Eflornithine

Eflornithine

SCHEMBL4510

Cl.NCCCC(N)(C(=O)O)C(F)F.O

nearest known ligand 0.96

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

ODC1

The experimentally established mechanism targets of Eflornithine. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
ODC1 known ✓ P11926 2/20 0.92
BLM P54132 3/20 0.96
LMNA P02545 3/20 0.96
KDM4E B2RXH2 1/20 0.96
MAPT P10636 1/20 0.96
RAB9A P51151 1/20 0.96
PMP22 Q01453 1/20 0.96
SMN1; SMN2 Q16637 1/20 0.96
ARG1 P05089 3/20 0.59
ARG2 P78540 2/20 0.39
NPSR1 Q6W5P4 2/20 0.34
THRB P10828 2/20 0.32
KMT2A Q03164 2/20 0.32
GABRR3 A8MPY1 1/20 0.32
GABRP O00591 1/20 0.32
GABRD O14764 1/20 0.32
HDAC3 O15379 1/20 0.32
GABBR2 O75899 1/20 0.32
CYP1A2 P05177 1/20 0.32
GABRA1 P14867 1/20 0.32

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Eflornithine, (S)- SCHEMBL559145 1.00 BLM (0.96) BLMLMNAKDM4EMAPTRAB9A
D-Eflornithine SCHEMBL3238104 1.00 BLM (0.96) BLMLMNAKDM4EMAPTRAB9A
Eflornithine SCHEMBL5051665 1.00 BLM (0.96) BLMLMNAKDM4EMAPTRAB9A
Eflornithine SCHEMBL1397750 1.00 BLM (0.96) BLMLMNAKDM4EMAPTRAB9A
Eflornithine SCHEMBL4809264 1.00 BLM (0.96) BLMLMNAKDM4EMAPTRAB9A
Eflornithine SCHEMBL6779168 0.98 BLM (1.00) BLMLMNAKDM4EMAPTRAB9A
Eflornithine, (S)- SCHEMBL6779172 0.98 BLM (1.00) BLMLMNAKDM4EMAPTRAB9A
Eflornithine SCHEMBL3022583 0.98 BLM (1.00) BLMLMNAKDM4EMAPTRAB9A
Eflornithine, (S)- SCHEMBL1322403 0.98 BLM (1.00) BLMLMNAKDM4EMAPTRAB9A
D-Eflornithine SCHEMBL7208883 0.98 BLM (1.00) BLMLMNAKDM4EMAPTRAB9A

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Appears in 8577 patents — a generic fragment claimed broadly, so it's down-weighted as IP noise. Top by claim status then date:

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-20260137642-A1 METHODS OF TREATING PATIENTS HAVING TYPE 1 DIABETES WITH EFLORNITHINE CANCER PREVENTION PHARMACEUTICALS, INC. (US) 2026-05-21 US claimed
US-20260116861-A1 ISOXAZOLE HYDROXAMIC ACIDS AS HISTONE DEACETYLASE 6 INHIBITORS THE GEORGE WASHINGTON UNIVERSITY, A CONGRESSIONALLY CHARTERED NOT-FOR-PROFIT CORPORATION (US) 2026-04-30 US claimed
US-12605349-B2 Methods of treating grade 3 astrocytoma Orbus Therapeutics, Inc. (US) 2026-04-21 US claimed
US-20260060950-A1 METHODS OF TREATING GRADE 3 ASTROCYTOMA ORBUS THERAPEUTICS INC (US) 2026-03-05 US claimed
US-12522572-B2 Isoxazole hydroxamic acids as histone deacetylase 6 inhibitors THE GEORGE WASHINGTON UNIVERSITY, A CONGRESSIONALLY CHARTERED NOT-FOR-PROFIT CORPORATION (US) 2026-01-13 US claimed
EP-4524131-A1 SMALL MOLECULES FOR TREATING CANCER, INHABITING CHEMOKINE ACTIVITY AND/OR INDUCING CELL DEATH AlonBio Ltd. (IL) 2025-03-19 EP claimed
WO-2025050100-A1 COMPOSITIONS AND METHODS FOR TREATING HAIR AND SKIN CONDITIONS RELATED TO FOLLICULOPILOSEBACEOUS UNITS OLSEN ELISE A (US) 2025-03-06 WO claimed
US-12202803-B2 Small molecules for treating cancer, inhibiting chemokine activity and/or inducing cell death ALONBIO LTD. (IL) 2025-01-21 US claimed
WO-2024220593-A1 COMPOSITIONS AND METHODS FOR PREVENTION OF CHEMOTHERAPY- OR RADIATION-RELATED HAIR LOSS OLSEN ELISE A (US) 2024-10-24 WO claimed
US-20240343697-A1 ISOXAZOLE HYDROXAMIC ACIDS AS HISTONE DEACETYLASE 6 INHIBITORS THE GEORGE WASHINGTON UNIVERSITY, A CONGRESSIONALLY CHARTERED NOT-FOR-PROFIT CORPORATION (US) 2024-10-17 US claimed
US-6764493-B1 Tissue removal using biocompatible materials PEARL TECHNOLOGY HOLDINGS, LLC 2004-07-20 US claimed
US-6730809-B2 FORMED VIA CHEMICAL REDUCTION AND HYDROLYSIS WITH MINIMAL USE OF HALOGENATED SOLVENTS; COMPRISES USE OF INTERMEDIATES SUCH AS ETHYL 2-BENZYLIDENEAMINO-2-DIFLUOROMETHYL-4-CYANOBUTANOATE WOMEN FIRST HEALTHCARE, INC. 2004-05-04 US claimed
EP-1311266-A2 COMBINATION HIV THERAPY INCLUDING CAMPTOTHECIN SuperGen, Inc. (US) 2003-05-21 EP claimed
US-20030083384-A1 Processes for the production of alpha-difluoromethyl ornithine (DFMO) BRISTOL-MYERS SQUIBB COMPANY TO WOMEN FIRST HEALTHCARE, INC. 2003-05-01 US claimed
EP-0617968-B1 HIV protease inhibitors in pharmaceutical combinations for the treatment of AIDS MERCK & CO INC (US) 2003-01-08 EP claimed
EP-0692963-B1 USE OF TERBINAFINE FOR THE THERAPEUTIC TREATMENT OF PNEUMOCYSTOSIS VSL PHARMA LTD (IE) 2002-06-26 EP claimed
WO-2002038125-A2 TISSUE REMOVAL USING BIOCOMPATIBLE MATERIALS PEARL TECHNOLOGY HOLDINGS, LLC (US) 2002-05-16 WO claimed
WO-2002000168-A2 COMBINATION HIV THERAPY INCLUDING CAMPTOTHECIN SUPERGEN, INC. (US) 2002-01-03 WO claimed
EP-0692963-A1 USE OF TERBINAFINE FOR THE THERAPEUTIC TREATMENT OF PNEUMOCYSTOSIS Mendes S.R.L. (IT) 1996-01-24 EP claimed
WO-1994020082-A1 USE OF TERBINAFINE FOR THE THERAPEUTIC TREATMENT OF PNEUMOCYSTOSIS MENDES S.R.L. (IT) 1994-09-15 WO claimed