Semagacestat

Semagacestat

SCHEMBL29353755

CC(C)[C@H](O)C(=O)N[C@@H](C)C(=O)N[C@@H]1C(=O)N(C)CCc2ccccc21

nearest known ligand 1.00 ✓ in ChEMBL — recovers established targets

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

APH1AAPH1BNCSTNPSEN1PSEN2PSENEN

The experimentally established mechanism targets of Semagacestat. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 8)

geneUniProtsupporting neighboursconfidence
PSEN1 known ✓ P49768 19/20 1.00
PSEN2 known ✓ P49810 19/20 1.00
APH1B known ✓ Q8WW43 19/20 1.00
NCSTN known ✓ Q92542 19/20 1.00
APH1A known ✓ Q96BI3 19/20 1.00
PSENEN known ✓ Q9NZ42 19/20 1.00
XIAP P98170 1/20 0.69
SPPL2A Q8TCT8 1/20 0.43

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Semagacestat SCHEMBL417581 1.00 PSEN1 (1.00) PSEN1PSEN2APH1BNCSTNAPH1A
Semagacestat SCHEMBL12050112 1.00 PSEN1 (1.00) PSEN1PSEN2APH1BNCSTNAPH1A
Semagacestat SCHEMBL13387771 1.00 PSEN1 (1.00) PSEN1PSEN2APH1BNCSTNAPH1A
Semagacestat SCHEMBL14876852 1.00 PSEN1 (1.00) PSEN1PSEN2APH1BNCSTNAPH1A
Semagacestat SCHEMBL30579757 0.99 PSEN1 (0.98) PSEN1PSEN2APH1BNCSTNAPH1A
Semagacestat SCHEMBL1812166 0.99 PSEN1 (0.98) PSEN1PSEN2APH1BNCSTNAPH1A
SCHEMBL21577575 0.90 PSEN1 (0.81) PSEN1PSEN2APH1BNCSTNAPH1A
SCHEMBL18301563 0.86 PSEN1 (0.76) PSEN1PSEN2APH1BNCSTNAPH1A
SCHEMBL7849704 0.85 XIAP (0.77) PSEN1PSEN2APH1BNCSTNAPH1A
SCHEMBL4537099 0.85 PSEN1 (0.74) PSEN1PSEN2APH1BNCSTNAPH1A

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 592 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-12599587-B2 Chlorinated tetralin compounds and pharmaceutical compositions SPRINGWORKS THERAPEUTICS, INC. (US) 2026-04-14 US claimed
EP-4720261-A1 NOVEL CULTURE CONDITIONS FOR CLONAL EXPANSION OF NEPHRON PROGENITOR CELLS, GENERATION OF NEPHRON ORGANOIDS, AND RAPID AND SCALABLE MODELING OF POLYCYSTIC KIDNEY DISEASE University of Southern California (US) 2026-04-08 EP claimed
US-20260060960-A1 GAMMA-SECRETASE INHIBITORS FOR USE IN THE TREATMENT OF INHERITED EPIDERMOLYSIS BULLOSA OSPEDALE PEDIATRICO BAMBINO GESU (IT) 2026-03-05 US claimed
US-12559559-B2 Targeting Galectin-9 as a therapeutic strategy for T-cell exhaustion in T-cell acute lymphoblastic leukemia DANA-FARBER CANCER INSTITUTE, INC. (US) 2026-02-24 US claimed
US-20260034099-A1 CHLORINATED TETRALIN COMPOUNDS AND PHARMACEUTICAL COMPOSITIONS SPRINGWORKS THERAPEUTICS INC (US) 2026-02-05 US claimed
US-20260027084-A1 TREATMENT OF MULTIPLE MYELOMA SPRINGWORKS THERAPEUTICS INC (US) 2026-01-29 US claimed
US-20250340837-A1 CELLS UNIVERSITY OF GENEVA (CH) 2025-11-06 US claimed
US-20250304916-A1 METHODS AND COMPOSITIONS FOR GENERATING VASCULAR LEPTOMENINGEAL CELLS TRAILHEAD BIOSYSTEMS INC (US) 2025-10-02 US claimed
US-20250281638-A1 Compositions and Methods for Activating Natural Killer Cells CHIMERA BIOENGINEERING, INC. (US) 2025-09-11 US claimed
EP-4612298-A1 BCMA VH-ONLY CARS Dana-Farber Cancer Institute, Inc. (US) 2025-09-10 EP claimed
WO-2022200433-A1 IMIDAZO[1,2-B]PYRIDAZINE BASED TRICYCLIC COMPOUNDS AS INHIBITORS OF HASPIN AND THERAPEUTIC USES THEREOF Fundación Del Sector Público Estatal Centro Nacional De Investigaciones Oncológicas Carlos III (F.S.P. CNIO) (ES) 2022-09-29 WO claimed
WO-2022180150-A1 IMIDAZO[1,2-A]PYRAZINES AS INHIBITORS OF HASPIN AND THERAPEUTIC USES THEREOF Fundación Del Sector Público Estatal Centro Nacional De Investigaciones Oncológicas Carlos III (F.S.P. CNIO) (ES) 2022-09-01 WO claimed
EP-4045631-A1 PRODUCTION OF SKELETAL MUSCLE CELLS AND SKELETAL MUSCLE TISSUE FROM PLURIPOTENT STEM CELLS Georg-August-Universität Göttingen (DE) 2022-08-24 EP claimed
EP-4041308-A1 MODULATING LYMPHATIC VESSELS IN NEUROLOGICAL DISEASE University of Virginia Patent Foundation (US) 2022-08-17 EP claimed
WO-2022125392-A1 COMPOSITIONS AND METHODS FOR ACTIVATING T-CELLS CHIMERA BIOENGINEERING, INC. (US) 2022-06-16 WO claimed
WO-2022040447-A9 METHODS FOR TREATING RESPIRATORY DISEASES CHARACTERIZED BY MUCUS HYPERSECRETION THE BOARD OF TRUSTEES OF THE LELAND STANFORD JUNIOR UNIVERSITY (US) 2022-06-16 WO claimed
US-11319363-B2 Humanized tau antibodies in Alzheimer's disease AXON NEUROSCIENCE SE (CY) 2022-05-03 US claimed
EP-3969444-A1 COMPOSITIONS AND METHODS FOR THE TREATMENT OF NEUROLOGICAL DISEASES AND DISORDERS The Regents of the University of California (US) 2022-03-23 EP claimed
EP-3970725-A1 A GAMMA SECRETASE INHIBITOR FOR TREATING HEARING LOSS Massachusetts Eye & Ear Infirmary (US) 2022-03-23 EP claimed
WO-2022040447-A2 METHODS FOR TREATING RESPIRATORY DISEASES CHARACTERIZED BY MUCUS HYPERSECRETION THE BOARD OF TRUSTEES OF THE LELAND STANFORD JUNIOR UNIVERSITY (US) 2022-02-24 WO claimed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (5 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-20260060960-A1 GAMMA-SECRETASE INHIBITORS FOR USE IN THE TREATMENT OF INHERITED EPIDERMOLYSIS BULLOSA BACE1, BACE2, PSENEN PSEN1 11/4885PSEN2 28/4885APH1B 102/4885
US-20260034099-A1 CHLORINATED TETRALIN COMPOUNDS AND PHARMACEUTICAL COMPOSITIONS BACE1, BACE2, DSG1 PSEN1 11/4885PSEN2 16/4885APH1B 89/4885
US-12599587-B2 Chlorinated tetralin compounds and pharmaceutical compositions CLIC1, CLCN2, CSNK1D PSEN1 464/4885PSEN2 447/4885APH1B 3750/4885
US-20260027084-A1 TREATMENT OF MULTIPLE MYELOMA BACE1, BACE2, CD47 PSEN1 150/4885PSEN2 505/4885APH1B 39/4885
US-12559559-B2 Targeting Galectin-9 as a therapeutic strategy for T-cell exhaustion in T-cell acute lymphoblastic leukemia LGALS9, LGALS3BP, LGALS1 PSEN1 2403/4885PSEN2 2764/4885APH1B 997/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.