Arimoclomol

Arimoclomol

SCHEMBL196123

[O-][n+]1cccc(/C(Cl)=N\OC[C@H](O)CN2CCCCC2)c1

nearest known ligand 0.54

Full drug profile on Sugi Atlas →

Predicted protein targets (top 7)

geneUniProtsupporting neighboursconfidence
HSF1 Q00613 15/20 0.54
CYP2D6 P10635 1/20 0.43
TSHR P16473 1/20 0.43
HIF1A Q16665 1/20 0.43
ATM Q13315 1/20 0.42
ACE2 Q9BYF1 1/20 0.42
ABCB1 P08183 2/20 0.42

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Arimoclomol SCHEMBL12254223 1.00 HSF1 (0.54) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL12254225 1.00 HSF1 (0.54) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL2324741 1.00 HSF1 (0.54) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL1896428 1.00 HSF1 (0.54) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL25257807 1.00 HSF1 (0.54) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL5699241 1.00 HSF1 (0.54) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL25258754 1.00 HSF1 (0.54) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL5699253 0.99 HSF1 (0.53) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL7052423 0.99 HSF1 (0.53) HSF1CYP2D6TSHRHIF1AATM
Arimoclomol SCHEMBL5699251 0.99 HSF1 (0.53) HSF1CYP2D6TSHRHIF1AATM

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 1154 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-20260097008-A1 ACETYL LEUCINE FOR USE IN TREATING NIEMANN-PICK DISEASE TYPE C INTRABIO INC. 2026-04-09 US claimed
US-12576076-B2 Use of HSP70 as a regulator of enzymatic activity Zevra Denmark A/S (DK) 2026-03-17 US claimed
EP-4702057-A1 IN VIVO IMAGING OF AN ALS BIOMARKER AND MEANS THEREFOR AL-S Pharma AG (CH) 2026-03-04 EP claimed
US-20250382291-A1 SUBSTITUTED PYRROLO[2,3-b]PYRIDINES FOR SUPPRESSING TOXIC ENDOPLASMIC RETICULUM STRESS UNIV COLUMBIA (US) 2025-12-18 US claimed
EP-4171559-B1 ARIMOCLOMOL FOR TREATING GAUCHER DISEASE ZEVRA DENMARK AS (DK) 2025-09-10 EP claimed
EP-4608399-A1 ARIMOCLOMOL COMPOSITIONS FOR USE IN TREATING NIEMANN PICK DISEASE TYPE C (NPC) Zevra Denmark A/S (DK) 2025-09-03 EP claimed
US-20250268748-A1 TREATMENT OF SPINAL MUSCULAR ATROPHY BY INDUCING HEAT SHOCK RESPONSE THE RESEARCH INSTITUTE AT NATIONWIDE CHILDREN’S HOSPITAL 2025-08-28 US claimed
EP-3837011-B1 TOFACITINIB FOR USE IN TREATING, DELAYING PROGRESSION OF OR REDUCING THE SEVERITY OF AMYOTROPHIC LATERAL SCLEROSIS UNIV MICHIGAN REGENTS (US) 2025-07-09 EP claimed
WO-2025111482-A1 COMPLEXING AGENT SALT FORMULATIONS OF PHARMACEUTICAL COMPOUNDS AT LOW STOICHIOMETRIC RATIOS BEXSON BIOMEDICAL, INC. (US) 2025-05-30 WO claimed
WO-2025088514-A1 METTL3-METTL14-COMPLEX INHIBITORS FOR THE TREATMENT OF NEUROMUSCULAR DEGENERATIVE PATHOLOGIES CAUSED BY OR LINKED TO MUTATIONS IN THE FUS GENE Università degli Studi di Roma “La Sapienza” (IT) 2025-05-01 WO claimed
WO-2009035473-A2 METHOD OF TREATING BINGE EATING DISORDER, OBESITY RESULTING FROM BINGE EATING BEHAVIOR AND DEPRESSIVE DISORDERS SANFILIPPO LOUIS C (US) 2009-03-19 WO claimed
WO-2008137149-A1 DIABETIC WOUND HEALING CYTRX CORPORATION (US) 2008-11-13 WO claimed
WO-2008133884-A2 METHODS AND COMPOSITIONS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS COMBINATORX, INCORPORATED (US) 2008-11-06 WO claimed
WO-2008116165-A2 METHODS AND SYSTEMS OF DELIVERING MEDICATION VIA INHALATION NEXT SAFETY, INC. (US) 2008-09-25 WO claimed
EP-1954244-A1 LYOPHILIZATION PROCESS AND PRODUCTS OBTAINED THEREBY Scidose, Llc (US) 2008-08-13 EP claimed
WO-2008070010-A2 HYDROXYLAMINE DERIVATIVES FOR THE TREATMENT OF STROKE CYTRX CORPORATION (US) 2008-06-12 WO claimed
US-20080066741-A1 METHODS AND SYSTEMS OF DELIVERING MEDICATION VIA INHALATION HUNTER, CHARLES ERIC 2008-03-20 US claimed
WO-2008021210-A2 METHODS AND COMPOSITIONS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS COMBINATORX, INCORPORATED (US) 2008-02-21 WO claimed
WO-2007061529-A1 LYOPHILIZATION PROCESS AND PRODUCTS OBTAINED THEREBY SCIDOSE LLC. (US) 2007-05-31 WO claimed
US-20070116729-A1 Lyophilization process and products obtained thereby SCIDOSE LLC 2007-05-24 US claimed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (3 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-12576076-B2 Use of HSP70 as a regulator of enzymatic activity HSPB1, HSPA1B, HSPD1 HSF1 22/4885CYP2D6 2631/4885TSHR 4461/4885
US-20260097008-A1 ACETYL LEUCINE FOR USE IN TREATING NIEMANN-PICK DISEASE TYPE C NPC1, NPC1L1, NAA50 HSF1 3863/4885CYP2D6 3272/4885TSHR 4247/4885
US-20250382291-A1 SUBSTITUTED PYRROLO[2,3-b]PYRIDINES FOR SUPPRESSING TOXIC ENDOPLASMIC RETICULUM STRESS HSPA5, ATP2A1, DNAJC10 HSF1 98/4885CYP2D6 3832/4885TSHR 4023/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.