Predicted protein targets (top 20)
| gene | UniProt | supporting neighbours | confidence | |
|---|---|---|---|---|
| ▸ | KMT2A | Q03164 | 3/20 | 0.37 |
| ▸ | LMNA | P02545 | 3/20 | 0.37 |
| ▸ | MEN1 | O00255 | 2/20 | 0.37 |
| ▸ | NPSR1 | Q6W5P4 | 1/20 | 0.37 |
| ▸ | PAOX | Q6QHF9 | 1/20 | 0.34 |
| ▸ | USP2 | O75604 | 1/20 | 0.33 |
| ▸ | HTT | P42858 | 1/20 | 0.33 |
| ▸ | SIGMAR1 | Q99720 | 2/20 | 0.32 |
| ▸ | POLB | P06746 | 1/20 | 0.32 |
| ▸ | SLC22A2 | O15244 | 1/20 | 0.32 |
| ▸ | SLC22A1 | O15245 | 1/20 | 0.32 |
| ▸ | ALDH1A1 | P00352 | 1/20 | 0.32 |
| ▸ | TSHR | P16473 | 1/20 | 0.32 |
| ▸ | ACHE | P22303 | 1/20 | 0.32 |
| ▸ | MAPK1 | P28482 | 1/20 | 0.32 |
| ▸ | CYP2C19 | P33261 | 1/20 | 0.32 |
| ▸ | KDM4E | B2RXH2 | 1/20 | 0.31 |
| ▸ | CHEK1 | O14757 | 1/20 | 0.31 |
| ▸ | PIM1 | P11309 | 1/20 | 0.31 |
| ▸ | IDO1 | P14902 | 1/20 | 0.31 |
Click a target to see other patent compounds predicted against it — the reverse direction, in place.
Similar compounds — the chemically nearest patent molecules
Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.
| Compound | similarity | top predicted | shared targets | |
|---|---|---|---|---|
| SCHEMBL229973 | 0.83 | PAOX (0.43) | KMT2ALMNAMEN1NPSR1PAOX | |
| SCHEMBL2230862 | 0.82 | PAOX (0.37) | KMT2ALMNAMEN1NPSR1PAOX | |
| SCHEMBL250410 | 0.78 | CYP2C19 (0.43) | KMT2ALMNAMEN1NPSR1PAOX | |
| SCHEMBL11323396 | 0.76 | PAOX (0.48) | KMT2ALMNAMEN1NPSR1PAOX | |
| SCHEMBL7366067 | 0.76 | PAOX (0.39) | KMT2ALMNAMEN1NPSR1PAOX | |
| Ammonia Solution, Strong SCHEMBL11798888 | 0.76 | CYP2C19 (0.41) | KMT2ALMNAMEN1NPSR1PAOX | |
| SCHEMBL8803099 | 0.76 | CYP2C19 (0.41) | KMT2ALMNAMEN1NPSR1PAOX | |
| SCHEMBL13006198 | 0.76 | LMNA (0.38) | KMT2ALMNAMEN1NPSR1PAOX | |
| SCHEMBL10643000 | 0.75 | KMT2A (0.43) | KMT2ALMNAMEN1NPSR1PAOX | |
| SCHEMBL9776421 | 0.75 | DNM1 (0.39) | ALDH1A1TSHR |
Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.
Patent provenance — the patents this molecule appears in, and who filed them
Claimed or disclosed in 164 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.
| Patent | Title | Assignee | Published | Priority | Filing | Country | Status |
|---|---|---|---|---|---|---|---|
| WO-2024105063-A1 | ANTISENSE OLIGONUCLEOTIDES FOR TREATMENT OF USHER 2A. EXONS 39-40 | STICHTING RADBOUD UNIVERSITAIR MEDISCH CENTRUM (NL) | 2024-05-23 | — | — | WO | disclosed |
| US-20240141339-A1 | Oligonucleotide Comprising Inosine for Treating DMD | BIOMARIN TECHNOLOGIES B.V. (NL) | 2024-05-02 | — | — | US | disclosed |
| EP-4359526-A1 | ALLELE-SPECIFIC SILENCING THERAPY FOR DFNA21 USING ANTISENSE OLIGONUCLEOTIDES | Stichting Radboud universitair medisch centrum (NL) | 2024-05-01 | — | — | EP | disclosed |
| WO-2024074668-A1 | ANTISENSE OLIGONUCLEOTIDES FOR TREATMENT OF USHER 2A. EXONS 30-31 | STICHTING RADBOUD UNIVERSITAIR MEDISCH CENTRUM (NL) | 2024-04-11 | — | — | WO | disclosed |
| WO-2024074670-A1 | ANTISENSE OLIGONUCLEOTIDES FOR TREATMENT OF USHER 2A. EXON 68 | STICHTING RADBOUD UNIVERSITAIR MEDISCH CENTRUM (NL) | 2024-04-11 | — | — | WO | disclosed |
| US-11920132-B2 | Oligonucleotide therapy for Leber congenital amaurosis | PROQR THERAPEUTICS II B.V. (NL) | 2024-03-05 | — | — | US | disclosed |
| US-11739324-B2 | Antisense oligonucleotides rescue aberrant splicing of ABCA4 | STICHTING KATHOLIEKE UNIVERSITEIT (NL) | 2023-08-29 | — | — | US | disclosed |
| EP-4183399-A1 | METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST EXON 52 OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE | Academisch Ziekenhuis Leiden (NL) | 2023-05-24 | — | — | EP | disclosed |
| US-20230151362-A1 | METHODS AND MEANS FOR EFFICIENT DKIPPING OF EXON 45 IN DUCHENNE MUSCULAR DYSTROPHY PRE-MRNA | ACADEMISCH ZIEKENHUIS LEIDEN (NL) | 2023-05-18 | — | — | US | disclosed |
| US-11634714-B2 | Oligonucleotide comprising an inosine for treating DMD | BIOMARIN TECHNOLOGIES B.V. (NL) | 2023-04-25 | — | — | US | disclosed |
| US-20100184833-A1 | METHODS AND MEANS FOR TREATING DNA REPEAT INSTABILITY ASSOCIATED GENETIC DISORDERS | PROSENTA TECHNOLOGIES B.V. (NL) | 2010-07-22 | — | — | US | disclosed |
| EP-2203173-A2 | MEANS AND METHODS FOR COUNTERACTING MUSCLE DISORDERS | Academisch Ziekenhuis Leiden (NL) | 2010-07-07 | — | — | EP | disclosed |
| WO-2010050802-A2 | METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53. | ACADEMISCH ZIEKENHUIS LEIDEN (NL) | 2010-05-06 | — | — | WO | disclosed |
| WO-2010050801-A1 | METHODS AND MEANS FOR EFFICIENT SKIPPING OF EXON 45 IN DUCHENNE MUSCULAR DYSTROPHY PRE-MRNA | PROSENSA TECHNOLOGIES B.V. (NL) | 2010-05-06 | — | — | WO | disclosed |
| WO-2009139630-A2 | METHOD FOR EFFICIENT EXON (44) SKIPPING IN DUCHENNE MUSCULAR DYSTROPHY AND ASSOCIATED MEANS | PROSENSA TECHNOLOGIES B.V. (NL) | 2009-11-19 | — | — | WO | disclosed |
| WO-2009099326-A1 | METHODS AND MEANS FOR TREATING DNA REPEAT INSTABILITY ASSOCIATED GENETIC DISORDERS | PROSENSA HOLDING BV (NL) | 2009-08-13 | — | — | WO | disclosed |
| WO-2009054725-A2 | MEANS AND METHODS FOR COUNTERACTING MUSCLE DISORDERS | ACADEMISCH ZIEKENHUIS LEIDEN (NL) | 2009-04-30 | — | — | WO | disclosed |
| EP-2049664-A1 | METHODS AND MEANS FOR TREATING DNA REPEAT INSTABILITY ASSOCIATED GENETIC DISORDERS | Prosensa Technologies B.V. (NL) | 2009-04-22 | — | — | EP | disclosed |
| WO-2008018795-A1 | METHODS AND MEANS FOR TREATING DNA REPEAT INSTABILITY ASSOCIATED GENETIC DISORDERS | PROSENSA TECHNOLOGIES B.V. (NL) | 2008-02-14 | — | — | WO | disclosed |
| US-20070231360-A1 | NEURAL CONDUIT AGENT DISSEMINATION | MINU, L.L.C. (US) | 2007-10-04 | — | — | US | disclosed |