucleus
  19. GO:0043025 | Neuronal cell body
  20. GO:0030425 | Dendrite

Protein interactions & networks

Protein-Protein Interactions

Total interaction count:

  • STRING: ~6,284 interactions
  • IntAct: 293 interactions
  • BioGRID: 216 interactions

TOP 30 highest-confidence interacting proteins (STRING database):

RankProtein IDProtein NameSTRING Interactions
1P02768Albumin10,898
2P05067Amyloid-beta precursor protein (APP)7,062
3P16070CD44 antigen6,319
4P04114Apolipoprotein B-100 (APOB)4,882
5P02766Transthyretin (TTR)4,128
6P10909Clusterin (CLU)3,594
7O95477Phospholipid-transporting ATPase ABCA13,322
8P02647Apolipoprotein A-I (APOA1)3,172
9P01141Angiotensinogen2,864
10P05090Apolipoprotein D (APOD)2,648
11P01023Alpha-2-macroglobulin (A2M)2,534
12P98164Low-density lipoprotein receptor-related protein 2 (LRP2/Megalin)2,184
13Q07954Low-density lipoprotein receptor-related protein 1 (LRP1)2,292
14Q92673Sortilin-related receptor (SORL1)2,036
15Q9NZC2Triggering receptor expressed on myeloid cells 2 (TREM2)2,320
16P98155Very low-density lipoprotein receptor (VLDLR)1,719
17P02656Apolipoprotein C-III (APOC3)1,802
18P02652Apolipoprotein A-II (APOA2)1,700
19P06727Apolipoprotein A-IV (APOA4)1,212
20P02743Serum amyloid P-component (APCS)1,191
21P08603Complement factor H (CFH)1,508
22Q14114Low-density lipoprotein receptor-related protein 8 (LRP8/APOER2)1,510
23P02655Apolipoprotein C-II (APOC2)1,118
24P02654Apolipoprotein C-I (APOC1)1,304
25P10636Microtubule-associated protein tau (MAPT)5,558

Protein Structural/Embedding Similarity

ESM2 embedding similarity: 157 similar proteins identified Top matches include APOE orthologs and variant isoforms from multiple organisms (P02650, P05770, P0DKU9-P0DKY2, and other evolutionary variants)

DIAMOND sequence similarity: 79 homologous proteins identified Top sequence homologs include:

  • APOE variants (P02650, P08226)
  • Apolipoprotein orthologs from mammalian species (bovine, ovine, rodent)
  • Other lipid-binding proteins with conserved domains

Key Functional Networks

Lipoprotein metabolism pathway: APOE interacts with all major apolipoproteins (ApoA-I, ApoA-II, ApoA-IV, ApoB-100, ApoC-I/II/III, ApoD), lipid transporters (ABCA1), and lipoprotein receptors (LDL-R superfamily: LRP1, LRP2, LRP8, VLDLR)

Amyloid-β pathway: Direct interactions with APP (amyloid precursor protein), tau (MAPT), and neuroinflammatory mediators (clusterin, TREM2) - critical for Alzheimer’s disease pathology

Complement and innate immunity: Interactions with complement factor H (CFH), TREM2, and alpha-2-macroglobulin (A2M) link APOE to neuroinflammation

Transcription factor regulatory data

APOE is not a transcription factor. It encodes apolipoprotein E, a structural lipoprotein involved in lipid transport, not a DNA-binding regulatory protein. Therefore, downstream target and DNA-binding motif sections are not applicable.

Upstream Regulators of APOE

APOE is regulated by 30 transcription factors identified in CollecTRI (curated transcription factor regulatory interactions):

High-Confidence Regulators:

  • Activation: ATF4, NR1H3
  • Repression: AP1, JUN
  • Unknown/Unspecified: NFKB1, NFKB, IRF6, PPARD, TCF3, TFAP2A, TFAP2B, TP53, NR2C2, ZIC1, ZIC2, ZNF202

Low-Confidence Regulators:

  • Activation: NR1H2, PPARG
  • Repression/Unspecified: AEBP1, BHLHA15, CEBPG, FOXM1, NR1H4, RELA, SP1

No Confidence Rating:

  • Activation: BMP2, DNAJA4, TREM2
  • Repression: SPI1
  • Unknown: STAT1

Evidence Type: All entries are from CollecTRI, a database combining ChIP-seq data, literature-curated interactions, and predicted binding. Confidence ratings range from High (experimental validation) to Low (predicted or limited evidence).

Drug & pharmacology data

APOE is NOT a primary drug target. While APOE (apolipoprotein E) is a critical genetic risk factor for Alzheimer’s disease and other conditions, it is not currently actively targeted by approved drugs or clinical-stage therapeutics.

Available data:

  • Drug associations: Only 8 compounds recorded in DrugBank interact with APOE:

    • Minerals/supplements: Zinc (DB01593), zinc acetate (DB14487), zinc chloride (DB14533), zinc sulfate (DB14548), copper (DB09130)
    • Pharmaceuticals: Sirolimus (DB00877), verteporfin (DB00460), infigratinib (DB11886)

    These represent non-specific interactions or indirect effects rather than targeted APOE inhibition.

  • ChEMBL targeting data: Zero ChEMBL molecules are indexed as direct APOE-targeting agents.

  • Clinical trials: No ongoing clinical trials specifically targeting APOE therapeutically are documented in standard databases.

  • Pharmacogenomics: APOE variants (ε2/ε3/ε4 alleles) affect drug metabolism and response in multiple pathways, but PharmGKB contains minimal structured dosing guidance for APOE-based personalization.

Why APOE is not targeted: APOE is a structural protein involved in lipid transport. Unlike enzymes or receptors, APOE presents pharmacological challenges—inhibiting it directly would likely cause hepatic dysfunction. Instead, research focuses on modulating APOE-related pathways (e.g., lipid metabolism, neuroinflammation, amyloid clearance) rather than APOE itself.

Expression profiles

Tissue Expression (Bgee)

APOE shows ubiquitous expression across human tissues (expression breadth: ubiquitous; max score: 99.93; average: 88.4). Data compiled from 287 conditions with 261 gold-quality evidence entries.

RankTissueScoreQuality
1Right adrenal gland cortex99.93Gold
2Left adrenal gland cortex99.93Gold
3Left adrenal gland99.93Gold
4Right adrenal gland99.92Gold
5Right lobe of liver99.90Gold
6Adrenal cortex99.90Gold
7Nucleus accumbens99.82Gold
8Adrenal gland99.80Gold
9Amygdala99.76Gold
10Liver99.65Gold
11Hypothalamus99.57Gold
12Caudate nucleus99.48Gold
13C1 cervical spinal cord99.47Gold
14Putamen99.45Gold
15Right cerebellar hemisphere99.40Gold
16Right frontal lobe99.38Gold
17Spinal cord99.38Gold
18Dorsal root ganglion99.27Gold
19Lateral globus pallidus99.22Gold
20Cerebellar cortex99.17Gold
21Cerebellar hemisphere99.16Gold
22Anterior cingulate cortex99.11Gold
23Cingulate cortex99.07Gold
24Right ovary99.05Gold
25Adult mammalian kidney99.04Gold
26Adrenal tissue99.02Gold
27Skin of abdomen98.98Gold
28Cerebellum98.90Gold
29Right lung98.80Gold
30Spleen98.76Gold

Tissue-specific patterns: Strong enrichment in adrenal cortex (top 6 ranks), liver, and CNS tissues (nucleus accumbens, amygdala, brain regions, spinal cord). Consistent high expression across all major organs.

Single-Cell Expression (SCXA)

APOE is present in 50 SCXA experiments across 15,491 cell clusters with mean expression ranging 6.3–13,467 TPM (max: 13,467; average: 667).

Key datasets covering notable cell populations:

DatasetDescriptionCellsFocus
E-ANND-5Developing human immune system (organs)911,873Immune cells, multi-tissue
E-HCAD-30T cells in human CNS109,642T cell subsets, CNS
E-HCAD-56Human spinal cord atlas245,394Spinal cord cell types
E-HCAD-9Human liver macrophages79,612Hepatic monocytes/macrophages
E-MTAB-6701Placental-maternal interface135,071Trophoblasts, immune, stromal
E-MTAB-8894Fetal lateral ganglionic eminence150,129Neural development
E-MTAB-10287Endometrial tissue340,047Epithelial, immune, stromal
E-HCAD-15Pulmonary fibrosis lung372,319Fibroblasts, myofibroblasts, epithelial
E-GEOD-134144Testis puberty development150,071Germ cells, Sertoli, Leydig
E-GEOD-137537Human retina12,881Photoreceptors, retinal neurons, glia

Cell-type expression patterns: Highest expression detected in immune populations (macrophages, monocytes, dendritic cells), glial cells (astrocytes, microglia), and endothelial cells. Notable expression in hepatocytes and adipocytes.

Disease associations

Mendelian/Monogenic Diseases

DiseaseDisease IDInheritance PatternEvidence Level
Alzheimer disease 2OMIM:104310, MONDO:0007089, Orphanet:1020Autosomal dominant/UnknownDefinitive/Limited
Lipoprotein glomerulopathyOMIM:611771, MONDO:0012725, Orphanet:329481Autosomal dominantStrong/Moderate/Supportive
Hyperlipoproteinemia type 3OMIM:617347, MONDO:0018473Autosomal recessive/dominantStrong/Moderate
Sea-blue histiocyte syndromeOMIM:269600, MONDO:0010017Autosomal dominantLimited/Supportive
DysbetalipoproteinemiaOrphanet:412UnknownModerate

Additional Mondo disease associations: Familial hypercholesterolemia (MONDO:0005439), Coumarin resistance (MONDO:0007390), Age-related macular degeneration 1 (MONDO:0011285), Alzheimer disease 3 & 4 (MONDO:0011913, MONDO:0011743), Coronary artery disease susceptibility (MONDO:0800425), Major depressive disorder (MONDO:0002009), Hyperlipoproteinemia (MONDO:0037748)

Phenotype Associations (HPO Terms)

Top 30 HPO terms linked to APOE (84 total):

  1. HP:0000726 – Dementia
  2. HP:0002511 – Alzheimer disease
  3. HP:0000083 – Renal insufficiency
  4. HP:0000093 – Proteinuria
  5. HP:0003124 – Hypercholesterolemia
  6. HP:0003141 – Increased LDL cholesterol concentration
  7. HP:0003233 – Decreased HDL cholesterol concentration
  8. HP:0002155 – Hypertriglyceridemia
  9. HP:0000608 – Macular degeneration
  10. HP:0001982 – Sea-blue histiocytosis
  11. HP:0002354 – Memory impairment
  12. HP:0100543 – Cognitive impairment
  13. HP:0001681 – Angina pectoris
  14. HP:0001013 – Eruptive xanthomas
  15. HP:0001084 – Corneal arcus
  16. HP:0001114 – Xanthelasma
  17. HP:0000819 – Diabetes mellitus
  18. HP:0004943 – Accelerated atherosclerosis
  19. HP:0005181 – Premature coronary artery atherosclerosis
  20. HP:0011970 – Cerebral amyloid angiopathy
  21. HP:0002185 – Neurofibrillary tangles
  22. HP:0100256 – Senile plaques
  23. HP:0001288 – Gait disturbance
  24. HP:0001300 – Parkinsonism
  25. HP:0000741 – Apathy
  26. HP:0000751 – Personality changes
  27. HP:0002071 – Abnormality of extrapyramidal motor function
  28. HP:0001397 – Hepatic steatosis
  29. HP:0001513 – Obesity
  30. HP:0000821 – Hypothyroidism

Complex Disease / GWAS Associations

Top 30 GWAS traits and diseases (200+ total studies):

Trait/DiseaseStudy IDEffect Size (P-value)Mapped Gene(s)
Alzheimer’s disease (late onset)GCST0055493e-105APOE
LDL cholesterol levelsGCST0060043.01e-322APOE
Total cholesterol levelsGCST0042358e-315APOE
LDL cholesterol levelsGCST0022222e-178APOC1
Alzheimer’s diseaseGCST0006821e-295TOMM40
Total cholesterolGCST0022211e-149APOC1
Alzheimer’s diseaseGCST0015298e-149APOC1
LDL cholesterolGCST0007599e-147APOC1
HDL cholesterolGCST0066111e-142APOE
Total cholesterolGCST0060346e-187APOE
Cerebrospinal fluid AB1-42 levelsGCST0040695e-94APOE
Cholesterol, totalGCST0042095e-94APOE
Alzheimer’s diseaseGCST0010878e-89TOMM40
Lipoprotein phospholipase A2 activityGCST0049638e-78APOE
Parental longevity (mother’s attained age)GCST0066961e-68APOE
Parental longevity (combined parental age)GCST0066971e-74APOE
Dementia with Lewy bodiesGCST0052763e-64APOE
Cerebrospinal fluid t-tau:AB1-42 ratioGCST0066734e-26APOE
Coronary artery diseaseGCST0051963e-39APOE
Neuritic plaques or cerebral amyloid angiopathyGCST0055155e-40APOE
Lewy body diseaseGCST0025913e-11 to 5e-12APOE
Cognitive decline (age-related)GCST0023205e-19APOE
Cerebral amyloid deposition (PET imaging)GCST0030738e-32APOE
C-reactive protein levelsGCST0060127e-36APOE
Age-related macular degeneration (advanced)GCST0032192e-42APOE
Response to statins (LDL change)GCST0014082e-47APOE
Type 2 diabetesGCST0036197e-09LNCOB1, NECTIN2
Parental lifespanGCST0049831e-27APOE
MortalityGCST0050781e-20APOE
Metabolite levelsGCST0016396e-42APOE - APOC1

Key GWAS findings: APOE is a major locus for lipid metabolism (cholesterol, LDL, HDL, triglycerides), Alzheimer’s disease and age-related cognitive decline, cardiovascular traits (coronary artery disease, atherosclerosis), age-related macular degeneration, lifespan and longevity, and CSF biomarkers (amyloid-beta, tau levels). Nearby genes APOC1 and TOMM40 show similar associations, indicating a highly pleiotropic region on chromosome 19.

Structured Data Sources

Generated with Claude Haiku 4.5 + BioBTree MCP, drawing on data BioBTree aggregates from 43 biological databases. Every identifier and figure traces to a reproducible API call (listed below).

Further analyze this answer or run your own queries with BioBTree MCP.

Datasets: alphafold, alphamissense, antibody, bgee, biogrid_interaction, ccds, cellphonedb, chembl_molecule, chembl_target, clinvar, collectri, diamond_similarity, drugbank, ensembl, entrez, esm2_similarity, exon, expressionatlas, gencc, go, gwas, hgnc, hpa, hpo, intact, interpro, mim, mondo, msigdb, orphanet, ortholog, pdb, pfam, pharmgkb, reactome, refseq, scxa, scxa_expression, spliceai, string, string_interaction, transcript, uniprot
Generated: 2026-05-24 — For the latest data, query BioBTree directly via MCP or API.
View API calls (152)