Topotecan

Topotecan

SCHEMBL3836

CC[C@@]1(O)C(=O)OCc2c1cc1n(c2=O)Cc2cc3c(CN(C)C)c(O)ccc3nc2-1

nearest known ligand 1.00 ✓ in ChEMBL — recovers established targets

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

TOP1

The experimentally established mechanism targets of Topotecan. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
TOP1 known ✓ P11387 19/20 1.00
MEN1 O00255 5/20 1.00
KMT2A Q03164 5/20 1.00
SMN1; SMN2 Q16637 5/20 1.00
KDM4E B2RXH2 4/20 1.00
CASP1 P29466 3/20 1.00
CASP7 P55210 3/20 1.00
HBB P68871 3/20 1.00
MAPT P10636 3/20 1.00
USP2 O75604 2/20 1.00
LMNA P02545 2/20 1.00
BRCA1 P38398 2/20 1.00
KEAP1 Q14145 2/20 1.00
NFE2L2 Q16236 2/20 1.00
HIF1A Q16665 2/20 1.00
CYP3A4 P08684 2/20 1.00
SLC22A2 O15244 1/20 1.00
TOP2A P11388 1/20 1.00
TOP2B Q02880 1/20 1.00
SLC47A2 Q86VL8 1/20 1.00

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Topotecan SCHEMBL31517322 1.00 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL29350221 1.00 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL30712226 1.00 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL14577671 1.00 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL9971346 1.00 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL3927536 1.00 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL5531617 1.00 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL29726458 1.00 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL10278 0.99 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E
Topotecan SCHEMBL418714 0.99 TOP1 (1.00) TOP1MEN1KMT2ASMN1; SMN2KDM4E

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Appears in 155497 patents — a generic fragment claimed broadly, so it's down-weighted as IP noise. Top by claim status then date:

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-20260144890-A1 ANTIBODY DRUG CONJUGATE COMPRISING NMT INHIBITOR CONJUGATED TO AN ANTIBODY MyricX Pharma Limited (GB) 2026-05-28 US claimed
US-20260144882-A1 ANTI-NECTIN-4 ANTIBODY DRUG CONJUGATE AND USE THEREOF BIO-THERA SOLUTIONS, LTD. (CN) 2026-05-28 US claimed
EP-4748859-A2 CHEMICALLY AND PHOTOCHEMICALLY INITIATED CELL MEMBRANE BLEBBING TO INDUCE CELL VESICLE PRODUCTION, MODIFICATIONS THEREOF, AND USES THEREOF The Regents of the University of California (US) 2026-05-27 EP claimed
EP-3607938-B1 PHARMACEUTICAL COMPOSITION SOVIC BRKICIC LJILJANA (HR) 2026-05-27 EP claimed
CN-122075497-A Use of NLRP3 agonist for tumor treatment 2026-05-26 CN claimed
CN-122079990-A Purino [1,2-a ] carbazoline derivative, and preparation method and application thereof 2026-05-26 CN claimed
CN-122094686-A Oncolytic adenovirus and topoisomerase I inhibitors for the treatment of cancer 2026-05-26 CN claimed
CN-116209439-B Cereblon protein modulators Saint Jude Children's Research Hospital Ltd. (US) 2026-05-26 CN claimed
US-20260141533-A1 QUANTITATIVE IMAGING BIOMARKER FOR LUNG CANCER THE TRUSTEES OF COLUMBIA UNIVERSITY IN THE CITY OF NEW YORK (US) 2026-05-21 US claimed
WO-2026105121-A1 ANTICANCER FORMULATIONS AND USES THEREOF INTRAGEL THERAPEUTICS LTD. (IL) 2026-05-21 WO claimed
EP-0572549-A1 TREATMENT OF NON-SMALL CELL LUNG CARCINOMA SMITHKLINE BEECHAM CORPORATION (US) 1993-12-08 EP claimed
EP-0572563-A1 TREATMENT OF ESOPHAGEAL CANCER SMITHKLINE BEECHAM CORPORATION (US) 1993-12-08 EP claimed
EP-0572557-A1 TREATMENT OF OVARIAN CANCER SMITHKLINE BEECHAM CORPORATION (US) 1993-12-08 EP claimed
WO-1993011770-A1 TREATMENT OF COLORECTAL CANCER SMITHKLINE BEECHAM CORPORATION (US) 1993-06-24 WO claimed
WO-1993009782-A1 COMBINATION CHEMOTHERAPY SMITHKLINE BEECHAM CORPORATION (US) 1993-05-27 WO claimed
WO-1992014471-A1 TREATMENT OF NON-SMALL CELL LUNG CARCINOMA SMITHKLINE BEECHAM CORPORATION (US) 1992-09-03 WO claimed
WO-1992014470-A1 TREATMENT OF ESOPHAGEAL CANCER SMITHKLINE BEECHAM CORPORATION (US) 1992-09-03 WO claimed
WO-1992014469-A1 TREATMENT OF OVARIAN CANCER SMITHKLINE BEECHAM CORPORATION (US) 1992-09-03 WO claimed
CN-1034724-A WATER SOLUBLE CAMPTOTHECIN ANALOGS SMITHKLINE BECKMAN CORP (US) 1989-08-16 CN claimed
EP-0321122-A2 Water soluble camptothecin analogs SMITHKLINE BEECHAM CORPORATION (US) 1989-06-21 EP claimed