Predicted protein targets (top 14)
| gene | UniProt | supporting neighbours | confidence | |
|---|---|---|---|---|
| ▸ | CFTR | P13569 | 1/20 | 0.67 |
| ▸ | HSD11B1 | P28845 | 1/20 | 0.48 |
| ▸ | LMNA | P02545 | 1/20 | 0.48 |
| ▸ | GBA1 | P04062 | 5/20 | 0.48 |
| ▸ | KDM4E | B2RXH2 | 2/20 | 0.47 |
| ▸ | GAA | P10253 | 1/20 | 0.47 |
| ▸ | MAPT | P10636 | 1/20 | 0.47 |
| ▸ | SMN1; SMN2 | Q16637 | 1/20 | 0.47 |
| ▸ | ALDH1A1 | P00352 | 3/20 | 0.46 |
| ▸ | PKM | P14618 | 2/20 | 0.45 |
| ▸ | CCR6 | P51684 | 1/20 | 0.45 |
| ▸ | NPC1 | O15118 | 1/20 | 0.44 |
| ▸ | USP2 | O75604 | 1/20 | 0.44 |
| ▸ | KMT2A | Q03164 | 1/20 | 0.44 |
Click a target to see other patent compounds predicted against it — the reverse direction, in place.
Similar compounds — the chemically nearest patent molecules
Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.
| Compound | similarity | top predicted | shared targets | |
|---|---|---|---|---|
| SCHEMBL5741493 | 0.99 | CFTR (0.65) | CFTRHSD11B1LMNAGBA1KDM4E | |
| SCHEMBL5742703 | 0.93 | CFTR (0.58) | CFTRHSD11B1LMNAGBA1KDM4E | |
| SCHEMBL5791138 | 0.93 | CFTR (0.57) | CFTRHSD11B1LMNAGBA1KDM4E | |
| SCHEMBL3821514 | 0.91 | CFTR (0.69) | CFTRHSD11B1LMNAGBA1KDM4E | |
| SCHEMBL3823433 | 0.90 | CFTR (0.67) | CFTRHSD11B1LMNAGBA1KDM4E | |
| SCHEMBL5739907 | 0.89 | CFTR (0.54) | CFTRHSD11B1LMNAGBA1KDM4E | |
| SCHEMBL5743239 | 0.89 | LMNA (0.55) | CFTRHSD11B1LMNAGBA1SMN1; SMN2 | |
| SCHEMBL5741485 | 0.89 | CFTR (0.51) | CFTRLMNAGBA1MAPTSMN1; SMN2 | |
| SCHEMBL5742915 | 0.89 | MEN1 (0.54) | CFTRLMNAGBA1KDM4EGAA | |
| SCHEMBL5742004 | 0.88 | CFTR (0.53) | CFTRLMNAGBA1KDM4EGAA |
Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.
Patent provenance — the patents this molecule appears in, and who filed them
Claimed or disclosed in 9 patents. claimed = in the patent's claims; disclosed = body only.
| Patent | Title | Assignee | Published | Priority | Filing | Country | Status |
|---|---|---|---|---|---|---|---|
| EP-2925317-A1 | A CFTR CORRECTOR FOR THE TEATMENT OF GENETIC DISORDERS AFFECTING STRIATED MUSCLE | Università Degli Studi Di Padova (IT) | 2015-10-07 | — | — | EP | claimed |
| WO-2014086687-A1 | A CFTR CORRECTOR FOR THE TEATMENT OF GENETIC DISORDERS AFFECTING STRIATED MUSCLE | UNIVERSITA' DEGLI STUDI DI PADOVA (IT) | 2014-06-12 | — | — | WO | claimed |
| EP-3030657-A1 | LIGASE E3 RNF185 INHIBITORS AND USES THEREOF | Commissariat à l'Energie Atomique et aux Energies Alternatives (FR) | 2016-06-15 | — | — | EP | disclosed |
| EP-2925317-A1 | A CFTR CORRECTOR FOR THE TEATMENT OF GENETIC DISORDERS AFFECTING STRIATED MUSCLE | Università Degli Studi Di Padova (IT) | 2015-10-07 | — | — | EP | disclosed |
| WO-2015018831-A1 | LIGASE E3 RNF185 INHIBITORS AND USES THEREOF | COMMISSARIAT A L'ENERGIE ATOMIQUE ET AUX ENERGIES ALTERNATIVES (FR) | 2015-02-12 | — | — | WO | disclosed |
| WO-2014086687-A1 | A CFTR CORRECTOR FOR THE TEATMENT OF GENETIC DISORDERS AFFECTING STRIATED MUSCLE | UNIVERSITA' DEGLI STUDI DI PADOVA (IT) | 2014-06-12 | — | — | WO | disclosed |
| WO-2009105234-A2 | METHODS AND COMPOSITIONS FOR THE TREATMENT OF DISORDERS ASSOCIATED WITH DEFECTS OF THE CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR GENE OR PROTEIN | COMBINATORX, INCORPORATED (US) | 2009-08-27 | — | — | WO | disclosed |
| EP-1646615-A1 | PYRIMIDINE DERIVATIVES AS MODULATORS OF ATP-BINDING CASSETTE TRANSPORTERS | Vertex Pharmaceuticals Incorporated (US) | 2006-04-19 | — | — | EP | disclosed |
| WO-2004111014-A1 | PYRIMIDINE DERIVATIVES AS MODULATORS OF ATP-BINDING CASSETTE TRANSPORTERS | VERTEX PHARMACEUTICALS INCORPORATED (US) | 2004-12-23 | — | — | WO | disclosed |