Sepiapterin

Sepiapterin

SCHEMBL258399

C[C@H](O)C(=O)C1=Nc2c([nH]c(N)nc2=O)NC1

nearest known ligand 0.65

Full drug profile on Sugi Atlas →

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
CASP7 P55210 2/20 0.65
HSD17B10 Q99714 2/20 0.65
KDM4E B2RXH2 2/20 0.65
MAPT P10636 2/20 0.65
BLM P54132 2/20 0.65
KMT2A Q03164 2/20 0.65
MEN1 O00255 1/20 0.65
RGS12 O14924 1/20 0.65
LMNA P02545 1/20 0.65
CYP3A4 P08684 1/20 0.65
CASP1 P29466 1/20 0.65
GNAI1 P63096 1/20 0.65
HIF1A Q16665 1/20 0.65
USP2 O75604 1/20 0.31
NOS1 P29475 1/20 0.31
PAH P00439 1/20 0.31
ALDH1A1 P00352 1/20 0.30
GLA P06280 1/20 0.30
HPGD P15428 1/20 0.30
PMP22 Q01453 1/20 0.30

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Sepiapterin SCHEMBL8288993 0.79 HSD17B10 (1.00) CASP7HSD17B10KDM4EMAPTBLM
Sepiapterin SCHEMBL7943016 0.79 HSD17B10 (1.00) CASP7HSD17B10KDM4EMAPTBLM
Sepiapterin SCHEMBL20374908 0.79 HSD17B10 (1.00) CASP7HSD17B10KDM4EMAPTBLM
SCHEMBL31673801 0.77 HSD17B10 (0.39) CASP7HSD17B10KDM4EMAPTBLM
SCHEMBL12559341 0.77 HSD17B10 (0.39) CASP7HSD17B10KDM4EMAPTBLM
SCHEMBL258510 0.77 HSD17B10 (0.39) CASP7HSD17B10KDM4EMAPTBLM
SCHEMBL22971947 0.77 HSD17B10 (0.39) CASP7HSD17B10KDM4EMAPTBLM
SCHEMBL13721723 0.76 KDM4E (0.38) CASP7HSD17B10KDM4EMAPTBLM
SCHEMBL7077081 0.74 KDM4E (0.33) CASP7HSD17B10KDM4EMAPTBLM
SCHEMBL7362056 0.74 KDM4E (0.33) CASP7HSD17B10KDM4EMAPTBLM

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 1022 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
EP-4748370-A2 COMPOSITIONS AND METHODS FOR INCREASING TETRAHYDROBIOPTERIN PLASMA EXPOSURE PTC Therapeutics MP, Inc. (US) 2026-05-27 EP claimed
US-12637465-B2 Pharmaceutically acceptable salts of sepiapterin PTC THERAPEUTICS MP, INC. (US) 2026-05-26 US claimed
US-20260137729-A1 RECOMBINANT BACTERIA EXPRESSING PHENYLALANINE AMMONIA LYASE, PHENYLALANINE TRANSPORTER AND L-AMINO ACID DEAMINASE FOR REDUCING HYPERPHENYLALANINEMIA SYNLOGIC OPERATING COMPANY, INC. (US) 2026-05-21 US claimed
US-20260091037-A1 METHODS FOR INCREASING SEPIAPTERIN PLASMA EXPOSURE PTC THERAPEUTICS MP INC (US) 2026-04-02 US claimed
EP-3801534-B1 TREATMENT OF PHENYLKETONURIA WITH SEPIAPTERIN PTC THERAPEUTICS MP INC (US) 2026-02-18 EP claimed
EP-4034122-B1 METHODS FOR TREATING HYPERPHENYLALANINEMIA PTC THERAPEUTICS MP INC (US) 2025-08-13 EP claimed
US-20250230164-A1 POLYMORPHS OF SEPIAPTERIN AND SALTS THEREOF CENSA PHARMACEUTICALS INC. 2025-07-17 US claimed
US-20250195529-A1 COMPOSITIONS AND METHODS FOR INCREASING TETRAHYDROBIOPTERIN PLASMA EXPOSURE PTC THERAPEUTICS MP, INC. 2025-06-19 US claimed
US-20250195526-A1 PHARMACEUTICAL COMPOSITIONS COMPRISING SEPIAPTERIN AND USES THEREOF PTC THERAPEUTICS MP, INC. 2025-06-19 US claimed
US-12329757-B2 Methods for increasing sepiapterin plasma exposure PTC THERAPEUTICS MP, INC. (US) 2025-06-17 US claimed
EP-1530463-A1 L-ARGININE CONTAINING PHARMACEUTICAL COMPOSITION Vasopharm Biotech GmbH (DE) 2005-05-18 EP claimed
WO-2005018620-A2 USE OF NITRIC OXIDE SYNTHASE (NOS) COFACTOR FOR THE TREATMENT OF SEXUAL DYSFUNCTION CELL CENTER COLOGNE GMBH (DE) 2005-03-03 WO claimed
EP-1202736-A4 NICOTINE IN THERAPEUTIC ANGIOGENESIS AND VASCULOGENESIS UNIV LELAND STANFORD JUNIOR (US) 2004-05-19 EP claimed
WO-2004017955-A1 L-ARGININE CONTAINING PHARMACEUTICAL COMPOSITION VASOPHARM BIOTECH GMBH (DE) 2004-03-04 WO claimed
US-20020128294-A1 Nicotine in therapeutic angiogenesis and vasculogenesis BOARD OF TRUSTEES OF THE LELAND STANFORD JUNIOR UNIVERSITY, THE 2002-09-12 US claimed
US-6417205-B1 Nicotine in therapeutic angiogenesis and vasculogenesis THE BOARD OF TRUSTEES OF THE LELAND STANFORD JR. UNIVERSITY 2002-07-09 US claimed
EP-1202736-A1 NICOTINE IN THERAPEUTIC ANGIOGENESIS AND VASCULOGENESIS THE BOARD OF TRUSTEES OF THE LELAND STANFORD JUNIOR UNIVERSITY (US) 2002-05-08 EP claimed
WO-2001008684-A1 NICOTINE IN THERAPEUTIC ANGIOGENESIS AND VASCULOGENESIS THE BOARD OF TRUSTEES OF THE LELAND STANFORD JUNIOR UNIVERSITY (US) 2001-02-08 WO claimed
EP-0278040-B1 USE OF PTERIDINES AND/OR PURINES OR OF A XANTHINEOXIDASE INHIBITOR FOR THE PREPARATION OF A MEDICAMENT FOR THE TREATMENT OF HEREDITARY DEGENERATIVE RETINAL DISEASES PHARM-ALLERGAN GMBH (DE) 1991-08-14 EP claimed
EP-0278040-A1 Use of pteridines and/or purines or of a xanthineoxidase inhibitor for the preparation of a medicament for the treatment of hereditary degenerative retinal diseases PHARM-ALLERGAN GMBH (DE) 1988-08-17 EP claimed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (7 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-20250230164-A1 POLYMORPHS OF SEPIAPTERIN AND SALTS THEREOF SPR, PAH, SORD CASP7 1781/4885HSD17B10 251/4885KDM4E 1231/4885
US-20260091037-A1 METHODS FOR INCREASING SEPIAPTERIN PLASMA EXPOSURE PAH, KMO, SHMT1 CASP7 3851/4885HSD17B10 134/4885KDM4E 764/4885
US-12329757-B2 Methods for increasing sepiapterin plasma exposure SPR, BHMT, BHMT2 CASP7 2442/4885HSD17B10 624/4885KDM4E 414/4885
US-20250195529-A1 COMPOSITIONS AND METHODS FOR INCREASING TETRAHYDROBIOPTERIN PLASMA EXPOSURE SPR, BHMT2, BHMT CASP7 2309/4885HSD17B10 198/4885KDM4E 570/4885
US-12637465-B2 Pharmaceutically acceptable salts of sepiapterin PAH, QDPR, SPR CASP7 4080/4885HSD17B10 107/4885KDM4E 2101/4885
US-20260137729-A1 RECOMBINANT BACTERIA EXPRESSING PHENYLALANINE AMMONIA LYASE, PHENYLALANINE TRANSPORTER AND L-AMINO ACID DEAMINASE FOR REDUCING HYPERPHENYLALANINEMIA ALAD, SLC1A5, ADA CASP7 3374/4885HSD17B10 566/4885KDM4E 2028/4885
US-20250195526-A1 PHARMACEUTICAL COMPOSITIONS COMPRISING SEPIAPTERIN AND USES THEREOF SPR, PCSK9, SLC6A7 CASP7 2399/4885HSD17B10 229/4885KDM4E 2569/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.