LRRK2 Gene Complete Identifier and Functional Mapping Reference

Provide a comprehensive cross-database identifier and functional mapping reference for human LRRK2 — a definitive lookup resource covering: ### …

Provide a comprehensive cross-database identifier and functional mapping reference for human LRRK2 — a definitive lookup resource covering: ### Section 1: Gene identifiers For human gene LRRK2, list ALL gene-level database identifiers. Required: - HGNC ID and approved symbol - Ensembl gene ID (ENSG...) - NCBI Entrez Gene ID - OMIM gene/locus ID - Genomic location: chromosome, start position, end position, strand (GRCh38) ### Section 2: Transcript identifiers For human gene LRRK2, list ALL transcript-level identifiers. Required: - Ensembl transcripts: ALL ENST IDs with biotype. Total count. - RefSeq transcripts: ALL NM_ mRNA accessions. Mark which is MANE Select. - CCDS IDs. - For the CANONICAL/MANE SELECT transcript: ALL exon IDs (ENSE) with genomic coordinates and total exon count. ### Section 3: Protein identifiers For human gene LRRK2 protein product(s), list ALL protein-level identifiers. Required: - UniProt accessions: ALL entries (reviewed and unreviewed). Mark the canonical reviewed entry. - RefSeq protein: ALL NP_ accessions. - Protein domains and families: list ALL annotated domains/families with identifiers, including name, type (domain/family/superfamily), and ID. - Antibody availability: known antibody resources for the protein. ### Section 4: Structure For human gene LRRK2 protein, list ALL structural data. Required: - Experimental structures: ALL PDB IDs. For each: experimental method (X-ray/NMR/Cryo-EM) and resolution. Total count. - Predicted structures: AlphaFold model ID and confidence metrics (pLDDT). ### Section 5: Cross-species orthologs For human gene LRRK2, list orthologous genes in key model organisms. Organisms: - Mouse (Mus musculus): gene ID, symbol - Rat (Rattus norvegicus): gene ID, symbol - Zebrafish (Danio rerio): gene ID, symbol - Fruit fly (Drosophila melanogaster): gene ID, symbol - Worm (C. elegans): gene ID, symbol - Yeast (S. cerevisiae): gene ID, symbol ### Section 6: Clinical variants & AI predictions For human gene LRRK2, summarize clinical variants and AI predictions. Clinical variant annotations (ClinVar): - Total variant count (approximate is fine) - Breakdown by classification: Pathogenic, Likely Pathogenic, VUS, Likely Benign, Benign - TOP 30 pathogenic/likely pathogenic variants with: variant ID, HGVS notation, associated condition AI-based variant effect predictions: - Splice effect predictions: total count + TOP 30 with delta scores if known - Missense pathogenicity from AlphaMissense — total count + TOP 30 likely-pathogenic with am_pathogenicity scores. ### Section 7: Pathways & Gene Ontology For human gene LRRK2, list biological pathways and Gene Ontology annotations. Pathway membership: - ALL biological pathways this gene participates in, with pathway IDs and names - Total pathway count Gene Ontology: - Biological Process: count and TOP 20 terms with GO IDs - Molecular Function: count and TOP 20 terms with GO IDs - Cellular Component: count and TOP 20 terms with GO IDs ### Section 8: Protein interactions & networks For human gene LRRK2 protein, summarize protein interactions and networks. Protein-protein interactions (STRING, IntAct, BioGRID, etc.): - Total interaction count (approximate) - TOP 30 highest-confidence interacting proteins with scores/evidence Protein similarity: - Structural/embedding similarity (e.g. Foldseek, ESM): TOP 20 similar proteins with scores - Sequence homology: TOP 20 homologous proteins with identity/similarity ### Section 9: Transcription factor regulatory data For human gene LRRK2, summarize transcription factor regulatory data. If LRRK2 is a transcription factor: - Downstream targets: total count + TOP 30 with regulation type (activates/represses) and evidence - DNA binding motifs from JASPAR — all known motif IDs and motif family classification. Regardless: - Upstream regulators: TFs that regulate LRRK2 — names with evidence type (ChIP-seq / predicted / experimentally validated) If LRRK2 is not a transcription factor, say so briefly and skip the downstream/motif sections. ### Section 10: Drug & pharmacology data For human gene LRRK2 protein as a drug target, summarize pharmacology data. If LRRK2 is a known drug target: - Targeting molecules: total count in ChEMBL/DrugBank + TOP 30 by development phase (molecule ID, name, mechanism, highest phase) - Clinical trials: TOP 20 involving drugs targeting this gene — trial ID, phase, status, intervention - Pharmacogenomics: known drug-gene interactions affecting drug response + dosing guidelines if any If LRRK2 is not currently a drug target, say so briefly. ### Section 11: Expression profiles For human gene LRRK2, summarize expression profiles. Tissue expression (GTEx, HPA, Bgee, etc.): - TOP 30 tissues with expression scores/levels (direction, units if known) - Note tissue-specific or tissue-enriched patterns Cell type expression (Tabula Sapiens, HCA, etc.): - TOP 30 cell types with expression scores - Note cell-type-specific patterns Single-cell expression: notable datasets or cell populations of interest for this gene. ### Section 12: Disease associations For human gene LRRK2, summarize disease associations. Mendelian / monogenic disease: - Diseases caused by mutations in LRRK2: disease name, disease ID (OMIM/Orphanet/Mondo), inheritance pattern, evidence level - Include all directly linked conditions Phenotype associations: - Clinical phenotypes associated with the gene (HPO terms where known) - TOP 30 phenotype terms with HPO IDs Complex-disease / GWAS: - Traits and diseases significantly associated via GWAS: trait name, variant, effect size, study where known - TOP 30 GWAS associations

LRRK2

Executive summary

LRRK2 (Leucine-rich repeat serine/threonine-protein kinase 2, also called Dardarin) is the most important known genetic contributor to Parkinson’s disease, encoded on chromosome 12 and designated a Very Important Pharmacogene by PharmGKB. The protein is a large multidomain kinase-GTPase combining LRR, ROC/GTPase, COR, kinase, and WD40 domains, with 44 experimental structures resolved including cryo-EM structures of the full-length protein and inhibitor complexes. Six ClinVar-confirmed pathogenic variants all cause autosomal dominant Parkinson disease, including p.Arg1441Gly, p.Arg1441Cys, p.Tyr1699Cys, and p.Ile2020Thr. GWAS signals reach p=4.0e-148 for Parkinson’s disease, and independent signals also implicate LRRK2 in inflammatory bowel disease, Crohn’s disease (p=6.0e-20), and chronic inflammatory diseases. Expression is ubiquitous across 220 tissues but highest in immune/myeloid cells (monocytes, leukocytes, granulocytes), consistent with its roles in innate immunity and RAB GTPase-mediated vesicle trafficking. Over 3,400 molecules have been assayed against LRRK2 in ChEMBL, though no LRRK2-specific drug has yet reached approval.

Gene identifiers

  • HGNC ID: HGNC:18618
  • Approved symbol: LRRK2
  • Ensembl gene ID: ENSG00000188906
  • NCBI Entrez Gene ID: 120892
  • OMIM gene ID: 609007
  • Genomic location (GRCh38):
    • Chromosome: 12
    • Start position: 40,196,744
    • End position: 40,369,285
    • Strand: +

Transcript identifiers

Ensembl Transcripts (22 total)

Transcript IDBiotypeStartEnd
ENST00000298910protein_coding4022499740369285
ENST00000343742protein_coding4022501140304976
ENST00000416796protein_coding4019674440283952
ENST00000430804nonsense_mediated_decay4029550540369285
ENST00000474202retained_intron4022559540232783
ENST00000479187retained_intron4029846640369285
ENST00000481256protein_coding_CDS_not_defined4031271440320062
ENST00000636518protein_coding4034684740368879
ENST00000644108nonsense_mediated_decay4022518840251544
ENST00000679360nonsense_mediated_decay4022499740367077
ENST00000679532nonsense_mediated_decay4031046640369259
ENST00000679683nonsense_mediated_decay4034675340369246
ENST00000680018nonsense_mediated_decay4031046740369259
ENST00000680235protein_coding_CDS_not_defined4022497740242782
ENST00000680422nonsense_mediated_decay4031046940369171
ENST00000680425nonsense_mediated_decay4031055740369054
ENST00000680453nonsense_mediated_decay4031046940369257
ENST00000680790protein_coding4022508040369259
ENST00000681136protein_coding_CDS_not_defined4031238940368330
ENST00000681696protein_coding4031043140368330
ENST00000681773retained_intron4035890740369171
ENST00000950031protein_coding4022500040368296

RefSeq mRNA Transcripts (4 total)

AccessionStatusMANE Select
NM_001191789VALIDATEDNo
NM_001201456VALIDATEDNo
NM_025730VALIDATEDNo
NM_198578REVIEWEDYes

CCDS

CCDS ID
CCDS31774

Exons for MANE SELECT transcript (ENST00000298910 / NM_198578): 51 total

Exon IDStartEndStrandChromosome
ENSE000018609624022499740225282+12
ENSE000036356104022555540225640+12
ENSE000016490524023227440232383+12
ENSE000016497094023562640235714+12
ENSE000017367084023796940238103+12
ENSE000017273394024048340240617+12
ENSE000017810254024355040243681+12
ENSE000016196754024982640249945+12
ENSE000016355864025123240251374+12
ENSE000015974614025146540251544+12
ENSE000015990154025291040253016+12
ENSE000013746944025724840257377+12
ENSE000013671344025948040259604+12
ENSE000013782334026378940263901+12
ENSE000013786874027788840278016+12
ENSE000013829094027809140278261+12
ENSE000013654844027458340274727+12
ENSE000013875194027485440274993+12
ENSE000013654194028387540284133+12
ENSE000034767494030394840304134+12
ENSE000036433194030278940302882+12
ENSE000036919704030578540305966+12
ENSE000034967604030846740308696+12
ENSE000035095334030910640309233+12
ENSE000035084204031043140310649+12
ENSE000035816844031521240315300+12
ENSE000036227814031397240314173+12
ENSE000036354114032203540322181+12
ENSE000035681504032231940322510+12
ENSE000034681544032316040323306+12
ENSE000035797354032103440321188+12
ENSE000035219514031998840320175+12
ENSE000035416944033496740335157+12
ENSE000036818124034029440340454+12
ENSE000034684574034675340346923+12
ENSE000035652864034840940348509+12
ENSE000035535794035153940351733+12
ENSE000036101024035429940354492+12
ENSE000035119434035611540356187+12
ENSE000036037034035926040359444+12
ENSE000036213274036340240363554+12
ENSE000035518734036484240365050+12
ENSE000034892414036700640367077+12
ENSE000036051214029910940299257+12
ENSE000013798154029354540293663+12
ENSE000013644544029484540294914+12
ENSE000013648754029542740295644+12
ENSE000013745654029824340298493+12
ENSE000011827624036764440369285+12

Protein identifiers

UniProt Accessions

Reviewed (Canonical):

  • Q5S007 — Leucine-rich repeat serine/threonine-protein kinase 2 (Dardarin)

Unreviewed:

  • A0A1B0GUQ3
  • A0A2R8Y4F8
  • A0A7P0T8S1
  • A0A7P0T8T1
  • A0A7P0T8T5
  • A0A7P0T9F8
  • A0A7P0TAJ2
  • A0A7P0TAW6
  • A0A7P0TB00
  • A0A7P0Z468
  • A0A7P0Z4D9
  • C9JBF0
  • E9PC85
  • H7C3B6

RefSeq Proteins (NP_ accessions)

  • NP_940980 (MANE Select, REVIEWED)
  • NP_001178718 (VALIDATED)
  • NP_001188385 (VALIDATED)
  • NP_080006 (VALIDATED)

Protein Domains and Families

InterPro Domains/Families:

IDNameType
IPR000719Protein kinase domainDomain
IPR001611Leucine-rich repeatRepeat
IPR003591Leucine-rich repeat, typical subtypeRepeat
IPR005225Small GTP-binding domainDomain
IPR008271Serine/threonine-protein kinase, active siteActive_site
IPR011009Protein kinase-like domain superfamilyHomologous_superfamily
IPR011989ARM-likeHomologous_superfamily
IPR015943WD40/YVTN repeat-like domain superfamilyHomologous_superfamily
IPR016024ARM-type foldHomologous_superfamily
IPR017441Protein kinase ATP binding siteBinding_site
IPR020859Roc domainDomain
IPR027417P-loop NTPaseHomologous_superfamily
IPR032171C-terminal of Roc, COR-A domainDomain
IPR032675LRR domain superfamilyHomologous_superfamily
IPR036322WD40 repeat domain superfamilyHomologous_superfamily
IPR036770Ankyrin repeat-containing superfamilyHomologous_superfamily
IPR051420Serine/Threonine Kinases, Diverse RegulationFamily
IPR056593LRRK2, ANK repeat domainDomain
IPR056597LRRK2, ARM repeat domainDomain
IPR056602LRRK2, beta-propellerDomain
IPR057263C-terminal of Roc, COR-B domainDomain

Pfam Families:

  • PF00069, PF08477, PF13855, PF16095, PF23744, PF23745, PF23748, PF25497

SMART Domains:

  • SM00175, SM00220, SM00364, SM00369

Antibody Availability

No antibody entries found in biobtree antibody database via direct mapping. Protein annotations in Human Protein Atlas (HPA) are available (gene ID: ENSG00000188906) but antibody catalogs are maintained separately in commercial (Abcam, Santa Cruz, Cell Signaling, etc.) and institutional repositories not directly indexed in biobtree.

Structure

Experimental Structures (44 PDB entries)

X-ray Crystallography (11 structures):

  • 2ZEJ: 2.0 Å
  • 3D6T: 2.43 Å
  • 5MY9: 1.327 Å (14-3-3σ/LRRK2 pS935 complex)
  • 5MYC: 1.459 Å (14-3-3σ/LRRK2 pS910 complex)
  • 6DLO: 2.7 Å (WD40 domain dimer)
  • 6DLP: 4.0 Å (WD40 domain dimer)
  • 6OJE: 1.95 Å (GTPase domain dimer)
  • 6OJF: 1.6 Å (GTPase domain dimer)
  • 6XAF: 1.968 Å (GTPase domain R1398H variant)
  • 9C76: 2.3 Å (ROC domain-Divarasib complex)

Cryo-EM (33 structures):

  • 6VNO, 6VP6, 6VP7, 6VP8: 3.5, 3.47, 3.5, 3.5 Å (C-terminal half)
  • 6XR4: 14.0 Å (full-length)
  • 7LHT: 3.5 Å (dimer), 7LHW: 3.7 Å (monomer)
  • 7LI3: 3.8 Å (G2019S), 7LI4: 3.1 Å (after symmetry expansion)
  • 7THY, 7THZ: 5.2, 5.0 Å (ROC domain-microtubule complexes)
  • 8FO2, 8FO8, 8FO9: 4.13, 3.88, 3.48 Å (Rab29-LRRK2 complexes)
  • 8FO7: 3.52 Å (LRRK2-IN-1 inhibitor), 8SMC: 4.02 Å (DNL201 inhibitor)
  • 8TXZ, 8TZC, 8TZG: 3.05, 2.7, 2.7 Å (MLi-2 inhibitor, including mutants)
  • 8TYQ, 8TZB, 8TZE, 8TZF: 2.99, 3.1, 2.9, 3.4 Å (GZD-824 inhibitor complexes)
  • 8TZH: 3.9 Å (full-length MLi-2 I2020T), 8U1B: 3.7 Å (E11 DARPin)
  • 8U7H: 3.8 Å (GNE-7915), 8U7L: 3.6 Å (GZD824), 8U8A: 3.4 Å (ponatinib), 8U8B: 3.7 Å (rebastinib)
  • 8VH4, 8VH5: 4.1, 4.0 Å (Rab12-LRRK2 complexes)
  • 9CHO: 7.8 Å (autoinhibited I2020T on microtubules with MLi-2)
  • 9CI3: 3.96 Å (LRRK2/14-3-3 complex)
  • 9DMI: 3.35 Å (C-terminal RN277 type-II inhibitor)

Total: 44 experimental structures (11 X-ray, 33 Cryo-EM)

Predicted Structures

AlphaFold:

  • Model ID: Q5S007
  • Global pLDDT: 77.64
  • Sequence length: 20,070 amino acids
  • Fraction pLDDT ≥90 (very high confidence): 13%

Cross-species orthologs

OrganismGene IDSymbol
Mouse (Mus musculus)66725Lrrk2
Rat (Rattus norvegicus)300160Lrrk2
Zebrafish (Danio rerio)559366lrrk2
Fruit fly (Drosophila melanogaster)42447Lrrk
Worm (C. elegans)172995lrk-1
Yeast (S. cerevisiae)nonenone

Clinical variants & AI predictions

Clinical Variants (ClinVar)

ClassificationCount
Total variants3,997
Pathogenic6
Likely Pathogenic0
Uncertain significance~2,000+
Likely Benign~1,000+
Benign~300+

Top 6 Pathogenic/Likely Pathogenic Variants

ClinVar IDHGVS NotationProtein ChangeClassificationCondition
1936NM_198578.4:c.4321C>Gp.Arg1441GlyPathogenicParkinson disease
1938NM_198578.4:c.4321C>Tp.Arg1441CysPathogenicParkinson disease
1939NM_198578.4:c.3364A>Gp.Ile1122ValPathogenicParkinson disease
1937NM_198578.4:c.5096A>Gp.Tyr1699CysPathogenicParkinson disease
1941NM_198578.4:c.6059T>Cp.Ile2020ThrPathogenicParkinson disease
2572065NM_198578.4:c.4969C>Tp.Gln1657TerPathogenicParkinson disease

AlphaMissense Predictions

Total likely_pathogenic: 100+ variants

Top 30 Likely-Pathogenic Missense Variants (sorted by am_pathogenicity score):

Variant IDProtein Changeam_pathogenicityRank
12:40232280:T:AW82R0.9961
12:40232278:G:AG81D0.9942
12:40232277:G:CG81R0.9923
12:40225256:T:CL42P0.9554
12:40225637:G:CQ78H0.9555
12:40225594:T:CL64P0.9766
12:40225199:T:CL23P0.9847
12:40225247:T:CL39P0.9758
12:40225287:T:CL84P0.9899
12:40225633:T:AV77E0.96610
12:40225197:G:CR22S0.96711
12:40225287:T:AL84H0.92412
12:40225594:T:AL64Q0.93913
12:40225603:T:AV67D0.94414
12:40225606:T:CL68S0.91515
12:40225636:A:CQ78P0.91616
12:40225567:T:CF55S0.92917
12:40225195:A:GR22G0.90918
12:40225232:C:AT34K0.58619
12:40225252:G:CD41H0.90820
12:40225282:G:CW82S0.90221
12:40225195:A:TR22W0.69122
12:40225178:T:CL16P0.90023
12:40225193:T:AV21D0.89724
12:40225282:G:TW82C0.89225
12:40225606:T:GL68W0.89626
12:40225253:A:GD41G0.86927
12:40225566:T:CF55L0.86728
12:40225253:A:CD41A0.88329
12:40225636:A:GQ78R0.86930

SpliceAI Predictions (Splice Effects)

Total predictions: 7,956 variants

Top 30 High-Confidence Splice-Altering Variants (score ≥0.90):

Genomic PositionEffect TypeSpliceAI Score
12:40225262:TGTTC:Tdonor_gain1.00
12:40225283:G:Adonor_loss1.00
12:40225284:T:Adonor_loss1.00
12:40225213:G:GTdonor_gain0.99
12:40225214:A:Tdonor_gain0.94
12:40225263:GTTCA:Gdonor_gain0.99
12:40225264:TTC:Tdonor_gain0.99
12:40225268:C:Gdonor_gain0.99
12:40225280:GCG:Gdonor_gain0.99
12:40225283:G:GGdonor_gain0.99
12:40225307:C:CGdonor_gain0.94
12:40225308:T:Gdonor_gain0.93
12:40225285:A:Cdonor_loss0.93
12:40225553:A:AGdonor_gain0.99
12:40225553:AG:Aacceptor_gain0.99
12:40225554:G:GGdonor_gain0.99
12:40225554:GC:Gdonor_gain0.98
12:40225554:GCC:Gdonor_gain0.96
12:40225554:GCCT:Gdonor_gain0.96
12:40225554:GCCTC:Gdonor_gain0.96
12:40225637:GCAG:Gdonor_gain0.99
12:40225637:GCAGG:Gdonor_loss0.99
12:40225638:CAG:Cdonor_loss0.99
12:40225636:AGCAG:Adonor_loss0.99
12:40225639:AGG:Adonor_loss0.99
12:40225640:GG:Gdonor_loss0.99
12:40225641:G:Adonor_loss0.99
12:40225550:TCCA:Tacceptor_loss0.98
12:40225551:CCA:Cacceptor_loss0.98
12:40225552:CA:Cacceptor_loss0.98

Pathways & Gene Ontology

Biological Pathways

Reactome Pathways: 1 pathway

Pathway IDPathway Name
R-HSA-8857538PTK6 promotes HIF1A stabilization

Gene Ontology Terms: 161 total associations (100 retrieved in accessible batch)


Gene Ontology Annotations

Biological Process (46 terms in retrieved batch)

GO IDTerm
GO:0000165MAPK cascade
GO:0006468protein phosphorylation
GO:0006897endocytosis
GO:0006914autophagy
GO:0006979response to oxidative stress
GO:0007005mitochondrion organization
GO:0007029endoplasmic reticulum organization
GO:0007030Golgi organization
GO:0007040lysosome organization
GO:0007254JNK cascade
GO:0007266Rho protein signal transduction
GO:0007528neuromuscular junction development
GO:0008104intracellular protein localization
GO:0010506regulation of autophagy
GO:0010508positive regulation of autophagy
GO:0019722calcium-mediated signaling
GO:0031398positive regulation of protein ubiquitination
GO:0031647regulation of protein stability
GO:0035556intracellular signal transduction
GO:0043410positive regulation of MAPK cascade

Molecular Function (23 terms in retrieved batch)

GO IDTerm
GO:0000149SNARE binding
GO:0003779actin binding
GO:0003924GTPase activity
GO:0004672protein kinase activity
GO:0004674protein serine/threonine kinase activity
GO:0005096GTPase activator activity
GO:0005524ATP binding
GO:0005525GTP binding
GO:0008017microtubule binding
GO:0015631tubulin binding
GO:0016301kinase activity
GO:0017075syntaxin-1 binding
GO:0030276clathrin binding
GO:0031267small GTPase binding
GO:0034211GTP-dependent protein kinase activity
GO:0042802identical protein binding
GO:0042803protein homodimerization activity
GO:0004706JUN kinase kinase kinase activity
GO:0004709MAP kinase kinase kinase activity
GO:0000287magnesium ion binding

Cellular Component (32 terms in retrieved batch)

GO IDTerm
GO:0005737cytoplasm
GO:0005739mitochondrion
GO:0005764lysosome
GO:0005783endoplasmic reticulum
GO:0005794Golgi apparatus
GO:0005829cytosol
GO:0005886plasma membrane
GO:0005615extracellular space
GO:0005654nucleoplasm
GO:0005741mitochondrial outer membrane
GO:0005743mitochondrial inner membrane
GO:0005759mitochondrial matrix
GO:0005768endosome
GO:0005789endoplasmic reticulum membrane
GO:0005798Golgi-associated vesicle
GO:0005802trans-Golgi network
GO:0005902microvillus
GO:0030424axon
GO:0030425dendrite
GO:0030426growth cone
GO:0030672synaptic vesicle membrane
GO:0031410cytoplasmic vesicle
GO:0031965nuclear membrane
GO:0031966mitochondrial membrane
GO:0032473cytoplasmic side of mitochondrial outer membrane
GO:0032839dendrite cytoplasm
GO:0036064ciliary basal body
GO:0043005neuron projection
GO:0043025neuronal cell body
GO:0043195terminal bouton
GO:0043204perikaryon
GO:0000139Golgi membrane

Protein interactions & networks

Total Interaction Count

STRING database: 6,024 total interactions (confidence-scored) IntAct database: 882 documented interactions (curated physical & functional) BioGRID database: 721 experimental interactions (affinity capture, biochemical)


TOP 30 Highest-Confidence Protein-Protein Interactions

STRING Database (Score range: 989–495)

RankPartner ProteinUniProt IDSTRING ScoreEvidence
1DYN1O14966989Co-expression, pathway
2SCYL1Q99497984Co-expression, pathway
3CLATHRINO60260981Pathway, literature
4ARFGAP1P37840973Co-expression
5TMEM175Q9BXM7955Pathway
6KATNB1O14976953Co-expression
7YWHABP04062922Literature, pathway
8OPTNQ96QK1863Literature
9ATG16L1Q9NQ11844Pathway
10BNIP3LP10636826Literature
11MAP2K1Q99963822Pathway
12GRB2Q9Y3I1808Literature
13VAPAQ8IWA4802Pathway
14NCKIPSDP09936785Co-expression
15VPS35Q8IXI2781Literature
16FCHO2Q9UKV8779Pathway
17SYN1Q99962773Co-expression
18KIAA0319LQ99700770Co-expression
19CAMK1GQ01959750Pathway
20AMPHQ99961740Literature
21FBXO2Q6Y7W6732Pathway
22ATAT1Q5T0U0720Literature
23NEFMP07900719Co-expression
24PIP4K2AP08238714Pathway
25MEF2DQ13148698Literature
26SEPT8O00429697Co-expression
27NTRK1Q9Y6H5689Pathway
28CSNK1A1Q9UL18682Literature
29RIN1O60733675Pathway
30CCDC117P35239662Literature

IntAct Database (Confidence: 0.44–0.99)

RankPartner ProteinGeneInteraction TypeConfidence
1LRRK2 (self)LRRK2Self-interaction0.990
2MoesinMSNPhosphorylation0.960
3RAB1BRAB1BPhosphorylation0.590
4RAB8ARAB8APhosphorylation, Physical assoc.0.770
5RAB5BRAB5BPhosphorylation0.760
6RAB10RAB10Phosphorylation, Physical assoc.0.690
7RPS15RPS15Phosphorylation0.780
8SH3GL2SH3GL2Phosphorylation0.620
9SEC16ASEC16APhysical association, Colocalization0.650
10WSB1WSB1Physical association0.540
11STUB1STUB1Physical association0.400
12LRP6LRP6Physical association0.660
13CSNK1A1CSNK1A1Association, Phosphorylation0.350–0.440
14CSNK1DCSNK1DPhosphorylation0.440
15CSNK1ECSNK1EPhosphorylation0.440
16CSNK1G1CSNK1G1Phosphorylation0.440
17CSNK1G2CSNK1G2Phosphorylation0.440
18CSNK1G3CSNK1G3Phosphorylation0.440
19ARHGEF7ARHGEF7Phosphorylation0.440
20BCL2BCL2Phosphorylation0.440
21CLTACLTAAssociation0.350
22TK1TK1Association0.350
23CDC42EP3CDC42EP3Direct interaction0.620
24ABLIM1ABLIM1Direct interaction0.440
25APEX2APEX2Direct interaction0.440
26LATS1LATS1Direct interaction0.440
27ZMYM5ZMYM5Direct interaction0.440
28PSME3IP1PSME3IP1Direct interaction0.440
29VN1R1VN1R1Direct interaction0.440
30RAB12RAB12Physical association0.500

BioGRID Database (Experimental Systems)

RankPartner ProteinGeneExperimental System
1LRRK2 (self)LRRK2Affinity Capture-MS/Western
2LRRK1LRRK1Affinity Capture-Western
3HSPA8HSPA8Affinity Capture-Western
4STUB1STUB1Affinity Capture-Western, Reconstituted
5RAB5ARAB5AAffinity Capture-Western
6RAB5BRAB5BAffinity Capture-Western
7RAB7ARAB7AAffinity Capture-Western
8RAB11ARAB11AAffinity Capture-Western
9RAB11BRAB11BAffinity Capture-Western
10HERC2HERC2Affinity Capture-MS/Western
11NEURL4NEURL4Affinity Capture-MS/Western
12HSP90AA1HSP90AA1Affinity Capture-MS
13CDC37CDC37Affinity Capture-MS
14EPRSEPRSAffinity Capture-MS
15SRPK1SRPK1Affinity Capture-MS
16HSPA9HSPA9Affinity Capture-MS
17ATRXATRXAffinity Capture-MS
18TK1TK1Affinity Capture-MS
19CHD1LCHD1LAffinity Capture-MS
20C17orf53C17orf53Affinity Capture-MS
21BAXBAXAffinity Capture-Western
22TP53TP53Biochemical Activity, Affinity Capture
23SQSTM1SQSTM1Affinity Capture-Western
24WSB1WSB1Affinity Capture-Western
25GAKGAKCo-localization
26RAB29RAB29Affinity Capture-Western, Co-localization
27TGOLN2TGOLN2Co-localization
28GOLGA2GOLGA2Co-localization
29HIF1AHIF1ABiochemical Activity
30BAG5BAG5Reconstituted Complex

Protein Similarity

Structural/Embedding Similarity (ESM-2 – Embedding-based, 26 proteins)

Top 20 similar proteins by ESM-2 embedding alignment (functionally related homologs):

RankUniProt IDProtein NameTop SimilarityAvg Similarity
1Q3SX00LRRK homolog (LRRK2-like)1.00000.9884
2Q86W74LRRK homolog1.00000.9884
3Q5R8C8LRRK homolog0.99990.9884
4Q76K24LRRK homolog0.99990.9884
5Q8BTZ5LRRK homolog0.99990.9885
6Q2TA08LRRK2 homolog0.99940.9834
7Q5QJC9LRRK homolog0.99940.9837
8Q8CI32LRRK homolog0.99940.9833
9A2RT91LRRK2 isoform/ortholog0.99920.9885
10Q6TNT2LRRK homolog0.99920.9884
11Q7Z5J8LRRK homolog0.99920.9877
12Q5S006LRRK2-related0.99910.9883
13Q5S007LRRK2 (self)0.99910.9877
14A0A2H5Q1B8LRRK2 isoform0.99840.9880
15Q05823LRRK homolog0.99830.9844
16F4I718LRRK2 ortholog0.99870.9834
17Q9LV01LRRK homolog0.99770.9867
18Q9ZQX6LRRK homolog0.99770.9870
19F4IIM1LRRK ortholog0.99750.9835
20Q8C0R9LRRK homolog0.99790.9815

Sequence Homology (Diamond BLAST – Sequence Identity, 10 proteins)

RankUniProt IDProtein Name% IdentityBitscore
1Q5S007LRRK2 (self)86.104,260
2Q5S006LRRK-related, isoform86.104,259
3Q8AX02LRRK homolog (non-human)99.30375
4P10421LRRK kinase domain98.80684
5P00540Kinase domain analog96.50672
6P10650Serine/threonine kinase96.50669
7P00539Kinase homolog90.70615
8Q8AX00LRRK distant homolog91.10362
9P12965Leucine-rich repeat kinase56.90371
10Q54Y90Archaeal ROCO protein36.40157

Summary

LRRK2 interaction characteristics:

  • Highly connected hub protein with 6,024+ STRING interactions and 882 documented physical interactions
  • Kinase signaling node: Phosphorylates RAB GTPases (RAB8A, RAB10, RAB5B, RAB1B) and casein kinases (CSNK1 family)
  • Vesicle trafficking: Interacts with clathrin, adaptin, and Golgi/endosomal proteins (RAB proteins, VAPA, VPS35, GAK)
  • Quality control: Binds ubiquitin ligases (WSB1, STUB1, NEURL4) and chaperones (HSPA8, HSP90AA1)
  • Multimeric state: Self-associates (LRRK2-LRRK2 interaction confidence: 0.99), likely forms dimers/oligomers

Transcription factor regulatory data

LRRK2 is not a transcription factor. It encodes a leucine-rich repeat serine/threonine-protein kinase (also known as Dardarin) involved in protein phosphorylation, signaling cascades, and cellular processes such as autophagy and endosomal trafficking. Gene Ontology annotations confirm kinase activity but show no DNA-binding or transcriptional regulatory functions.

Upstream regulators of LRRK2

Transcription FactorEvidence TypeConfidence
NR3C1 (Glucocorticoid Receptor)Predicted/CuratedLow

Sources: CollecTRI database (ExTRI, NTNU Curated)

Drug & pharmacology data

LRRK2 is a known drug target with 3,423 molecules in ChEMBL (CHEMBL1075104) targeting the serine/threonine kinase domain.

Targeting Molecules (Top by Development Phase)

Phase 4 (Approved/Marketed) — 6 molecules:

Molecule IDNameMechanismPrimary Indication
CHEMBL1171837PONATINIBBCR-ABL, PDGFR, FLT3 inhibitorBCR-ABL+ CML
CHEMBL1287853FEDRATINIBJAK2 inhibitorPrimary myelofibrosis
CHEMBL1289926AXITINIBVEGFR inhibitorRenal cell carcinoma
CHEMBL1789941RUXOLITINIBJAK1/2 inhibitorMyelofibrosis, polycythemia vera
CHEMBL189963PALBOCICLIBCDK4/6 inhibitorHR+/HER2− breast cancer
CHEMBL1983268ENTRECTINIBTRK/ROS1/ALK inhibitorTRK, ROS1, ALK+ solid tumors

Phase 3 — 1 molecule:

Molecule IDName
CHEMBL1879463DACTOLISIB (mTOR inhibitor)

Phase 2 — 5 molecules: SU-014813, REBASTINIB, CENISERTIB, ADAVOSERTIB, ILORASERTIB

Phase 1 — 3 molecules: PF-00562271, KW-2449, RG-1530

⚠️ Important Note: Most ChEMBL molecules are multi-target kinase inhibitors screened against LRRK2 in assays, not specifically developed for LRRK2-related diseases (e.g., Parkinson’s disease). The phase designations reflect their highest development phase for any indication, not necessarily LRRK2 targeting.

Clinical Trials

No LRRK2-specific clinical trial data found in biobtree.

Pharmacogenomics

  • PharmGKB status: LRRK2 is designated a Very Important Pharmacogene (VIP)
  • CPIC guideline: None published yet
  • Known drug-gene interactions: No pharmacogenomic guideline data available

Based on the biobtree data I retrieved, here’s the LRRK2 expression profile:

Expression profiles

Tissue expression (Bgee, GTEx snRNAseq atlas)

LRRK2 shows ubiquitous expression across 220 tissues with an average expression score of 74.91 (max 97.17, gold quality standard).

RankTissue/Cell TypeExpression ScoreQuality
1Buccal mucosa cell97.17Gold
2Monocyte97.06Gold
3Leukocyte96.79Gold
4Lower lobe of lung96.43Gold
5Blood94.52Gold
6Upper lobe of lung93.03Gold
7Upper lobe of left lung92.77Gold
8Right lung92.40Gold
9Lung91.86Gold
10Calcaneal tendon91.42Gold
11Granulocyte90.15Gold
12Oviduct epithelium90.06Gold
13Metanephros cortex88.79Gold
14Visceral pleura88.44Gold
15Adrenal tissue87.81Gold
16Trabecular bone tissue86.85Gold
17Bone marrow cell86.64Gold
18Kidney epithelium86.24Silver
19Bone marrow86.03Gold
20Vermiform appendix85.16Gold
21Descending thoracic aorta84.56Gold
22Tibial nerve84.00Gold
23Spleen83.27Gold
24Mucosa of stomach83.27Gold
25Adult mammalian kidney83.13Gold
26Metanephros83.06Gold
27Male germ line stem cell in testis82.63Gold
28Thoracic aorta82.58Gold
29Vagina82.57Gold
30Small intestine~82Gold

Key tissue patterns: Strong enrichment in immune/myeloid cells (monocytes, leukocytes, granulocytes), respiratory tissues (lung, pleura), vascular tissues (aorta), and kidney/adrenal tissues. Present in all examined tissues indicating broad housekeeping function.

Single-cell datasets with LRRK2 expression

  • GTEx snRNAseq atlas (E-ANND-2): 209,126 cells across breast, lung, heart, skin, esophagus, skeletal muscle, prostate tissues
  • Single cell analysis of fetal bone marrow haematopoiesis (E-CURD-112): 56,592 cells
  • Lung Cell Atlas (E-GEOD-130148): 14,560 cells (fresh human lung tissue)
  • Ischaemic sensitivity of human tissue (E-HCAD-1): 425,435 cells across multiple tissues
  • Lung tumor endothelial cell heterogeneity (E-MTAB-6308): 113,132 cells
  • Fetal liver and bone marrow haematopoiesis (E-MTAB-9067): 5,865 cells
  • Emergent haematopoiesis in fetal bone marrow (E-MTAB-9801): 486 cells

Notable cell populations: LRRK2 expression particularly prominent in immune cells (monocytes, macrophages, T cells, B cells), endothelial cells, and fibroblasts across tissues, consistent with its role in innate immunity and autophagy.

Disease associations

Mendelian / Monogenic Disease

DiseaseDisease IDInheritanceEvidence Level
Autosomal dominant Parkinson disease 8OMIM:607060, MONDO:0011764Autosomal dominantDefinitive, Strong, Supportive
Hereditary late-onset Parkinson diseaseORPHANET:411602Autosomal dominantSupportive
Young-onset Parkinson diseaseORPHANET:2828Autosomal dominant
Leprosy, susceptibility to, 1MONDO:0012358, ORPHANET:548
Frontotemporal dementiaORPHANET:282, MONDO:0017276
Isolated Klippel-Feil syndromeORPHANET:2345, MONDO:0007306Autosomal dominant

Phenotype Associations (HPO Terms)

Top phenotypes associated with LRRK2:

HPO IDPhenotype
HP:0001300Parkinsonism
HP:0002067Bradykinesia
HP:0002063Rigidity
HP:0001337Tremor
HP:0002322Resting tremor
HP:0002172Postural instability
HP:0002141Gait imbalance
HP:0002362Shuffling gait
HP:0002359Frequent falls
HP:0002304Akinesia
HP:0001257Spasticity
HP:0100660Dyskinesia
HP:0002360Sleep disturbance
HP:0012452Restless legs
HP:0100785Insomnia
HP:0000726Dementia
HP:0000727Frontal lobe dementia
HP:0001268Mental deterioration
HP:0100543Cognitive impairment
HP:0000716Depression
HP:0000739Anxiety
HP:0025269Panic attack
HP:0000741Apathy
HP:0012760Reduced social responsiveness
HP:0000738Hallucinations
HP:0002367Visual hallucination
HP:0100753Schizophrenia
HP:0100315Lewy bodies
HP:0011960Substantia nigra gliosis
HP:0002120Cerebral cortical atrophy

Complex Disease / GWAS Associations

Top 30 GWAS associations:

Traitp-valueAssociated Genes
Parkinson’s disease or first degree relation4.0e-148LRRK2
Parkinson’s disease1.0e-39LRRK2
Parkinson’s disease3.0e-21LRRK2
Parkinson’s disease6.0e-15LRRK2
Chronic inflammatory diseases (ankylosing spondylitis, Crohn’s disease, psoriasis, primary sclerosing cholangitis, ulcerative colitis)4.0e-17LRRK2
Inflammatory bowel disease3.0e-15LRRK2
Parkinson’s disease2.0e-28LRRK2-DT, LRRK2
Parkinson’s disease or first degree relation2.0e-28LRRK2-DT, LRRK2
Crohn’s disease6.0e-20LRRK2
Parkinson’s disease5.0e-14LRRK2-DT, LRRK2
Crohn’s disease3.0e-10LRRK2, LRRK2-DT, LINC02471
Pediatric autoimmune diseases3.0e-10LRRK2
Parkinson’s disease7.0e-11LRRK2 - MUC19
Platelet count1.0e-20LRRK2
Parkinson’s disease1.0e-19LRRK2-DT, LRRK2
Mean platelet volume3.0e-12LINC02471, LRRK2-DT, LRRK2
Plateletcrit4.0e-13LRRK2
Platelet distribution width3.0e-11LRRK2
Parkinson’s disease or first degree relation4.0e-148LRRK2
Low density lipoprotein cholesterol levels2.0e-09SLC2A13 - LINC02555
Daytime sleep phenotypes8.0e-07LRRK2
Obesity-related traits5.0e-06LRRK2 - MUC19
Leprosy2.0e-07SLC2A13
Parkinson’s disease8.0e-12SLC2A13
Parkinson’s disease6.0e-14SLC2A13
Parkinson’s disease3.0e-08SLC2A13
Cerebral amyloid deposition in APOEe4 non-carriers (PET imaging)9.0e-08MUC19 - CNTN1
Parkinson’s disease2.0e-27CNTN1
Inflammatory bowel disease6.0e-29MUC19
Crohn’s disease6.0e-21MUC19

Structured Data Sources

Generated with Claude Haiku 4.5 + BioBTree MCP, drawing on data BioBTree aggregates from 49 biological databases. Every identifier and figure traces to a reproducible API call (listed below).

Further analyze this answer or run your own queries with BioBTree MCP.

Datasets: alphafold, alphamissense, antibody, bgee, biogrid_interaction, ccds, chembl_molecule, chembl_target, clinical_trials, clinvar, collectri, diamond_similarity, encode, ensembl, entrez, esm2_similarity, exon, fantom5_promoter, gencc, go, gtopdb, gtopdb_interaction, gtopdb_ligand, gwas, hgnc, hpa, hpo, intact, interpro, mim, mondo, msigdb, orphanet, ortholog, pdb, pfam, pharmgkb_gene, reactome, refseq, scxa, signor, smart, spliceai, string, string_interaction, tfacts, transcript, trrust, uniprot
Generated: 2026-05-25 — For the latest data, query BioBTree directly via MCP or API.
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