Sapropterin

Sapropterin

SCHEMBL260185

C[C@H](O)[C@H](O)[C@H]1CNc2nc(N)[nH]c(=O)c2N1

nearest known ligand 1.00 ✓ in ChEMBL — recovers established targets

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

PAH

The experimentally established mechanism targets of Sapropterin. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
PAH known ✓ P00439 1/20 0.81
NOS1 P29475 10/20 1.00
CASP7 P55210 2/20 1.00
HSD17B10 Q99714 2/20 1.00
USP2 O75604 1/20 1.00
KDM4E B2RXH2 2/20 0.97
MAPT P10636 2/20 0.97
BLM P54132 2/20 0.97
KMT2A Q03164 2/20 0.97
ALDH1A1 P00352 1/20 0.97
GLA P06280 1/20 0.97
HPGD P15428 1/20 0.97
PMP22 Q01453 1/20 0.97
NPSR1 Q6W5P4 1/20 0.97
TDP1 Q9NUW8 1/20 0.97
NOS3 P29474 3/20 0.62
NOS2 P35228 3/20 0.62
MEN1 O00255 1/20 0.41
RGS12 O14924 1/20 0.41
LMNA P02545 1/20 0.41

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Sapropterin SCHEMBL21068033 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL4217501 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL29538547 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL29351671 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL7942378 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL29059706 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL14072498 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL14401407 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL31106620 0.99 KDM4E (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL1070424 0.99 KDM4E (1.00) NOS1CASP7HSD17B10USP2KDM4E

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 1445 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-20260148848-A1 BIOMARKERS FOR DIAGNOSIS AND TREATMENT OF ENDOCRINE HYPERTENSION, AND METHODS OF IDENTIFICATION THEREOF INSERM (INSTITUT NATIONAL DE LA SANTE ET DE LA RECHERCHE MEDICALE) (FR) 2026-05-28 US claimed
CN-122079949-A Near-infrared xanthene dye with adjustable structural symmetry and preparation method and application thereof 2026-05-26 CN claimed
CN-122059999-A Sulfur/carbon ligand bridged bimetallic complex, preparation method thereof and application thereof in dehalogenation of chloro/bromo alkane into corresponding alkane or alkene 大连理工大学 2026-05-19 CN claimed
CN-122030342-A Construction and maintenance method of brown planthopper pest-caused experimental population 广西壮族自治区农业科学院 2026-05-15 CN claimed
EP-4735457-A2 E-SELECTIVE METATHESIS CATALYSTS Verbio SE (DE) 2026-05-06 EP claimed
US-20250372660-A1 HIGH-ENERGY LITHIUM METAL BATTERIES ACHIEVED BY INORGANIC AND ORGANIC COATINGS BOARD OF TRUSTEES OF THE UNIVERSITY OF ARKANSAS (US) 2025-12-04 US claimed
EP-4642770-A1 TRIARYLSULFONIUM BASED PHOTOINITIATORS FOR LED CURE OF CATIONIC, FREE RADICAL AND HYBRID CATIONIC/FREE RADICAL FORMULATIONS ARKEMA France (FR) 2025-11-05 EP claimed
US-12404221-B2 Methods of arene alkenylation UNIVERSITY OF VIRGINIA PATENT FOUNDATION (US) 2025-09-02 US claimed
US-20250262613-A1 RARE EARTH AND GROUP 4 CATALYSTS FOR AMBIENT CONVERSION OF DINITROGEN TO SECONDARY SILYLAMINES THE REGENTS OF THE UNIVERSITY OF CALIFORNIA (US) 2025-08-21 US claimed
US-20250206918-A1 COMPOSITIONS AND METHODS FOR THE FABRICATION OF SUPRAMOLECULAR MATERIALS WITH NANOSTRUCTURES AND SPATIALLY DISTINCT FEATURES THE UNIVERSITY OF HONG KONG (CN) 2025-06-26 US claimed
CN-112812230-B Catalytic load polymer and preparation method and application thereof 浙江大学 2022-03-25 CN claimed
WO-2022056272-A1 ORGANO-ALUMINUM ANALYTES FOR NONAQUEOUS REDOX FLOW BATTERIES THE REGENTS OF THE UNIVERSITY OF CALIFORNIA (US) 2022-03-17 WO claimed
CN-114163627-A Double-function double-metal catalyst and its application 大连理工大学 2022-03-11 CN claimed
US-11260379-B2 Catalysts and methods for epoxide-based polymerizations CORNELL UNIVERSITY (US) 2022-03-01 US claimed
US-11248074-B2 Method for producing copolymer of polar group-containing allyl monomer THE UNIVERSITY OF TOKYO (JP) 2022-02-15 US claimed
CN-112851924-B Recyclable nitrogen-containing polycarbonate plastic synthesis method 大连理工大学 2022-02-15 CN claimed
CN-114040962-A Red fluorescence emitting compounds for organelle imaging 香港科技大学 2022-02-11 CN claimed
US-20220033740-A1 STAIN REMOVAL THROUGH NOVEL OXIDIZER AND CHELANT COMBINATION ECOLAB USA INC. 2022-02-03 US claimed
US-20170042899-A1 Use of Tetrahydrobiopterine Derivatives in the Treatment and Nutrition of Patients With Amino Acid Metabolic Disorders BIOMARIN PHARM INC (US) 2017-02-16 US claimed
US-20060211701-A1 Use of von tetrahydrobiopterine derivatives in the treatment and nutrition of patients with amino acid metabolic disorders BIOMARIN PHARMACEUTICAL INC. 2006-09-21 US claimed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (5 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-20060211701-A1 Use of von tetrahydrobiopterine derivatives in the treatment and nutrition of patients with amino acid metabolic disorders PAH, BCAT1, AADAT PAH 1/4885NOS1 671/4885CASP7 4768/4885
US-20250206918-A1 COMPOSITIONS AND METHODS FOR THE FABRICATION OF SUPRAMOLECULAR MATERIALS WITH NANOSTRUCTURES AND SPATIALLY DISTINCT FEATURES VCL, PICALM, SOD1 PAH 2648/4885NOS1 1634/4885CASP7 1998/4885
US-12404221-B2 Methods of arene alkenylation CYBB, CBR3, AHR PAH 264/4885NOS1 2135/4885CASP7 799/4885
US-20260148848-A1 BIOMARKERS FOR DIAGNOSIS AND TREATMENT OF ENDOCRINE HYPERTENSION, AND METHODS OF IDENTIFICATION THEREOF SHBG, HSD11B2, HSD11B1 PAH 83/4885NOS1 331/4885CASP7 4485/4885
US-20170042899-A1 Use of Tetrahydrobiopterine Derivatives in the Treatment and Nutrition of Patients With Amino Acid Metabolic Disorders PAH, AADAT, BCAT1 PAH 1/4885NOS1 545/4885CASP7 4674/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.