Ot-551

Ot-551

SCHEMBL3696276

CC1(C)CC(OC(=O)C2CC2)CC(C)(C)N1O.Cl

nearest known ligand 0.48

Full drug profile on Sugi Atlas →

Known targets — ChEMBL curated mechanism

ABL1ACEACHEACVR1ADRA1AADRA1BADRA1DADRA2AADRA2BADRA2CADRB1ADRB2ADRB3AGTR1ALKAVPR1AAVPR2BCHEBCRCA2CACNA1ACACNA1BCACNA1CCACNA1DCACNA1ECACNA1FCACNA1GCACNA1HCACNA1ICACNA1SCACNA2D1CACNA2D2CACNA2D3CACNA2D4CACNB1CACNB2CACNB3CACNB4CACNG1CACNG2CACNG3CACNG4CACNG5CACNG6CACNG7CACNG8CALCRLCASRCCR5CDK4CDK6CFBCHRM1CHRM2CHRM3CHRM4CHRM5CHRNA1CHRNA3CHRNA7CHRNB1CHRNB4CHRNDCHRNECHRNGCOXFA4COXFA4L2CRBNCSF1RCUL4ACYP19A1DDB1DPP4DRD1DRD2DRD3DRD4EDNRAEGFREML4ERBB2ERBB4ESR1ESR2FGFR1FGFR3FLT1FLT3FLT4GAAGABRA1GABRA2GABRA3GABRA4GABRA5GABRA6GABRB1GABRB2GABRB3GABRDGABREGABRG1GABRG2GABRG3GABRPGABRQGHSRGLAGNRHRGPD2GRIN1GRIN2AGRIN2BGRIN2CGRIN2DGRIN3AGRIN3BGSTP1HCN4HCRTR1HCRTR2HDAC1HDAC10HDAC11HDAC2HDAC3HDAC4HDAC5HDAC6HDAC7HDAC8HDAC9HRH1HRH2HRH3HSD11B1HSP90AA1HSP90AB1HTR1AHTR1BHTR1DHTR1EHTR1FHTR2AHTR2BHTR2CHTR3AHTR3BHTR3CHTR3DHTR3EHTR4HTR5AHTR6HTR7IMPDH1IMPDH2ITGA2BITGB3ITKJAK1JAK2KCNA1KCNA10KCNA2KCNA3KCNA4KCNA5KCNA6KCNA7KCNB1KCNB2KCNC1KCNC2KCNC3KCNC4KCND1KCND2KCND3KCNF1KCNG1KCNG2KCNG3KCNG4KCNH1KCNH2KCNH3KCNH4KCNH5KCNH6KCNH7KCNH8KCNJ2KCNJ3KCNJ5KCNK3KCNK9KCNQ1KCNQ2KCNQ3KCNQ4KCNQ5KCNS1KCNS2KCNS3KCNV1KCNV2KDRKITKLKB1LCKMMAOAMAOBMAPK14METMMP1MMP13MMP7MMP8MT-ND1MT-ND2MT-ND3MT-ND4MT-ND4LMT-ND5MT-ND6NDUFA1NDUFA10NDUFA11NDUFA12NDUFA13NDUFA2NDUFA3NDUFA5NDUFA6NDUFA7NDUFA8NDUFA9NDUFAB1NDUFAF1NDUFAF2NDUFAF3NDUFAF4NDUFB1NDUFB10NDUFB11NDUFB2NDUFB3NDUFB4NDUFB5NDUFB6NDUFB7NDUFB8NDUFB9NDUFC1NDUFC2NDUFS1NDUFS2NDUFS3NDUFS4NDUFS5NDUFS6NDUFS7NDUFS8NDUFV1NDUFV2NDUFV3NR3C1NS5ANTRK1NTRK2NTRK3ODC1OPRD1OPRK1OPRM1P2RY12PAHPARP1PDE3APDE3BPDE4APDE4BPDE4CPDE4DPDE5APDE7APDE7BPDE8APDE8BPDGFRAPDGFRBPIK3CAPIK3CDPNPPOLA1POLA2POLD1POLD2POLD3POLD4POLEPOLE2POLE3PPARGPRIM1PRIM2PRKCAPRKCBPRKCDPRKCEPRKCGPRKCHPRKCIPRKCQPRKCZPRKD1PRKD3PTGS1PTGS2RBX1RENRETROCK1ROCK2RPE65RRM1RRM2RRM2BS1PR1S1PR2S1PR3S1PR4S1PR5SCN10ASCN11ASCN1ASCN2ASCN3ASCN4ASCN5ASCN7ASCN8ASCN9ASCNN1ASCNN1BSCNN1GSIGMAR1SLC18A2SLC6A1SLC6A2SLC6A3SLC6A4SLC9A3SRCTACR1TOP1TOP2ATOP2BTTRTYMPdacAdacBdacCembAfolAftsIgyrAgyrBmrcAmrcBmrdAparCparEpolrplArplBrplCrplDrplErplFrplIrplJrplKrplLrplMrplNrplOrplPrplQrplRrplSrplTrplUrplVrplWrplXrplYrpmArpmBrpmCrpmDrpmErpmE2rpmFrpmGrpmG1rpmG2rpmG3rpmHrpmIrpmJrpsArpsBrpsCrpsDrpsErpsFrpsGrpsHrpsIrpsJrpsKrpsLrpsMrpsNrpsOrpsPrpsQrpsRrpsSrpsTrpsUykgMykgO

The experimentally established mechanism targets of Ot-551. The predicted profile below is derived independently by chemical similarity — agreement is a validation signal, a miss is honest.

Predicted protein targets (top 12)

geneUniProtsupporting neighboursconfidence
GAA known ✓ P10253 4/20 0.48
ESR1 known ✓ P03372 1/20 0.32
HTT P42858 2/20 0.48
L3MBTL1 Q9Y468 1/20 0.34
KDM4E B2RXH2 2/20 0.34
TSHR P16473 2/20 0.33
KMT2A Q03164 2/20 0.33
LMNA P02545 1/20 0.32
ALDH1A1 P00352 2/20 0.32
HSD17B10 Q99714 1/20 0.32
ALOX15 P16050 1/20 0.31
CYP2D6 P10635 1/20 0.30

Click a target to see other patent compounds predicted against it — the reverse direction, in place.

Similar compounds — the chemically nearest patent molecules

Nearest neighbours by Morgan-fingerprint cosine across the patent-compound collection, with each neighbour's top predicted target and the predicted targets it shares with this molecule.

Compoundsimilaritytop predictedshared targets
SCHEMBL7508350 0.98 GAA (0.46) GAAHTTL3MBTL1KDM4ETSHR
Ot-551 SCHEMBL3692374 0.98 GAA (0.46) GAAHTTL3MBTL1KDM4ETSHR
SCHEMBL1535623 0.98 GAA (0.46) GAAHTTL3MBTL1KDM4ETSHR
SCHEMBL19976794 0.92 HTT (0.42) GAAHTTL3MBTL1TSHRKMT2A
SCHEMBL19636872 0.92 GAA (0.42) GAAHTTL3MBTL1TSHRKMT2A
SCHEMBL19884611 0.90 GAA (0.41) GAAHTTL3MBTL1TSHRKMT2A
SCHEMBL19636873 0.90 GAA (0.43) GAAHTTL3MBTL1TSHRKMT2A
SCHEMBL13554257 0.89 GAA (0.40) GAAHTTL3MBTL1TSHRKMT2A
SCHEMBL17931223 0.88 GAA (0.39) GAAHTTL3MBTL1
SCHEMBL22241054 0.88 GAA (0.39) GAAHTT

Similarity is cosine over the 2,048-bit Morgan fingerprint (≈ Tanimoto). Identical fingerprints score 1.00.

Patent provenance — the patents this molecule appears in, and who filed them

Claimed or disclosed in 44 patents — showing the first 20. claimed = in the patent's claims; disclosed = body only.

PatentTitleAssigneePublishedPriorityFilingCountryStatus
US-20240050371-A1 W/O/W MICROEMULSIONS FOR OCULAR ADMINISTRATION UNIVERSITY OF TENNESSEE RESEARCH FOUNDATION (US) 2024-02-15 US claimed
US-20210386722-A1 Treatment of Covid-19 with Nitroxides PROCTOR PETER HERBERT (US) 2021-12-16 US claimed
US-20200383915-A1 W/O/W MICROEMULSIONS FOR OCULAR ADMINISTRATION UNIVERSITY OF TENNESSEE RESEARCH FOUNDATION 2020-12-10 US claimed
US-7589107-B2 Amelioration of vitrectomy-induced cataracts OTHERA HOLDING, INC. (US) 2009-09-15 US claimed
US-20080312283-A1 Use of Hydroxylamine Derivates for Inhibiting Vitrectomy-Induced Cataracts OTHERA PHARMACEUTICALS, INC. (US) 2008-12-18 US claimed
US-20060292190-A1 Amelioration of vitrectomy-induced cataracts OTHERA PHARMACEUTICALS, INC. (US) 2006-12-28 US claimed
WO-2006127592-A2 USE OF HYDROXYLAMINE DERIVATES FOR INHIBITING VITRECTOMY-INDUCED CATARACTS OTHERA PHARMACEUTICALS, INC. (US) 2006-11-30 WO claimed
US-20250041219-A1 W/O/W MICROEMULSIONS FOR OCULAR ADMINISTRATION UNIVERSITY OF TENNESSEE RESEARCH FOUNDATION 2025-02-06 US disclosed
US-20240423937-A1 METHODS OF TREATING PAIN AND USES THEREOF UNIVERSITY OF TENNESSEE RESEARCH FOUNDATION 2024-12-26 US disclosed
US-20240156765-A1 METHODS OF NEUROPROTECTION AND USES THEREOF UNIVERSITY OF TENNESSEE RESEARCH FOUNDATION 2024-05-16 US disclosed
US-20240050371-A1 W/O/W MICROEMULSIONS FOR OCULAR ADMINISTRATION UNIVERSITY OF TENNESSEE RESEARCH FOUNDATION (US) 2024-02-15 US disclosed
US-20240041808-A1 METHODS OF NEUROPROTECTION AND USES THEREOF UNIVERSITY OF TENNESSEE RESEARCH FOUNDATION 2024-02-08 US disclosed
US-11826467-B2 W/O/W microemulsions for ocular administration UNIVERSITY OF TENNESSEE RESEARCH FOUNDATION (US) 2023-11-28 US disclosed
WO-2006127592-A2 USE OF HYDROXYLAMINE DERIVATES FOR INHIBITING VITRECTOMY-INDUCED CATARACTS OTHERA PHARMACEUTICALS, INC. (US) 2006-11-30 WO disclosed
EP-1689354-A2 AMELIORATION OF CATARACTS, MACULAR DEGENERATION AND OTHER OPHTHALMIC DISEASES Othera Pharmaceuticals, Inc. (US) 2006-08-16 EP disclosed
WO-2005055926-A2 AMELIORATION OF CATARACTS, MACULAR DEGENERATION AND OTHER OPHTHALMIC DISEASES OTHERA PHARMACEUTICALS, INC. (US) 2005-06-23 WO disclosed
US-20050131025-A1 Amelioration of cataracts, macular degeneration and other ophthalmic diseases COLBY PHARMACEUTICAL COMPANY 2005-06-16 US disclosed
EP-1507826-A2 AMELIORATION OF THE DEVELOPMENT OF CATARACTS AND OTHER OPTHALMIC DISEASES Othera Pharmaceuticals, Inc. (US) 2005-02-23 EP disclosed
US-20040002461-A1 Amelioration of the development of cataracts and other ophthalmic diseases COLBY PHARMACEUTICAL COMPANY 2004-01-01 US disclosed
WO-2003096991-A2 AMELIORATION OF THE DEVELOPMENT OF CATARACTS AND OTHER OPTHALMIC DISEASES OTHERA PHARMACEUTICALS, INC. (US) 2003-11-27 WO disclosed

Patent text — is the patent's own abstract consistent with the prediction?

For each of this compound's patents that has machine-readable text (7 of them — usually the abstract, not the full specification), we ask MedCPT which protein the text reads most about, and where the chemistry-predicted target lands among 4885 human targets. A high rank means the patent's own wording is consistent with the prediction — a weak, independent signal, not proof of activity.

PatentTitleText reads most aboutPredicted target · text-rank
US-20240041808-A1 METHODS OF NEUROPROTECTION AND USES THEREOF NLN, BDNF, GAP43 GAA 1315/4885ESR1 4854/4885HTT 40/4885
US-20060292190-A1 Amelioration of vitrectomy-induced cataracts CRYAB, CRYAA, VIM GAA 1847/4885ESR1 4731/4885HTT 15/4885
US-20240423937-A1 METHODS OF TREATING PAIN AND USES THEREOF ACHE, PDE6G, PTGES3 GAA 1080/4885ESR1 4826/4885HTT 1470/4885
US-20240156765-A1 METHODS OF NEUROPROTECTION AND USES THEREOF NLN, BDNF, GAP43 GAA 1315/4885ESR1 4854/4885HTT 40/4885
US-20050131025-A1 Amelioration of cataracts, macular degeneration and other ophthalmic diseases C1R, CRYAB, C9 GAA 4234/4885ESR1 3747/4885HTT 331/4885
US-20080312283-A1 Use of Hydroxylamine Derivates for Inhibiting Vitrectomy-Induced Cataracts CRYAB, CRYAA, HAAO GAA 2623/4885ESR1 4617/4885HTT 6/4885
US-20040002461-A1 Amelioration of the development of cataracts and other ophthalmic diseases PDE6D, PDE6H, CCR1 GAA 3517/4885ESR1 4785/4885HTT 115/4885

“Text reads most about” is the patent abstract's nearest protein in MedCPT space (background-debiased). Only ~1.4% of patents have machine-readable text, so most compounds won't have this panel.