Predicted protein targets (top 20)
| gene | UniProt | supporting neighbours | confidence | |
|---|---|---|---|---|
| ▸ | SMN1; SMN2 | Q16637 | 2/20 | 0.54 |
| ▸ | OGG1 | O15527 | 1/20 | 0.52 |
| ▸ | NPC1 | O15118 | 3/20 | 0.51 |
| ▸ | RAB9A | P51151 | 2/20 | 0.51 |
| ▸ | HSP90AA1 | P07900 | 2/20 | 0.51 |
| ▸ | HPGD | P15428 | 2/20 | 0.51 |
| ▸ | ALDH1A1 | P00352 | 2/20 | 0.51 |
| ▸ | NFKB1 | P19838 | 1/20 | 0.51 |
| ▸ | CASP3 | P42574 | 1/20 | 0.51 |
| ▸ | NFKB2 | Q00653 | 1/20 | 0.51 |
| ▸ | RELA | Q04206 | 1/20 | 0.51 |
| ▸ | SENP8 | Q96LD8 | 1/20 | 0.51 |
| ▸ | SENP7 | Q9BQF6 | 1/20 | 0.51 |
| ▸ | SENP6 | Q9GZR1 | 1/20 | 0.51 |
| ▸ | MEN1 | O00255 | 1/20 | 0.48 |
| ▸ | KMT2A | Q03164 | 1/20 | 0.48 |
| ▸ | L3MBTL1 | Q9Y468 | 1/20 | 0.48 |
| ▸ | TSHR | P16473 | 1/20 | 0.47 |
| ▸ | HDAC3 | O15379 | 1/20 | 0.46 |
| ▸ | HDAC1 | Q13547 | 1/20 | 0.46 |
Click a target to see other patent compounds predicted against it — the reverse direction, in place.
Similar compounds — the chemically nearest patent molecules
Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.
| Compound | similarity | top predicted | shared targets | |
|---|---|---|---|---|
| SCHEMBL29123079 | 0.83 | CYP1A2 (0.62) | SMN1; SMN2NPC1RAB9AALDH1A1NFKB1 | |
| SCHEMBL28804019 | 0.82 | SMN1; SMN2 (0.69) | SMN1; SMN2OGG1NPC1RAB9AHPGD | |
| SCHEMBL8007465 | 0.82 | LMNA (0.60) | SMN1; SMN2NPC1RAB9AHPGDALDH1A1 | |
| SCHEMBL29122556 | 0.80 | EPHX2 (0.50) | ALDH1A1 | |
| SCHEMBL4347910 | 0.79 | SMN1; SMN2 (0.44) | SMN1; SMN2NPC1RAB9AHPGDALDH1A1 | |
| SCHEMBL29122533 | 0.79 | PKM (0.72) | SMN1; SMN2NPC1RAB9AHPGDALDH1A1 | |
| SCHEMBL1665183 | 0.78 | OGG1 (0.59) | SMN1; SMN2OGG1NPC1RAB9AHSP90AA1 | |
| SCHEMBL9490115 | 0.78 | HSP90AA1 (0.71) | SMN1; SMN2OGG1NPC1RAB9AHSP90AA1 | |
| SCHEMBL4907648 | 0.78 | NPC1 (0.57) | SMN1; SMN2OGG1NPC1RAB9AHSP90AA1 | |
| SCHEMBL24185290 | 0.77 | OGG1 (0.57) | SMN1; SMN2OGG1NPC1RAB9AHSP90AA1 |
Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.
Patent provenance — the patents this molecule appears in, and who filed them
Claimed or disclosed in 2 patents. claimed = in the patent's claims; disclosed = body only.
| Patent | Title | Assignee | Published | Priority | Filing | Country | Status |
|---|---|---|---|---|---|---|---|
| EP-4735422-A1 | SUBSTITUTED CYCLIC COMPOUNDS AND METHODS OF TREATING PHENYLKETONURIA AND OTHER AMINO ACIDURIAS | Sanofi (FR) | 2026-05-06 | — | — | EP | disclosed |
| WO-2025006827-A1 | SUBSTITUTED CYCLIC COMPOUNDS AND METHODS OF TREATING PHENYLKETONURIA AND OTHER AMINO ACIDURIAS | GENZYME CORPORATION (US) | 2025-01-02 | — | — | WO | disclosed |