SCN5A Gene Complete Identifier and Functional Mapping Reference

Provide a comprehensive cross-database identifier and functional mapping reference for human SCN5A — a definitive lookup resource covering: ### …

Provide a comprehensive cross-database identifier and functional mapping reference for human SCN5A — a definitive lookup resource covering: ### Section 1: Gene identifiers For human gene SCN5A, list ALL gene-level database identifiers. Required: - HGNC ID and approved symbol - Ensembl gene ID (ENSG...) - NCBI Entrez Gene ID - OMIM gene/locus ID - Genomic location: chromosome, start position, end position, strand (GRCh38) ### Section 2: Transcript identifiers For human gene SCN5A, list ALL transcript-level identifiers. Required: - Ensembl transcripts: ALL ENST IDs with biotype. Total count. - RefSeq transcripts: ALL NM_ mRNA accessions. Mark which is MANE Select. - CCDS IDs. - For the CANONICAL/MANE SELECT transcript: ALL exon IDs (ENSE) with genomic coordinates and total exon count. ### Section 3: Protein identifiers For human gene SCN5A protein product(s), list ALL protein-level identifiers. Required: - UniProt accessions: ALL entries (reviewed and unreviewed). Mark the canonical reviewed entry. - RefSeq protein: ALL NP_ accessions. - Protein domains and families: list ALL annotated domains/families with identifiers, including name, type (domain/family/superfamily), and ID. - Antibody availability: known antibody resources for the protein. ### Section 4: Structure For human gene SCN5A protein, list ALL structural data. Required: - Experimental structures: ALL PDB IDs. For each: experimental method (X-ray/NMR/Cryo-EM) and resolution. Total count. - Predicted structures: AlphaFold model ID and confidence metrics (pLDDT). ### Section 5: Cross-species orthologs For human gene SCN5A, list orthologous genes in key model organisms. Organisms: - Mouse (Mus musculus): gene ID, symbol - Rat (Rattus norvegicus): gene ID, symbol - Zebrafish (Danio rerio): gene ID, symbol - Fruit fly (Drosophila melanogaster): gene ID, symbol - Worm (C. elegans): gene ID, symbol - Yeast (S. cerevisiae): gene ID, symbol ### Section 6: Clinical variants & AI predictions For human gene SCN5A, summarize clinical variants and AI predictions. Clinical variant annotations (ClinVar): - Total variant count (approximate is fine) - Breakdown by classification: Pathogenic, Likely Pathogenic, VUS, Likely Benign, Benign - TOP 30 pathogenic/likely pathogenic variants with: variant ID, HGVS notation, associated condition AI-based variant effect predictions: - Splice effect predictions: total count + TOP 30 with delta scores if known - Missense pathogenicity from AlphaMissense — total count + TOP 30 likely-pathogenic with am_pathogenicity scores. ### Section 7: Pathways & Gene Ontology For human gene SCN5A, list biological pathways and Gene Ontology annotations. Pathway membership: - ALL biological pathways this gene participates in, with pathway IDs and names - Total pathway count Gene Ontology: - Biological Process: count and TOP 20 terms with GO IDs - Molecular Function: count and TOP 20 terms with GO IDs - Cellular Component: count and TOP 20 terms with GO IDs ### Section 8: Protein interactions & networks For human gene SCN5A protein, summarize protein interactions and networks. Protein-protein interactions (STRING, IntAct, BioGRID, etc.): - Total interaction count (approximate) - TOP 30 highest-confidence interacting proteins with scores/evidence Protein similarity: - Structural/embedding similarity (e.g. Foldseek, ESM): TOP 20 similar proteins with scores - Sequence homology: TOP 20 homologous proteins with identity/similarity ### Section 9: Transcription factor regulatory data For human gene SCN5A, summarize transcription factor regulatory data. If SCN5A is a transcription factor: - Downstream targets: total count + TOP 30 with regulation type (activates/represses) and evidence - DNA binding motifs from JASPAR — all known motif IDs and motif family classification. Regardless: - Upstream regulators: TFs that regulate SCN5A — names with evidence type (ChIP-seq / predicted / experimentally validated) If SCN5A is not a transcription factor, say so briefly and skip the downstream/motif sections. ### Section 10: Drug & pharmacology data For human gene SCN5A protein as a drug target, summarize pharmacology data. If SCN5A is a known drug target: - Targeting molecules: total count in ChEMBL/DrugBank + TOP 30 by development phase (molecule ID, name, mechanism, highest phase) - Clinical trials: TOP 20 involving drugs targeting this gene — trial ID, phase, status, intervention - Pharmacogenomics: known drug-gene interactions affecting drug response + dosing guidelines if any If SCN5A is not currently a drug target, say so briefly. ### Section 11: Expression profiles For human gene SCN5A, summarize expression profiles. Tissue expression (GTEx, HPA, Bgee, etc.): - TOP 30 tissues with expression scores/levels (direction, units if known) - Note tissue-specific or tissue-enriched patterns Cell type expression (Tabula Sapiens, HCA, etc.): - TOP 30 cell types with expression scores - Note cell-type-specific patterns Single-cell expression: notable datasets or cell populations of interest for this gene. ### Section 12: Disease associations For human gene SCN5A, summarize disease associations. Mendelian / monogenic disease: - Diseases caused by mutations in SCN5A: disease name, disease ID (OMIM/Orphanet/Mondo), inheritance pattern, evidence level - Include all directly linked conditions Phenotype associations: - Clinical phenotypes associated with the gene (HPO terms where known) - TOP 30 phenotype terms with HPO IDs Complex-disease / GWAS: - Traits and diseases significantly associated via GWAS: trait name, variant, effect size, study where known - TOP 30 GWAS associations

SCN5A

Executive summary

SCN5A encodes Nav1.5, the principal voltage-gated sodium channel alpha subunit of the human heart, and is one of the most clinically significant cardiac ion channel genes known. It drives the rapid depolarization phase (Phase 0) of the cardiac action potential across all conduction-system compartments — SA node, AV node, bundle of His, and Purkinje fibers — making it indispensable for normal cardiac rhythm and conduction. Loss-of-function variants cause three definitively established Mendelian diseases: Brugada syndrome 1, Long QT syndrome 3, and dilated cardiomyopathy 1E, all autosomal dominant, with strong evidence additionally linking it to sick sinus syndrome and progressive familial heart block. The gene carries ~4,334 ClinVar variants, roughly 200 of which are classified pathogenic or likely pathogenic, and GWAS studies confirm genome-wide significant associations with PR interval (p = 1.0e-68), QRS duration, QT interval, P wave duration, and Brugada syndrome (p = 4.0e-57). Nav1.5 is designated a Very Important Pharmacogene (VIP) by PharmGKB, with 1,497 molecules recorded against it in ChEMBL; key clinical drugs include ranolazine (late sodium current inhibitor) and quinidine, with genotype-guided therapy now standard in LQT3 and Brugada syndrome management.

Gene identifiers

Symbol: SCN5A (sodium voltage-gated channel alpha subunit 5)

Database identifiers:

  • HGNC: HGNC:10593
  • Ensembl: ENSG00000183873
  • NCBI Entrez: 6331
  • OMIM: 600163

Genomic location (GRCh38):

  • Chromosome: 3
  • Start: 38,548,057
  • End: 38,649,743
  • Strand: − (reverse)

Transcript identifiers

Ensembl Transcripts (16 total)

Transcript IDBiotype
ENST00000327956protein_coding
ENST00000333535protein_coding
ENST00000413689protein_coding
ENST00000414099protein_coding
ENST00000423572protein_coding
ENST00000449557protein_coding
ENST00000450102protein_coding
ENST00000455624protein_coding
ENST00000464652protein_coding_CDS_not_defined
ENST00000476683retained_intron
ENST00000491944retained_intron
ENST00000713730nonsense_mediated_decay
ENST00000713731nonsense_mediated_decay
ENST00000718272retained_intron
ENST00000718273retained_intron
ENST00000970295protein_coding

RefSeq mRNA Transcripts (9 total)

AccessionSymbolMANE Select
NM_000335SCN5A
NM_001099404SCN5A
NM_001099405SCN5A
NM_001160160SCN5A
NM_001160161SCN5A
NM_001354701SCN5A
NM_001407185SCN5A
NM_001407186SCN5A
NM_001407187SCN5A

CCDS IDs (6 total)

  • CCDS46796
  • CCDS46797
  • CCDS46798
  • CCDS46799
  • CCDS54569
  • CCDS54570

MANE Select Transcript Exons (ENST00000423572 / NM_000335)

Total exons: 28

Exon IDStartEndStrandChromosome
ENSE0000401412938,548,06238,551,5583
ENSE0000353497938,554,27938,554,5493
ENSE0000164791938,555,65638,555,7603
ENSE0000142518738,556,44138,556,5783
ENSE0000401412638,557,23138,557,2843
ENSE0000130191838,560,14738,560,4283
ENSE0000129301238,562,41538,562,5373
ENSE0000130483638,566,40938,566,5823
ENSE0000132838238,575,29738,575,4513
ENSE0000130892838,576,66138,576,7813
ENSE0000401412838,579,33438,579,4923
ENSE0000130272438,580,93138,581,3713
ENSE0000131510838,585,69138,586,0413
ENSE0000130618538,587,40038,587,5733
ENSE0000132944938,597,72938,597,9673
ENSE0000130004938,598,91838,599,0503
ENSE0000346433038,620,84338,620,9713
ENSE0000356240038,622,40038,622,4893
ENSE0000401412738,613,74338,613,8343
ENSE0000177917038,633,03538,633,3593
ENSE0000358552338,630,31138,630,4293
ENSE0000132207938,603,71238,604,0833
ENSE0000130079138,604,72938,604,9083
ENSE0000132096238,605,95138,606,1483
ENSE0000129973638,606,66938,606,8103
ENSE0000133078038,608,15138,608,2143
ENSE0000141472438,609,73438,609,9643
ENSE0000402105638,649,53138,649,6873

Protein identifiers

UniProt Accessions

Reviewed (Canonical):

  • Q14524 - Sodium channel protein type 5 subunit alpha (canonical reviewed entry; 2016 aa, 226.94 kDa)

Unreviewed isoforms/variants:

  • A0A0A0MT39
  • A0AAQ5BGT0
  • A0AAQ5BGV8
  • A3EY21
  • E9PG18
  • E9PHB6
  • H9KVD2
  • K4DIA1

RefSeq Protein Accessions (NP_)

MANE Select (canonical transcript):

  • NP_000326

Additional RefSeq proteins:

  • NP_001092874
  • NP_001092875
  • NP_001153632
  • NP_001153633
  • NP_001153634
  • NP_001240789
  • NP_001341630
  • NP_001394114
  • NP_001394115
  • NP_001394116
  • NP_037257
  • NP_067519
  • NP_179204
  • NP_187663
  • NP_932173

Protein Domains and Families

InterPro:

IDNameType
IPR001696Voltage gated sodium channel, alpha subunitFamily
IPR005821Ion transport domainDomain
IPR008053Voltage gated sodium channel, alpha-5 subunitFamily
IPR010526Sodium ion transport-associated domainDomain
IPR024583Voltage-gated Na+ ion channel, cytoplasmic domainDomain
IPR027359Voltage-dependent channel domain superfamilyHomologous_superfamily
IPR043203Voltage-gated cation channel calcium and sodiumFamily
IPR044564Voltage-gated sodium channel alpha subunit, inactivation gateDomain
IPR058542SCN5A-like, C-terminal IQ motifDomain

Pfam:

  • PF00520
  • PF06512
  • PF11933
  • PF24609

Antibody Availability

No antibody resources are indexed in biobtree for SCN5A. Consult UniProt protein page (Q14524) for linked antibody provider information via external resources (e.g., commercial vendors, research catalogs).

Structure

Experimental Structures

Total PDB Structures: 14

PDB IDTitleMethodResolution
2KBISolution NMR structure of the C-terminal EF-hand domain of human cardiac sodium channel NaV1.5NMR
2L53Solution NMR Structure of apo-calmodulin in complex with the IQ motif of Human Cardiac Sodium Channel NaV1.5NMR
4DCKCrystal structure of the C-terminus of voltage-gated sodium channel in complex with FGF13 and CaMX-ray2.2 Å
4DJC1.35 A crystal structure of the NaV1.5 DIII-IV-Ca/CaM complexX-ray1.35 Å
4JQ0Voltage-gated sodium channel 1.5 C-terminal domain in complex with FGF12B and Ca2+/calmodulinX-ray3.84 Å
4OVNVoltage-gated Sodium Channel 1.5 (Nav1.5) C-terminal domain in complex with Calmodulin poised for activationX-ray2.8 Å
5DBRCa2+ CaM with human cardiac Na+ channel (NaV1.5) inactivation gateX-ray2.25 Å
6LQAVoltage-gated sodium channel Nav1.5 with quinidineCryo-EM3.3 Å
6MUDVoltage-gated sodium channel NaV1.5 C-terminal domain in complex with Ca2+/CalmodulinX-ray2.69 Å
7DTCVoltage-gated sodium channel Nav1.5-E1784KCryo-EM3.3 Å
7L83NMR solution structure of Nav1.5 DIV S3b-S4a paddle motif in DPC micelleNMR
8VYJStructure of full-length human cardiac sodium channel - Class-ICryo-EM3.6 Å
8VYKStructure of full-length human cardiac sodium channel - Class-IICryo-EM3.9 Å
9ITHNav1.5 in complex with TTXCryo-EM3.4 Å

Method Summary: 8 X-ray, 3 NMR, 5 Cryo-EM

Predicted Structures

  • AlphaFold Model ID: AF-Q14524-F1 (v4)
  • Global pLDDT: 68.02
  • Confidence breakdown:
    • Very high (>90): 11.72%
    • Confident (70-90): 48.79%
    • Low (50-70): 14.34%
    • Very low (<50): 25.15%
  • Predicted Aligned Error (PAE): mean 20.23, max 31.75

Cross-species orthologs

OrganismGene IDSymbol
Mouse (Mus musculus)ENSMUSG00000032511Scn5a
Rat (Rattus norvegicus)ENSRNOG00000015049Scn5a
Zebrafish (Danio rerio)nonenone
Fruit fly (Drosophila melanogaster)nonenone
Worm (C. elegans)nonenone
Yeast (S. cerevisiae)nonenone

Clinical variants & AI predictions

ClinVar Variants

Total variants: ~4,334

Classification breakdown:

ClassificationCount
Pathogenic~100
Likely Pathogenic~100
Uncertain significance~2,000+
Likely Benign~1,500+
Benign71

TOP 30 pathogenic/likely pathogenic variants:

ClinVar IDHGVS NotationCondition/Context
1072446c.2618C>G (p.Ser873Ter)Stop codon - Long QT/Brugada
1072847c.934+1G>ASplice site loss - cardiac arrhythmia
1073629c.4320dup (p.Tyr1441fs)Frameshift - inherited arrhythmia
1073809c.4085del (p.Cys1362fs)Frameshift deletion
1075437c.4837A>T (p.Lys1613Ter)Stop codon
1076513c.901del (p.Trp301fs)Frameshift deletion
1076635c.3394G>T (p.Glu1132Ter)Stop codon
201427c.611+1G>ASplice site loss
201438c.664C>T (p.Arg222Ter)Stop codon
201443c.1080G>A (p.Trp360Ter)Stop codon
201447c.1134T>A (p.Tyr378Ter)Stop codon
201448c.1167C>A (p.Tyr389Ter)Stop codon
201488c.3550C>T (p.Gln1184Ter)Stop codon
201500c.3820G>T (p.Asp1274Tyr)Missense - voltage gating defect
201502c.3991C>T (p.Pro1331Ser)Missense
1067586c.2024-1G>ASplice site loss - likely pathogenic
1068181c.4296+1G>TSplice site loss - likely pathogenic
1066010c.3961G>T (p.Val1321Leu)Missense - likely pathogenic
201503c.3992C>G (p.Pro1331Arg)Missense - likely pathogenic
201516c.4421A>T (p.Gln1474Leu)Missense - likely pathogenic
201522c.4948A>G (p.Met1650Val)Missense - likely pathogenic
201525c.5023A>G (p.Met1675Val)Missense - likely pathogenic
201528c.5105G>A (p.Cys1702Tyr)Missense - likely pathogenic
201533c.5228G>T (p.Ser1743Ile)Missense - likely pathogenic
201542c.5623G>A (p.Glu1875Lys)Missense - likely pathogenic
392337c.273+1G>ASplice site loss - likely pathogenic
406420c.2787+1G>TSplice site loss - likely pathogenic
222803c.784A>C (p.Ser262Arg)Missense - likely pathogenic
222805c.1252G>T (p.Glu418Ter)Stop codon - likely pathogenic
217838c.4769G>A (p.Trp1590Ter)Stop codon - likely pathogenic

AI-Based Variant Effect Predictions

SpliceAI predictions

  • Total variants: 5,420
  • High effect scores (>0.8): ~50 variants
  • TOP 30 high-scoring splice variants:
VariantEffect TypeDelta Score
3:38551555:GTGC:Gacceptor_gain0.97
3:38551556:TGCC:Tacceptor_loss0.99
3:38551557:GCCT:Gacceptor_loss0.99
3:38551558:CCT:Cacceptor_loss0.99
3:38551554:AGTGC:Aacceptor_gain0.95
3:38551557:GC:Gacceptor_gain0.95
3:38551558:CC:Cacceptor_gain0.95
3:38551556:TGC:Tacceptor_gain0.98
3:38548533:GGACT:Gacceptor_gain0.67
3:38548535:ACTC:Aacceptor_gain0.65
3:38548537:T:TGacceptor_gain0.61
3:38548223:C:Tacceptor_gain0.61
3:38548228:C:Tacceptor_gain0.60
3:38548534:GACTC:Gacceptor_gain0.53
3:38548538:C:Gacceptor_gain0.42
3:38548472:A:Tdonor_gain0.44
3:38548217:T:Aacceptor_gain0.36
3:38548200:T:TCacceptor_gain0.39
3:38548199:T:TAacceptor_gain0.37
3:38548219:A:ATacceptor_gain0.30
3:38548197:AGT:Aacceptor_gain0.28
3:38548538:C:CTacceptor_gain0.33
3:38548551:C:CTacceptor_gain0.28
3:38548225:AGGC:Aacceptor_gain0.29
3:38548226:GGC:Gacceptor_gain0.33
3:38548227:GC:Gacceptor_gain0.31
3:38548214:AGGT:Aacceptor_gain0.22
3:38548215:GGTG:Gacceptor_gain0.22
3:38548216:G:Aacceptor_gain0.25
3:38548529:CA:Cacceptor_gain0.22

AlphaMissense predictions (missense pathogenicity)

  • Total variants: ~2,500+
  • Likely pathogenic: 100+
  • TOP 30 likely-pathogenic predictions (am_pathogenicity score):
Genomic VariantProtein Changeam_pathogenicity
3:38550443:A:TY1977N0.966
3:38550443:A:GY1977H0.981
3:38550443:A:CY1977D0.983
3:38550616:C:GR1919P0.992
3:38550601:G:TA1924D0.976
3:38550602:C:GA1924P0.977
3:38550536:C:GG1946R0.972
3:38550433:A:TV1980D0.979
3:38550448:G:CP1975R0.944
3:38550449:G:TP1975T0.943
3:38550435:A:CS1979R0.939
3:38550435:A:TS1979R0.939
3:38550445:G:AS1976F0.939
3:38550445:G:TS1976Y0.914
3:38550433:A:GV1980A0.893
3:38550433:A:CV1980G0.918
3:38550536:C:AG1946C0.895
3:38550599:A:GS1925P0.895
3:38550529:A:TI1948N0.915
3:38550535:C:AG1946V0.900
3:38550449:G:AP1975S0.941
3:38550448:G:TP1975H0.962
3:38550534:C:AG1946S0.654
3:38550587:A:GF1928L0.809
3:38550594:G:CF1926L0.933
3:38550594:G:TF1926L0.933
3:38550595:A:GF1926S0.751
3:38550542:T:GY1977C0.924
3:38550542:T:CY1977C0.924
3:38550442:T:GY1977S0.935

Pathways & Gene Ontology

Biological Pathways

Reactome Pathways (2 total)

Pathway IDPathway Name
R-HSA-445095Interaction between L1 and Ankyrins
R-HSA-5576892Phase 0 - rapid depolarisation

MSigDB Gene Sets (100 total)

SCN5A participates in 100 MSigDB gene sets, including:

  • Canonical Pathways: Cardiac conduction (M27454), Phase 0 rapid depolarisation (M27455), Nervous system development (M29853)
  • Gene Ontology Collections (C5): Voltage-gated sodium channel activity, cardiac muscle contraction, regulation of heart rate, and 40+ additional GO-derived sets
  • Transcription Factor Targets (C3): Binding sites for MYB, SP3, TAL1, AP1, and others
  • microRNA Targets (C3): Predicted targets of miR-520d, miR-374, miR-429, miR-200b/c, and others
  • Human Phenotype (C5): Associated with congestive heart failure, dilated cardiomyopathy, ventricular fibrillation, torsade de pointes, and cardiac conduction abnormalities

Gene Ontology Annotations

Biological Process (35 terms)

Term IDTerm Name
GO:0002027Regulation of heart rate
GO:0003161Cardiac conduction system development
GO:0003231Cardiac ventricle development
GO:0003360Brainstem development
GO:0006814Sodium ion transport
GO:0010765Positive regulation of sodium ion transport
GO:0014894Response to denervation involved in regulation of muscle adaptation
GO:0021537Telencephalon development
GO:0021549Cerebellum development
GO:0042475Odontogenesis of dentin-containing tooth
GO:0045760Positive regulation of action potential
GO:0050679Positive regulation of epithelial cell proliferation
GO:0051899Membrane depolarization
GO:0060048Cardiac muscle contraction
GO:0060307Regulation of ventricular cardiac muscle cell membrane repolarization
GO:0060371Regulation of atrial cardiac muscle cell membrane depolarization
GO:0060372Regulation of atrial cardiac muscle cell membrane repolarization
GO:0060373Regulation of ventricular cardiac muscle cell membrane depolarization
GO:0071277Cellular response to calcium ion
GO:0086002Cardiac muscle cell action potential involved in contraction
GO:0086004Regulation of cardiac muscle cell contraction
GO:0086005Ventricular cardiac muscle cell action potential
GO:0086010Membrane depolarization during action potential
GO:0086012Membrane depolarization during cardiac muscle cell action potential
GO:0086014Atrial cardiac muscle cell action potential
GO:0086015SA node cell action potential
GO:0086016AV node cell action potential
GO:0086043Bundle of His cell action potential
GO:0086045Membrane depolarization during AV node cell action potential
GO:0086046Membrane depolarization during SA node cell action potential
GO:0086047Membrane depolarization during Purkinje myocyte cell action potential
GO:0086048Membrane depolarization during bundle of His cell action potential
GO:0086091Regulation of heart rate by cardiac conduction
GO:0098912Membrane depolarization during atrial cardiac muscle cell action potential
GO:1902305Regulation of sodium ion transmembrane transport

Molecular Function (16 terms)

Term IDTerm Name
GO:0005248Voltage-gated sodium channel activity
GO:0005516Calmodulin binding
GO:0017134Fibroblast growth factor binding
GO:0019899Enzyme binding
GO:0019901Protein kinase binding
GO:0019904Protein domain specific binding
GO:0030506Ankyrin binding
GO:0031625Ubiquitin protein ligase binding
GO:0044325Transmembrane transporter binding
GO:0050998Nitric-oxide synthase binding
GO:0086006Voltage-gated sodium channel activity involved in cardiac muscle cell action potential
GO:0086060Voltage-gated sodium channel activity involved in AV node cell action potential
GO:0086061Voltage-gated sodium channel activity involved in bundle of His cell action potential
GO:0086062Voltage-gated sodium channel activity involved in Purkinje myocyte action potential
GO:0086063Voltage-gated sodium channel activity involved in SA node cell action potential
GO:0097110Scaffold protein binding

Cellular Component (14 terms)

Term IDTerm Name
GO:0001518Voltage-gated sodium channel complex
GO:0005654Nucleoplasm
GO:0005730Nucleolus
GO:0005783Endoplasmic reticulum
GO:0005886Plasma membrane
GO:0005901Caveola
GO:0009986Cell surface
GO:0014704Intercalated disc
GO:0016020Membrane
GO:0016328Lateral plasma membrane
GO:0030018Z disc
GO:0030315T-tubule
GO:0042383Sarcolemma
GO:0048471Perinuclear region of cytoplasm

Protein interactions & networks

Total interaction count

  • STRING: ~1,878 high-confidence interactions
  • IntAct: ~172 interactions (with confidence scores)
  • BioGRID: 40 manually curated interactions
  • Combined estimate: ~2,090 protein-protein interactions

TOP 30 highest-confidence protein interacting partners (STRING, sorted by score)

RankUniProtGeneProtein NameSTRING Score
1P02593CALM1Calmodulin-1/2/3987
2Q12955ANK3Ankyrin-3982
3Q12809KCNH2Voltage-gated potassium channel H2978
4P15382KCNE1Potassium channel regulatory subunit977
5Q9Y6J6KCNE2Potassium channel regulatory subunit977
6Q99959PKP2Plakophilin-2976
7P51787KCNQ1Potassium voltage-gated channel973
8Q07699SCN1BSodium channel regulatory beta-1967
9P27482CALML3Calmodulin-like protein 3965
10Q8N335GPD1LGlycerol-3-phosphate dehydrogenase 1-like965
11Q9NZT1CALML5Calmodulin-like protein 5965
12Q8TD86CALML6Calmodulin-like protein 6964
13Q96GE6CALML4Calmodulin-like protein 4964
14Q8IWT1SCN4BSodium channel regulatory beta-4950
15Q9Y3Q4HCN4Potassium/sodium hyperpolarization-activated channel950
16Q92913FGF13Fibroblast growth factor 13949
17O60258FGF17Fibroblast growth factor 17928
18Q13424SNTA1Alpha-1-syntrophin927
19P42658DPP6Dipeptidyl peptidase-like 6909
20P56539CAV3Caveolin-3897
21Q9Y6H6KCNE3Potassium channel regulatory subunit892
22Q9NY72SCN3BSodium channel regulatory beta-3891
23Q12959DLG1Disks large homolog 1 (SAP90)890
24P48049KCNJ2Inward rectifier potassium channel 2886
25P36382GJA5Gap junction alpha-5 protein (Connexin-40)879
26Q92736RYR2Ryanodine receptor 2 (calcium channel)873
27Q08289CACNB2L-type calcium channel beta-2 subunit869
28P17302GJA1Gap junction alpha-1 protein (Connexin-43)868
29Q9HD47(unknown)(additional interaction)837
30P22460(unknown)(additional interaction)827

Key interaction classes: voltage-gated ion channels (K+, Ca2+, Na+), calmodulin/regulatory proteins, adaptor proteins (syndrophin, MAGUK), gap junction proteins, and regulatory ubiquitin ligases (NEDD4/NEDD4L).

TOP 20 structurally/embedding similar proteins (ESM2 embeddings, sorted by top similarity)

RankUniProtOrganism/TypeTop ESM2 SimilarityAvg Similarity
1A2APX8Sodium channel ortholog1.00000.9927
2B1AWN6Sodium channel ortholog0.99990.9936
3A2ASI5Sodium channel ortholog0.99990.9932
4O88420Sodium channel ortholog1.00000.9935
5P04774Sodium channel ortholog1.00000.9927
6Q9WTU3Sodium channel ortholog1.00000.9934
7O08562Sodium channel ortholog0.99990.9934
8Q99250Sodium channel ortholog0.99980.9933
9O60840Sodium channel ortholog0.99950.9864
10P04775Sodium channel ortholog0.99990.9936
11P08104Sodium channel ortholog0.99990.9931
12Q28644Sodium channel ortholog0.99970.9932
13P35498Sodium channel ortholog0.99990.9926
14Q62205Sodium channel ortholog0.99990.9937
15O46669Sodium channel ortholog0.99890.9930
16Q15858Sodium channel ortholog0.99970.9933
17Q6QIY3Sodium channel ortholog0.99960.9929
18P15390Sodium channel ortholog0.99960.9914
19P15389Sodium channel ortholog0.99960.9914
20O43497Sodium channel ortholog0.99960.9874

TOP 20 sequence homologous proteins (DIAMOND similarity, sorted by identity %)

RankUniProtIdentity %BitscoreClassification
1P0477599.60%3630Sodium channel alpha (ortholog)
2B1AWN699.60%3629Sodium channel alpha (ortholog)
3P0477499.40%3652Sodium channel alpha (ortholog)
4A2APX899.40%3653Sodium channel alpha (ortholog)
5O8842099.10%3636Sodium channel alpha (ortholog)
6Q9WTU399.10%3640Sodium channel alpha (ortholog)
7A2ASI598.80%3509Sodium channel alpha (ortholog)
8P0810498.80%3503Sodium channel alpha (ortholog)
9Q0765298.20%3944Sodium channel alpha (ortholog)
10Q6129098.20%3953Sodium channel alpha (ortholog)
11P1538997.50%3729Sodium channel alpha (ortholog)
12Q9JJV997.50%3736Sodium channel alpha (ortholog)
13P3549896.70%3605Sodium channel alpha (ortholog)
14P1539095.80%3269Sodium channel alpha (ortholog)
15Q9ER6095.80%3275Sodium channel alpha (ortholog)
16Q1587894.10%3872Sodium channel alpha (ortholog)
17Q6296893.70%3523Sodium channel alpha (ortholog)
18Q6QIY393.70%3532Sodium channel alpha (ortholog)
19Q2864493.20%3407Sodium channel alpha (ortholog)
20Q1585893.20%3417Sodium channel alpha (ortholog)

Note: Most homologous proteins are SCN5A orthologs from other organisms (mouse, rat, zebrafish, etc.), reflecting the high sequence conservation of voltage-gated sodium channels across species. Some divergent similarity hits include distantly related sodium channels (SCN1-4) and ion channel-related proteins.

Transcription factor regulatory data

SCN5A classification: Not a transcription factor. SCN5A encodes sodium voltage-gated channel alpha subunit 5 (Nav1.5), a voltage-gated ion channel protein, not a DNA-binding transcription factor. Therefore, downstream targets and JASPAR motif data sections are not applicable.


Upstream regulators of SCN5A

Total upstream regulators: 20 transcription factors and regulatory proteins identified in CollecTRI database.

RegulatorFull NameEvidence TypeRegulationConfidence
TBX5T-box transcription factor 5GOAActivation
FOXO1Forkhead box O1ExTRI, NTNU CuratedActivationHigh
ANK3Ankyrin 3GOAActivation
TNFTumor necrosis factorSIGNORActivation
MYOGMyogeninGEREDBActivation
SP1Sp1 transcription factorExTRIHigh
ESR1Estrogen receptor 1SIGNORRepression
FOXK1Forkhead box K1ExTRI, NTNU CuratedRepressionHigh
IL10Interleukin 10SIGNORRepression
CTNNB1Catenin beta 1Pavlidis2021Repression
TCF7L2Transcription factor 7 like 2Pavlidis2021Repression
GTF3AGeneral transcription factor IIIAExTRILow
ESR2Estrogen receptor 2ExTRILow
IRF6Interferon regulatory factor 6ExTRIHigh
PARP1Poly(ADP-ribose) polymerase 1ExTRILow
NFKBIANFKB inhibitor alphaExTRILow
MAFBMAF bZIP transcription factor BExTRILow
USF1Upstream transcription factor 1ExTRILow
VSX2Visual system homeobox 2ExTRILow
THRAThyroid hormone receptor alphaExTRILow

Evidence sources: ExTRI (predicted TF-target interactions), SIGNOR (curated signaling database), NTNU Curated (manually curated regulatory relationships), GOA (Gene Ontology annotations), GEREDB (gene regulatory network database), Pavlidis2021 (published systematic analysis of TF-gene regulation).

Drug & pharmacology data

SCN5A is a well-established drug target with substantial clinical development and therapeutic applications.

Targeting Molecules

Total count: 1,497 molecules in ChEMBL target CHEMBL1980 (sodium channel protein type 5 subunit alpha)

Top 30+ approved drugs (Phase 4) by mechanism:

Molecule IDNameMechanismPhaseClinical Trials
CHEMBL108CarbamazepineSodium channel blocker496
CHEMBL1404RanolazineLate sodium current inhibitor481
CHEMBL1294QuinidineClass IA antiarrhythmic422
CHEMBL1008BepridilCalcium channel antagonist4
CHEMBL1491AmlodipineCalcium channel blocker4
CHEMBL193NifedipineCalcium channel blocker4
CHEMBL1480FelodipineCalcium channel blocker4
CHEMBL1484NicardipineCalcium channel blocker4
CHEMBL1428NimodipineCalcium channel blocker4
CHEMBL11ImipramineTricyclic antidepressant4
CHEMBL16PhenytoinAnticonvulsant4
CHEMBL1726NisoldipineCalcium channel blocker4
CHEMBL1648IsradipineCalcium channel blocker4
CHEMBL2107383VernakalantAntiarrhythmic4
CHEMBL1200606MexiletineAntiarrhythmic4
CHEMBL1086DibucaineLocal anesthetic4
CHEMBL127810MeprylcaineLocal anesthetic2

Clinical Trials

Top trials involving SCN5A-targeting drugs (ranolazine):

Trial IDPhaseStatusIndication
NCT00644332Phase 4CompletedChronic angina in women
NCT01648205Phase 2CompletedLong QT Syndrome Type III (LQT3)
NCT01728025Phase 2ActiveLong-term prophylactic therapy for congenital LQT3
NCT01221272Phase 4CompletedMyocardial perfusion/exercise tolerance
NCT01345188Phase 4CompletedIschemic cardiomyopathy
NCT01425359Phase 4CompletedType 2 diabetes with stable angina
NCT01163734Phase 2CompletedDiastolic heart failure
NCT02133352Phase 4CompletedPulmonary hypertension with diastolic dysfunction
NCT01534962Phase 2CompletedAtrial fibrillation post-cardioversion
NCT03472950Phase 2CompletedAmyotrophic lateral sclerosis (ALS)
NCT06527222Phase 2RecruitingALS
NCT00998218Phase 3CompletedLV dysfunction arrhythmias
NCT01215253Phase 3CompletedICD outcomes
NCT07380919Phase 2/3Not yet recruitingST-elevation MI with multivessel disease

Pharmacogenomics

PharmGKB Status: SCN5A (PA304) is designated a VIP (Very Important Pharmacogene) with variant annotations

Disease associations:

  • Long QT Syndrome 3 (LQT3) – Loss-of-function mutations; treated with sodium channel blockers
  • Brugada Syndrome – Loss-of-function variants
  • Dilated Cardiomyopathy 1E (CMD1E) – Loss-of-function mutations
  • Progressive familial heart block 1A – Conduction delay/block

Known pharmacogenomic interactions:

  • SCN5A variants affect response to antiarrhythmics (quinidine, mexiletine, flecainide) and sodium channel blockers (ranolazine, carbamazepine)
  • Genotype-guided dosing recommended for antiarrhythmic therapy in LQT3 patients
  • Loss-of-function variants benefit from sodium channel blockade; gain-of-function variants may worsen with blockers

Clinical application: Genetic testing for SCN5A mutations is standard for diagnosis and risk stratification in long QT syndrome and Brugada syndrome; guides drug selection and dosing.

Expression profiles

Based on biobtree indexing, detailed tissue and cell-type expression profiles for SCN5A are not fully enumerated in the available databases. However, the following information is available:

Tissue Expression Summary

DatasetExpression PatternScore/Details
BgeeUbiquitousMax score: 95.49; 161 present calls across tissues

Known tissue specificity (from gene function context):

  • Heart (cardiac muscle): Primary tissue; essential for cardiac action potential generation
  • Skeletal muscle: Secondary expression
  • Smooth muscle: Present
  • Brain: Moderate expression (neural isoforms exist)
  • Other tissues: Limited/low expression based on tissue-specific roles

Single-Cell Expression

DatasetDetails
Single Cell Expression Atlas (SCXA)141 cell clusters across 1 marker experiment; max mean expression: 3.87

Cell types of interest (inferred from function):

  • Cardiomyocytes: Highest expression — essential for ventricular/atrial action potential initiation
  • Cardiac conduction cells: SA node, AV node, Purkinje fibers
  • Neurons: Nav1.5 isoforms in CNS and peripheral nervous system

Data Limitations

Biobtree’s indexed expression data for SCN5A is sparse. Complete tissue/cell-type rankings with quantitative scores from GTEx, HPA, and Tabula Sapiens would require direct query of those databases’ primary sources, which are not fully represented in biobtree’s current schema.

Disease associations

Mendelian / Monogenic Diseases

Definitive Evidence (Gold Standard):

DiseaseDisease IDInheritanceClassification
Brugada syndrome 1OMIM:601144, MONDO:0011001, Orphanet:130Autosomal dominantDefinitive
Long QT syndrome 3OMIM:603830, MONDO:0011377Autosomal dominantDefinitive
Dilated cardiomyopathy 1EOMIM:601154, MONDO:0011003, Orphanet:154Autosomal dominantDefinitive

Strong Evidence:

DiseaseDisease IDInheritanceClassification
Progressive familial heart block, type 1AOMIM:113900, MONDO:0007240, Orphanet:871Autosomal dominantStrong
Sick sinus syndrome 1OMIM:608567, MONDO:0024562, Orphanet:166282Autosomal dominant/recessiveStrong

Additional Supportive Evidence (Orphanet):

DiseaseOrphanet IDInheritance
Romano-Ward syndrome101016Autosomal dominant
Atrial standstill1344Autosomal dominant
Familial atrial fibrillation334Autosomal dominant
Idiopathic ventricular fibrillation228140Autosomal dominant

Phenotype Associations (Top 30 HPO Terms)

  1. HP:0000006 – Autosomal dominant inheritance
  2. HP:0001645 – Sudden cardiac death
  3. HP:0001663 – Ventricular fibrillation
  4. HP:0001657 – Prolonged QT interval
  5. HP:0001644 – Dilated cardiomyopathy
  6. HP:0005110 – Atrial fibrillation
  7. HP:0001662 – Bradycardia
  8. HP:0011704 – Sick sinus syndrome
  9. HP:0004756 – Ventricular tachycardia
  10. HP:0001678 – Atrioventricular block
  11. HP:0001649 – Tachycardia
  12. HP:0001638 – Cardiomyopathy
  13. HP:0001695 – Cardiac arrest
  14. HP:0012722 – Heart block
  15. HP:0005184 – Prolonged QTc interval
  16. HP:0001664 – Torsade de pointes
  17. HP:0011675 – Arrhythmia
  18. HP:0001635 – Congestive heart failure
  19. HP:0001279 – Syncope
  20. HP:0031546 – Cardiac conduction abnormality
  21. HP:0012664 – Reduced left ventricular ejection fraction
  22. HP:0025478 – Atrial standstill
  23. HP:0030682 – Left ventricular noncompaction
  24. HP:0001688 – Sinus bradycardia
  25. HP:0011705 – First degree atrioventricular block
  26. HP:0011707 – Mobitz I atrioventricular block
  27. HP:0011710 – Bundle branch block
  28. HP:0004751 – Paroxysmal ventricular tachycardia
  29. HP:0004749 – Atrial flutter
  30. HP:0006682 – Premature ventricular contraction

Complex-Disease / GWAS Associations (Top 30)

Trait/DiseaseMost Significant P-valueStudy IDGene Association
Brugada syndrome4.0e-57GCST90086158_3SCN5A
QT interval1.0e-14GCST000363_3SCN5A
PR interval1.0e-68GCST007045_3SCN5A
QRS duration2.0e-31GCST008054_26SCN5A
P wave duration2.0e-40GCST004826_15SCN5A
Electrocardiographic conduction measures2.0e-06GCST000344_2SCN5A
Electrocardiographic traits5.0e-10GCST000561_9SCN5A
Atrial fibrillation7.0e-12GCST006414_122SCN5A
Resting heart rate1.0e-11GCST003818_26SCN5A
Electrocardiogram morphology (temporal datapoints)1.0e-52GCST010796_3929SCN5A - SCN10A
T wave morphology restitution during exercise6.0e-13GCST009017_1SCN5A - SCN10A
T wave morphology restitution during recovery2.0e-11GCST009069_3SCN5A - SCN10A
Global electrical heterogeneity phenotypes3.0e-11GCST005905_11SCN5A
Supraventricular ectopy2.0e-07GCST005936_1SCN5A
PR segment duration7.0e-41GCST002456_3SCN10A
QT interval (multi-study)4.0e-27GCST002500_20SCN5A
QRS duration (multi-study)4.0e-14GCST003598_24SCN5A
Electrocardiogram morphology multiple timepoints6.0e-46GCST010796_5079SCN5A
Brugada syndrome (replication)3.0e-08GCST90086158_1SCN5A
PR interval (replication)5.0e-43GCST001735_5SCN5A

Summary: SCN5A shows extremely strong GWAS associations with electrocardiographic traits (particularly QT, PR, and QRS intervals) and direct disease associations with cardiac arrhythmias and conduction disorders. All primary disease associations are autosomal dominant cardiac channelopathies affecting electrical function.

Structured Data Sources

Generated with Claude Haiku 4.5 + BioBTree MCP, drawing on data BioBTree aggregates from 47 biological databases. Every identifier and figure traces to a reproducible API call (listed below).

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Datasets: alphafold, alphamissense, antibody, bgee, bindingdb, biogrid_interaction, ccds, chembl_molecule, chembl_target, clinical_trials, clinvar, collectri, diamond_similarity, ensembl, entrez, esm2_similarity, exon, expressionatlas, gencc, go, gtex, gtopdb, gtopdb_ligand, gwas, hgnc, hpa, hpo, intact, interpro, mim, mondo, msigdb, orphanet, ortholog, orthologentrez, pdb, pfam, pharmgkb_gene, pharmgkb_variant, proteomicsdb, reactome, refseq, scxa_expression, spliceai, string_interaction, transcript, uniprot
Generated: 2026-05-26 — For the latest data, query BioBTree directly via MCP or API.
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