Sugi Predict
/ Targets
/ MPDU1
Top predicted compounds (top 20 by supporting neighbours, then confidence)
| Compound | Confidence | Supporting neighbours |
|---|
Clinical trials — most relevant to MPDU1 by text similarity (a relevance ranking, not an exhaustive list)
| Trial | Phase | Status |
|---|
| Comparison of Pharmacokinetic, Safety, Tolerability of Alpha-1 MP and Prolastin In Alpha1-antitrypsin Deficient Adults |
PHASE3 | COMPLETED |
| 24-Week Study to Assess the PD, Safety, Tolerability, and PK of GLM101 in Participants With PMM2-CDG |
PHASE2 | COMPLETED |
| Open-Label Extension Study to Assess GLM101 in PMM2-CDG Patients |
PHASE2 | ENROLLING_BY_INVITATION |
| The Effect of Triheptanoin on Fatty Acid Oxidation and Exercise Tolerance in Patients With Glycogenoses |
PHASE2 | COMPLETED |
| RGX-111 Gene Therapy in Patients With MPS I |
PHASE1/PHASE2 | SUSPENDED |
| A Study Evaluating the Safety and Pharmacokinetics of Aldurazyme® (Laronidase) in MPS I Patients Less Than 5 Years Old |
PHASE2 | COMPLETED |
| A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of JWK008 in Patients With Mucopolysaccharidosis Type I |
PHASE1 | RECRUITING |
| The Natural History of Alpha-Mannosidosis |
nan | COMPLETED |
| Biomarker for Mannosidosis Disease (BioMannosidosis) |
nan | WITHDRAWN |
| Using D-Galactose as a Food Supplement in Congenital Disorders of Glycosylation |
nan | COMPLETED |
| Biomarker for Mucolipidosis Disorder Type I, II, III, IV (BioML) |
nan | WITHDRAWN |
| Biomarker for Hurler Disease (BioHurler) |
nan | WITHDRAWN |
| Glycosylation in Patients With Galactosaemia |
nan | COMPLETED |
| Incidence and Consequences of Disorders of Glycosylation in Patients With Conotruncal and Septal Heart Defects |
nan | UNKNOWN |
| Biomarker for Sanfilippo Type A-B-C-D Disease (BioSanfilippo) |
nan | WITHDRAWN |
| Mucopolysaccharidosis I (MPS I) Registry |
nan | COMPLETED |
| Registry Gangliosidoses |
nan | UNKNOWN |
| Characterization of the Patient Population With Galactosialidosis |
nan | COMPLETED |
| Clinical Biomarkers in Alpha-mannosidosis |
nan | COMPLETED |
| Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic Resonance Imaging |
nan | COMPLETED |
| Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B) |
nan | COMPLETED |
| Detection of Pompe Disease in Adult Patients With Myopathies of Uncertain Origin or With Asymptomatic Hyper-CK-emia |
nan | UNKNOWN |
| The Natural History of Sialidosis Type I |
nan | RECRUITING |
| A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB |
nan | COMPLETED |
| Longitudinal Studies of the Glycoproteinoses |
nan | COMPLETED |
| Screening of Lysosomal Storage Disorders Diseases in Minority Groups |
nan | UNKNOWN |
| Natural History of Glycosphingolipid Storage Disorders and Glycoprotein Disorders |
nan | RECRUITING |
| Genetic Studies of Lysosomal Storage Disorders |
nan | ENROLLING_BY_INVITATION |
| Effect of Primary Non-surgical Endodontic Therapy on Glycaemic Control in Type 2 Diabetic Patients With Asymptomatic Apical Periodontitis |
nan | COMPLETED |
| The LD Lync Study - Natural History Study of Lipodystrophy Syndromes |
nan | RECRUITING |
Related proteins — ESM-2 sequence neighbours (a MPDU1 binder may also engage these)