⚠ Novel chemotype — no close known analogue (best Tanimoto < 0.3). Unexplored chemical space relative to ChEMBL.
Similar compounds — the chemically nearest patent molecules
Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.
| Compound | similarity | top predicted | shared targets | |
|---|---|---|---|---|
| SCHEMBL1768217 | 0.69 | — | — | |
| SCHEMBL19204571 | 0.69 | — | — | |
| Hydrochloric Acid SCHEMBL13386456 | 0.67 | CA12 (0.57) | — | |
| SCHEMBL4910334 | 0.67 | — | — | |
| SCHEMBL6628483 | 0.65 | — | — | |
| SCHEMBL5951421 | 0.65 | — | — | |
| SCHEMBL28276651 | 0.65 | — | — | |
| SCHEMBL11726606 | 0.65 | AKR1B1 (0.42) | — | |
| SCHEMBL4912649 | 0.65 | — | — | |
| SCHEMBL4906012 | 0.65 | — | — |
Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.
Patent provenance — the patents this molecule appears in, and who filed them
Claimed or disclosed in 353 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.
| Patent | Title | Assignee | Published | Priority | Filing | Country | Status |
|---|---|---|---|---|---|---|---|
| US-20250144226-A1 | METHODS AND COMPOUNDS FOR THE TREATMENT OF GENETIC DISEASE | Design Therapeutics, Inc. | 2025-05-08 | — | — | US | claimed |
| EP-4319788-A1 | REGULATION OF CELLS AND ORGANISMS | Tets, Victor (US) | 2024-02-14 | — | — | EP | claimed |
| WO-2022214966-A1 | REGULATION OF CELLS AND ORGANISMS | TETS VICTOR (US) | 2022-10-13 | — | — | WO | claimed |
| US-20210283265-A1 | METHODS AND COMPOUNDS FOR THE TREATMENT OF GENETIC DISEASE | Design Therapeutics, Inc. | 2021-09-16 | — | — | US | claimed |
| EP-3774773-A1 | METHODS AND COMPOUNDS FOR THE TREATMENT OF GENETIC DISEASE | Design Therapeutics, Inc. (US) | 2021-02-17 | — | — | EP | claimed |
| WO-2019200161-A1 | METHODS AND COMPOUNDS FOR THE TREATMENT OF GENETIC DISEASE | DESIGN THERAPEUTICS INC. (US) | 2019-10-17 | — | — | WO | claimed |
| US-10357478-B2 | Polyamide compound and pharmaceutical composition for treating mitochondrial genetic diseases | TRIPLEX THERAPEUTICS INC. (JP) | 2019-07-23 | — | — | US | claimed |
| CN-109535133-A | Pyrrole-imidazole class heterocycle polypeptide, the drug comprising pyrrole-imidazole class heterocycle polypeptide and application | 深圳先进技术研究院 | 2019-03-29 | — | — | CN | claimed |
| CN-108236603-A | A kind of Allercur polyamide liposome and preparation method thereof and application thereof | 深圳先进技术研究院 | 2018-07-03 | — | — | CN | claimed |
| US-20170071912-A1 | Polyamide Compound and Pharmaceutical Composition for Treating Mitochondrial Genetic Diseases | TRIPLEX THERAPEUTICS INC. (JP) | 2017-03-16 | — | — | US | claimed |
| US-6958240-B1 | Inhibition of major groove DNA binding proteins by modified polyamides | CALIFORNIA INSTIUTE OF TECHNOLOGY (US) | 2005-10-25 | — | — | US | claimed |
| WO-2005033077-A1 | SEQUENCE SELECTIVE PYRROLE AND IMIDAZOLE POLYAMIDE METALLOCOMPLEXES | UNIVERSITY OF WESTERN SYDNEY (AU) | 2005-04-14 | — | — | WO | claimed |
| WO-2004083365-A2 | COMPOUNDS AND THEIR USE FOR SPECIFIC AND SIMULTANEOUS INHIBITION OF GENES INVOLVED IN DISEASES AND RELATED DRUGS | INSERM (Institut National de la Santé et de la Recherche Médicale) (FR) | 2004-09-30 | — | — | WO | claimed |
| EP-1307470-A2 | LINKED, SEQUENCE-SPECIFIC DNA-BINDING MOLECULES | UNIVERSITE DE GENEVE (CH) | 2003-05-07 | — | — | EP | claimed |
| WO-2002095022-A2 | SEQUENCE-SPECIFIC DNA BINDING COMPOUNDS AND THEIR USE IN TARGETING TELOMERES AND OTHER DNA SEQUENCES | UNIVERSITE DE GENEVE (CH) | 2002-11-28 | — | — | WO | claimed |
| US-20020169296-A1 | Linked, sequence-specific DNA-binding molecules | UNIVERSITE DE GENEVE (CH) | 2002-11-14 | — | — | US | claimed |
| US-6472537-B1 | POLYMERS FROM PRIMARY AMINE AND CARBOXYLIC ACID SUBSTITUTED PYROLE, HYDROXYPYROLE AND IMIDAZOLE MONOMERS AND HAVING 4-AMINOBUTYRIC ACID LINKER FORMING HAIRPIN TURNS AND OPTION-ALLY AMINO ACID RESIDUES; BINDING TO SPECIFIC | CALIFORNIA INSTITUTE OF TECHNOLOGY | 2002-10-29 | — | — | US | claimed |
| WO-2002004476-A2 | LINKED, SEQUENCE-SPECIFIC DNA-BINDING MOLECULES | UNIVERSITE DE GENEVE (CH) | 2002-01-17 | — | — | WO | claimed |
| EP-1162961-A2 | REGULATION OF HER2/neu ONCONGENE EXPRESSION BY SYNTHETIC POLYAMIDES | The Scripps Research Institute (US) | 2001-12-19 | — | — | EP | claimed |
| WO-2000015209-A2 | REGULATION OF HER2/neu ONCONGENE EXPRESSION BY SYNTHETIC POLYAMIDES | THE SCRIPPS RESEARCH INSTITUTE (US) | 2000-03-23 | — | — | WO | claimed |