Duvoglustat

Duvoglustat

SCHEMBL12017698

OC[C@H]1NCC(O)C(O)C1O

nearest known ligand 1.00 ✓ in ChEMBL — recovers established targets

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

GAAGLA

The experimentally established mechanism targets of Duvoglustat. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
GAA known ✓ P10253 6/20 1.00
GLA known ✓ P06280 4/20 1.00
FUCA1 P04066 4/20 1.00
MGAM O43451 4/20 1.00
GBA2 Q9HCG7 3/20 1.00
SI P14410 3/20 1.00
AGL P35573 3/20 1.00
MEN1 O00255 2/20 1.00
ALOX15 P16050 2/20 1.00
KMT2A Q03164 2/20 1.00
GBA1 P04062 2/20 1.00
LCT P09848 2/20 1.00
GBA3 Q9H227 2/20 1.00
MAN2B1 O00754 1/20 1.00
MAN2B2 Q9Y2E5 1/20 1.00
ALDH1A1 P00352 1/20 1.00
CYP2C19 P33261 1/20 1.00
TREH O43280 1/20 1.00
GANAB Q14697 1/20 1.00
MGAM2 Q2M2H8 1/20 1.00

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Duvoglustat SCHEMBL13298786 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL4619759 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL15896653 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL142573 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL10028910 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL12269503 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL24518227 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL2163281 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL13061461 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2
Duvoglustat SCHEMBL21104989 1.00 GAA (1.00) GAAFUCA1GLAMGAMGBA2

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 17 patents. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-20220184185-A1 MRNA BASED ENZYME REPLACEMENT THERAPY COMBINED WITH A PHARMACOLOGICAL CHAPERONE FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS MODERNATX, INC. 2022-06-16 US disclosed
US-20220142998-A1 Methods Of Treating Fabry Disease In Patients Having The G9331A Mutation In The GLA Gene AMICUS THERAPEUTICS, INC. (US) 2022-05-12 US disclosed
US-11241422-B2 Methods for treatment of Fabry disease AMICUS THERAPEUTICS, INC. (US) 2022-02-08 US disclosed
US-11234972-B2 Methods of treating fabry disease in patients having the G9331A mutation in the GLA gene AMICUS THERAPEUTICS, INC. (US) 2022-02-01 US disclosed
US-RE48608-E1 Method to predict response to pharmacological chaperone treatment of diseases AMICUS THERAPEUTICS, INC. (US) 2021-06-29 US disclosed
US-10813921-B2 Method to predict response to pharmacological chaperone treatment of diseases AMICUS THERAPEUTICS, INC. (US) 2020-10-27 US disclosed
US-20200215043-A1 Methods Of Treating Fabry Disease In Patients Having The G9331A Mutation In The GLA Gene AMICUS THERAPEUTICS, INC. (US) 2020-07-09 US disclosed
US-10537564-B2 Methods of treating fabry disease in patients having the G9331A mutation in the GLA gene AMICUS THERAPEUTICS, INC. (US) 2020-01-21 US disclosed
US-10406143-B2 Methods for treatment of fabry disease AMICUS THERAPEUTICS, INC. (US) 2019-09-10 US disclosed
US-10383864-B2 Methods for treatment of Fabry disease AMICUS THERAPEUTICS, INC. (US) 2019-08-20 US disclosed
US-20190183869-A1 TREATMENT OF FABRY DISEASE IN ERT-NAÏVE AND ERT-EXPERIENCED PATIENTS AMICUS THERAPEUTICS, INC. 2019-06-20 US disclosed
US-20190000818-A1 Method To Predict Response To Pharmacological Chaperone Treatment Of Diseases WILMINGTON TRUST, NATIONAL ASSOCIATION 2019-01-03 US disclosed
US-20190000819-A1 Methods Of Treating Fabry Disease In Patients Having The G9331A Mutation In The GLA Gene WILMINGTON TRUST, NATIONAL ASSOCIATION 2019-01-03 US disclosed
US-9000011-B2 Methods for treatment of Fabry disease AMICUS THERAPEUTICS, INC. (US) 2015-04-07 US disclosed
US-9000011-B2 Methods for treatment of Fabry disease AMICUS THERAPEUTICS, INC. (US) 2015-04-07 US disclosed
US-20120220632-A1 Methods For Treatment of Fabry Disease AMICUS THERAPEUTICS, INC. (US) 2012-08-30 US disclosed
US-20120220632-A1 Methods For Treatment of Fabry Disease AMICUS THERAPEUTICS, INC. (US) 2012-08-30 US disclosed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (13 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-10406143-B2 Methods for treatment of fabry disease GAA, HSP90B1, GBA1 GAA 1/4885GLA 17/4885FUCA1 118/4885
US-20220142998-A1 Methods Of Treating Fabry Disease In Patients Having The G9331A Mutation In The GLA Gene GAA, GLA, GBA1 GAA 1/4885GLA 2/4885FUCA1 136/4885
US-11241422-B2 Methods for treatment of Fabry disease GAA, HSP90B1, GBA1 GAA 1/4885GLA 17/4885FUCA1 118/4885
US-10383864-B2 Methods for treatment of Fabry disease GAA, HSP90B1, GBA1 GAA 1/4885GLA 17/4885FUCA1 118/4885
US-20190000819-A1 Methods Of Treating Fabry Disease In Patients Having The G9331A Mutation In The GLA Gene GAA, GLA, GBA1 GAA 1/4885GLA 2/4885FUCA1 136/4885
US-20190183869-A1 TREATMENT OF FABRY DISEASE IN ERT-NAÏVE AND ERT-EXPERIENCED PATIENTS GBA1, GBA2, GAA GAA 3/4885GLA 7/4885FUCA1 52/4885
US-11234972-B2 Methods of treating fabry disease in patients having the G9331A mutation in the GLA gene GAA, GLA, GBA1 GAA 1/4885GLA 2/4885FUCA1 136/4885
US-20190000818-A1 Method To Predict Response To Pharmacological Chaperone Treatment Of Diseases MAN2B1, GAA, GBA1 GAA 2/4885GLA 12/4885FUCA1 24/4885
US-10537564-B2 Methods of treating fabry disease in patients having the G9331A mutation in the GLA gene GAA, GLA, GBA1 GAA 1/4885GLA 2/4885FUCA1 136/4885
US-20120220632-A1 Methods For Treatment of Fabry Disease GAA, HSP90B1, GBA1 GAA 1/4885GLA 17/4885FUCA1 118/4885
US-20200215043-A1 Methods Of Treating Fabry Disease In Patients Having The G9331A Mutation In The GLA Gene GAA, GLA, GBA1 GAA 1/4885GLA 2/4885FUCA1 136/4885
US-20220184185-A1 MRNA BASED ENZYME REPLACEMENT THERAPY COMBINED WITH A PHARMACOLOGICAL CHAPERONE FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS GAA, GBA1, GBA2 GAA 1/4885GLA 9/4885FUCA1 15/4885
US-10813921-B2 Method to predict response to pharmacological chaperone treatment of diseases MAN2B1, GAA, GBA1 GAA 2/4885GLA 12/4885FUCA1 24/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.