Sapropterin

Sapropterin

SCHEMBL7942378

CC(O)C(O)C1CNc2nc(N)[nH]c(=O)c2N1

nearest known ligand 1.00 ✓ in ChEMBL — recovers established targets

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

PAH

The experimentally established mechanism targets of Sapropterin. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 20)

geneUniProtsupporting neighboursconfidence
PAH known ✓ P00439 1/20 0.81
NOS1 P29475 10/20 1.00
CASP7 P55210 2/20 1.00
HSD17B10 Q99714 2/20 1.00
USP2 O75604 1/20 1.00
KDM4E B2RXH2 2/20 0.97
MAPT P10636 2/20 0.97
BLM P54132 2/20 0.97
KMT2A Q03164 2/20 0.97
ALDH1A1 P00352 1/20 0.97
GLA P06280 1/20 0.97
HPGD P15428 1/20 0.97
PMP22 Q01453 1/20 0.97
NPSR1 Q6W5P4 1/20 0.97
TDP1 Q9NUW8 1/20 0.97
NOS3 P29474 3/20 0.62
NOS2 P35228 3/20 0.62
MEN1 O00255 1/20 0.41
RGS12 O14924 1/20 0.41
LMNA P02545 1/20 0.41

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
Sapropterin SCHEMBL21068033 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL4217501 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL29538547 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL29351671 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL29059706 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL14072498 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL260185 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL14401407 1.00 NOS1 (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL31106620 0.99 KDM4E (1.00) NOS1CASP7HSD17B10USP2KDM4E
Sapropterin SCHEMBL1070424 0.99 KDM4E (1.00) NOS1CASP7HSD17B10USP2KDM4E

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 25 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-20220268782-A1 METHODS FOR PREDICTING AND TREATING CARDIAC DYSFUNCTION INSERM INSTITUT NATIONAL DE LA SANTE EAT DE LA RECH MEDICALE (FR) 2022-08-25 US disclosed
EP-3999071-A1 METHODS FOR PREDICTING AND TREATING CARDIAC DYSFUNCTION Institut National de la Santé et de la Recherche Médicale (INSERM) (FR) 2022-05-25 EP disclosed
EP-3977999-A1 TREATMENT OF PHENYLKETONURIA WITH BH4 BioMarin Pharmaceutical Inc. (US) 2022-04-06 EP disclosed
US-10738335-B2 Methods of producing nor-opioid and nal-opioid benzylisoquinoline alkaloids ANTHEIA, INC. (US) 2020-08-11 US disclosed
US-20190144900-A1 METHODS OF PRODUCING NOR-OPIOID AND NAL-OPIOID BENZYLISOQUINOLINE ALKALOIDS HERCULES CAPITAL, INC., AS AGENT 2019-05-16 US disclosed
EP-2309983-B1 PHARMACEUTICAL FORM COMPRISING TETRAHYDROBIOPTERIN ORPHA SWISS GMBH (CH) 2019-04-24 EP disclosed
US-20170042899-A1 Use of Tetrahydrobiopterine Derivatives in the Treatment and Nutrition of Patients With Amino Acid Metabolic Disorders BIOMARIN PHARM INC (US) 2017-02-16 US disclosed
US-20170042899-A1 Use of Tetrahydrobiopterine Derivatives in the Treatment and Nutrition of Patients With Amino Acid Metabolic Disorders BIOMARIN PHARM INC (US) 2017-02-16 US disclosed
US-20160251691-A1 Compositions Comprising A Polypeptide Having Cellulolytic Enhancing Activity And A Nitrogen-Containing Compound And Uses Thereof NOVOZYMES INC (US) 2016-09-01 US disclosed
US-9353391-B2 Compositions comprising a polypeptide having cellulolytic enhancing activity and a nitrogen-containing compound and uses thereof NOVOZYMES, INC. (US) 2016-05-31 US disclosed
US-20110144117-A1 Pharmaceutical Dosage Form Containing Tetrahydrobiopterin ORPHA SWISS GMBH (CH) 2011-06-16 US disclosed
US-7820667-B2 Methods of treating hypertension DAIICHI SANKYO COMPANY, LIMITED (JP) 2010-10-26 US disclosed
US-7820667-B2 Methods of treating hypertension DAIICHI SANKYO COMPANY, LIMITED (JP) 2010-10-26 US disclosed
WO-2010017570-A2 PHARMACEUTICAL FORM COMPRISING TETRAHYDROBIOPTERIN ORPHA SWISS GMBH (CH) 2010-02-18 WO disclosed
US-20080221111-A1 Roflumilast and sepiapterin; (6R)-L-erythro-5,6,7,8-tetrahydrobiopterin; prevention, treatment of respiratory diseases NYCOMED GMBH (DE) 2008-09-11 US disclosed
US-20080221111-A1 Roflumilast and sepiapterin; (6R)-L-erythro-5,6,7,8-tetrahydrobiopterin; prevention, treatment of respiratory diseases NYCOMED GMBH (DE) 2008-09-11 US disclosed
US-20070049599-A1 Use of bh4 for the treatment of respiratory diseases ALTANA PHARMA AG (DE) 2007-03-01 US disclosed
US-20070049599-A1 Use of bh4 for the treatment of respiratory diseases ALTANA PHARMA AG (DE) 2007-03-01 US disclosed
WO-2006120176-A2 COMBINATION OF THE PDE4 INHIBITOR ROFLUMILAST AND A TETRAHYDROBIOPTERIN DERIVATIVE NYCOMED GMBH (DE) 2006-11-16 WO disclosed
WO-2005041975-A1 USE OF BH4 FOR THE TREATMENT OF RESPIRATORY DISEASES ALTANA PHARMA AG (DE) 2005-05-12 WO disclosed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (4 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-20070049599-A1 Use of bh4 for the treatment of respiratory diseases BHMT, BHMT2, PAH PAH 3/4885NOS1 233/4885CASP7 3145/4885
US-20080221111-A1 Roflumilast and sepiapterin; (6R)-L-erythro-5,6,7,8-tetrahydrobiopterin; prevention, treatment of respiratory diseases SPR, PAH, QDPR PAH 2/4885NOS1 264/4885CASP7 1166/4885
US-20170042899-A1 Use of Tetrahydrobiopterine Derivatives in the Treatment and Nutrition of Patients With Amino Acid Metabolic Disorders PAH, AADAT, BCAT1 PAH 1/4885NOS1 545/4885CASP7 4674/4885
US-20110144117-A1 Pharmaceutical Dosage Form Containing Tetrahydrobiopterin QDPR, MTHFD2, DHODH PAH 18/4885NOS1 611/4885CASP7 2361/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.