Acetylcarnitine

Acetylcarnitine

SCHEMBL677128

CC(=O)O[C@@H](CC(=O)[O-])C[N+](C)(C)C

nearest known ligand 1.00 ✓ in ChEMBL — recovers established targets

Full drug profile on Sugi Atlas →

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
MEN1 O00255 3/20 1.00
KMT2A Q03164 3/20 1.00
CYP1A2 P05177 1/20 1.00
HRH1 P35367 1/20 1.00
CYP2C19 P33261 2/20 0.69
RECQL P46063 1/20 0.69
SMN1; SMN2 Q16637 2/20 0.68
LMNA P02545 1/20 0.68
SLC25A20 O43772 3/20 0.58
TSHR P16473 3/20 0.58
TP53 P04637 2/20 0.58
CYP2D6 P10635 2/20 0.58
MAPT P10636 2/20 0.58
SLC6A5 Q9Y345 2/20 0.58
KDM4E B2RXH2 1/20 0.58
CYP3A4 P08684 1/20 0.58
CYP2C9 P11712 1/20 0.58
NFKB1 P19838 1/20 0.58
THPO P40225 1/20 0.58
HIF1A Q16665 1/20 0.58

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Acetylcarnitine SCHEMBL118455 1.00 MEN1 (1.00) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL28017793 1.00 MEN1 (1.00) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL69781 1.00 MEN1 (1.00) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL3004014 0.98 MEN1 (0.96) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL1331768 0.98 MEN1 (0.96) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL1330152 0.98 MEN1 (0.96) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL9300885 0.98 MEN1 (0.96) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL387375 0.98 MEN1 (0.96) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL4378230 0.98 MEN1 (0.96) MEN1KMT2ACYP1A2HRH1CYP2C19
Acetylcarnitine SCHEMBL951660 0.98 MEN1 (0.96) MEN1KMT2ACYP1A2HRH1CYP2C19

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 105 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
WO-2023012092-A1 A COMBINED PREPARATION FOR THE TREATMENT OF POMPE DISEASE UNIVERSITÀ DEGLI STUDI DI NAPOLI "FEDERICO II" (IT) 2023-02-09 WO claimed
US-5432199-A Use of acetyl D-carnitine in the therapeutic treatment of glaucoma, and pharmaceutical compositions useful in such treatment SIGMA-TAU INDUSTRIE FARMACEUTICHE RIUNITE S.P.A. (IT) 1995-07-11 US claimed
EP-0446268-B1 USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA Sigma-Tau Industrie Farmaceutiche Riunite S.p.A. (IT) 1993-04-14 EP claimed
US-5145871-A USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA, AND PHARMACEUTICAL COMPOSITIONS USEFUL IN SUCH TREATMENT SIGMA-TAU INDUSTRIE FARMACEUTICHE RIUNITE S.P.A. (IT) 1992-09-08 US claimed
EP-0446268-A1 USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA. SIGMA TAU IND FARMACEUTI (IT) 1991-09-18 EP claimed
WO-1990006111-A1 USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA SIGMA-TAU INDUSTRIE FARMACEUTICHE RIUNITE S.P.A. (IT) 1990-06-14 WO claimed
EP-4667007-A2 NOVEL ASSOCIATION OF GASTRODIA ELATA AND VITAMIN B Futura S.r.l. (IT) 2025-12-24 EP disclosed
EP-4663194-A2 NOVEL ASSOCIATION OF ACTIVE INGREDIENTS, PHARMACEUTICAL AND/OR NUTRACEUTICAL COMPOSITIONS CONTAINING IT AND THEIR USE IN THE PREVENTION AND REPAIR OF DAMAGE TO THE CENTRAL AND PERIPHERAL NERVOUS SYSTEM Futura S.r.l. (IT) 2025-12-17 EP disclosed
EP-4647078-A2 NOVEL ASSOCIATION OF GASTRODIA ELATA, CITICOLINE, L-ACETYLCARNITINE AND VITAMIN B Futura S.r.l. (IT) 2025-11-12 EP disclosed
EP-4643864-A2 NOVEL ASSOCIATION OF GASTRODIA ELATA, CITICOLINE, L-ACETYLCARNITINE, VITAMIN B AND VITAMIN D Futura S.r.l. (IT) 2025-11-05 EP disclosed
EP-4640222-A2 NOVEL ASSOCIATION OF GASTRODIA ELATA, CITICOLINE, L-ACETYLCARNITINE AND VITAMIN D Futura S.r.l. (IT) 2025-10-29 EP disclosed
EP-4631508-A2 NOVEL ASSOCIATION OF GASTRODIA ELATA AND VITAMIN D Futura S.r.l. (IT) 2025-10-15 EP disclosed
EP-4626452-A1 NOVEL ASSOCIATION OF ACTIVE INGREDIENTS, PHARMACEUTICAL AND/OR NUTRACEUTICAL COMPOSITIONS CONTAINING IT AND THEIR USE IN THE PREVENTION AND REPAIR OF DAMAGE TO THE CENTRAL AND PERIPHERAL NERVOUS SYSTEM Futura S.r.l. (IT) 2025-10-08 EP disclosed
US-5145871-A USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA, AND PHARMACEUTICAL COMPOSITIONS USEFUL IN SUCH TREATMENT SIGMA-TAU INDUSTRIE FARMACEUTICHE RIUNITE S.P.A. (IT) 1992-09-08 US disclosed
US-5145871-A USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA, AND PHARMACEUTICAL COMPOSITIONS USEFUL IN SUCH TREATMENT SIGMA-TAU INDUSTRIE FARMACEUTICHE RIUNITE S.P.A. (IT) 1992-09-08 US disclosed
EP-0446268-A1 USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA. SIGMA TAU IND FARMACEUTI (IT) 1991-09-18 EP disclosed
EP-0446268-A1 USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA. SIGMA TAU IND FARMACEUTI (IT) 1991-09-18 EP disclosed
WO-1990006111-A1 USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA SIGMA-TAU INDUSTRIE FARMACEUTICHE RIUNITE S.P.A. (IT) 1990-06-14 WO disclosed
WO-1990006111-A1 USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA SIGMA-TAU INDUSTRIE FARMACEUTICHE RIUNITE S.P.A. (IT) 1990-06-14 WO disclosed
WO-1990006111-A1 USE OF ACETYL D-CARNITINE IN THE THERAPEUTIC TREATMENT OF GLAUCOMA SIGMA-TAU INDUSTRIE FARMACEUTICHE RIUNITE S.P.A. (IT) 1990-06-14 WO disclosed