Sapropterin

Sapropterin

SCHEMBL1534380

CC(O)C(O)C1CNc2[nH]c(N)nc(=O)c2N1

nearest known ligand 0.65

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

PAH

The experimentally established mechanism targets of Sapropterin. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
PAH known ✓ P00439 1/20 0.62
NOS1 P29475 6/20 0.65
CASP7 P55210 2/20 0.65
HSD17B10 Q99714 2/20 0.65
USP2 O75604 1/20 0.65
KDM4E B2RXH2 2/20 0.64
MAPT P10636 2/20 0.64
BLM P54132 2/20 0.64
KMT2A Q03164 2/20 0.64
ALDH1A1 P00352 1/20 0.64
GLA P06280 1/20 0.64
HPGD P15428 1/20 0.64
PMP22 Q01453 1/20 0.64
NPSR1 Q6W5P4 1/20 0.64
TDP1 Q9NUW8 1/20 0.64
NOS3 P29474 2/20 0.52
NOS2 P35228 2/20 0.52
MEN1 O00255 1/20 0.31
RGS12 O14924 1/20 0.31
LMNA P02545 1/20 0.31

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Sapropterin SCHEMBL31673726 1.00 NOS1 (0.65) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL25915067 1.00 NOS1 (0.65) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL20769839 1.00 NOS1 (0.65) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL25915163 1.00 NOS1 (0.65) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL28826011 1.00 NOS1 (0.65) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL37480 1.00 NOS1 (0.65) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL258544 1.00 NOS1 (0.65) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL1650464 0.99 NOS1 (0.64) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL21046203 0.99 KDM4E (0.66) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL1070420 0.99 KDM4E (0.66) NOS1CASP7HSD17B10USP2KDM4E

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 15 patents. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-20240115573-A1 Managing the Acute and Long-Term Effects of Coronaviral Infections and Compositions Related Thereto UNIV EMORY (US) 2024-04-11 US disclosed
EP-4313020-A1 MANAGING THE ACUTE AND LONG-TERM EFFECTS OF CORONAVIRAL INFECTIONS AND COMPOSITIONS RELATED THERETO Emory University (US) 2024-02-07 EP disclosed
WO-2023122298-A1 PROTEIN STABILIZING COMPOUNDS CONTAINING USP28 AND/OR USP25 TARGETING LIGANDS Stablix, Inc. (US) 2023-06-29 WO disclosed
WO-2022272133-A2 PROTEIN STABILIZING COMPOUNDS CONTAINING USP7 LIGANDS Stablix, Inc. (US) 2022-12-29 WO disclosed
WO-2022204517-A1 MANAGING THE ACUTE AND LONG-TERM EFFECTS OF CORONAVIRAL INFECTIONS AND COMPOSITIONS RELATED THERETO EMORY UNIVERSITY (US) 2022-09-29 WO disclosed
CN-114814063-A Method for detecting tetrahydrobiopterin in human body 宁波熙宁检测技术有限公司 2022-07-29 CN disclosed
CN-112522222-B Novel tryptophan hydroxylase mutant and application thereof 河北维达康生物科技有限公司 2021-12-07 CN disclosed
CN-112522222-A Novel tryptophan hydroxylase mutant and application thereof 保定保利瑞合生物科技有限公司 2021-03-19 CN disclosed
US-20180221371-A1 TREATMENT FOR THE FETUS WITH CONGENITAL HEART DISEASE CHILDREN'S NATIONAL MEDICAL CENTER (US) 2018-08-09 US disclosed
US-20170087157-A1 NITRIC OXIDE-MODULATING BONE-TARGETING COMPLEXES ELWHA LLC 2017-03-30 US disclosed
US-20170087175-A1 NITRIC OXIDE-MODULATING BONE-TARGETING COMPLEXES ELWHA LLC 2017-03-30 US disclosed
US-20170087221-A1 NITRIC OXIDE-MODULATING BONE-TARGETING COMPLEXES ELWHA LLC 2017-03-30 US disclosed
US-20140309186-A1 Metabolomics-Based Identification of Disease-Causing Agents GEORGIA TECH RESEARCH CORPORATION 2014-10-16 US disclosed
US-20110246081-A1 Metabolomics-Based Identification of Disease-Causing Agents GEORGIA TECH RESEARCH CORPORATION (US) 2011-10-06 US disclosed
WO-2011034397-A2 METHOD FOR PREDICTING DRUG TARGETS AND SCREENING FOR DRUGS FOR PATHOGENIC MICROORGANISMS USING ESSENTIAL METABOLITES 한국과학기술원 (KR) 2011-03-24 WO disclosed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (1 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-20180221371-A1 TREATMENT FOR THE FETUS WITH CONGENITAL HEART DISEASE HIF1AN, HIF1A, EGLN3 PAH 17/4885NOS1 915/4885CASP7 2709/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.