Apilimod

Apilimod

SCHEMBL29459498

Cc1cccc(/C=N/Nc2cc(N3CCOCC3)nc(OCCc3ccccn3)n2)c1

nearest known ligand 1.00 ✓ in ChEMBL — recovers established targets

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

PIKFYVE

The experimentally established mechanism targets of Apilimod. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
PIKFYVE known ✓ Q9Y2I7 5/20 1.00
TYK2 P29597 2/20 1.00
SYK P43405 2/20 1.00
IRAK4 Q9NWZ3 2/20 1.00
FES P07332 1/20 1.00
FER P16591 1/20 1.00
FRK P42685 1/20 1.00
CAMK1D Q8IU85 1/20 1.00
KDM4E B2RXH2 7/20 0.65
MAPT P10636 6/20 0.65
LMNA P02545 4/20 0.65
HPGD P15428 1/20 0.65
BRSK1 Q8TDC3 1/20 0.65
ALDH1A1 P00352 3/20 0.53
SENP7 Q9BQF6 1/20 0.53
SENP6 Q9GZR1 1/20 0.53
L3MBTL1 Q9Y468 2/20 0.51
NPC1 O15118 2/20 0.47
RAB9A P51151 2/20 0.47
MEN1 O00255 3/20 0.46

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Apilimod SCHEMBL426299 1.00 PIKFYVE (1.00) PIKFYVETYK2SYKIRAK4FES
Apilimod SCHEMBL29365634 1.00 PIKFYVE (1.00) PIKFYVETYK2SYKIRAK4FES
Apilimod SCHEMBL29387519 1.00 PIKFYVE (1.00) PIKFYVETYK2SYKIRAK4FES
Apilimod SCHEMBL426300 1.00 PIKFYVE (1.00) PIKFYVETYK2SYKIRAK4FES
SCHEMBL18121499 0.97 PIKFYVE (0.94) PIKFYVETYK2SYKIRAK4FES
SCHEMBL20507067 0.97 PIKFYVE (0.94) PIKFYVETYK2SYKIRAK4FES
SCHEMBL18115419 0.96 PIKFYVE (0.92) PIKFYVETYK2SYKIRAK4FES
SCHEMBL18115421 0.96 PIKFYVE (0.92) PIKFYVETYK2SYKIRAK4FES
Apilimod SCHEMBL3082382 0.95 PIKFYVE (0.91) PIKFYVETYK2SYKIRAK4FES
Apilimod SCHEMBL3082380 0.95 PIKFYVE (0.91) PIKFYVETYK2SYKIRAK4FES

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 12 patents. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
WO-2025030033-A1 APILIMOD COMPOSITIONS AND METHODS OF USE ORPHAI THERAPEUTICS INC. (US) 2025-02-06 WO disclosed
US-20240374523-A1 STABILIZED APILIMOD COMPOSITIONS AND USES THEREOF ACADIA WOODS PARTNERS, LLC 2024-11-14 US disclosed
WO-2024191947-A1 PIKFYVE INHIBITOR COMBINATION THERAPY ORPHAI THERAPEUTICS INC. (US) 2024-09-19 WO disclosed
WO-2024107448-A1 APILIMOD COMBINATION THERAPY ORPHAI THERAPEUTICS INC. (US) 2024-05-23 WO disclosed
EP-4351585-A1 STABILIZED APILIMOD COMPOSITIONS AND USES THEREOF Orphai Therapeutics Inc. (US) 2024-04-17 EP disclosed
EP-4308103-A1 ANTIVIRAL COMPOSITIONS AND METHODS AI Therapeutics, Inc. (US) 2024-01-24 EP disclosed
WO-2024015281-A1 APILIMOD COMBINATION THERAPY AI Therapeutics, Inc. (US) 2024-01-18 WO disclosed
WO-2024015286-A1 APILIMOD COMBINATION THERAPY AI Therapeutics, Inc. (US) 2024-01-18 WO disclosed
WO-2022261499-A1 STABILIZED APILIMOD COMPOSITIONS AND USES THEREOF AI Therapeutics, Inc. (US) 2022-12-15 WO disclosed
EP-4100016-A1 ANTI-VIRAL COMPOSITIONS AND METHODS OF USE AI Therapeutics, Inc. (US) 2022-12-14 EP disclosed
WO-2022197667-A1 ANTIVIRAL COMPOSITIONS AND METHODS YOUNG PETER R (US) 2022-09-22 WO disclosed
EP-3956358-A1 ALPHA4BETA7 INHIBITOR AND IL-23 INHIBITOR COMBINATION THERAPY MILLENNIUM PHARMACEUTICALS, INC. (US) 2022-02-23 EP disclosed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (1 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-20240374523-A1 STABILIZED APILIMOD COMPOSITIONS AND USES THEREOF PRNP, PARK7, API5 PIKFYVE 362/4885TYK2 3975/4885SYK 2066/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.