SCHEMBL1469250

SCHEMBL1469250

OC[C@H]1N[C@H](CO)[C@@H](O)[C@H](O)[C@H]1O

nearest known ligand 1.00 ✓ in ChEMBL — recovers established targets

Predicted protein targets (top 8)

geneUniProtsupporting neighboursconfidence
MGAM O43451 5/20 1.00
FUCA1 P04066 5/20 1.00
GLA P06280 5/20 1.00
GANC Q8TET4 2/20 1.00
GAA P10253 2/20 1.00
AGL P35573 3/20 0.93
GBA2 Q9HCG7 1/20 0.93
GBA1 P04062 1/20 0.93

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
SCHEMBL14654237 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL1479404 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL2265529 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL2265531 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL9379987 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL1879685 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL20466285 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL7824407 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL7811568 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA
SCHEMBL18271004 1.00 MGAM (1.00) MGAMFUCA1GLAGANCGAA

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 228 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
WO-2024069235-A2 COMPOSITIONS CONTAINING OLIGONUCLEOTIDES WITH THERANOSTIC APPLICATIONS Sixfold Bioscience Ltd. (GB) 2024-04-04 WO claimed
US-20220184185-A1 MRNA BASED ENZYME REPLACEMENT THERAPY COMBINED WITH A PHARMACOLOGICAL CHAPERONE FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS MODERNATX, INC. 2022-06-16 US claimed
US-20210228560-A1 Combination of a Compound Having the Ability to Rearrange a Lysosomal Enzyme and Ambroxol and/or a Derivative of Ambroxol CENTOGENE IP GMBH (DE) 2021-07-29 US claimed
EP-2793872-B1 COMBINATION OF A COMPOUND HAVING THE ABILITY TO REARRANGE A LYSOSOMAL ENZYME AND AMBROXOL AND/OR A DERIVATIVE OF AMBROXOL CENTOGENE IP GMBH (DE) 2021-03-10 EP claimed
EP-1896083-B1 A METHOD FOR THE TREATMENT OF POMPE DISEASE USING 1-DEOXYNOJIRIMYCIN AND DERIVATIVES AMICUS THERAPEUTICS INC (US) 2016-03-02 EP claimed
US-20160051528-A1 Method for the Treatment of Pompe Disease Using 1-Deoxynojirimycin Derivatives WILMINGTON TRUST, NATIONAL ASSOCIATION 2016-02-25 US claimed
EP-2932982-A1 A method for the treatment of pompe disease using 1-deoxynojirimycin and derivatives Amicus Therapeutics, Inc. (US) 2015-10-21 EP claimed
US-20150258081-A1 COMBINATION OF A COMPOUND HAVING THE ABILITY TO REARRANGE A LYSOSOMAL ENZYME AND AMBROXOL AND/OR A DERIVATIVE OF AMBROXOL CENTOGENE IP GMBH (DE) 2015-09-17 US claimed
EP-2793872-A1 COMBINATION OF A COMPOUND HAVING THE ABILITY TO REARRANGE A LYSOSOMAL ENZYME AND AMBROXOL AND/OR A DERIVATIVE OF AMBROXOL Centogene IP GmbH (DE) 2014-10-29 EP claimed
WO-2013091897-A1 COMBINATION OF A COMPOUND HAVING THE ABILITY TO REARRANGE A LYSOSOMAL ENZYME AND AMBROXOL AND/OR A DERIVATIVE OF AMBROXOL CENTOGENE GMBH (DE) 2013-06-27 WO claimed
US-20110070643-A1 Utilization of Pharmacological Chaperones to Improve Manufacturing and Purification of Biologics AMICUS THERAPEUTICS, INC. 2011-03-24 US claimed
WO-2010138608-A1 UTILIZATION OF PHARMACOLOGICAL CHAPERONES TO IMPROVE MANUFACTURING AND PURIFICATION OF BIOLOGICS AMICUS THERAPEUTICS, INC. (US) 2010-12-02 WO claimed
US-7514453-B2 Preventing degradation of mutant enzymes associated with lysosomal storage diseases in mammalian cells AMICUS THERAPEUTICS INC. (US) 2009-04-07 US claimed
EP-1896083-A2 A METHOD FOR THE TREATMENT OF POMPE DISEASE USING 1-DEOXYNOJIRIMYCIN AND DERIVATIVES Amicus Therapeutics, Inc. (US) 2008-03-12 EP claimed
US-20070021381-A1 Stabilizing the mutant enzyme by administering a reversible competitive inhibitor consisting an iminosugar, 4-epi-isofagomine or 1-deoxygalactonojirimycin; Gaucher's disease; lysosomal storage diseases MOUNT SINAI SCHOOL OF MEDICINE OF NEW YORK UNIVERSITY (US) 2007-01-25 US claimed
US-20060264467-A1 Method for the treatment of Pompe disease using 1-deoxynojirimycin and derivatives WILMINGTON TRUST, NATIONAL ASSOCIATION 2006-11-23 US claimed
WO-2006125141-A2 A METHOD FOR THE TREATMENT OF POMPE DISEASE USING 1-DEOXYNOJIRIMYCIN DERIVATIVES AMICUS THERAPEUTICS, INC. (US) 2006-11-23 WO claimed
US-6774135-B2 1-DEOXY-GALACTONOJIRIMYCIN AND RELATED COMPOUNDS USED TO TREAT FABRY DISEASE MOUNT SINAI SCHOOL OF MEDICINE OF NEW YORK UNIVERSITY 2004-08-10 US claimed
US-6589964-B2 Administering a competitive inhibitor of the enzyme in an amount effective to enhance enzyme activtiy, selected from 2,5-dideoxy- 2,5-imino-D-mannitol, 3,4-diepi- alpha -homonojirimycin, 5-O- deoxyglactonojirimycin, calystegines MOUNT SINAI SCHOOL OF MEDICINE OF NEW YORK UNIVERSITY 2003-07-08 US claimed
US-6583158-B1 Competitive inhibitors of the enzymes, in particular imino sugars and related compounds MOUNT SINAI SCHOOL OF MEDICINE OF NEW YORK UNIVERSITY 2003-06-24 US claimed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (6 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-20210228560-A1 Combination of a Compound Having the Ability to Rearrange a Lysosomal Enzyme and Ambroxol and/or a Derivative of Ambroxol CMA1, MAN2B1, GBA3 MGAM 674/4885FUCA1 113/4885GLA 45/4885
US-20160051528-A1 Method for the Treatment of Pompe Disease Using 1-Deoxynojirimycin Derivatives GAA, MAN2B1, MAN1B1 MGAM 10/4885FUCA1 89/4885GLA 76/4885
US-20060264467-A1 Method for the treatment of Pompe disease using 1-deoxynojirimycin and derivatives GAA, MAN2B1, MAN1B1 MGAM 10/4885FUCA1 74/4885GLA 85/4885
US-20070021381-A1 Stabilizing the mutant enzyme by administering a reversible competitive inhibitor consisting an iminosugar, 4-epi-isofagomine or 1-deoxygalactonojirimycin; Gaucher's disease; lysosomal storage diseases GBA1, GBA2, GALC MGAM 11/4885FUCA1 42/4885GLA 24/4885
US-20150258081-A1 COMBINATION OF A COMPOUND HAVING THE ABILITY TO REARRANGE A LYSOSOMAL ENZYME AND AMBROXOL AND/OR A DERIVATIVE OF AMBROXOL MAN2B1, CMA1, GBA1 MGAM 221/4885FUCA1 56/4885GLA 51/4885
US-20220184185-A1 MRNA BASED ENZYME REPLACEMENT THERAPY COMBINED WITH A PHARMACOLOGICAL CHAPERONE FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS GAA, GBA1, GBA2 MGAM 25/4885FUCA1 15/4885GLA 9/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.