⚠ Novel chemotype — no close known analogue (best Tanimoto < 0.3). Unexplored chemical space relative to ChEMBL.
Similar compounds — the chemically nearest patent molecules
Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.
| Compound | similarity | top predicted | shared targets | |
|---|---|---|---|---|
| SCHEMBL784167 | 0.73 | — | — | |
| SCHEMBL1514201 | 0.72 | — | — | |
| SCHEMBL2524893 | 0.72 | CA2 (0.33) | — | |
| SCHEMBL28132111 | 0.69 | — | — | |
| SCHEMBL3501702 | 0.69 | — | — | |
| SCHEMBL7731451 | 0.69 | — | — | |
| Phosphoric Acid SCHEMBL26662213 | 0.67 | CA2 (0.38) | — | |
| Phosphoramidic Acid SCHEMBL220946 | 0.67 | LAP3 (0.32) | — | |
| SCHEMBL20335184 | 0.65 | — | — | |
| SCHEMBL2048661 | 0.65 | CTSA (0.35) | — |
Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.
Patent provenance — the patents this molecule appears in, and who filed them
Claimed or disclosed in 38 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.
| Patent | Title | Assignee | Published | Priority | Filing | Country | Status |
|---|---|---|---|---|---|---|---|
| US-10760076-B2 | Use of single-stranded antisense oligonucleotide in prevention or treatment of genetic diseases involving a trinucleotide repeat expansion | PROQR THERAPEUTICS II B.V. (NL) | 2020-09-01 | — | — | US | claimed |
| US-20240229026-A1 | CHIRAL CONTROL | WAVE LIFE SCIENCES LTD. (SG) | 2024-07-11 | — | — | US | disclosed |
| WO-2024009306-A1 | COMPOSITIONS AND METHODS FOR TREATING PRIMARY CILIARY DYSKINESIA | SKIP THERAPEUTICS LTD. (IL) | 2024-01-11 | — | — | WO | disclosed |
| WO-2023200893-A1 | SMALL MOLECULE ENHANCERS OF ANTISENSE OLIGO ACTIVITY | OREGON STATE UNIVERSITY (US) | 2023-10-19 | — | — | WO | disclosed |
| EP-4219516-A2 | CHIRAL CONTROL | Wave Life Sciences Ltd. (SG) | 2023-08-02 | — | — | EP | disclosed |
| US-11643657-B2 | Chiral control | WAVE LIFE SCIENCES LTD. (SG) | 2023-05-09 | — | — | US | disclosed |
| EP-2872147-B1 | METHOD FOR MAKING CHIRAL OLIGONUCLEOTIDES | WAVE LIFE SCIENCES LTD (SG) | 2022-12-21 | — | — | EP | disclosed |
| US-20220280548-A1 | COMBINATION THERAPY FOR SPINAL MUSCULAR ATROPHY | BIOGEN MA INC. (US) | 2022-09-08 | — | — | US | disclosed |
| EP-4013387-A1 | COMBINATION THERAPY FOR SPINAL MUSCULAR ATROPHY | Biogen MA Inc. (US) | 2022-06-22 | — | — | EP | disclosed |
| US-20210308281-A1 | COMBINATION THERAPY FOR SPINAL MUSCULAR ATROPHY | BIOGEN MA INC. (US) | 2021-10-07 | — | — | US | disclosed |
| EP-2454370-A1 | MICRORNA-24 | Julius-Maximilians-Universität Würzburg (DE) | 2012-05-23 | — | — | EP | disclosed |
| WO-2011006669-A1 | MICRORNA-24 | JULIUS-MAXIMILIANS-UNIVERSITÄT WÜRZBURG (DE) | 2011-01-20 | — | — | WO | disclosed |
| EP-2249874-A1 | METHODS AND MEANS FOR TREATING DNA REPEAT INSTABILITY ASSOCIATED GENETIC DISORDERS | ProSensa Holding BV (NL) | 2010-11-17 | — | — | EP | disclosed |
| WO-2009099326-A1 | METHODS AND MEANS FOR TREATING DNA REPEAT INSTABILITY ASSOCIATED GENETIC DISORDERS | PROSENSA HOLDING BV (NL) | 2009-08-13 | — | — | WO | disclosed |
| EP-2049664-A1 | METHODS AND MEANS FOR TREATING DNA REPEAT INSTABILITY ASSOCIATED GENETIC DISORDERS | Prosensa Technologies B.V. (NL) | 2009-04-22 | — | — | EP | disclosed |
| WO-2008018795-A1 | METHODS AND MEANS FOR TREATING DNA REPEAT INSTABILITY ASSOCIATED GENETIC DISORDERS | PROSENSA TECHNOLOGIES B.V. (NL) | 2008-02-14 | — | — | WO | disclosed |
| EP-1874791-A1 | METHODS AND COMPOSITIONS FOR REGULATED EXPRESSION OF NUCLEIC ACID AT POST-TRANSCRIPTIONAL LEVEL | The University of North Carolina at Chapel Hill (US) | 2008-01-09 | — | — | EP | disclosed |
| WO-2006119137-A1 | METHODS AND COMPOSITIONS FOR REGULATED EXPRESSION OF NUCLEIC ACID AT POST-TRANSCRIPTIONAL LEVEL | THE UNIVERSITY OF NORTH CAROLINA AT CHAPEL HILL (US) | 2006-11-09 | — | — | WO | disclosed |
| EP-1529105-A1 | METHODS TO REPROGRAM SPLICE SITE SELECTION IN PRE-MESSENGER RNAS | Université de Sherbrooke (CA) | 2005-05-11 | — | — | EP | disclosed |
| WO-2004015106-A1 | METHODS TO REPROGRAM SPLICE SITE SELECTION IN PRE-MESSENGER RNAS | UNIVERSITé DE SHERBROOKE (CA) | 2004-02-19 | — | — | WO | disclosed |